{"id":8898,"date":"2026-10-30T14:28:56","date_gmt":"2026-10-30T11:28:56","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=8898"},"modified":"2026-10-30T14:35:21","modified_gmt":"2026-10-30T11:35:21","slug":"pepr-124-rt001-duchenne","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/ar\/pepr-124-rt001-duchenne\/","title":{"rendered":"PEPR-124 (RT001): \u062f\u0648\u0627\u0621 \u0645\u0631\u0634\u062d \u062a\u0645 \u0627\u0643\u062a\u0634\u0627\u0641\u0647 \u0628\u0648\u0627\u0633\u0637\u0629 \u0627\u0644\u0630\u0643\u0627\u0621 \u0627\u0644\u0627\u0635\u0637\u0646\u0627\u0639\u064a\u060c \u0648\u0644\u0627 \u064a\u0639\u062a\u0645\u062f \u0639\u0644\u0649 \u0627\u0644\u0637\u0641\u0631\u0627\u062a\u060c \u0644\u0639\u0644\u0627\u062c \u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a"},"content":{"rendered":"<p class=\"wp-block-paragraph\"><strong>PEPR-124 (\u0627\u0644\u0645\u0639\u0631\u0648\u0641 \u0623\u064a\u0636\u064b\u0627 \u0628\u0627\u0633\u0645 RT001) \u0647\u0648 \u062f\u0648\u0627\u0621 \u0645\u0631\u0634\u062d \u062a\u0645 \u0627\u0643\u062a\u0634\u0627\u0641\u0647 \u0628\u0648\u0627\u0633\u0637\u0629 \u0627\u0644\u0630\u0643\u0627\u0621 \u0627\u0644\u0627\u0635\u0637\u0646\u0627\u0639\u064a \u062a\u0645 \u062a\u0637\u0648\u064a\u0631\u0647 \u0628\u0648\u0627\u0633\u0637\u0629 \u0634\u0631\u0643\u0629 Peptris Technologies\u060c \u0648\u0647\u064a \u0634\u0631\u0643\u0629 \u0646\u0627\u0634\u0626\u0629 \u0645\u0642\u0631\u0647\u0627 \u0628\u0646\u063a\u0627\u0644\u0648\u0631\u0648 \u0641\u064a \u0627\u0644\u0647\u0646\u062f\u060c \u0648\u064a\u0633\u062a\u0647\u062f\u0641 \u0639\u0644\u0649 \u0648\u062c\u0647 \u0627\u0644\u062a\u062d\u062f\u064a\u062f \u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a (DMD).<\/strong><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u062a\u0623\u0633\u0633\u062a \u0634\u0631\u0643\u0629 \u0628\u064a\u0628\u062a\u0631\u064a\u0633 \u0639\u0627\u0645 \u0662\u0660\u0661\u0669\u060c \u0648\u062a\u0639\u0645\u0644 \u0627\u0646\u0637\u0644\u0627\u0642\u0627\u064b \u0645\u0646 \u0645\u0631\u0643\u0632 C-CAMP\u060c \u0648\u062a\u0633\u062a\u062e\u062f\u0645 \u0627\u0644\u0630\u0643\u0627\u0621 \u0627\u0644\u0627\u0635\u0637\u0646\u0627\u0639\u064a \u0648\u0627\u0644\u0643\u064a\u0645\u064a\u0627\u0621 \u0627\u0644\u062a\u0648\u0644\u064a\u062f\u064a\u0629 \u0644\u062a\u0635\u0645\u064a\u0645 \u062c\u0632\u064a\u0626\u0627\u062a \u0645\u064f\u062d\u0633\u0651\u0646\u0629 \u0644\u0639\u0644\u0627\u062c \u0623\u0645\u0631\u0627\u0636 \u0643\u0627\u0646\u062a \u062a\u064f\u0639\u062a\u0628\u0631 \u0633\u0627\u0628\u0642\u0627\u064b &quot;\u063a\u064a\u0631 \u0642\u0627\u0628\u0644\u0629 \u0644\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u062f\u0648\u0627\u0626\u064a&quot;\u060c \u0645\u062b\u0644 \u0627\u0644\u0623\u0645\u0631\u0627\u0636 \u0627\u0644\u0646\u0627\u062f\u0631\u0629 \u0648\u0627\u0644\u0633\u0631\u0637\u0627\u0646 \u0648\u0627\u0644\u0627\u0644\u062a\u0647\u0627\u0628\u0627\u062a. \u0648\u0628\u062f\u0639\u0645 \u0645\u0646 \u0645\u0646\u062d\u0629 \u062c\u062f\u064a\u062f\u0629 \u0628\u0642\u064a\u0645\u0629 \u0668\u0666 \u0643\u0631\u0648\u0631 \u0631\u0648\u0628\u064a\u0629 (\u0645\u0627 \u064a\u0639\u0627\u062f\u0644 \u0669,\u0660\u0664\u0667,\u0662\u0660\u0660 \u062f\u0648\u0644\u0627\u0631 \u0623\u0645\u0631\u064a\u0643\u064a \u062a\u0642\u0631\u064a\u0628\u0627\u064b) \u0645\u0646 \u0635\u0646\u062f\u0648\u0642 RDI\u060c \u0628\u0647\u062f\u0641 \u0627\u0644\u062a\u0648\u0633\u0639 \u0644\u062a\u0635\u0628\u062d \u0634\u0631\u0643\u0629 \u0645\u062a\u0643\u0627\u0645\u0644\u0629 \u0644\u0627\u0643\u062a\u0634\u0627\u0641 \u0627\u0644\u0623\u062f\u0648\u064a\u0629 \u0645\u0639 \u0627\u0644\u0627\u0633\u062a\u0641\u0627\u062f\u0629 \u0645\u0646 \u0628\u064a\u0626\u0629 \u0627\u0644\u0647\u0646\u062f \u0645\u0646\u062e\u0641\u0636\u0629 \u0627\u0644\u062a\u0643\u0644\u0641\u0629\u060c \u0646\u062c\u062d\u062a \u0628\u064a\u0628\u062a\u0631\u064a\u0633 \u0641\u064a \u062a\u0631\u062e\u064a\u0635 \u0647\u0630\u0627 \u0627\u0644\u0623\u0635\u0644 \u0627\u0644\u0645\u064f\u0639\u0627\u062f \u0627\u0633\u062a\u062e\u062f\u0627\u0645\u0647 \u0639\u0627\u0644\u0645\u064a\u0627\u064b. \u0648\u0643\u0645\u0627 \u064a\u064f\u0624\u0643\u062f \u0627\u0644\u0645\u0624\u0633\u0633 \u0627\u0644\u0645\u0634\u0627\u0631\u0643 \u0648\u0627\u0644\u0631\u0626\u064a\u0633 \u0627\u0644\u062a\u0646\u0641\u064a\u0630\u064a\u060c \u0641\u064a\u0646\u0643\u0627\u062a\u0627\u0633\u0648\u0628\u0631\u0627\u0645\u0627\u0646\u064a\u0627\u0646 \u0646\u0627\u0631\u0627\u064a\u0627\u0646\u0627\u0646 (\u0641\u064a\u0646\u0643\u0627\u062a)\u060c &quot;\u064a\u064f\u0633\u0631\u0651\u0639 \u0627\u0644\u0630\u0643\u0627\u0621 \u0627\u0644\u0627\u0635\u0637\u0646\u0627\u0639\u064a \u0648\u062a\u064a\u0631\u0629 \u0627\u0644\u0639\u0645\u0644\u060c \u0644\u0643\u0646 \u0627\u0644\u0639\u0644\u0645 \u064a\u0628\u0642\u0649 \u0647\u0648 \u0627\u0644\u0623\u0633\u0627\u0633&quot;. \u064a\u064f\u0645\u062b\u0644 \u0647\u0630\u0627 \u0627\u0644\u062a\u0642\u062f\u0645 \u0625\u0646\u062c\u0627\u0632\u0627\u064b \u0628\u0627\u0644\u063a \u0627\u0644\u0623\u0647\u0645\u064a\u0629 \u0644\u0646\u062d\u0648 \u0664\u0660\u0660,\u0660\u0660\u0660 \u0645\u0631\u064a\u0636 \u0628\u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0627\u0644\u062f\u0648\u0634\u064a\u0646\u064a \u0641\u064a \u0627\u0644\u0647\u0646\u062f\u060c \u0648\u0627\u0644\u0630\u064a\u0646 \u0643\u0627\u0646\u0648\u0627 \u064a\u0648\u0627\u062c\u0647\u0648\u0646 \u0633\u0627\u0628\u0642\u0627\u064b \u062e\u064a\u0627\u0631\u0627\u062a \u0639\u0644\u0627\u062c\u064a\u0629 \u0645\u062d\u062f\u0648\u062f\u0629 \u0644\u0644\u063a\u0627\u064a\u0629.<\/p>\n\n\n\n<div class=\"wp-block-rank-math-toc-block\" id=\"rank-math-toc\"><h2>\u062c\u062f\u0648\u0644 \u0627\u0644\u0645\u062d\u062a\u0648\u064a\u0627\u062a<\/h2><nav><ul><li><a href=\"#discovery-and-structural-overview\">PEPR-124: \u0627\u0644\u0627\u0643\u062a\u0634\u0627\u0641 \u0648\u0646\u0638\u0631\u0629 \u0639\u0627\u0645\u0629 \u0639\u0644\u0649 \u0627\u0644\u0628\u0646\u064a\u0629<\/a><\/li><li><a href=\"#mechanism-of-action-mutation-agnostic-utrophin-upregulation\">\u0622\u0644\u064a\u0629 \u0627\u0644\u0639\u0645\u0644: \u0632\u064a\u0627\u062f\u0629 \u062a\u0646\u0638\u064a\u0645 \u0627\u0644\u064a\u0648\u062a\u0631\u0648\u0641\u064a\u0646 \u0628\u063a\u0636 \u0627\u0644\u0646\u0638\u0631 \u0639\u0646 \u0627\u0644\u0637\u0641\u0631\u0629<\/a><\/li><li><a href=\"#preclinical-efficacy-and-safety-data\">\u0628\u064a\u0627\u0646\u0627\u062a \u0627\u0644\u0641\u0639\u0627\u0644\u064a\u0629 \u0648\u0627\u0644\u0633\u0644\u0627\u0645\u0629 \u0642\u0628\u0644 \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629<\/a><\/li><li><a href=\"#commercialization-strategic-licensing-and-regulatory-status\">\u0627\u0644\u062a\u0633\u0648\u064a\u0642\u060c \u0648\u0627\u0644\u062a\u0631\u062e\u064a\u0635 \u0627\u0644\u0627\u0633\u062a\u0631\u0627\u062a\u064a\u062c\u064a\u060c \u0648\u0627\u0644\u0648\u0636\u0639 \u0627\u0644\u062a\u0646\u0638\u064a\u0645\u064a<\/a><\/li><li><a href=\"#future-outlook-the-hybrid-clinical-path\">\u0627\u0644\u062a\u0648\u0642\u0639\u0627\u062a \u0627\u0644\u0645\u0633\u062a\u0642\u0628\u0644\u064a\u0629: \u0627\u0644\u0645\u0633\u0627\u0631 \u0627\u0644\u0633\u0631\u064a\u0631\u064a \u0627\u0644\u0647\u062c\u064a\u0646<\/a><\/li><li><a href=\"#references\">\u0645\u0631\u0627\u062c\u0639<\/a><\/li><\/ul><\/nav><\/div>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 id=\"discovery-and-structural-overview\" class=\"wp-block-heading\">PEPR-124: \u0627\u0644\u0627\u0643\u062a\u0634\u0627\u0641 \u0648\u0646\u0638\u0631\u0629 \u0639\u0627\u0645\u0629 \u0639\u0644\u0649 \u0627\u0644\u0628\u0646\u064a\u0629<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u062a\u0645 \u0627\u0643\u062a\u0634\u0627\u0641 PEPR-124 \u0641\u064a \u0627\u0644\u0623\u0635\u0644 \u0628\u0648\u0627\u0633\u0637\u0629 Peptris Technologies\u060c \u062d\u064a\u062b \u0642\u0627\u0645\u062a \u0628\u0646\u0634\u0631 \u0645\u0646\u0635\u062a\u0647\u0627 \u0627\u0644\u062d\u0633\u0627\u0628\u064a\u0629 \u0627\u0644\u062e\u0627\u0635\u0629 (pepAI) \u0641\u064a C-CAMP \u0644\u0631\u0633\u0645 \u062e\u0631\u0627\u0626\u0637 \u0644\u0644\u0645\u0633\u0627\u062d\u0627\u062a \u0627\u0644\u0643\u064a\u0645\u064a\u0627\u0626\u064a\u0629 \u0627\u0644\u0648\u0627\u0633\u0639\u0629 \u0648\u0639\u0632\u0644 \u0627\u0644\u062c\u0632\u064a\u0626\u0627\u062a \u0627\u0644\u0635\u063a\u064a\u0631\u0629 \u0627\u0644\u0648\u0638\u064a\u0641\u064a\u0629.