{"id":8843,"date":"2026-10-04T10:08:04","date_gmt":"2026-10-04T07:08:04","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=8843"},"modified":"2026-10-04T10:08:07","modified_gmt":"2026-10-04T07:08:07","slug":"rag-18-duchenne-first-in-human-data-wms-2026","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/ar\/rag-18-duchenne-first-in-human-data-wms-2026\/","title":{"rendered":"\u0623\u0639\u0644\u0646\u062a \u0634\u0631\u0643\u0629 Ractigen Therapeutics \u0639\u0646 \u0628\u064a\u0627\u0646\u0627\u062a \u0625\u064a\u062c\u0627\u0628\u064a\u0629 \u0645\u0646 \u0627\u0644\u062a\u062c\u0627\u0631\u0628 \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629 \u0627\u0644\u0623\u0648\u0644\u0649 \u0639\u0644\u0649 \u0627\u0644\u0628\u0634\u0631 \u0644\u0639\u0644\u0627\u062c RAG-18 \u0641\u064a \u062f\u0648\u0634\u064a\u0646."},"content":{"rendered":"<p class=\"wp-block-paragraph\"><strong>\u0642\u062f\u0645\u062a \u0634\u0631\u0643\u0629 Ractigen Therapeutics \u0628\u064a\u0627\u0646\u0627\u062a \u0625\u064a\u062c\u0627\u0628\u064a\u0629 \u0623\u0648\u0644\u064a\u0629 \u0639\u0644\u0649 \u0627\u0644\u0628\u0634\u0631 \u0644\u0640 RAG-18 (NCT07282652)\u060c \u0648\u0647\u0648 \u0639\u0644\u0627\u062c \u062a\u062c\u0631\u064a\u0628\u064a \u0644\u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a (\u062f\u0648\u0634\u064a\u0646) \u064a\u0633\u062a\u062e\u062f\u0645 \u0627\u0644\u062d\u0645\u0636 \u0627\u0644\u0646\u0648\u0648\u064a \u0627\u0644\u0631\u064a\u0628\u064a \u0627\u0644\u0645\u0646\u0634\u0637 \u0627\u0644\u0635\u063a\u064a\u0631 (saRNA) \u0644\u0632\u064a\u0627\u062f\u0629 \u0625\u0646\u062a\u0627\u062c \u0627\u0644\u064a\u0648\u062a\u0631\u0648\u0641\u064a\u0646.<\/strong> \u0639\u064f\u0631\u0636\u062a \u0628\u064a\u0627\u0646\u0627\u062a \u0627\u0644\u0645\u0631\u062d\u0644\u0629 \u0627\u0644\u0623\u0648\u0644\u0649 \u0645\u0646 \u0627\u0644\u062f\u0631\u0627\u0633\u0629 \u0641\u064a \u0627\u0644\u0645\u0624\u062a\u0645\u0631 \u0627\u0644\u0633\u0646\u0648\u064a \u0627\u0644\u062d\u0627\u062f\u064a \u0648\u0627\u0644\u062b\u0644\u0627\u062b\u064a\u0646 \u0644\u0644\u062c\u0645\u0639\u064a\u0629 \u0627\u0644\u0639\u0627\u0644\u0645\u064a\u0629 \u0644\u0644\u0639\u0636\u0644\u0627\u062a (WMS 2026) \u0641\u064a \u0647\u064a\u0631\u0648\u0634\u064a\u0645\u0627\u060c \u0627\u0644\u064a\u0627\u0628\u0627\u0646. \u062a\u064f\u0642\u062f\u0651\u0645 \u0627\u0644\u0646\u062a\u0627\u0626\u062c \u0623\u062f\u0644\u0629 \u0633\u0631\u064a\u0631\u064a\u0629 \u0645\u0628\u0643\u0631\u0629 \u0639\u0644\u0649 \u0642\u062f\u0631\u0629 \u0627\u0644\u062d\u0645\u0636 \u0627\u0644\u0646\u0648\u0648\u064a \u0627\u0644\u0631\u064a\u0628\u0648\u0632\u064a \u0627\u0644\u0635\u063a\u064a\u0631 \u0627\u0644\u0645\u062c\u0632\u0623 (saRNA) \u0639\u0644\u0649 \u0627\u0644\u0648\u0635\u0648\u0644 \u0625\u0644\u0649 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0627\u0644\u0647\u064a\u0643\u0644\u064a\u0629 \u0627\u0644\u0628\u0634\u0631\u064a\u0629 \u0648\u062a\u0646\u0634\u064a\u0637 \u0628\u0631\u0648\u062a\u064a\u0646 \u0637\u0628\u064a\u0639\u064a \u0641\u064a\u0647\u0627. \u0644\u0644\u0645\u0632\u064a\u062f \u0645\u0646 \u0627\u0644\u0645\u0639\u0644\u0648\u0645\u0627\u062a: <a href=\"https:\/\/dmdwarrior.com\/clinical-trials\/rag-18-early-phase-1-clinical-trial-for-duchenne-muscular-dystrophy\/\">NCT07282652<\/a><\/p>\n\n\n\n<h2 class=\"wp-block-heading\">\u0645\u0627 \u0647\u0648 \u0627\u0644\u064a\u0648\u062a\u0631\u0648\u0641\u064a\u0646 \u0648\u0644\u0645\u0627\u0630\u0627 \u0647\u0648 \u0645\u0647\u0645\u061f<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u0627\u0644\u064a\u0648\u062a\u0631\u0648\u0641\u064a\u0646 \u0628\u0631\u0648\u062a\u064a\u0646 \u0637\u0628\u064a\u0639\u064a \u064a\u0634\u0628\u0647 \u0627\u0644\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0641\u064a \u062a\u0631\u0643\u064a\u0628\u0647. \u0641\u064a \u0645\u0631\u0636 \u062f\u0648\u0634\u064a\u0646\u060c \u064a\u0624\u062f\u064a \u0646\u0642\u0635 \u0627\u0644\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0627\u0644\u0648\u0638\u064a\u0641\u064a \u0625\u0644\u0649 \u062a\u0644\u0641 \u0623\u0644\u064a\u0627\u0641 \u0627\u0644\u0639\u0636\u0644\u0627\u062a. \u064a\u0645\u0643\u0646 \u0644\u0644\u064a\u0648\u062a\u0631\u0648\u0641\u064a\u0646 \u0623\u0646 \u064a\u062d\u0644 \u0645\u062d\u0644 \u0627\u0644\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0641\u064a \u063a\u0634\u0627\u0621 \u0627\u0644\u0639\u0636\u0644\u0629\u060c \u0628\u063a\u0636 \u0627\u0644\u0646\u0638\u0631 \u0639\u0646 \u0646\u0648\u0639 \u0637\u0641\u0631\u0629 \u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0627\u0644\u062f\u0648\u0634\u064a\u0646\u064a \u0644\u062f\u0649 \u0627\u0644\u0634\u062e\u0635.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0644\u0647\u0630\u0627 \u0627\u0644\u0633\u0628\u0628\u060c \u0642\u062f \u064a\u064f\u0648\u0641\u0631 \u0631\u0641\u0639 \u0645\u0633\u062a\u0648\u0649 \u0627\u0644\u064a\u0648\u062a\u0631\u0648\u0641\u064a\u0646 \u0646\u0647\u062c\u064b\u0627 \u0639\u0644\u0627\u062c\u064a\u064b\u0627 \u0644\u0627 \u064a\u0639\u062a\u0645\u062f \u0639\u0644\u0649 \u0627\u0644\u0637\u0641\u0631\u0629 \u0627\u0644\u062c\u064a\u0646\u064a\u0629 \u0627\u0644\u062e\u0627\u0635\u0629 \u0628\u0627\u0644\u0645\u0631\u064a\u0636. \u0635\u064f\u0645\u0645 RAG-18 \u0644\u0632\u064a\u0627\u062f\u0629 \u0625\u0646\u062a\u0627\u062c \u0627\u0644\u062c\u0633\u0645 \u0627\u0644\u0637\u0628\u064a\u0639\u064a \u0644\u0644\u064a\u0648\u062a\u0631\u0648\u0641\u064a\u0646 \u0628\u062f\u0644\u0627\u064b \u0645\u0646 \u0625\u062f\u062e\u0627\u0644 \u062c\u064a\u0646 \u0628\u062f\u064a\u0644.