{"id":8153,"date":"2026-06-24T15:04:11","date_gmt":"2026-06-24T12:04:11","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=8153"},"modified":"2026-06-24T15:51:29","modified_gmt":"2026-06-24T12:51:29","slug":"regenxbio-completes-rgx-202-confirmatory-study-for-duchenne-muscular-dystrophy","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/ar\/regenxbio-completes-rgx-202-confirmatory-study-for-duchenne-muscular-dystrophy\/","title":{"rendered":"\u0634\u0631\u0643\u0629 REGENXBIO \u062a\u064f\u0643\u0645\u0644 \u062f\u0631\u0627\u0633\u0629 \u062a\u0623\u0643\u064a\u062f\u064a\u0629 \u0644\u0639\u0642\u0627\u0631 RGX-202 \u0644\u0639\u0644\u0627\u062c \u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a"},"content":{"rendered":"<p class=\"wp-block-paragraph\">\u0623\u0639\u0644\u0646\u062a \u0634\u0631\u0643\u0629 REGENXBIO \u0639\u0646 \u0625\u062a\u0645\u0627\u0645 \u062a\u062c\u0631\u0628\u0629 \u0625\u0639\u0637\u0627\u0621 \u0627\u0644\u062c\u0631\u0639\u0627\u062a \u0644\u0644\u0645\u0631\u0636\u0649 \u0641\u064a \u0627\u0644\u062f\u0631\u0627\u0633\u0629 \u0627\u0644\u062a\u0623\u0643\u064a\u062f\u064a\u0629 \u0644\u0639\u0644\u0627\u062c\u0647\u0627 \u0627\u0644\u062c\u064a\u0646\u064a \u0627\u0644\u062a\u062c\u0631\u064a\u0628\u064a RGX-202 \u0644\u0645\u0631\u0636 \u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a (DMD). \u064a\u064f\u0645\u062b\u0644 \u0647\u0630\u0627 \u0627\u0644\u0625\u0646\u062c\u0627\u0632 \u0627\u0644\u0647\u0627\u0645 \u0627\u0643\u062a\u0645\u0627\u0644 \u0628\u0631\u0646\u0627\u0645\u062c \u0627\u0644\u062a\u0637\u0648\u064a\u0631 \u0627\u0644\u062a\u0633\u062c\u064a\u0644\u064a \u0644\u0644\u0634\u0631\u0643\u0629\u060c \u0648\u064a\u062f\u0639\u0645 \u062a\u0642\u062f\u064a\u0645 \u0637\u0644\u0628 \u062a\u0631\u062e\u064a\u0635 \u0627\u0644\u0645\u0646\u062a\u062c\u0627\u062a \u0627\u0644\u0628\u064a\u0648\u0644\u0648\u062c\u064a\u0629 (BLA) \u0627\u0644\u0645\u064f\u062e\u0637\u0637 \u0644\u0647 \u0625\u0644\u0649 \u0625\u062f\u0627\u0631\u0629 \u0627\u0644\u063a\u0630\u0627\u0621 \u0648\u0627\u0644\u062f\u0648\u0627\u0621 \u0627\u0644\u0623\u0645\u0631\u064a\u0643\u064a\u0629 (FDA) \u0641\u064a \u0627\u0644\u0631\u0628\u0639 \u0627\u0644\u062b\u0627\u0644\u062b \u0645\u0646 \u0639\u0627\u0645 2026.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u062a\u062a\u0648\u0642\u0639 \u0627\u0644\u0634\u0631\u0643\u0629 \u0623\u0646\u0647 \u0641\u064a \u062d\u0627\u0644\u0629 \u0627\u0644\u0645\u0648\u0627\u0641\u0642\u0629\u060c \u064a\u0645\u0643\u0646 \u0623\u0646 \u064a\u0635\u0628\u062d RGX-202 \u0623\u062d\u062f \u0627\u0644\u0639\u0644\u0627\u062c\u0627\u062a \u0627\u0644\u062c\u064a\u0646\u064a\u0629 \u0627\u0644\u062a\u0627\u0644\u064a\u0629 \u0627\u0644\u0645\u062a\u0627\u062d\u0629 \u0644\u0644\u0623\u0634\u062e\u0627\u0635 \u0627\u0644\u0645\u0635\u0627\u0628\u064a\u0646 \u0628\u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a.