<\/strong> \u0648\u0628\u0641\u0636\u0644 \u0645\u0646\u062d\u0629 \u0635\u0646\u062f\u0648\u0642 \u0627\u0644\u0628\u062d\u062b \u0648\u0627\u0644\u062a\u0637\u0648\u064a\u0631 \u0627\u0644\u0623\u062e\u064a\u0631\u0629 \u0627\u0644\u0628\u0627\u0644\u063a\u0629 86 \u0643\u0631\u0648\u0631 \u0631\u0648\u0628\u064a\u0629\u060c \u062a\u062a\u0648\u0633\u0639 \u0627\u0644\u0634\u0631\u0643\u0629 \u0628\u0646\u0634\u0627\u0637 \u0644\u062a\u0635\u0628\u062d \u0634\u0631\u0643\u0629 \u0645\u062a\u0643\u0627\u0645\u0644\u0629 \u0644\u0627\u0643\u062a\u0634\u0627\u0641 \u0627\u0644\u0623\u062f\u0648\u064a\u0629 \u0645\u0639 \u0627\u0644\u0627\u0633\u062a\u0641\u0627\u062f\u0629 \u0645\u0646 \u0627\u0646\u062e\u0641\u0627\u0636 \u062a\u0643\u0627\u0644\u064a\u0641 \u0627\u0644\u062a\u0634\u063a\u064a\u0644 \u0641\u064a \u0627\u0644\u0647\u0646\u062f \u0644\u0628\u0646\u0627\u0621 \u062d\u0644\u0648\u0644 \u062f\u0627\u0626\u0645\u0629 \u0648\u0645\u062a\u0627\u062d\u0629 \u0644\u0644\u0623\u0645\u0631\u0627\u0636 \u0627\u0644\u062a\u064a \u064a\u0635\u0639\u0628 \u0639\u0644\u0627\u062c\u0647\u0627.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0639\u0644\u0649 \u0639\u0643\u0633 \u0627\u0644\u0645\u0631\u0643\u0628\u0627\u062a \u0627\u0644\u0645\u0635\u0646\u0639\u0629 \u062d\u062f\u064a\u062b\u064b\u0627 \u0648\u0627\u0644\u062a\u064a \u062a\u0646\u0637\u0648\u064a \u0639\u0644\u0649 \u0645\u062e\u0627\u0637\u0631 \u0639\u0627\u0644\u064a\u0629 \u0641\u064a \u0627\u0644\u062a\u0637\u0628\u064a\u0642\u0627\u062a \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629\u060c \u064a\u064f\u0639\u062f\u0651 PEPR-124 \u0645\u0631\u0643\u0628\u064b\u0627 \u0645\u064f\u0639\u0627\u062f \u0627\u0633\u062a\u062e\u062f\u0627\u0645\u0647. \u0648\u064a\u0639\u0646\u064a \u0647\u0630\u0627 \u0627\u0644\u062a\u0635\u0646\u064a\u0641 \u0627\u0644\u0627\u0633\u062a\u0631\u0627\u062a\u064a\u062c\u064a \u0623\u0646 \u0627\u0644\u062c\u0632\u064a\u0621 \u0627\u0644\u0623\u0633\u0627\u0633\u064a \u064a\u062a\u0645\u062a\u0639 \u0628\u0645\u0644\u0641\u0627\u062a \u0623\u0645\u0627\u0646 \u0623\u0633\u0627\u0633\u064a\u0629 \u0631\u0627\u0633\u062e\u0629\u060c \u0645\u0645\u0627 \u064a\u064f\u0642\u0644\u0644 \u0628\u0634\u0643\u0644 \u0643\u0628\u064a\u0631 \u0645\u0646 \u0645\u062f\u0629 \u0627\u0644\u062a\u062d\u0642\u0642 \u0642\u0628\u0644 \u0627\u0644\u0633\u0631\u064a\u0631\u064a \u0627\u0644\u062a\u064a \u062a\u0633\u062a\u063a\u0631\u0642 \u0639\u0627\u062f\u0629\u064b \u0639\u0642\u062f\u064b\u0627 \u0645\u0646 \u0627\u0644\u0632\u0645\u0646\u060c \u0648\u064a\u064f\u062e\u0641\u0641 \u0645\u0646 \u062d\u0627\u0644\u0627\u062a \u0641\u0634\u0644 \u0627\u0644\u0633\u0645\u064a\u0629 \u0623\u0648 \u0639\u062f\u0645 \u0627\u0644\u0627\u0633\u062a\u0642\u0631\u0627\u0631 \u0623\u062b\u0646\u0627\u0621 \u0627\u0644\u062a\u0637\u0648\u064a\u0631.<\/p>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 id=\"mechanism-of-action-mutation-agnostic-utrophin-upregulation\" class=\"wp-block-heading\">\u0622\u0644\u064a\u0629 \u0627\u0644\u0639\u0645\u0644: \u0632\u064a\u0627\u062f\u0629 \u062a\u0646\u0638\u064a\u0645 \u0627\u0644\u064a\u0648\u062a\u0631\u0648\u0641\u064a\u0646 \u0628\u063a\u0636 \u0627\u0644\u0646\u0638\u0631 \u0639\u0646 \u0627\u0644\u0637\u0641\u0631\u0629<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u064a\u064f\u0639\u062f\u0651 \u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0627\u0644\u062f\u0648\u0634\u064a\u0646\u064a \u0627\u0636\u0637\u0631\u0627\u0628\u064b\u0627 \u0639\u0635\u0628\u064a\u064b\u0627 \u0639\u0636\u0644\u064a\u064b\u0627 \u0643\u0627\u0631\u062b\u064a\u064b\u0627 \u0648\u0645\u062a\u0641\u0627\u0642\u0645\u064b\u0627\u060c \u064a\u0646\u062c\u0645 \u0639\u0646 \u0623\u062e\u0637\u0627\u0621 \u062c\u064a\u0646\u064a\u0629 \u062a\u0645\u0646\u0639 \u0625\u0646\u062a\u0627\u062c \u0627\u0644\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0627\u0644\u0648\u0638\u064a\u0641\u064a\u060c \u0648\u0647\u0648 \u0628\u0631\u0648\u062a\u064a\u0646 \u0623\u0633\u0627\u0633\u064a \u064a\u064f\u062b\u0628\u0651\u062a \u0623\u063a\u0634\u064a\u0629 \u062e\u0644\u0627\u064a\u0627 \u0627\u0644\u0639\u0636\u0644\u0627\u062a. \u0648\u062a\u064f\u0639\u062a\u0628\u0631 \u062a\u0642\u0646\u064a\u0627\u062a \u062a\u0635\u062d\u064a\u062d \u0627\u0644\u062c\u064a\u0646\u0627\u062a \u0627\u0644\u0642\u064a\u0627\u0633\u064a\u0629 (\u0645\u062b\u0644 \u062d\u0630\u0641 \u0627\u0644\u0625\u0643\u0633\u0648\u0646) \u0645\u062d\u062f\u0648\u062f\u0629 \u0644\u0623\u0646\u0647\u0627 \u062a\u0633\u062a\u0647\u062f\u0641 \u0645\u062a\u063a\u064a\u0631\u0627\u062a \u062c\u064a\u0646\u064a\u0629 \u0645\u062d\u062f\u062f\u0629.