AGAMREE（Vamorolone）临床试验长期安全性研究
研究概览
- 年龄
- 2岁及以上
- 阶段
- 观察性
- 申办方
- Catalyst Pharmaceuticals
- 治疗方式
- 减轻炎症
- 变异要求
- 患者目前持有AGAMREE的有效处方，或正在使用AGAMREE。
- 适用性别
- 男性
- 行走能力
- 可行走与不可行走
- 研究开始（实际）
- 2024-09-25
- 主要完成（预计）
- 2032-02
- 研究完成（预计）
- 2032-02
- 入组人数（预计）
- 250
- 国家
- 美国波多黎各
研究要求与标准
类固醇使用
尚未提供
纳入标准
- 在了解登记库性质并说明后，患者或父母/法定监护人愿意且能够签署书面知情同意书，并在任何登记相关程序开始前签署
- 患者和/或父母/监护人愿意且能够完成生活质量（QoL）问卷
- 男性患者至少2岁
- 经基因检测或肌肉活检（抗肌萎缩蛋白抗体3、1或2染色缺失，或抗肌萎缩蛋白免疫组化或Western blot）确认DMD（杜氏肌营养不良症）诊断
排除标准
任何AGAMREE®禁忌症或研究者认为会影响登记参与、表现或登记评估结果解读的医学状况。
联系人与地点
联系人与地点
联系人
- 姓名：Syune Nersisyan, PhD
- 电话号码：(305) 420-3200
- 邮箱：[email protected]
地点
本研究共有 33 个地点
United States
Arizona 地点
Phoenix, Arizona, United States, 85016
正在招募
Phoenix Children's Hospital
联系人: Saunder Bernes, MD
联系邮箱: [email protected]
联系电话: 602 933 0956
Arkansas 地点
Little Rock, Arkansas, United States, 72202
正在招募
Arkansas Childrens Hospital
联系人: Aravindhan Veerapandiyan, MD
联系邮箱: [email protected]
联系电话: (501) 364-1850
California 地点
Loma Linda, California, United States, 92354
尚未开始招募
Loma Linda University Pediatric Subspecialty Clinics
联系人: Monica Pizana
联系邮箱: [email protected]
联系电话: 909-558-5830
Los Angeles, California, United States, 90027
尚未开始招募
Children's Hospital Los Angeles
联系人: Dana O'Rourke, MD
联系邮箱: [email protected]
联系电话: 323 660 2450
Madera, California, United States, 93636
尚未开始招募
Valley Children's Hospital
联系人: Claudia Nayares
联系邮箱: [email protected]
联系电话: (559) 353-3000
Palo Alto, California, United States, 94305
尚未开始招募
Stanford University
联系人: Jenna Klotz, MD
联系电话: 408 426 5590
Sacramento, California, United States, 95817
尚未开始招募
University of California, Davis
联系人: Craig McDonald, MD
联系邮箱: [email protected]
联系电话: 916 734 7041
District of Columbia 地点
Washington D.C., District of Columbia, United States, 20010
尚未开始招募
Children's National Health System
联系人: Christopher Spurney, MD
联系邮箱: [email protected]
联系电话: 202-476-2185
Florida 地点
Gainesville, Florida, United States, 32610
尚未开始招募
University of Florida Clinical and Translational Science Institue
联系人: Julie Berthy, NP
联系邮箱: [email protected]
联系电话: 352 273 8700
Miami, Florida, United States, 33136
尚未开始招募
University of Miami
联系人: Branden Couto
联系邮箱: [email protected]
Miami, Florida, United States, 33155
正在招募
Nicklaus Children's Hospital
联系人: Migvis Monduy, MD
联系邮箱: [email protected]
联系电话: 305 663 8330
Orlando, Florida, United States, 32827
正在招募
Nemours Children's Hospital
联系人: Omer Abdul Hamid, MD
联系邮箱: [email protected]
联系电话: 407 650 7715
St. Petersburg, Florida, United States, 33701
尚未开始招募
Johns Hopkins All Children's Hospital
联系人: Susan Dvojack
联系邮箱: [email protected]
联系电话: 727-898-7451
Illinois 地点
Chicago, Illinois, United States, 60611
正在招募
Lurie Children's Hospital of Chicago
联系人: Nancy Kuntz, MD
联系邮箱: [email protected]
联系电话: 312 227 4000
Indiana 地点
Indianapolis, Indiana, United States, 46202
正在招募
Indiana University Health - Riley Hospital for Children
联系人: Marcia Felker, MD
联系邮箱: [email protected]
联系电话: 317 278 7364
Kansas 地点
Kansas City, Kansas, United States, 66205
正在招募
University of Kansas Medical Center
