{"id":8567,"date":"2026-08-24T13:49:06","date_gmt":"2026-08-24T10:49:06","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=8567"},"modified":"2026-08-24T16:14:23","modified_gmt":"2026-08-24T13:14:23","slug":"pbgene-dmd-first-patient-dosed-gene-editing-study","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/ar\/pbgene-dmd-first-patient-dosed-gene-editing-study\/","title":{"rendered":"\u064a\u062f\u062e\u0644 \u0627\u0644\u0639\u0644\u0627\u062c PBGENE-DMD \u0627\u0644\u062a\u062c\u0627\u0631\u0628 \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629: \u0623\u0648\u0644 \u0645\u0631\u064a\u0636 \u064a\u062a\u0644\u0642\u0649 \u0627\u0644\u062c\u0631\u0639\u0629 \u0641\u064a \u062f\u0631\u0627\u0633\u0629 \u062a\u0639\u062f\u064a\u0644 \u062c\u064a\u0646\u0627\u062a \u062f\u0648\u0634\u064a\u0646"},"content":{"rendered":"<p class=\"wp-block-paragraph\">\u0644\u0642\u062f \u062d\u0642\u0642 \u0645\u0634\u0631\u0648\u0639 Precision BioSciences \u0625\u0646\u062c\u0627\u0632\u0627\u064b \u0647\u0627\u0645\u0627\u064b \u0641\u064a \u0645\u062c\u0627\u0644 \u062a\u0639\u062f\u064a\u0644 \u062c\u064a\u0646\u0627\u062a \u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a (DMD). <strong>\u0623\u0639\u0644\u0646\u062a \u0627\u0644\u0634\u0631\u0643\u0629 \u0641\u064a 24 \u0623\u063a\u0633\u0637\u0633 2026 \u0623\u0646\u0647 \u062a\u0645 \u0625\u0639\u0637\u0627\u0621 \u0627\u0644\u062c\u0631\u0639\u0629 \u0627\u0644\u0623\u0648\u0644\u0649 \u0644\u0644\u0645\u0631\u064a\u0636 \u0641\u064a \u0627\u0644\u0645\u0631\u062d\u0644\u0629 1\/2 \u0645\u0646 \u0627\u0644\u062a\u062c\u0631\u0628\u0629 \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629 FUNCTION-DMD \u0627\u0644\u062a\u064a \u062a\u0642\u064a\u0651\u0645 PBGENE-DMD\u060c \u0648\u0647\u0648 \u0639\u0644\u0627\u062c \u062a\u062c\u0631\u064a\u0628\u064a \u0644\u062a\u062d\u0631\u064a\u0631 \u0627\u0644\u062c\u064a\u0646\u0627\u062a \u0641\u064a \u0627\u0644\u062c\u0633\u0645 \u0627\u0644\u062d\u064a \u0644\u0645\u0631\u0636 \u062f\u0648\u0634\u064a\u0646.<\/strong> \u062a\u0645 \u0625\u0639\u0637\u0627\u0621 \u0627\u0644\u062c\u0631\u0639\u0629 \u0627\u0644\u0623\u0648\u0644\u0649 \u0641\u064a \u0645\u0633\u062a\u0634\u0641\u0649 \u0623\u0631\u0643\u0646\u0633\u0627\u0633 \u0644\u0644\u0623\u0637\u0641\u0627\u0644\u060c \u0648\u0647\u0648 \u0645\u0631\u0643\u0632 \u0645\u062a\u062e\u0635\u0635 \u0641\u064a \u0631\u0639\u0627\u064a\u0629 \u0645\u0631\u0636\u0649 \u062f\u0648\u0634\u064a\u0646.<\/p>\n\n\n\n<div class=\"wp-block-rank-math-toc-block\" id=\"rank-math-toc\"><h2>\u062c\u062f\u0648\u0644 \u0627\u0644\u0645\u062d\u062a\u0648\u064a\u0627\u062a<\/h2><nav><ul><li><a href=\"#what-is-pbgene-dmd\">\u0645\u0627 \u0647\u0648 PBGENE-DMD\u061f<\/a><\/li><li><a href=\"#why-exons-45-55-matter-in-duchenne\">\u0644\u0645\u0627\u0630\u0627 \u062a\u064f\u0639\u062f\u0651 \u0627\u0644\u0625\u0643\u0633\u0648\u0646\u0627\u062a \u0645\u0646 45 \u0625\u0644\u0649 55 \u0645\u0647\u0645\u0629 \u0641\u064a \u062f\u0648\u0634\u064a\u0646\u061f<\/a><\/li><li><a href=\"#function-dmd-phase-1-2-trial-begins\">\u0628\u062f\u0621 \u0627\u0644\u0645\u0631\u062d\u0644\u0629 \u0627\u0644\u0623\u0648\u0644\u0649\/\u0627\u0644\u062b\u0627\u0646\u064a\u0629 \u0645\u0646 \u0627\u0644\u062a\u062c\u0627\u0631\u0628 \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629 FUNCTION-DMD<\/a><\/li><li><a href=\"#how-pbgene-dmd-differs-from-microdystrophin\">\u0643\u064a\u0641 \u064a\u062e\u062a\u0644\u0641 PBGENE-DMD \u0639\u0646 \u0627\u0644\u0645\u064a\u0643\u0631\u0648\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646<\/a><\/li><li><a href=\"#what-should-dmd-families-watch-next\">\u0645\u0627 \u0627\u0644\u0630\u064a \u064a\u062c\u0628 \u0639\u0644\u0649 \u0639\u0627\u0626\u0644\u0627\u062a \u0645\u0631\u0636\u0649 \u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0627\u0644\u062f\u0648\u0634\u064a\u0646\u064a \u0645\u0634\u0627\u0647\u062f\u062a\u0647 \u0644\u0627\u062d\u0642\u0627\u064b\u061f<\/a><\/li><\/ul><\/nav><\/div>\n\n\n\n<h2 id=\"what-is-pbgene-dmd\" class=\"wp-block-heading\">\u0645\u0627 \u0647\u0648 PBGENE-DMD\u061f<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u0635\u064f\u0645\u0645 \u0627\u0644\u0639\u0644\u0627\u062c PBGENE-DMD \u0644\u0645\u0639\u0627\u0644\u062c\u0629 \u0627\u0644\u062e\u0644\u0644 \u0627\u0644\u062c\u064a\u0646\u064a \u0627\u0644\u0623\u0633\u0627\u0633\u064a \u0628\u062f\u0644\u0627\u064b \u0645\u0646 \u0645\u062c\u0631\u062f \u0625\u064a\u0635\u0627\u0644 \u0628\u0631\u0648\u062a\u064a\u0646 \u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0645\u064f\u062e\u062a\u0635\u0631. \u064a\u0633\u062a\u062e\u062f\u0645 \u0647\u0630\u0627 \u0627\u0644\u0639\u0644\u0627\u062c \u0646\u0648\u0643\u0644\u064a\u0627\u0632\u064a\u0646 \u0645\u062a\u0643\u0627\u0645\u0644\u064a\u0646 \u0645\u0646 \u0646\u0648\u0639 ARCUS\u060c \u064a\u062a\u0645 \u0625\u064a\u0635\u0627\u0644\u0647\u0645\u0627 \u0639\u0628\u0631 \u0646\u0627\u0642\u0644 \u0641\u064a\u0631\u0648\u0633\u064a \u0645\u0631\u062a\u0628\u0637 \u0628\u0627\u0644\u063a\u062f\u062f (AAV) \u0648\u0627\u062d\u062f\u060c \u0644\u0627\u0633\u062a\u0626\u0635\u0627\u0644 \u0627\u0644\u0625\u0643\u0633\u0648\u0646\u0627\u062a \u0645\u0646 45 \u0625\u0644\u0649 55 \u0645\u0646 \u062c\u064a\u0646 DMD. \u0648\u0627\u0644\u0647\u062f\u0641 \u0647\u0648 \u0627\u0633\u062a\u0639\u0627\u062f\u0629 \u0625\u0637\u0627\u0631 \u0627\u0644\u0642\u0631\u0627\u0621\u0629 \u0627\u0644\u0635\u062d\u064a\u062d \u0648\u062a\u0645\u0643\u064a\u0646 \u0625\u0646\u062a\u0627\u062c \u0628\u0631\u0648\u062a\u064a\u0646 \u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0648\u0638\u064a\u0641\u064a \u0634\u0628\u0647 \u0643\u0627\u0645\u0644 \u0627\u0644\u0637\u0648\u0644.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u062a\u064f\u0639\u062f\u0651 \u0647\u0630\u0647 \u0627\u0644\u0627\u0633\u062a\u0631\u0627\u062a\u064a\u062c\u064a\u0629 \u0630\u0627\u062a \u0623\u0647\u0645\u064a\u0629 \u0639\u0644\u0645\u064a\u0629 \u0628\u0627\u0644\u063a\u0629\u060c \u0625\u0630 \u0633\u0628\u0642 \u062f\u0631\u0627\u0633\u0629 \u062a\u0639\u062f\u064a\u0644 \u0627\u0644\u062c\u064a\u0646\u0627\u062a \u0643\u0648\u0633\u064a\u0644\u0629 \u0644\u0625\u0632\u0627\u0644\u0629 \u0627\u0644\u0645\u0646\u0627\u0637\u0642 \u0627\u0644\u0645\u064f\u0639\u0637\u0650\u0651\u0644\u0629 \u0641\u064a \u062c\u064a\u0646 \u0627\u0644\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0648\u0627\u0633\u062a\u0639\u0627\u062f\u0629 \u0627\u0644\u062a\u0639\u0628\u064a\u0631 \u0639\u0646\u0647. \u0648\u0642\u062f \u0623\u0638\u0647\u0631\u062a \u0627\u0644\u062f\u0631\u0627\u0633\u0627\u062a \u0627\u0644\u062a\u062c\u0631\u064a\u0628\u064a\u0629 \u062d\u0630\u0641 \u0627\u0644\u0625\u0643\u0633\u0648\u0646\u0627\u062a \u0645\u0646 45 \u0625\u0644\u0649 55 \u0648\u0627\u0633\u062a\u0639\u0627\u062f\u0629 \u0627\u0644\u062a\u0639\u0628\u064a\u0631 \u0639\u0646 \u0627\u0644\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0641\u064a \u0646\u0645\u0627\u0630\u062c \u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0627\u0644\u062f\u0648\u0634\u064a\u0646\u064a. \u0644\u0644\u0645\u0632\u064a\u062f \u0645\u0646 \u0627\u0644\u0645\u0639\u0644\u0648\u0645\u0627\u062a: <a href=\"https:\/\/dmdwarrior.com\/ar\/precision-biosciences-pbgene-dmd-restores-production-of-nearly-full-length-dystrophin-protein\/\" target=\"_blank\" data-type=\"post\" data-id=\"3860\" rel=\"noreferrer noopener\">PBGENE-DMD<\/a><\/p>\n\n\n\n<h2 id=\"why-exons-45-55-matter-in-duchenne\" class=\"wp-block-heading\">\u0644\u0645\u0627\u0630\u0627 \u062a\u064f\u0639\u062f\u0651 \u0627\u0644\u0625\u0643\u0633\u0648\u0646\u0627\u062a \u0645\u0646 45 \u0625\u0644\u0649 55 \u0645\u0647\u0645\u0629 \u0641\u064a \u062f\u0648\u0634\u064a\u0646\u061f<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u062a\u0645\u062b\u0644 \u0645\u0646\u0637\u0642\u0629 \u0627\u0644\u0625\u0643\u0633\u0648\u0646 45-55 \u0646\u0642\u0637\u0629 \u0633\u0627\u062e\u0646\u0629 \u0631\u0626\u064a\u0633\u064a\u0629 \u0644\u0637\u0641\u0631\u0627\u062a DMD. <strong>\u062a\u0634\u064a\u0631 \u062a\u0642\u062f\u064a\u0631\u0627\u062a Precision BioSciences \u0625\u0644\u0649 \u0623\u0646 \u0627\u0644\u0637\u0641\u0631\u0627\u062a \u0641\u064a \u0647\u0630\u0647 \u0627\u0644\u0645\u0646\u0637\u0642\u0629 \u0642\u062f \u062a\u062c\u0639\u0644 \u0645\u0627 \u064a\u0642\u0631\u0628 \u0645\u0646 60 \u0628\u0627\u0644\u0645\u0627\u0626\u0629 \u0645\u0646 \u0627\u0644\u0623\u0648\u0644\u0627\u062f \u0627\u0644\u0645\u0635\u0627\u0628\u064a\u0646 \u0628\u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0627\u0644\u062f\u0648\u0634\u064a\u0646\u064a \u0642\u0627\u0628\u0644\u064a\u0646 \u0644\u0644\u0639\u0644\u0627\u062c \u0628\u0648\u0627\u0633\u0637\u0629 PBGENE-DMD.<\/strong><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0645\u0639 \u0630\u0644\u0643\u060c \u0644\u0627 \u064a\u0646\u0628\u063a\u064a \u0627\u0644\u062e\u0644\u0637 \u0628\u064a\u0646 \u0627\u0644\u0623\u0647\u0644\u064a\u0629 \u0627\u0644\u062c\u064a\u0646\u064a\u0629 \u0648\u0627\u0644\u0641\u0639\u0627\u0644\u064a\u0629 \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629. \u0641\u0642\u062f \u064a\u0643\u0648\u0646 \u0644\u062f\u0649 \u0627\u0644\u0645\u0631\u064a\u0636 \u0637\u0641\u0631\u0629 \u0641\u064a \u0627\u0644\u0645\u0646\u0637\u0642\u0629 \u0627\u0644\u0645\u0633\u062a\u0647\u062f\u0641\u0629\u060c \u0648\u0645\u0639 \u0630\u0644\u0643 \u064a\u062d\u062a\u0627\u062c \u0625\u0644\u0649 \u062a\u0642\u064a\u064a\u0645 \u0625\u0636\u0627\u0641\u064a \u0642\u0628\u0644 \u062a\u062d\u062f\u064a\u062f \u0645\u0627 \u0625\u0630\u0627 \u0643\u0627\u0646\u062a \u0627\u0644\u0645\u0634\u0627\u0631\u0643\u0629 \u0641\u064a \u062a\u062c\u0631\u0628\u0629 \u0633\u0631\u064a\u0631\u064a\u0629 \u0623\u0648 \u0627\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u0645\u0633\u062a\u0642\u0628\u0644\u064a \u0645\u0646\u0627\u0633\u0628\u0629.<\/p>\n\n\n\n<h2 id=\"function-dmd-phase-1-2-trial-begins\" class=\"wp-block-heading\">\u0628\u062f\u0621 \u0627\u0644\u0645\u0631\u062d\u0644\u0629 \u0627\u0644\u0623\u0648\u0644\u0649\/\u0627\u0644\u062b\u0627\u0646\u064a\u0629 \u0645\u0646 \u0627\u0644\u062a\u062c\u0627\u0631\u0628 \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629 FUNCTION-DMD<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u062a\u062c\u0631\u064a \u062f\u0631\u0627\u0633\u0629 FUNCTION-DMD \u062d\u0627\u0644\u064a\u064b\u0627 \u0639\u0645\u0644\u064a\u0629 \u062a\u0633\u062c\u064a\u0644 \u0645\u0631\u0636\u0649 \u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0627\u0644\u062f\u0648\u0634\u064a\u0646\u064a \u0627\u0644\u0642\u0627\u062f\u0631\u064a\u0646 \u0639\u0644\u0649 \u0627\u0644\u0645\u0634\u064a \u0648\u0627\u0644\u0630\u064a\u0646 \u062a\u062a\u0631\u0627\u0648\u062d \u0623\u0639\u0645\u0627\u0631\u0647\u0645 \u0628\u064a\u0646 2 \u06487 \u0633\u0646\u0648\u0627\u062a \u0648\u0627\u0644\u0630\u064a\u0646 \u064a\u0639\u0627\u0646\u0648\u0646 \u0645\u0646 \u0637\u0641\u0631\u0627\u062a \u0628\u064a\u0646 \u0627\u0644\u0625\u0643\u0633\u0648\u0646\u0627\u062a 45 \u064855.<\/strong> \u062a\u0634\u0627\u0631\u0643 \u0639\u062f\u0629 \u0645\u0648\u0627\u0642\u0639 \u0633\u0631\u064a\u0631\u064a\u0629 \u0645\u062a\u062e\u0635\u0635\u0629 \u0641\u064a \u0627\u0644\u0648\u0644\u0627\u064a\u0627\u062a \u0627\u0644\u0645\u062a\u062d\u062f\u0629 \u0627\u0644\u0623\u0645\u0631\u064a\u0643\u064a\u0629 \u0641\u064a \u062f\u0631\u0627\u0633\u0629 \u062f\u0648\u0634\u064a\u0646\u060c \u0648\u0645\u0646 \u0627\u0644\u0645\u062a\u0648\u0642\u0639 \u0627\u0644\u062d\u0635\u0648\u0644 \u0639\u0644\u0649 \u0628\u064a\u0627\u0646\u0627\u062a \u0627\u0644\u0633\u0644\u0627\u0645\u0629 \u0627\u0644\u0623\u0648\u0644\u064a\u0629 \u0628\u062d\u0644\u0648\u0644 \u0646\u0647\u0627\u064a\u0629 \u0639\u0627\u0645 2026. \u0627\u0643\u062a\u0634\u0641 \u0627\u0644\u0622\u0646: <a href=\"https:\/\/dmdwarrior.com\/ar\/duchenne-exon-deletion-tool\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u0623\u062f\u0627\u0629 \u062d\u0630\u0641 \u0625\u0643\u0633\u0648\u0646 \u062f\u0648\u0634\u064a\u0646<\/a><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0627\u0644\u0623\u0648\u0644\u0648\u064a\u0629 \u0627\u0644\u0642\u0635\u0648\u0649 \u0647\u064a \u0627\u0644\u0633\u0644\u0627\u0645\u0629. \u0648\u0644\u0623\u0646 \u062a\u0642\u0646\u064a\u0629 PBGENE-DMD \u062a\u064f\u0639\u062f\u0651\u0644 \u0627\u0644\u062d\u0645\u0636 \u0627\u0644\u0646\u0648\u0648\u064a \u0628\u0634\u0643\u0644 \u062f\u0627\u0626\u0645\u060c \u064a\u062c\u0628 \u0639\u0644\u0649 \u0627\u0644\u0628\u0631\u0646\u0627\u0645\u062c \u0627\u0644\u0633\u0631\u064a\u0631\u064a \u0623\u0646 \u064a\u062d\u062f\u062f \u0644\u064a\u0633 \u0641\u0642\u0637 \u0645\u0627 \u0625\u0630\u0627 \u0643\u0627\u0646 \u0627\u0644\u062a\u0639\u062f\u064a\u0644 \u064a\u062d\u062f\u062b\u060c \u0628\u0644 \u0623\u064a\u0636\u0627\u064b \u0645\u0627 \u0625\u0630\u0627 \u0643\u0627\u0646 \u0627\u0644\u0639\u0644\u0627\u062c \u064a\u064f\u0646\u062a\u062c \u0645\u0633\u062a\u0648\u0649 \u0645\u0642\u0628\u0648\u0644\u0627\u064b \u0645\u0646 \u0627\u0644\u0633\u0644\u0627\u0645\u0629 \u0648\u062a\u0623\u062b\u064a\u0631\u0627\u062a \u0628\u064a\u0648\u0644\u0648\u062c\u064a\u0629 \u0648\u0648\u0638\u064a\u0641\u064a\u0629 \u0630\u0627\u062a \u0645\u063a\u0632\u0649.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0647\u0630\u0627 \u0627\u0644\u062a\u0645\u064a\u064a\u0632 \u0628\u0627\u0644\u063a \u0627\u0644\u0623\u0647\u0645\u064a\u0629. \u0641\u0627\u0644\u0646\u062c\u0627\u062d \u0641\u064a \u0627\u0644\u062a\u062c\u0627\u0631\u0628 \u0645\u0627 \u0642\u0628\u0644 \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629 \u0644\u0627 \u064a\u0636\u0645\u0646 \u0627\u0644\u0641\u0639\u0627\u0644\u064a\u0629 \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629. \u0648\u062a\u0624\u0643\u062f \u0625\u0631\u0634\u0627\u062f\u0627\u062a FDA \u0644\u062a\u0637\u0648\u064a\u0631 \u0623\u062f\u0648\u064a\u0629 \u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0627\u0644\u062f\u0648\u0634\u064a\u0646\u064a \u0639\u0644\u0649 \u0623\u0647\u0645\u064a\u0629 \u0627\u0644\u0646\u062a\u0627\u0626\u062c \u0630\u0627\u062a \u0627\u0644\u062f\u0644\u0627\u0644\u0629 \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629\u060c \u0648\u062a\u0634\u062c\u0639 \u0639\u0644\u0649 \u0627\u0644\u062a\u0642\u064a\u064a\u0645 \u0627\u0644\u0634\u0627\u0645\u0644 \u0644\u0644\u0623\u0639\u0631\u0627\u0636 \u0627\u0644\u0647\u064a\u0643\u0644\u064a\u0629 \u0648\u0627\u0644\u062a\u0646\u0641\u0633\u064a\u0629 \u0648\u0627\u0644\u0642\u0644\u0628\u064a\u0629 \u062d\u064a\u062b\u0645\u0627 \u0623\u0645\u0643\u0646. \u0644\u0644\u0645\u0632\u064a\u062f \u0645\u0646 \u0627\u0644\u0645\u0639\u0644\u0648\u0645\u0627\u062a: <a href=\"https:\/\/dmdwarrior.com\/clinical-trials\/pbgene-dmd-phase-1-2a-clinical-trial-for-duchenne-function-dmd\/\" target=\"_blank\" rel=\"noreferrer noopener\">PBGENE-DMD \u0627\u0644\u0645\u0631\u062d\u0644\u0629 1\/2\u0623 \u0645\u0646 \u0627\u0644\u062a\u062c\u0627\u0631\u0628 \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629<\/a><\/p>\n\n\n\n<h2 id=\"how-pbgene-dmd-differs-from-microdystrophin\" class=\"wp-block-heading\">\u0643\u064a\u0641 \u064a\u062e\u062a\u0644\u0641 PBGENE-DMD \u0639\u0646 \u0627\u0644\u0645\u064a\u0643\u0631\u0648\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u064a\u064f\u0639\u062f\u0651 \u0645\u0635\u062f\u0631 \u0627\u0644\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0627\u0644\u0645\u064f\u0633\u062a\u0647\u062f\u0641 \u0623\u062d\u062f \u0627\u0644\u0641\u0631\u0648\u0642\u0627\u062a \u0627\u0644\u0631\u0626\u064a\u0633\u064a\u0629. \u064a\u0647\u062f\u0641 \u0645\u0634\u0631\u0648\u0639 PBGENE-DMD \u0625\u0644\u0649 \u062a\u0639\u062f\u064a\u0644 \u062c\u064a\u0646 DMD \u0627\u0644\u062e\u0627\u0635 \u0628\u0627\u0644\u0645\u0631\u064a\u0636\u060c \u0645\u0645\u0627 \u0642\u062f \u064a\u0633\u0645\u062d \u0628\u0625\u0646\u062a\u0627\u062c \u062f\u0627\u062e\u0644\u064a \u0644\u0628\u0631\u0648\u062a\u064a\u0646 \u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0634\u0628\u0647 \u0643\u0627\u0645\u0644 \u0627\u0644\u0637\u0648\u0644. \u0648\u064a\u062e\u062a\u0644\u0641 \u0647\u0630\u0627 \u0639\u0646 \u0623\u0633\u0627\u0644\u064a\u0628 \u0627\u0644\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0627\u0644\u0645\u0635\u063a\u0631\u060c \u0627\u0644\u062a\u064a \u062a\u064f\u062f\u062e\u0644 \u0628\u0646\u064a\u0629 \u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0645\u064f\u062e\u062a\u0635\u0631\u0629.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0623\u0638\u0647\u0631\u062a \u062f\u0631\u0627\u0633\u0629 Precision BioSciences \u0646\u062a\u0627\u0626\u062c \u0645\u0627 \u0642\u0628\u0644 \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629 \u0645\u0634\u062c\u0639\u0629\u060c \u0628\u0645\u0627 \u0641\u064a \u0630\u0644\u0643 \u0627\u0633\u062a\u0639\u0627\u062f\u0629 \u0627\u0644\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0648\u062a\u062d\u0633\u064a\u0646\u0627\u062a \u0648\u0638\u064a\u0641\u064a\u0629 \u0641\u064a \u0627\u0644\u0646\u0645\u0627\u0630\u062c \u0627\u0644\u062d\u064a\u0648\u0627\u0646\u064a\u0629. \u0625\u0644\u0627 \u0623\u0646 \u0647\u0630\u0647 \u0627\u0644\u0646\u062a\u0627\u0626\u062c \u0644\u0627 \u062a\u0632\u0627\u0644 \u0641\u064a \u0645\u0631\u062d\u0644\u0629 \u0645\u0627 \u0642\u0628\u0644 \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629\u060c \u0648\u0628\u0627\u0644\u062a\u0627\u0644\u064a \u0644\u0627 \u064a\u0645\u0643\u0646\u0647\u0627 \u0627\u0644\u062c\u0632\u0645 \u0628\u062d\u062f\u0648\u062b \u0641\u0648\u0627\u0626\u062f \u0645\u0645\u0627\u062b\u0644\u0629 \u0644\u062f\u0649 \u0627\u0644\u0628\u0634\u0631.<\/p>\n\n\n\n<h2 id=\"what-should-dmd-families-watch-next\" class=\"wp-block-heading\">\u0645\u0627 \u0627\u0644\u0630\u064a \u064a\u062c\u0628 \u0639\u0644\u0649 \u0639\u0627\u0626\u0644\u0627\u062a \u0645\u0631\u0636\u0649 \u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0627\u0644\u062f\u0648\u0634\u064a\u0646\u064a \u0645\u0634\u0627\u0647\u062f\u062a\u0647 \u0644\u0627\u062d\u0642\u0627\u064b\u061f<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u062a\u062a\u0645\u062b\u0644 \u0623\u0647\u0645 \u0627\u0644\u0645\u062d\u0637\u0627\u062a \u0627\u0644\u0631\u0626\u064a\u0633\u064a\u0629 \u0641\u064a \u0628\u064a\u0627\u0646\u0627\u062a \u0627\u0644\u0633\u0644\u0627\u0645\u0629 \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629\u060c \u0648\u0627\u0633\u062a\u0639\u0627\u062f\u0629 \u0627\u0644\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646\u060c \u0648\u0627\u0644\u0646\u062a\u0627\u0626\u062c \u0627\u0644\u0648\u0638\u064a\u0641\u064a\u0629\u060c \u0648\u0627\u0633\u062a\u062f\u0627\u0645\u0629 \u0627\u0644\u0646\u062a\u0627\u0626\u062c. \u064a\u0646\u0628\u063a\u064a \u0639\u0644\u0649 \u0627\u0644\u0639\u0627\u0626\u0644\u0627\u062a \u0627\u0644\u062a\u0645\u064a\u064a\u0632 \u0628\u062f\u0642\u0629 \u0628\u064a\u0646 \u0646\u062a\u0627\u0626\u062c \u0627\u0644\u062f\u0631\u0627\u0633\u0627\u062a \u0645\u0627 \u0642\u0628\u0644 \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629 \u0627\u0644\u062a\u064a \u062a\u064f\u0639\u0644\u0646 \u0639\u0646\u0647\u0627 \u0627\u0644\u0634\u0631\u0643\u0627\u062a \u0648\u0627\u0644\u0623\u062f\u0644\u0629 \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629 \u0627\u0644\u0628\u0634\u0631\u064a\u0629 \u0627\u0644\u062a\u064a \u062e\u0636\u0639\u062a \u0644\u0645\u0631\u0627\u062c\u0639\u0629 \u0627\u0644\u0623\u0642\u0631\u0627\u0646.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u064a\u064f\u0639\u062f \u0645\u0631\u0636 \u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0627\u0644\u062f\u0648\u0634\u064a\u0646\u064a \u0645\u0631\u0636\u064b\u0627 \u0645\u062a\u0639\u062f\u062f \u0627\u0644\u0623\u0646\u0638\u0645\u0629 \u064a\u0634\u0645\u0644 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0627\u0644\u0647\u064a\u0643\u0644\u064a\u0629 \u0648\u0627\u0644\u0642\u0644\u0628\u064a\u0629 \u0648\u0627\u0644\u062a\u0646\u0641\u0633\u064a\u0629\u060c \u0645\u0645\u0627 \u064a\u062c\u0639\u0644 \u0627\u0644\u062a\u0642\u064a\u064a\u0645 \u0627\u0644\u0634\u0627\u0645\u0644 \u0623\u0645\u0631\u064b\u0627 \u0636\u0631\u0648\u0631\u064a\u064b\u0627.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0644\u0630\u0627\u060c \u062a\u064f\u0645\u062b\u0644 \u062c\u0631\u0639\u0629 \u0627\u0644\u0645\u0631\u064a\u0636 \u0627\u0644\u0623\u0648\u0644\u0649 \u0628\u062f\u0627\u064a\u0629\u064b \u0648\u0644\u064a\u0633\u062a \u0646\u0647\u0627\u064a\u0629\u064b. \u0648\u0642\u062f \u0627\u0646\u062a\u0642\u0644 \u0639\u0642\u0627\u0631 PBGENE-DMD \u0627\u0644\u0622\u0646 \u0645\u0646 \u0645\u0631\u062d\u0644\u0629 \u0627\u0644\u062a\u0637\u0648\u064a\u0631 \u0627\u0644\u0645\u062e\u062a\u0628\u0631\u064a \u0625\u0644\u0649 \u0627\u0644\u062a\u062c\u0627\u0631\u0628 \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629 \u0639\u0644\u0649 \u0627\u0644\u0628\u0634\u0631. \u0648\u0627\u0644\u0633\u0624\u0627\u0644 \u0627\u0644\u062a\u0627\u0644\u064a \u0647\u0648 \u0645\u0627 \u0625\u0630\u0627 \u0643\u0627\u0646\u062a \u0627\u0633\u062a\u0631\u0627\u062a\u064a\u062c\u064a\u0629 \u062a\u0639\u062f\u064a\u0644 \u0627\u0644\u062c\u064a\u0646\u0627\u062a \u0647\u0630\u0647 \u0642\u0627\u062f\u0631\u0629 \u0639\u0644\u0649 \u062a\u0631\u062c\u0645\u0629 \u0648\u0639\u0648\u062f\u0647\u0627 \u0627\u0644\u0628\u064a\u0648\u0644\u0648\u062c\u064a\u0629 \u0628\u0623\u0645\u0627\u0646 \u0625\u0644\u0649 \u0641\u0648\u0627\u0626\u062f \u0645\u0633\u062a\u062f\u0627\u0645\u0629 \u0648\u0645\u0644\u0645\u0648\u0633\u0629 \u0644\u0644\u0623\u0634\u062e\u0627\u0635 \u0627\u0644\u0645\u0635\u0627\u0628\u064a\u0646 \u0628\u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0627\u0643\u062a\u0634\u0641 \u0627\u0644\u0645\u0632\u064a\u062f: <a href=\"https:\/\/dmdwarrior.com\/ar\/clinical-trials\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u0627\u0633\u062a\u0643\u0634\u0641 \u0627\u0644\u062a\u062c\u0627\u0631\u0628 \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629 \u0644\u0645\u0631\u0636 \u062f\u0648\u0634\u064a\u0646 <\/a><\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><\/p>","protected":false},"excerpt":{"rendered":"<p>Precision BioSciences has reached an important milestone in Duchenne muscular dystrophy (DMD) gene editing. The company announced on August 24, 2026, that the first patient has been dosed in the Phase 1\/2 FUNCTION-DMD clinical trial evaluating PBGENE-DMD, an investigational in vivo gene-editing therapy for Duchenne. The first dose was administered at Arkansas Children\u2019s Hospital, a [&hellip;]<\/p>\n","protected":false},"author":5,"featured_media":8568,"comment_status":"open","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[27],"tags":[726,242,359,72,725,314,724,313],"class_list":["post-8567","post","type-post","status-publish","format-standard","has-post-thumbnail","category-research","tag-arcus-gene-editing","tag-clinical-trials","tag-full-length-dystrophin","tag-gene-editing","tag-gene-editing-therapy","tag-pbgene-dmd","tag-pbgene-dmd-therapy","tag-precision-biosciences"],"subtitle":"\u062d\u0642\u0642\u062a \u062a\u0642\u0646\u064a\u0629 PBGENE-DMD \u0625\u0646\u062c\u0627\u0632\u064b\u0627 \u0647\u0627\u0645\u064b\u0627 \u0641\u064a \u0623\u0628\u062d\u0627\u062b \u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a. \u0641\u0642\u062f \u062a\u0644\u0642\u0649 \u0623\u0648\u0644 \u0645\u0631\u064a\u0636 \u062c\u0631\u0639\u0629 \u0645\u0646 \u0627\u0644\u0645\u0631\u062d\u0644\u0629 \u0627\u0644\u0623\u0648\u0644\u0649\/\u0627\u0644\u062b\u0627\u0646\u064a\u0629 \u0645\u0646 \u0627\u0644\u062a\u062c\u0627\u0631\u0628 \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629 \u0644\u062a\u0642\u0646\u064a\u0629 FUNCTION-DMD. \u0647\u0644 \u064a\u064f\u0645\u0643\u0646 \u0623\u0646 \u064a\u064f\u0628\u0634\u0651\u0631 \u0627\u0644\u062a\u0639\u062f\u064a\u0644 \u0627\u0644\u062c\u064a\u0646\u064a \u0628\u0639\u0635\u0631 \u062c\u062f\u064a\u062f \u0644\u0639\u0644\u0627\u062c \u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a\u061f","_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/posts\/8567","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/users\/5"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/comments?post=8567"}],"version-history":[{"count":5,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/posts\/8567\/revisions"}],"predecessor-version":[{"id":8574,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/posts\/8567\/revisions\/8574"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/media\/8568"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/media?parent=8567"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/categories?post=8567"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/tags?post=8567"}],"curies":[{"name":"\u0648\u0648\u0631\u062f\u0628\u0631\u064a\u0633","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}