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u064a\u062a\u062c\u0627\u0648\u0632 PEPR-124 \u0647\u0630\u0627 \u0627\u0644\u0642\u064a\u062f \u0645\u0646 \u062e\u0644\u0627\u0644 \u062a\u0637\u0628\u064a\u0642 \u0646\u0647\u062c \u0639\u0644\u0627\u062c\u064a \u0644\u0627 \u064a\u0639\u062a\u0645\u062f \u0639\u0644\u0649 \u0627\u0644\u0637\u0641\u0631\u0627\u062a:<\/strong><\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li><strong>\u0627\u0644\u0628\u0631\u0648\u062a\u064a\u0646 \u0627\u0644\u0645\u0633\u062a\u0647\u062f\u0641:<\/strong> \u064a\u0631\u0643\u0632 \u0639\u0644\u0649 \u0632\u064a\u0627\u062f\u0629 \u062a\u0646\u0638\u064a\u0645 \u0627\u0644\u064a\u0648\u062a\u0631\u0648\u0641\u064a\u0646\u060c \u0648\u0647\u0648 \u0628\u0631\u0648\u062a\u064a\u0646 \u0645\u0645\u0627\u062b\u0644 \u0628\u0646\u064a\u0648\u064a\u064b\u0627 \u0648\u0645\u0637\u0627\u0628\u0642 \u0648\u0638\u064a\u0641\u064a\u064b\u0627 \u0644\u0644\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0641\u064a \u0627\u0644\u062a\u0637\u0648\u0631 \u0627\u0644\u062c\u0646\u064a\u0646\u064a.<\/li>\n\n\n\n<li><strong>\u0627\u0644\u062a\u0639\u0648\u064a\u0636 \u0627\u0644\u062e\u0644\u0648\u064a:<\/strong> \u0645\u0646 \u062e\u0644\u0627\u0644 \u0625\u062d\u062f\u0627\u062b \u0632\u064a\u0627\u062f\u0629 \u062f\u0627\u0626\u0645\u0629 \u0641\u064a \u0645\u0633\u062a\u0648\u064a\u0627\u062a \u0627\u0644\u064a\u0648\u062a\u0631\u0648\u0641\u064a\u0646 \u0627\u0644\u0645\u062d\u0644\u064a\u0629\u060c \u0641\u0625\u0646\u0647 \u064a\u0639\u0648\u0636 \u0639\u0646 \u063a\u064a\u0627\u0628 \u0625\u0637\u0627\u0631 \u0627\u0644\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646\u060c \u0645\u0645\u0627 \u064a\u062d\u0645\u064a \u0623\u0644\u064a\u0627\u0641 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0645\u0646 \u0627\u0644\u0625\u062c\u0647\u0627\u062f \u0627\u0644\u0645\u064a\u0643\u0627\u0646\u064a\u0643\u064a \u0628\u063a\u0636 \u0627\u0644\u0646\u0638\u0631 \u0639\u0646 \u0627\u0644\u062a\u0633\u0644\u0633\u0644 \u0627\u0644\u062c\u064a\u0646\u064a \u0627\u0644\u062f\u0642\u064a\u0642 \u0644\u062d\u0630\u0641 \u0627\u0644\u0637\u0641\u0644.<\/li>\n<\/ul>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 id=\"preclinical-efficacy-and-safety-data\" class=\"wp-block-heading\">\u0628\u064a\u0627\u0646\u0627\u062a \u0627\u0644\u0641\u0639\u0627\u0644\u064a\u0629 \u0648\u0627\u0644\u0633\u0644\u0627\u0645\u0629 \u0642\u0628\u0644 \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u0623\u0638\u0647\u0631\u062a \u0627\u0644\u062a\u062c\u0627\u0631\u0628 \u0645\u0627 \u0642\u0628\u0644 \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629 \u0627\u0644\u062a\u064a \u0639\u064f\u0631\u0636\u062a \u0641\u064a \u0646\u062f\u0648\u0627\u062a \u0639\u0644\u0645\u064a\u0629 \u0631\u0626\u064a\u0633\u064a\u0629\u060c \u0628\u0645\u0627 \u0641\u064a \u0630\u0644\u0643 \u0627\u0644\u0645\u0624\u062a\u0645\u0631 \u0627\u0644\u0633\u0631\u064a\u0631\u064a \u0648\u0627\u0644\u0639\u0644\u0645\u064a \u0644\u062c\u0645\u0639\u064a\u0629 \u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a (MDA)\u060c \u0645\u0624\u0634\u0631\u0627\u062a \u0639\u0644\u0627\u062c\u064a\u0629 \u0647\u0627\u0645\u0629:<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li><strong>\u0627\u0644\u0627\u062e\u062a\u0628\u0627\u0631\u0627\u062a \u0627\u0644\u0645\u0639\u0645\u0644\u064a\u0629:<\/strong> \u0646\u062c\u062d PEPR-124 \u0641\u064a \u062a\u062d\u0642\u064a\u0642 \u062a\u0646\u0638\u064a\u0645 \u0627\u0644\u064a\u0648\u062a\u0631\u0648\u0641\u064a\u0646 \u0627\u0644\u0645\u0639\u062a\u0645\u062f \u0639\u0644\u0649 \u0627\u0644\u062c\u0631\u0639\u0629 \u0641\u064a \u0627\u0644\u062e\u0644\u0627\u064a\u0627 \u0627\u0644\u0639\u0636\u0644\u064a\u0629 C2C12 \u0648\u0643\u0630\u0644\u0643 \u0627\u0644\u062e\u0644\u0627\u064a\u0627 \u0627\u0644\u062c\u0630\u0639\u064a\u0629 \u0645\u062a\u0639\u062f\u062f\u0629 \u0627\u0644\u0642\u062f\u0631\u0627\u062a \u0627\u0644\u0645\u0633\u062a\u062d\u062b\u0629 \u0627\u0644\u0628\u0634\u0631\u064a\u0629 (hIPSCs) \u0627\u0644\u0645\u0634\u062a\u0642\u0629 \u0645\u0628\u0627\u0634\u0631\u0629 \u0645\u0646 \u0645\u0631\u0636\u0649 \u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0627\u0644\u062f\u0648\u0634\u064a\u0646\u064a \u0627\u0644\u0628\u0634\u0631\u064a.