Elevidys EXPEDITION 3期临床试验
研究概览
- 年龄
- 2岁及以上
- 阶段
- 干预性
- 申办方
- Sarepta Therapeutics
- 治疗方式
- 基因治疗
- 变异要求
- 本研究旨在通过单一临床试验以统一方法监测既往临床研究中接受Elevidys的参与者的长期安全性和疗效。本研究不会给予任何研究药物。
- 适用性别
- 男性
- 行走能力
- 可行走与不可行走
- 研究开始（实际）
- 2023-09-27
- 主要完成（预计）
- 2033-10-31
- 研究完成（预计）
- 2033-10-31
- 入组人数（预计）
- 400
- 国家
- 美国比利时德国中国香港特别行政区意大利日本西班牙台湾英国
研究要求与标准
纳入标准
- 在既往临床研究中接受过delandistrogene moxeparvovec治疗杜氏肌营养不良症
- 有父母或法定照护者，或≥18岁且能够理解并遵守研究访视计划及所有其他方案要求
排除标准
不适用
联系人与地点
联系人与地点
地点
本研究共有 38 个地点
United States
Arkansas 地点
Little Rock, Arkansas, United States, 72202
Arkansas Children's Hospital
California 地点
Los Angeles, California, United States, 90095
UCLA Medical Center
Palo Alto, California, United States, 94304
Lucile Packard Children's Hospital Stanford (LPCH)
Sacramento, California, United States, 95817
University of California, Davis
San Diego, California, United States, 92123
Rady Children's Hospital
Colorado 地点
Aurora, Colorado, United States, 80045-7106
Children's Hospital of Colorado
Florida 地点
Gainesville, Florida, United States, 32610
University of Florida Clinical Research Center
Illinois 地点
Chicago, Illinois, United States, 60611
Ann & Robert H. Lurie Children's Hospital of Chicago
Iowa 地点
Iowa City, Iowa, United States, 52242
University of Iowa ICTS Clinical Research Unit
Maryland 地点
Baltimore, Maryland, United States, 21287
The Johns Hopkins Hospital, Rubenstein Child Health Bldg
Massachusetts 地点
Boston, Massachusetts, United States, 02115
Boston Children's Hospital
Missouri 地点
St Louis, Missouri, United States, 63110
Washington University School of Medicine
New York 地点
New York, New York, United States, 10032
Columbia University Pediatric Neuromuscular Center
Rochester, New York, United States, 14642
University of Rochester Medical Center
North Carolina 地点
Durham, North Carolina, United States, 27705
Lenox Baker Children's Hospital (Duke University)
Ohio 地点
Columbus, Ohio, United States, 43205
Nationwide Children's Hospital
Oregon 地点
Portland, Oregon, United States, 97239
Oregon Health and Science University
Pennsylvania 地点
Philadelphia, Pennsylvania, United States, 19104
Chiildren's Hospital of Philadelphia
Texas 地点
Dallas, Texas, United States, 75207
Children's Health Specialty Center
Utah 地点
Salt Lake City, Utah, United States, 84132
University of Utah Health
Virginia 地点
Norfolk, Virginia, United States, 23510
Children's Hospital of The King's Daughters
Wisconsin 地点
Milwaukee, Wisconsin, United States, 53226
Children's Hospital Wisconsin
Belgium
East Flanders 地点
Ghent, East Flanders, Belgium, 9000
Universitair Ziekenhuis Gent, Neuromuscular Reference Centre (NMRC)
Germany
North Rhine-Westphalia 地点
Essen, North Rhine-Westphalia, Germany, 45147
Universitätsklinikum Essen - Klinik für Kinderheilkunde I
Hong Kong
Hong Kong, Hong Kong
Hong Kong Children's Hospital
Italy
Genova, Italy, 16147
UOC Neurologia Pediatrica e Malattie Muscolari, Istituto G. Gaslini, Istituto Pediatrico di Ricovero e Cura a Carattere Scientifico
Milan, Italy, 20122
UOC Neurologia, Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico
Roma, Italy, 00168
UOC Neuropsichiatria Infantile, Area Salute del Bambino, Fondazione Policlinico Universitario A. Gemelli IRCCS, Universita Cattoclica del Sacro Cuore
Japan
Hyōgo 地点
Kobe, Hyōgo, Japan, 650-0017
Kobe University Hospital
Tokyo 地点
Kodaira, Tokyo, Japan, 187-8551
National Center of Neurology and Psychiatry
Tokyo, Japan, 1628666
Tokyo Women's Medical University Hospital
Spain
Barcelona 地点
Esplugues de Llobregat, Barcelona, Spain, 08950
Hospital Sant Joan de Deu
Valencia, Spain, 46026
Hospital Universitario y Politecnico La fe. Neurology Department
Taiwan
Kaohsiung City, Taiwan, 807
Kaohsiung Medical University Chung-Ho Memorial Hospital
Taipei, Taiwan, 100225
National Taiwan University Hospital
United Kingdom
Greater London 地点
London, Greater London, United Kingdom, WC1N 1EJ
Great Ormond Street Hospital For Children NHS Foundation Trust
Oxfordshire 地点
Oxford, Oxfordshire, United Kingdom, OX3 9DU
Oxford University Hospitals NHS Foundation Trust
Newcastle upon Tyne, United Kingdom, NE1 3BZ
Institute of Translational and Clinical Research
临床试验注册
NCT 编号
NCT05967351本信息仅供教育参考。做出医疗决定前请务必咨询研究负责人。