<\/p>\n\n\n\n<h2 class=\"wp-block-heading\">\u0643\u064a\u0641 \u064a\u0639\u0645\u0644 \u062c\u0647\u0627\u0632 RAG-18\u061f<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u064a\u0633\u062a\u062e\u062f\u0645 RAG-18 \u062a\u0642\u0646\u064a\u0629 \u062a\u0646\u0634\u064a\u0637 \u0627\u0644\u062d\u0645\u0636 \u0627\u0644\u0646\u0648\u0648\u064a \u0627\u0644\u0631\u064a\u0628\u0648\u0632\u064a Ractigen Therapeutics&#039; \u0648\u064a\u062a\u0645 \u0625\u064a\u0635\u0627\u0644\u0647 \u0639\u0628\u0631 \u062a\u0642\u0646\u064a\u0629 LiCO\u2122 \u0627\u0644\u062e\u0627\u0635\u0629 \u0628\u0627\u0644\u0634\u0631\u0643\u0629. \u0648\u064a\u064f\u0639\u0637\u0649 \u0639\u0646 \u0637\u0631\u064a\u0642 \u0627\u0644\u062d\u0642\u0646 \u0627\u0644\u0648\u0631\u064a\u062f\u064a \u0634\u0647\u0631\u064a\u0627\u064b.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0635\u064f\u0645\u0645 \u0647\u0630\u0627 \u0627\u0644\u0639\u0644\u0627\u062c \u0644\u0627\u0633\u062a\u062e\u062f\u0627\u0645 \u0622\u0644\u064a\u0627\u062a \u0627\u0644\u0646\u0633\u062e \u0627\u0644\u062e\u0644\u0648\u064a\u0629 \u0627\u0644\u0630\u0627\u062a\u064a\u0629 \u0644\u0632\u064a\u0627\u062f\u0629 \u0625\u0646\u062a\u0627\u062c \u0627\u0644\u064a\u0648\u062a\u0631\u0648\u0641\u064a\u0646. \u0648\u0647\u0648 \u0644\u0627 \u064a\u0633\u062a\u062e\u062f\u0645 \u0646\u0627\u0642\u0644\u0627\u064b \u0641\u064a\u0631\u0648\u0633\u064a\u0627\u064b \u0623\u0648 \u062a\u0639\u062f\u064a\u0644\u0627\u064b \u062f\u0627\u0626\u0645\u0627\u064b \u0644\u0644\u062d\u0645\u0636 \u0627\u0644\u0646\u0648\u0648\u064a. \u0648\u0642\u062f \u062d\u0635\u0644 \u062f\u0648\u0627\u0621 RAG-18 \u0623\u064a\u0636\u0627\u064b \u0639\u0644\u0649 \u062a\u0635\u0646\u064a\u0641 \u062f\u0648\u0627\u0621 \u0627\u0644\u064a\u062a\u064a\u0645 \u0648\u062a\u0635\u0646\u064a\u0641 \u0627\u0644\u0623\u0645\u0631\u0627\u0636 \u0627\u0644\u0646\u0627\u062f\u0631\u0629 \u0644\u062f\u0649 \u0627\u0644\u0623\u0637\u0641\u0627\u0644 \u0645\u0646 \u0625\u062f\u0627\u0631\u0629 \u0627\u0644\u063a\u0630\u0627\u0621 \u0648\u0627\u0644\u062f\u0648\u0627\u0621 \u0627\u0644\u0623\u0645\u0631\u064a\u0643\u064a\u0629 (\u0631\u0642\u0645 FDA).<\/p>\n\n\n\n<h2 class=\"wp-block-heading\">\u0645\u0627\u0630\u0627 \u0623\u0638\u0647\u0631 \u0627\u0644\u0645\u0634\u0627\u0631\u0643\u0648\u0646 \u0627\u0644\u062b\u0644\u0627\u062b\u0629 \u0627\u0644\u0623\u0648\u0627\u0626\u0644\u061f<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u062c\u0627\u0621\u062a \u0627\u0644\u0628\u064a\u0627\u0646\u0627\u062a \u0627\u0644\u0645\u0628\u0644\u063a \u0639\u0646\u0647\u0627 \u0645\u0646 \u0627\u0644\u0645\u062c\u0645\u0648\u0639\u0629 \u0627\u0644\u0623\u0648\u0644\u0649 \u0627\u0644\u0645\u0643\u0648\u0646\u0629 \u0645\u0646 \u062b\u0644\u0627\u062b\u0629 \u0623\u0648\u0644\u0627\u062f \u0642\u0627\u062f\u0631\u064a\u0646 \u0639\u0644\u0649 \u0627\u0644\u0645\u0634\u064a \u062a\u062a\u0631\u0627\u0648\u062d \u0623\u0639\u0645\u0627\u0631\u0647\u0645 \u0628\u064a\u0646 4 \u0648 15 \u0639\u0627\u0645\u064b\u0627 \u0645\u0635\u0627\u0628\u064a\u0646 \u0628\u0645\u0631\u0636 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0645\u0624\u0643\u062f \u0648\u0631\u0627\u062b\u064a\u064b\u0627. <strong>\u062a\u0644\u0642\u0648\u0627 15 \u0645\u0644\u063a \u0645\u0646 RAG-18 \u0634\u0647\u0631\u064a\u064b\u0627 \u0648\u062a\u0645\u062a \u0645\u062a\u0627\u0628\u0639\u062a\u0647\u0645 \u062d\u062a\u0649 \u0627\u0644\u064a\u0648\u0645 169.<\/strong><\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u0623\u0638\u0647\u0631\u062a \u062e\u0632\u0639\u0627\u062a \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0632\u064a\u0627\u062f\u0629 \u062a\u062a\u0631\u0627\u0648\u062d \u0645\u0646 3.5 \u0625\u0644\u0649 5.3 \u0623\u0636\u0639\u0627\u0641 \u0641\u064a \u0627\u0644\u064a\u0648\u062a\u0631\u0648\u0641\u064a\u0646 \u0641\u064a \u063a\u0634\u0627\u0621 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0645\u0642\u0627\u0631\u0646\u0629 \u0628\u0627\u0644\u062e\u0637 \u0627\u0644\u0623\u0633\u0627\u0633\u064a.<\/strong> \u0644\u0627\u062d\u0638 \u0627\u0644\u0628\u0627\u062d\u062b\u0648\u0646 \u0623\u064a\u0636\u064b\u0627 \u062a\u063a\u064a\u0631\u0627\u062a \u0641\u064a \u0628\u0646\u064a\u0629 \u0627\u0644\u0639\u0636\u0644\u0627\u062a\u060c \u0628\u0645\u0627 \u0641\u064a \u0630\u0644\u0643 \u0632\u064a\u0627\u062f\u0629 \u062d\u062c\u0645 \u0623\u0644\u064a\u0627\u0641 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0648\u0627\u0646\u062e\u0641\u0627\u0636 \u0646\u0633\u0628\u0629 \u0627\u0644\u062f\u0647\u0648\u0646 \u0641\u064a\u0647\u0627. \u0648\u0623\u0638\u0647\u0631 \u0627\u0644\u062a\u0635\u0648\u064a\u0631 \u0628\u0627\u0644\u0631\u0646\u064a\u0646 \u0627\u0644\u0645\u063a\u0646\u0627\u0637\u064a\u0633\u064a \u0644\u0644\u0639\u0636\u0644\u0627\u062a \u0627\u0646\u062e\u0641\u0627\u0636\u064b\u0627 \u0641\u064a \u0627\u0644\u0645\u0624\u0634\u0631\u0627\u062a \u0627\u0644\u0645\u0631\u062a\u0628\u0637\u0629 \u0628\u0627\u0644\u0648\u0630\u0645\u0629 \u0627\u0644\u0639\u0636\u0644\u064a\u0629 \u0627\u0644\u0646\u0634\u0637\u0629 \u0648\u0627\u0644\u0627\u0644\u062a\u0647\u0627\u0628. \u0627\u0642\u0631\u0623 \u0627\u0644\u0645\u0632\u064a\u062f: <a href=\"https:\/\/dmdwarrior.com\/ar\/ractigen-therapeutics-rag-18-sarna-early-phase-1-clinical-trial-nct07282652-for-duchenne\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u0633\u0644\u0627\u0645\u0629 \u0648\u062a\u062d\u0645\u0644 RAG-18<\/a><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0623\u0638\u0647\u0631\u062a \u0627\u0644\u0646\u062a\u0627\u0626\u062c \u0627\u0644\u0648\u0638\u064a\u0641\u064a\u0629 \u0645\u0624\u0634\u0631\u0627\u062a \u0645\u062a\u0628\u0627\u064a\u0646\u0629\u060c \u0648\u0644\u0643\u0646\u0647\u0627 \u0625\u064a\u062c\u0627\u0628\u064a\u0629 \u0623\u0648 \u0645\u0633\u062a\u0642\u0631\u0629 \u0628\u0634\u0643\u0644 \u0639\u0627\u0645. \u0641\u0642\u062f \u062d\u0633\u0651\u0646 \u0623\u062d\u062f \u0627\u0644\u0645\u0634\u0627\u0631\u0643\u064a\u0646 \u0645\u0633\u0627\u0641\u0629 \u0645\u0634\u064a\u0647 \u0641\u064a \u0627\u062e\u062a\u0628\u0627\u0631 \u0627\u0644\u0633\u062a \u062f\u0642\u0627\u0626\u0642 \u0628\u0645\u0642\u062f\u0627\u0631 36.5 \u0645\u062a\u0631\u064b\u0627\u060c \u0628\u064a\u0646\u0645\u0627 \u062d\u0627\u0641\u0638 \u0645\u0634\u0627\u0631\u0643 \u0622\u062e\u0631 \u0639\u0644\u0649 \u0645\u0633\u0627\u0641\u0629 \u0645\u0634\u064a\u0647. \u0623\u0645\u0627 \u0627\u0644\u0645\u0634\u0627\u0631\u0643 \u0627\u0644\u062b\u0627\u0644\u062b\u060c \u0641\u0642\u062f \u0634\u0647\u062f \u0627\u0646\u062e\u0641\u0627\u0636\u064b\u0627 \u0641\u064a \u0645\u0633\u0627\u0641\u0629 \u0645\u0634\u064a\u0647 \u0628\u0645\u0642\u062f\u0627\u0631 62.5 \u0645\u062a\u0631\u064b\u0627. \u0648\u0623\u0638\u0647\u0631\u062a \u0642\u064a\u0627\u0633\u0627\u062a \u0648\u0638\u0627\u0626\u0641 \u0627\u0644\u0631\u0626\u0629 \u0627\u062a\u062c\u0627\u0647\u0627\u062a \u0639\u062f\u062f\u064a\u0629 \u0625\u064a\u062c\u0627\u0628\u064a\u0629 \u0644\u062f\u0649 \u0627\u0644\u0645\u0634\u0627\u0631\u0643\u064a\u0646 \u0627\u0644\u062b\u0644\u0627\u062b\u0629. \u0648\u0638\u0644\u062a \u0648\u0638\u0627\u0626\u0641 \u0627\u0644\u0642\u0644\u0628 \u0636\u0645\u0646 \u0627\u0644\u062d\u062f\u0648\u062f \u0627\u0644\u0637\u0628\u064a\u0639\u064a\u0629 \u062e\u0644\u0627\u0644 \u0641\u062a\u0631\u0629 \u0627\u0644\u0645\u062a\u0627\u0628\u0639\u0629 \u0627\u0644\u062a\u064a \u0627\u0633\u062a\u0645\u0631\u062a 24 \u0623\u0633\u0628\u0648\u0639\u064b\u0627.<\/p>\n\n\n\n<h2 class=\"wp-block-heading\">\u0627\u0644\u0633\u0644\u0627\u0645\u0629 \u0648\u0627\u0644\u062e\u0637\u0648\u0627\u062a \u0627\u0644\u062a\u0627\u0644\u064a\u0629<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u0623\u0638\u0647\u0631 \u062f\u0648\u0627\u0621 RAG-18 \u0633\u0644\u0627\u0645\u0629 \u0648\u062a\u062d\u0645\u0644\u0627\u064b \u062c\u064a\u062f\u064a\u0646 \u0641\u064a \u0627\u0644\u0645\u062c\u0645\u0648\u0639\u0629 \u0627\u0644\u0623\u0648\u0644\u0649. \u0644\u0645 \u062a\u064f\u0633\u062c\u0651\u0644 \u0623\u064a \u0633\u0645\u064a\u0629 \u062a\u062d\u062f\u0651 \u0645\u0646 \u0627\u0644\u062c\u0631\u0639\u0629\u060c \u0623\u0648 \u0623\u062d\u062f\u0627\u062b \u0636\u0627\u0626\u0631\u0629 \u062e\u0637\u064a\u0631\u0629\u060c \u0623\u0648 \u0623\u062d\u062f\u0627\u062b \u0636\u0627\u0626\u0631\u0629 \u0645\u0646 \u0627\u0644\u062f\u0631\u062c\u0629 \u0627\u0644\u062b\u0627\u0644\u062b\u0629 \u0623\u0648 \u0623\u0639\u0644\u0649 \u0638\u0647\u0631\u062a \u0623\u062b\u0646\u0627\u0621 \u0627\u0644\u0639\u0644\u0627\u062c. \u0648\u0643\u0627\u0646\u062a \u0627\u0644\u0623\u062d\u062f\u0627\u062b \u0627\u0644\u0636\u0627\u0626\u0631\u0629 \u0627\u0644\u0645\u064f\u0628\u0644\u0651\u063a \u0639\u0646\u0647\u0627 \u062e\u0641\u064a\u0641\u0629 \u0648\u0645\u0624\u0642\u062a\u0629.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u062a\u0645 \u062a\u0633\u062c\u064a\u0644 \u0627\u0644\u0645\u062c\u0645\u0648\u0639\u0629 \u0627\u0644\u062b\u0627\u0646\u064a\u0629 \u0628\u0627\u0644\u0643\u0627\u0645\u0644\u060c \u0648\u0627\u0644\u062a\u064a \u062a\u0633\u062a\u062e\u062f\u0645 \u062c\u0631\u0639\u0629 \u0634\u0647\u0631\u064a\u0629 \u0642\u062f\u0631\u0647\u0627 30 \u0645\u0644\u063a\u060c \u0648\u062a\u0633\u062a\u0645\u0631 \u0645\u062a\u0627\u0628\u0639\u0629 \u0627\u0644\u0633\u0644\u0627\u0645\u0629.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u062a\u0648\u0641\u0631 \u0647\u0630\u0647 \u0627\u0644\u0646\u062a\u0627\u0626\u062c \u0627\u0644\u0645\u0628\u0643\u0631\u0629 \u062f\u0644\u064a\u0644\u0627\u064b \u0633\u0631\u064a\u0631\u064a\u0627\u064b \u0639\u0644\u0649 \u0622\u0644\u064a\u0629 \u062a\u0646\u0634\u064a\u0637 \u0627\u0644\u062d\u0645\u0636 \u0627\u0644\u0646\u0648\u0648\u064a \u0627\u0644\u0631\u064a\u0628\u064a \u0641\u064a \u062f\u0648\u0634\u064a\u0646\u060c \u0645\u0645\u0627 \u064a\u062f\u0644 \u0639\u0644\u0649 \u0623\u0646 RAG-18 \u064a\u0645\u0643\u0646 \u0623\u0646 \u064a\u0632\u064a\u062f \u0645\u0646 \u0627\u0644\u064a\u0648\u062a\u0631\u0648\u0641\u064a\u0646 \u0641\u064a \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0627\u0644\u0647\u064a\u0643\u0644\u064a\u0629 \u0627\u0644\u0628\u0634\u0631\u064a\u0629.<\/strong> \u0648\u0645\u0639 \u0630\u0644\u0643\u060c \u0643\u0627\u0646\u062a \u0627\u0644\u0646\u062a\u0627\u0626\u062c \u0627\u0644\u0648\u0638\u064a\u0641\u064a\u0629 \u0645\u062a\u0628\u0627\u064a\u0646\u0629 \u0628\u064a\u0646 \u0627\u0644\u0645\u0634\u0627\u0631\u0643\u064a\u0646 \u0627\u0644\u062b\u0644\u0627\u062b\u0629\u060c \u0648\u0644\u0627 \u062a\u0632\u0627\u0644 \u0627\u0644\u062f\u0631\u0627\u0633\u0629 \u0641\u064a \u0645\u0631\u062d\u0644\u0629 \u0645\u0628\u0643\u0631\u0629.