<\/li>\n\n\n\n<li><strong>\u0648\u0638\u064a\u0641\u0629 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0641\u064a \u0627\u0644\u062c\u0633\u0645 \u0627\u0644\u062d\u064a:<\/strong> \u0641\u064a \u0646\u0645\u0627\u0630\u062c \u0627\u0644\u0641\u0626\u0631\u0627\u0646 \u0627\u0644\u0645\u0635\u0627\u0628\u0629 \u0628\u0645\u0631\u0636 D2-Mdx \u0627\u0644\u062d\u0627\u062f \u0627\u0644\u062a\u064a \u062a\u0645 \u062a\u0642\u064a\u064a\u0645\u0647\u0627 \u0639\u0644\u0649 \u0641\u062a\u0631\u0627\u062a 28 \u064a\u0648\u0645\u064b\u0627 \u064890 \u064a\u0648\u0645\u064b\u0627 (\u0628\u062c\u0631\u0639\u0627\u062a \u062a\u062a\u0631\u0627\u0648\u062d \u0628\u064a\u0646 25 \u0648100 \u0645\u0644\u063a\u0645\/\u0643\u063a\u0645)\u060c \u0623\u062f\u0649 \u0627\u0644\u0645\u0631\u0643\u0628 \u0625\u0644\u0649 \u062a\u062d\u0633\u064a\u0646\u0627\u062a \u0643\u0628\u064a\u0631\u0629 \u0641\u064a \u0642\u0648\u0629 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0627\u0644\u0639\u0627\u0645\u0629\u060c \u0648\u0642\u0648\u0629 \u0627\u0644\u0642\u0628\u0636\u0629\u060c \u0648\u0627\u062e\u062a\u0628\u0627\u0631\u0627\u062a \u0632\u0645\u0646 \u0627\u0644\u062a\u0639\u0644\u0642\u060c \u0648\u0627\u0644\u0623\u062f\u0627\u0621 \u0627\u0644\u0639\u0627\u0645 \u0639\u0644\u0649 \u062c\u0647\u0627\u0632 \u0627\u0644\u0645\u0634\u064a.<\/li>\n\n\n\n<li><strong>\u0623\u0648\u062c\u0647 \u0627\u0644\u062a\u0622\u0632\u0631 \u0627\u0644\u0646\u0627\u062a\u062c\u0629 \u0639\u0646 \u0627\u0644\u062c\u0645\u0639 \u0628\u064a\u0646 \u0627\u0644\u0645\u0643\u0648\u0646\u0627\u062a:<\/strong> \u0639\u0646\u062f \u0625\u0639\u0637\u0627\u0626\u0647 \u0628\u0627\u0644\u062a\u0632\u0627\u0645\u0646 \u0645\u0639 \u0627\u0644\u0643\u0648\u0631\u062a\u064a\u0643\u0648\u0633\u062a\u064a\u0631\u0648\u064a\u062f \u062f\u064a\u0641\u0644\u0627\u0632\u0627\u0643\u0648\u0631\u062a \u0627\u0644\u0645\u0639\u064a\u0627\u0631\u064a \u0644\u0644\u0631\u0639\u0627\u064a\u0629\u060c \u062d\u0642\u0642 PEPR-124 \u062d\u0645\u0627\u064a\u0629 \u0647\u064a\u0643\u0644\u064a\u0629 \u0641\u0627\u0626\u0642\u0629 \u0644\u0644\u0639\u0636\u0644\u0627\u062a\u060c \u0648\u062a\u062d\u0633\u0646\u064b\u0627 \u0641\u064a \u0627\u0644\u0642\u062f\u0631\u0629 \u0639\u0644\u0649 \u0627\u0644\u062a\u062d\u0645\u0644 \u0623\u062b\u0646\u0627\u0621 \u0627\u0644\u062a\u0639\u0644\u0642\u060c \u0648\u0627\u0646\u062e\u0641\u0627\u0636\u064b\u0627 \u0645\u0644\u062d\u0648\u0638\u064b\u0627 \u0641\u064a \u0645\u0633\u062a\u0648\u0649 \u0627\u0644\u0643\u0631\u064a\u0627\u062a\u064a\u0646 \u0643\u064a\u0646\u0627\u0632 \u0641\u064a \u0627\u0644\u062f\u0645 (\u0648\u0647\u0648 \u0645\u0624\u0634\u0631 \u062d\u064a\u0648\u064a \u0630\u0647\u0628\u064a \u0641\u064a \u0627\u0644\u062f\u0645 \u0644\u062a\u062f\u0645\u064a\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0627\u0644\u0645\u0633\u062a\u0645\u0631).<\/li>\n\n\n\n<li><strong>\u0645\u0644\u0641 \u0627\u0644\u0633\u0644\u0627\u0645\u0629:<\/strong> \u0648\u0627\u0644\u0623\u0647\u0645 \u0645\u0646 \u0630\u0644\u0643\u060c \u0623\u0646 PEPR-124 \u0644\u0645 \u064a\u064f\u0638\u0647\u0631 \u0623\u064a \u0623\u062d\u062f\u0627\u062b \u0636\u0627\u0631\u0629 \u062a\u062a\u0639\u0644\u0642 \u0628\u0646\u0645\u0648 \u0648\u0632\u0646 \u0627\u0644\u062c\u0633\u0645 \u0623\u0648 \u0627\u0644\u0633\u0645\u064a\u0629 \u0627\u0644\u0623\u064a\u0636\u064a\u0629\u060c \u0645\u0645\u0627 \u064a\u0648\u0641\u0631 \u0647\u0627\u0645\u0634 \u0623\u0645\u0627\u0646 \u0645\u0646\u0627\u0633\u0628 \u0645\u0642\u0627\u0631\u0646\u0629 \u0628\u0627\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u0623\u062d\u0627\u062f\u064a \u0628\u0627\u0644\u0643\u0648\u0631\u062a\u064a\u0643\u0648\u0633\u062a\u064a\u0631\u0648\u064a\u062f \u0639\u0644\u0649 \u0627\u0644\u0645\u062f\u0649 \u0627\u0644\u0637\u0648\u064a\u0644.