联系人: Jeffrey Statland, MD
联系邮箱: [email protected]
联系电话: 913 588 6970
Massachusetts 地点
North Worcester, Massachusetts, United States, 01655
正在招募
University of Massachusetts Memorial Medical Center
联系人: Stephen M. Chrzanowski, MD, PhD
联系邮箱: [email protected]
联系电话: (774) 441-7615
Michigan 地点
Grand Rapids, Michigan, United States, 49503
正在招募
Helen DeVos Children's Hospital
联系人: Jena Krueger, MD
联系邮箱: [email protected]
联系电话: 616-447-5836
Minnesota 地点
Minneapolis, Minnesota, United States, 55455
尚未开始招募
Masonic Children's Hospital - Discovery Clinic
联系人: Jenny Myhre
联系邮箱: [email protected]
联系电话: 612-365-6777
New York 地点
The Bronx, New York, United States, 10467-2403
尚未开始招募
The Children's Hospital at Montefiore
联系人: Channelle Mooyoung
联系邮箱: [email protected]
联系电话: (718) 920-4378
North Carolina 地点
Charlotte, North Carolina, United States, 28207
正在招募
Atrium Health Neurosciences Institute
联系人: Urvi Desai, MD
联系邮箱: [email protected]
联系电话: 704 468 0101
Durham, North Carolina, United States, 27710
正在招募
Duke University Medical Center and Childrens Health Center
联系人: Mai ElMallah, MD
联系邮箱: [email protected]
联系电话: (919) 681-3364
Ohio 地点
Cincinnati, Ohio, United States, 45229
正在招募
Cincinnati Children's Hospital Medical Center
联系人: Meghan McAnally, MD
联系邮箱: [email protected]
联系电话: 513 636 9285
Pennsylvania 地点
Hershey, Pennsylvania, United States, 17033
正在招募
Penn State Milton S. Hershey Medical Center- Penn State Hershey Neuroscience Institute
联系人: Dustin Paul, MD
联系邮箱: [email protected]
联系电话: 717-531-3828
Philadelphia, Pennsylvania, United States, 19104
正在招募
Children's Hospital of Philadelphia (CHOP)
联系人: Sabrina Yum, MD
联系邮箱: [email protected]
联系电话: 215 590 4719
Texas 地点
Dallas, Texas, United States, 75235
正在招募
University of Texas Southwestern Medical Center
联系人: Kaitlin Batley, MD
联系邮箱: [email protected]
联系电话: 214 456 9561
Denton, Texas, United States, 76208
正在招募
Neurology Rare Disease Center - Neurology & Neuromuscular Care Center
联系人: Diana Castro, MD
联系邮箱: [email protected]
联系电话: 972 982 7411
San Antonio, Texas, United States, 78229
正在招募
The University of Texas Health Science Center at San Antonio
联系人: Matthew Wicklund, MD
联系邮箱: [email protected]
联系电话: 210 450 0500
Virginia 地点
Charlottesville, Virginia, United States, 22903
正在招募
University of Virginia Health System (UVAHS) - Pediatric Neuromuscular Center
联系人: Rebecca Scharf, MD
联系邮箱: [email protected]
联系电话: 434 924 1647
Washington 地点
Seattle, Washington, United States, 98105
正在招募
Seattle Children's Hospital
联系人: Seth Perlman, MD
联系邮箱: [email protected]
联系电话: 206-987-0804
Wisconsin 地点
Milwaukee, Wisconsin, United States, 53226
尚未开始招募
Children's Wisconsin
联系人: Rebecca Rehborg
联系邮箱: [email protected]
联系电话: 877-607-5280
Puerto Rico
Puerto Rico 地点
San Juan, Puerto Rico, Puerto Rico, 00912
正在招募
San Jorge Children's Hospital
联系人: Yaritza Berrios
联系邮箱: [email protected]
联系电话: 787-758-2525
San Juan, Puerto Rico, Puerto Rico, 00927
正在招募
FDI Clinical Research
联系人: Alexandra Montalvo Acevedo, MD
联系邮箱: [email protected]
联系电话: 787 722 1248
临床试验注册
NCT 编号
NCT06564974本信息仅供教育参考。做出医疗决定前请务必咨询研究负责人。