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u0627\u0643\u062a\u0634\u0641 \u0627\u0644\u0645\u0632\u064a\u062f<\/strong>:\u00a0<a href=\"https:\/\/dmdwarrior.com\/clinical-trials\/map\/\" target=\"_blank\" rel=\"noopener\">\u062e\u0631\u064a\u0637\u0629 \u0645\u0648\u0627\u0642\u0639 \u0627\u0644\u062a\u062c\u0627\u0631\u0628 \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629 \u0644\u0645\u0631\u0636 \u062f\u0648\u0634\u064a\u0646<\/a><\/p>","protected":false},"excerpt":{"rendered":"<p>Ractigen Therapeutics has presented positive first-in-human data for RAG-18 (NCT07282652), an investigational treatment for Duchenne muscular dystrophy (Duchenne) that uses small activating RNA (saRNA) to increase the production of utrophin. The Phase I study data were presented at the 31st Annual Congress of the World Muscle Society (WMS 2026) in Hiroshima, Japan. The results provide [&hellip;]<\/p>\n","protected":false},"author":11,"featured_media":8845,"comment_status":"closed","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[281],"tags":[123,466,467,465,925],"class_list":["post-8843","post","type-post","status-publish","format-standard","has-post-thumbnail","category-press-releases","tag-china","tag-ractigen-therapeutics","tag-rag-18","tag-sarna","tag-utrophin"],"subtitle":"\u064a\u064f\u0639\u062f\u0651 RAG-18 \u0646\u0647\u062c\u064b\u0627 \u0639\u0644\u0627\u062c\u064a\u064b\u0627 \u0648\u0627\u0639\u062f\u064b\u0627 \u0644\u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a. \u062a\u064f\u0638\u0647\u0631 \u0627\u0644\u0628\u064a\u0627\u0646\u0627\u062a \u0627\u0644\u0623\u0648\u0644\u064a\u0629 \u0627\u0631\u062a\u0641\u0627\u0639\u064b\u0627 \u0641\u064a \u0645\u0633\u062a\u0648\u0649 \u0627\u0644\u064a\u0648\u062a\u0631\u0648\u0641\u064a\u0646 \u0641\u064a \u0627\u0644\u0639\u0636\u0644\u0627\u062a\u060c \u0645\u0645\u0627 \u064a\u064f\u0642\u062f\u0651\u0645 \u0644\u0645\u062d\u0629 \u0623\u0648\u0644\u064a\u0629 \u0639\u0646 \u062a\u0646\u0634\u064a\u0637 \u0627\u0644\u062d\u0645\u0636 \u0627\u0644\u0646\u0648\u0648\u064a \u0627\u0644\u0631\u064a\u0628\u0648\u0632\u064a (RNA) \u0644\u062f\u0649 \u0627\u0644\u0628\u0634\u0631. \u0648\u0644\u0643\u0646 \u0645\u0627 \u062f\u0644\u0627\u0644\u0629 \u0630\u0644\u0643 \u0628\u0627\u0644\u0646\u0633\u0628\u0629 \u0644\u0644\u0645\u0631\u0636\u0649\u061f","_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/posts\/8843","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/users\/11"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/comments?post=8843"}],"version-history":[{"count":2,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/posts\/8843\/revisions"}],"predecessor-version":[{"id":8846,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/posts\/8843\/revisions\/8846"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/media\/8845"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/media?parent=8843"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/categories?post=8843"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/tags?post=8843"}],"curies":[{"name":"\u0648\u0648\u0631\u062f\u0628\u0631\u064a\u0633","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}