<\/li>\n<\/ul>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 id=\"commercialization-strategic-licensing-and-regulatory-status\" class=\"wp-block-heading\">\u0627\u0644\u062a\u0633\u0648\u064a\u0642\u060c \u0648\u0627\u0644\u062a\u0631\u062e\u064a\u0635 \u0627\u0644\u0627\u0633\u062a\u0631\u0627\u062a\u064a\u062c\u064a\u060c \u0648\u0627\u0644\u0648\u0636\u0639 \u0627\u0644\u062a\u0646\u0638\u064a\u0645\u064a<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u0628\u0647\u062f\u0641 \u062a\u0633\u0631\u064a\u0639 \u0627\u0644\u062a\u0637\u0648\u064a\u0631 \u0627\u0644\u0633\u0631\u064a\u0631\u064a \u0627\u0644\u062f\u0648\u0644\u064a\u060c \u0648\u0642\u0639\u062a \u0634\u0631\u0643\u0629 Peptris Technologies \u0627\u062a\u0641\u0627\u0642\u064a\u0629 \u062a\u0631\u062e\u064a\u0635 \u0639\u0627\u0644\u0645\u064a\u0629 \u0645\u0639 \u0634\u0631\u0643\u0629 Revio Therapeutics\u060c \u0648\u0647\u064a \u0634\u0631\u0643\u0629 \u0646\u0627\u0634\u0626\u0629 \u0645\u062a\u062e\u0635\u0635\u0629 \u0641\u064a \u0627\u0644\u0623\u062f\u0648\u064a\u0629 \u0645\u0642\u0631\u0647\u0627 \u0627\u0644\u0648\u0644\u0627\u064a\u0627\u062a \u0627\u0644\u0645\u062a\u062d\u062f\u0629 \u0627\u0644\u0623\u0645\u0631\u064a\u0643\u064a\u0629\u060c \u0648\u062a\u062a\u062e\u0635\u0635 \u0641\u064a \u062a\u062d\u0633\u064a\u0646 \u0627\u0644\u0623\u062f\u0648\u064a\u0629 \u0627\u0644\u0645\u0639\u062a\u0645\u062f\u0629.<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li><strong>\u062a\u062e\u0635\u064a\u0635\u0627\u062a \u0627\u0644\u0633\u0648\u0642:<\/strong> \u062a\u0645\u062a\u0644\u0643 \u0634\u0631\u0643\u0629 Revio Therapeutics \u062d\u0642\u0648\u0642 \u0627\u0644\u062a\u0637\u0648\u064a\u0631 \u0648\u0627\u0644\u062a\u0633\u0648\u064a\u0642 \u0627\u0644\u062d\u0635\u0631\u064a\u0629 \u0639\u0644\u0649 \u0645\u0633\u062a\u0648\u0649 \u0627\u0644\u0639\u0627\u0644\u0645\u060c \u0628\u064a\u0646\u0645\u0627 \u062a\u062d\u062a\u0641\u0638 \u0634\u0631\u0643\u0629 Peptris \u0628\u0627\u0644\u062d\u0642\u0648\u0642 \u0627\u0644\u062a\u062c\u0627\u0631\u064a\u0629 \u0627\u0644\u062e\u0627\u0635\u0629 \u0628\u0623\u0633\u0648\u0627\u0642 \u062f\u0648\u0644 \u0627\u0644\u0628\u0631\u064a\u0643\u0633.<\/li>\n\n\n\n<li><strong>\u062a\u0635\u0646\u064a\u0641 \u0627\u0644\u062f\u0648\u0627\u0621 \u0627\u0644\u064a\u062a\u064a\u0645 FDA:<\/strong> \u062d\u0642\u0642 \u0647\u0630\u0627 \u0627\u0644\u0645\u0646\u062a\u062c \u0625\u0646\u062c\u0627\u0632\u0627\u064b \u062a\u0646\u0638\u064a\u0645\u064a\u0627\u064b \u0647\u0627\u0645\u0627\u064b \u0639\u0646\u062f\u0645\u0627 \u0645\u0646\u062d\u062a \u0625\u062f\u0627\u0631\u0629 \u0627\u0644\u063a\u0630\u0627\u0621 \u0648\u0627\u0644\u062f\u0648\u0627\u0621 \u0627\u0644\u0623\u0645\u0631\u064a\u0643\u064a\u0629 (US FDA) \u062a\u0635\u0646\u064a\u0641 \u062f\u0648\u0627\u0621 \u0627\u0644\u064a\u062a\u064a\u0645 (ODD) \u0644\u0644\u062f\u0648\u0627\u0621 RT001\/PEPR-124. \u064a\u0648\u0641\u0631 \u0647\u0630\u0627 \u0627\u0644\u0648\u0636\u0639 \u0627\u0644\u062a\u0646\u0638\u064a\u0645\u064a \u062d\u0648\u0627\u0641\u0632 \u0644\u0644\u062a\u0637\u0648\u064a\u0631\u060c \u0648\u0625\u0639\u0641\u0627\u0621\u0627\u062a \u0636\u0631\u064a\u0628\u064a\u0629 \u0644\u0644\u0627\u062e\u062a\u0628\u0627\u0631\u0627\u062a \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629\u060c \u0648\u0625\u0639\u0641\u0627\u0621\u064b \u0645\u0646 \u0631\u0633\u0648\u0645 PDUFA\u060c \u0648\u062d\u0635\u0631\u064a\u0629 \u0645\u062d\u062a\u0645\u0644\u0629 \u0641\u064a \u0627\u0644\u0633\u0648\u0642 \u0628\u0639\u062f \u0627\u0644\u0645\u0648\u0627\u0641\u0642\u0629.<\/li>\n<\/ul>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 id=\"future-outlook-the-hybrid-clinical-path\" class=\"wp-block-heading\">\u0627\u0644\u062a\u0648\u0642\u0639\u0627\u062a \u0627\u0644\u0645\u0633\u062a\u0642\u0628\u0644\u064a\u0629: \u0627\u0644\u0645\u0633\u0627\u0631 \u0627\u0644\u0633\u0631\u064a\u0631\u064a \u0627\u0644\u0647\u062c\u064a\u0646<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u0627\u0639\u062a\u0628\u0627\u0631\u064b\u0627 \u0645\u0646 \u0623\u0648\u0627\u062e\u0631 \u0639\u0627\u0645 2026\u060c \u0635\u064f\u0646\u0650\u0651\u0641 PEPR-124 \u0643\u0623\u0635\u0644 \u062c\u0627\u0647\u0632 \u0644\u0644\u0645\u0631\u062d\u0644\u0629 \u0627\u0644\u062b\u0627\u0646\u064a\u0629 \u0645\u0646 \u0627\u0644\u062a\u062c\u0627\u0631\u0628 \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629. \u0648\u062a\u0633\u062a\u0641\u064a\u062f \u0634\u0631\u0643\u0629 Revio Therapeutics \u0645\u0646 \u0627\u0644\u0645\u0633\u0627\u0631 \u0627\u0644\u0647\u062c\u064a\u0646 \u0627\u0644\u062a\u0646\u0638\u064a\u0645\u064a 505(\u0628)(2) \u0627\u0644\u062e\u0627\u0635 \u0628\u0640 FDA.<\/strong> \u064a\u064f\u0645\u0643\u0651\u0646 \u0647\u0630\u0627 \u0627\u0644\u0631\u0627\u0639\u064a \u0645\u0646 \u0627\u0644\u0631\u062c\u0648\u0639 \u0625\u0644\u0649 \u0628\u064a\u0627\u0646\u0627\u062a \u0627\u0644\u0633\u0644\u0627\u0645\u0629 \u0627\u0644\u062d\u0627\u0644\u064a\u0629 \u0644\u0644\u062c\u0632\u064a\u0621 \u0627\u0644\u0635\u063a\u064a\u0631 \u0627\u0644\u0623\u0633\u0627\u0633\u064a\u060c \u0645\u0645\u0627 \u064a\u064f\u0644\u063a\u064a \u0627\u0644\u062d\u0627\u062c\u0629 \u0625\u0644\u0649 \u0625\u062c\u0631\u0627\u0621 \u062a\u062c\u0627\u0631\u0628 \u0633\u0644\u0627\u0645\u0629 \u0625\u0636\u0627\u0641\u064a\u0629 \u0645\u0646 \u0627\u0644\u0645\u0631\u062d\u0644\u0629 \u0627\u0644\u0623\u0648\u0644\u0649 \u0639\u0644\u0649 \u0645\u062a\u0637\u0648\u0639\u064a\u0646 \u0623\u0635\u062d\u0627\u0621. \u0648\u062a\u064f\u062c\u0631\u064a \u0634\u0631\u0643\u0629 Revio \u062d\u0627\u0644\u064a\u064b\u0627 \u0627\u0633\u062a\u0639\u062f\u0627\u062f\u0627\u062a\u0647\u0627 \u0644\u0639\u0642\u062f \u0627\u062c\u062a\u0645\u0627\u0639\u0627\u062a \u062a\u0645\u0647\u064a\u062f\u064a\u0629 \u0644\u062a\u0642\u062f\u064a\u0645 \u0637\u0644\u0628 \u062f\u0648\u0627\u0621 \u062a\u062c\u0631\u064a\u0628\u064a \u062c\u062f\u064a\u062f (IND) \u0645\u0639 \u0634\u0631\u0643\u0629 US FDA \u0644\u0648\u0636\u0639 \u0627\u0644\u0644\u0645\u0633\u0627\u062a \u0627\u0644\u0623\u062e\u064a\u0631\u0629 \u0639\u0644\u0649 \u0647\u064a\u0643\u0644\u064a\u0629 \u0627\u0644\u0645\u0631\u062d\u0644\u0629 \u0627\u0644\u062b\u0627\u0646\u064a\u0629 \u0645\u0646 \u0627\u0644\u062a\u062c\u0627\u0631\u0628 \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629 \u0627\u0644\u0642\u0627\u062f\u0645\u0629 \u0639\u0644\u0649 \u0627\u0644\u0623\u0637\u0641\u0627\u0644 \u0627\u0644\u0645\u064f\u0634\u062e\u0651\u0635\u064a\u0646 \u0628\u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0627\u0644\u062f\u0648\u0634\u064a\u0646\u064a (DMD).<\/p>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 id=\"references\" class=\"wp-block-heading\">\u0645\u0631\u0627\u062c\u0639<\/h2>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u0634\u0631\u0643\u0629 \u0631\u064a\u0641\u064a\u0648 \u062b\u064a\u0631\u0627\u0628\u064a\u0648\u062a\u0643\u0633. <em>\u201c&quot;Revio \u062a\u062a\u0639\u0627\u0648\u0646 \u0645\u0639 Peptris \u0644\u0644\u062d\u0635\u0648\u0644 \u0639\u0644\u0649 \u062a\u0631\u062e\u064a\u0635 RT001 (PEPR124) \u0644\u0639\u0644\u0627\u062c \u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a.&quot;\u201d<\/em> <a href=\"https:\/\/www.reviotx.com\/blog\/revio-partners-with-peptris\" target=\"_blank\" rel=\"noopener\">\u0645\u062f\u0648\u0646\u0629 \u0631\u064a\u0641\u064a\u0648 \u062b\u064a\u0631\u0627\u0628\u064a\u0648\u062a\u0643\u0633<\/a>.<\/li>\n\n\n\n<li>\u0642\u0635\u062a\u0643. <em>\u201c&quot;\u062a\u0633\u062a\u062e\u062f\u0645 \u0634\u0631\u0643\u0629 Peptris \u0627\u0644\u0630\u0643\u0627\u0621 \u0627\u0644\u0627\u0635\u0637\u0646\u0627\u0639\u064a \u0648\u062a\u0645\u0646\u062d \u062a\u0631\u062e\u064a\u0635\u064b\u0627 \u0644\u0639\u0644\u0627\u062c \u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a\u061b \u0648\u062a\u0641\u0648\u0632 \u0628\u0645\u0646\u062d\u0629 \u0628\u062d\u062b \u0648\u062a\u0637\u0648\u064a\u0631 \u0628\u0642\u064a\u0645\u0629 86 \u0643\u0631\u0648\u0631 \u0631\u0648\u0628\u064a\u0629.&quot;\u201d<\/em> <a href=\"https:\/\/yourstory.com\/2026\/08\/peptris-ai-drug-discovery\" target=\"_blank\" rel=\"noopener\">YourStory Tech Media<\/a>.<\/li>\n\n\n\n<li>\u0623\u062e\u0628\u0627\u0631 \u0643\u0644\u064a\u0641\u0627\u0644. <em>\u201c&quot;\u0634\u0631\u0643\u0629 Peptris \u062a\u0631\u062e\u0635 \u0623\u0648\u0644 \u062f\u0648\u0627\u0621 \u062a\u0645 \u0627\u0643\u062a\u0634\u0627\u0641\u0647 \u0628\u0648\u0627\u0633\u0637\u0629 \u0627\u0644\u0630\u0643\u0627\u0621 \u0627\u0644\u0627\u0635\u0637\u0646\u0627\u0639\u064a \u0641\u064a \u0627\u0644\u0647\u0646\u062f \u0644\u0634\u0631\u0643\u0629 Revio Therapeutics \u0644\u0639\u0644\u0627\u062c \u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a.&quot;\u201d<\/em> <a href=\"https:\/\/clival.com\/news\/peptris-licenses-indias-first-ai-discovered-drug-to-revio-therapeutics\" target=\"_blank\" rel=\"noopener\">\u0623\u0633\u0648\u0627\u0642 \u0643\u0644\u064a\u0641\u0627\u0644 \u0644\u0644\u062a\u0643\u0646\u0648\u0644\u0648\u062c\u064a\u0627 \u0627\u0644\u062d\u064a\u0648\u064a\u0629<\/a>.<\/li>\n\n\n\n<li>\u0634\u0631\u0643\u0629 \u0631\u064a\u0641\u064a\u0648 \u062b\u064a\u0631\u0627\u0628\u064a\u0648\u062a\u0643\u0633. <em>\u201c&quot;\u0625\u0646\u062c\u0627\u0632 \u062a\u0646\u0638\u064a\u0645\u064a \u0647\u0627\u0645 RT001: \u0645\u0646\u062d FDA \u062a\u0635\u0646\u064a\u0641 \u062f\u0648\u0627\u0621 \u0627\u0644\u064a\u062a\u064a\u0645 \u0644\u0628\u0631\u0646\u0627\u0645\u062c \u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a.&quot;\u201d<\/em> <a href=\"https:\/\/www.reviotx.com\/blog\/%20rt001-regulatory-milestone\" target=\"_blank\" rel=\"noopener\">\u0623\u062e\u0628\u0627\u0631 \u0631\u064a\u0641\u064a\u0648 \u062b\u064a\u0631\u0627\u0628\u064a\u0648\u062a\u0643\u0633<\/a>.<\/li>\n\n\n\n<li>\u062c\u0645\u0639\u064a\u0629 \u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a (MDA). <em>\u201c&quot;PEPR124 (RT001): \u062f\u0648\u0627\u0621 \u062c\u0632\u064a\u0626\u064a \u0635\u063a\u064a\u0631 \u0645\u0639\u0627\u062f \u0627\u0633\u062a\u062e\u062f\u0627\u0645\u0647 \u0643\u0639\u0644\u0627\u062c \u0622\u0645\u0646 \u0648\u063a\u064a\u0631 \u0645\u0631\u062a\u0628\u0637 \u0628\u0627\u0644\u0637\u0641\u0631\u0629 \u0644\u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a.&quot;\u201d<\/em> <a href=\"https:\/\/www.mdaconference.org\/abstract-library\/pepr124-rt001-a-repurposed-small-molecule-drug-as-a-mutation-agnostic-and-safe-therapeutic-for-duchenne-muscular-dystrophy\/\" target=\"_blank\" rel=\"noopener\">\u0645\u0643\u062a\u0628\u0629 \u0645\u0644\u062e\u0635\u0627\u062a \u0645\u0624\u062a\u0645\u0631\u0627\u062a MDA<\/a>.<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\"><\/p>","protected":false},"excerpt":{"rendered":"<p>PEPR-124 (also designated as RT001) is an AI-discovered drug candidate developed by Peptris Technologies, a Bengaluru startup based in India, specifically targeting Duchenne Muscular Dystrophy (DMD). Founded in 2019 and operating from C-CAMP, Peptris uses artificial intelligence and generative chemistry to design optimized molecules for once &#8220;undruggable&#8221; diseases like rare illnesses, cancer, and inflammation. Supported [&hellip;]<\/p>\n","protected":false},"author":3,"featured_media":8901,"comment_status":"closed","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[27],"tags":[83,937,938,939,940,925],"class_list":["post-8898","post","type-post","status-publish","format-standard","has-post-thumbnail","category-research","tag-india","tag-pepr-124","tag-peptris-technologies","tag-revio-therapeutics","tag-rt001","tag-utrophin"],"subtitle":"\u0647\u0644 \u064a\u064f\u0645\u0643\u0646 \u0644\u062f\u0648\u0627\u0621\u064d \u0645\u064f\u0643\u062a\u0634\u0641\u064d \u0628\u0648\u0627\u0633\u0637\u0629 \u0627\u0644\u0630\u0643\u0627\u0621 \u0627\u0644\u0627\u0635\u0637\u0646\u0627\u0639\u064a \u0623\u0646 \u064a\u064f\u0642\u062f\u0651\u0645 \u0646\u0647\u062c\u064b\u0627 \u062c\u062f\u064a\u062f\u064b\u0627 \u0644\u0639\u0644\u0627\u062c \u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a\u061f \u064a\u0647\u062f\u0641 \u062f\u0648\u0627\u0621 PEPR-124 (RT001)\u060c \u0627\u0644\u0630\u064a \u0637\u0648\u0651\u0631\u062a\u0647 \u0634\u0631\u0643\u0629 Peptris Technologies\u060c \u0625\u0644\u0649 \u062a\u0639\u0632\u064a\u0632 \u0647\u0631\u0645\u0648\u0646 \u0627\u0644\u064a\u0648\u062a\u0631\u0648\u0641\u064a\u0646 \u0628\u063a\u0636 \u0627\u0644\u0646\u0638\u0631 \u0639\u0646 \u0627\u0644\u0637\u0641\u0631\u0629 \u0627\u0644\u062c\u064a\u0646\u064a\u0629 \u0627\u0644\u0645\u064f\u0633\u0628\u0628\u0629 \u0644\u0644\u0645\u0631\u0636. \u0627\u0643\u062a\u0634\u0641 \u0646\u062a\u0627\u0626\u062c \u0627\u0644\u062f\u0631\u0627\u0633\u0627\u062a \u0645\u0627 \u0642\u0628\u0644 \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629 \u0648\u0622\u0641\u0627\u0642 \u062a\u0637\u0648\u064a\u0631\u0647.","_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/posts\/8898","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/users\/3"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/comments?post=8898"}],"version-history":[{"count":4,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/posts\/8898\/revisions"}],"predecessor-version":[{"id":8905,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/posts\/8898\/revisions\/8905"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/media\/8901"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/media?parent=8898"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/categories?post=8898"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/tags?post=8898"}],"curies":[{"name":"\u0648\u0648\u0631\u062f\u0628\u0631\u064a\u0633","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}