<\/p>\n\n\n\n<h2 class=\"wp-block-heading\">\u062a\u0645 \u0627\u0644\u0627\u0646\u062a\u0647\u0627\u0621 \u0645\u0646 \u0628\u0631\u0646\u0627\u0645\u062c \u062a\u0637\u0648\u064a\u0631 RGX-202 \u0642\u0628\u0644 \u0627\u0644\u0645\u0648\u0639\u062f \u0627\u0644\u0645\u062d\u062f\u062f<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u0648\u0641\u0642\u064b\u0627 \u0644\u0634\u0631\u0643\u0629 REGENXBIO\u060c \u062a\u0645 \u0627\u0644\u0627\u0646\u062a\u0647\u0627\u0621 \u0645\u0646 \u0627\u0644\u062a\u0633\u062c\u064a\u0644 \u0648\u062a\u062d\u062f\u064a\u062f \u0627\u0644\u062c\u0631\u0639\u0627\u062a \u0641\u064a \u0627\u0644\u062f\u0631\u0627\u0633\u0629 \u0627\u0644\u062a\u0623\u0643\u064a\u062f\u064a\u0629 \u0641\u064a \u0648\u0642\u062a \u0623\u0628\u0643\u0631 \u0645\u0646 \u0627\u0644\u0645\u062a\u0648\u0642\u0639 \u0646\u0638\u0631\u064b\u0627 \u0644\u0644\u0627\u0647\u062a\u0645\u0627\u0645 \u0627\u0644\u0642\u0648\u064a \u0645\u0646 \u0643\u0644 \u0645\u0646 \u0627\u0644\u0645\u0631\u0636\u0649 \u0648\u0627\u0644\u0628\u0627\u062d\u062b\u064a\u0646 \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u064a\u0646.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u064a\u064f\u062a\u064a\u062d \u0625\u062a\u0645\u0627\u0645 \u0647\u0630\u0647 \u0627\u0644\u062f\u0631\u0627\u0633\u0629 \u0644\u0644\u0634\u0631\u0643\u0629 \u0627\u0644\u0645\u0636\u064a \u0642\u062f\u0645\u064b\u0627 \u0641\u064a \u062a\u0642\u062f\u064a\u0645 \u0637\u0644\u0628 \u062a\u0631\u062e\u064a\u0635 \u0627\u0644\u0645\u0646\u062a\u062c \u0627\u0644\u0628\u064a\u0648\u0644\u0648\u062c\u064a (BLA) \u0627\u0644\u0645\u064f\u062e\u0637\u0637 \u0644\u0647 \u0628\u0645\u0648\u062c\u0628 \u0645\u0633\u0627\u0631 \u0627\u0644\u0645\u0648\u0627\u0641\u0642\u0629 \u0627\u0644\u0645\u064f\u0639\u062c\u0651\u0644\u0629 \u0627\u0644\u062e\u0627\u0635 \u0628\u0631\u0642\u0645 FDA. \u0627\u0642\u0631\u0623 \u0627\u0644\u0645\u0632\u064a\u062f: <a href=\"https:\/\/dmdwarrior.com\/ar\/biologics-license-application-bla\/\" target=\"_blank\" data-type=\"post\" data-id=\"5027\" rel=\"noreferrer noopener\">\u0645\u0627\u0630\u0627 \u062a\u0639\u0646\u064a BLA \u0641\u064a \u0627\u0644\u0645\u0648\u0627\u0641\u0642\u0627\u062a \u0639\u0644\u0649 \u0627\u0644\u0623\u062f\u0648\u064a\u0629 FDA\u061f<\/a><\/p>\n\n\n\n<h3 class=\"wp-block-heading\">\u0645\u0627 \u0647\u0648 \u0645\u0633\u0627\u0631 \u0627\u0644\u0645\u0648\u0627\u0641\u0642\u0629 \u0627\u0644\u0645\u0639\u062c\u0644\u0629\u061f<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u0635\u064f\u0645\u0645 \u0645\u0633\u0627\u0631 \u0627\u0644\u0645\u0648\u0627\u0641\u0642\u0629 \u0627\u0644\u0645\u064f\u0639\u062c\u0651\u0644 \u0644\u0645\u0633\u0627\u0639\u062f\u0629 \u0627\u0644\u0639\u0644\u0627\u062c\u0627\u062a \u0627\u0644\u0648\u0627\u0639\u062f\u0629 \u0644\u0644\u0623\u0645\u0631\u0627\u0636 \u0627\u0644\u062e\u0637\u064a\u0631\u0629 \u0639\u0644\u0649 \u0627\u0644\u0648\u0635\u0648\u0644 \u0625\u0644\u0649 \u0627\u0644\u0645\u0631\u0636\u0649 \u0628\u0634\u0643\u0644 \u0623\u0633\u0631\u0639. \u0648\u0628\u0645\u0648\u062c\u0628 \u0647\u0630\u0647 \u0627\u0644\u0639\u0645\u0644\u064a\u0629\u060c \u064a\u0645\u0643\u0646 \u0623\u0646 \u062a\u062d\u0635\u0644 \u0627\u0644\u0639\u0644\u0627\u062c\u0627\u062a \u0639\u0644\u0649 \u0627\u0644\u0645\u0648\u0627\u0641\u0642\u0629 \u0628\u0646\u0627\u0621\u064b \u0639\u0644\u0649 \u0645\u0624\u0634\u0631\u0627\u062a \u0628\u062f\u064a\u0644\u0629 - \u0645\u062b\u0644 \u0627\u0644\u0645\u0624\u0634\u0631\u0627\u062a \u0627\u0644\u062d\u064a\u0648\u064a\u0629 - \u0627\u0644\u062a\u064a \u064a\u064f\u0631\u062c\u0651\u062d \u0623\u0646 \u062a\u062a\u0646\u0628\u0623 \u0628\u0627\u0644\u0641\u0627\u0626\u062f\u0629 \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u062a\u0639\u062a\u0642\u062f \u0634\u0631\u0643\u0629 REGENXBIO \u0623\u0646 RGX-202 \u064a\u0641\u064a \u0628\u0647\u0630\u0647 \u0627\u0644\u0645\u062a\u0637\u0644\u0628\u0627\u062a \u0628\u0646\u0627\u0621\u064b \u0639\u0644\u0649 \u0628\u064a\u0627\u0646\u0627\u062a \u0627\u0644\u062a\u0639\u0628\u064a\u0631 \u0639\u0646 \u0627\u0644\u0645\u064a\u0643\u0631\u0648\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646\u060c \u0648\u0627\u0644\u0646\u062a\u0627\u0626\u062c \u0627\u0644\u0648\u0638\u064a\u0641\u064a\u0629\u060c \u0648\u0645\u0644\u0641 \u0627\u0644\u0633\u0644\u0627\u0645\u0629 \u0627\u0644\u062e\u0627\u0635 \u0628\u0647.<\/p>\n\n\n\n<h2 class=\"wp-block-heading\">\u0645\u0646 \u0627\u0644\u0645\u0642\u0631\u0631 \u062a\u0642\u062f\u064a\u0645 \u0637\u0644\u0628 \u0628\u0631\u0627\u0621\u0629 \u0627\u0644\u0627\u062e\u062a\u0631\u0627\u0639 \u0631\u0642\u0645 FDA \u0641\u064a \u0627\u0644\u0631\u0628\u0639 \u0627\u0644\u062b\u0627\u0644\u062b \u0645\u0646 \u0639\u0627\u0645 2026<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u062a\u062e\u0637\u0637 \u0634\u0631\u0643\u0629 REGENXBIO \u0644\u0628\u062f\u0621 \u062a\u0642\u062f\u064a\u0645 \u0637\u0644\u0628 \u062a\u0631\u062e\u064a\u0635 \u0627\u0644\u0645\u0646\u062a\u062c \u0627\u0644\u0628\u064a\u0648\u0644\u0648\u062c\u064a (BLA) \u062e\u0644\u0627\u0644 \u0627\u0644\u0631\u0628\u0639 \u0627\u0644\u062b\u0627\u0644\u062b \u0645\u0646 \u0639\u0627\u0645 2026.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0645\u0646 \u0627\u0644\u0645\u062a\u0648\u0642\u0639 \u0623\u0646 \u064a\u062a\u0636\u0645\u0646 \u0627\u0644\u0637\u0644\u0628 \u0645\u0627 \u064a\u0644\u064a:<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u0628\u064a\u0627\u0646\u0627\u062a \u0627\u0644\u0633\u0644\u0627\u0645\u0629 \u0645\u0646 63 \u0645\u0634\u0627\u0631\u0643\u064b\u0627 \u0645\u0633\u062c\u0644\u064a\u0646 \u0641\u064a \u0627\u0644\u062f\u0631\u0627\u0633\u0627\u062a \u0627\u0644\u0645\u062d\u0648\u0631\u064a\u0629 \u0648\u0627\u0644\u062a\u0623\u0643\u064a\u062f\u064a\u0629 \u0644\u0640 AFFINITY DUCHENNE\u00ae.<\/li>\n\n\n\n<li>\u0628\u064a\u0627\u0646\u0627\u062a \u0627\u0644\u0641\u0639\u0627\u0644\u064a\u0629 \u0645\u0646 30 \u0645\u0634\u0627\u0631\u0643\u064b\u0627 \u0641\u064a \u0627\u0644\u062f\u0631\u0627\u0633\u0629 \u0627\u0644\u0645\u062d\u0648\u0631\u064a\u0629.<\/li>\n\n\n\n<li>\u0646\u062a\u0627\u0626\u062c \u0627\u0644\u062a\u0642\u064a\u064a\u0645 \u0627\u0644\u0648\u0638\u064a\u0641\u064a \u0644\u0645\u062f\u0629 \u0627\u062b\u0646\u064a \u0639\u0634\u0631 \u0634\u0647\u0631\u064b\u0627 \u0644\u0645\u0627 \u0644\u0627 \u064a\u0642\u0644 \u0639\u0646 \u0646\u0635\u0641 \u0627\u0644\u0645\u0634\u0627\u0631\u0643\u064a\u0646 \u0641\u064a \u0627\u0644\u062f\u0631\u0627\u0633\u0629 \u0627\u0644\u0645\u062d\u0648\u0631\u064a\u0629.<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\">\u0625\u0630\u0627 \u0633\u0627\u0631\u062a \u0645\u0631\u0627\u062c\u0639\u0629 FDA \u0643\u0645\u0627 \u0647\u0648 \u0645\u062a\u0648\u0642\u0639\u060c \u062a\u0639\u062a\u0642\u062f \u0627\u0644\u0634\u0631\u0643\u0629 \u0623\u0646 RGX-202 \u0642\u062f \u064a\u062d\u0635\u0644 \u0639\u0644\u0649 \u0627\u0644\u0645\u0648\u0627\u0641\u0642\u0629 \u062e\u0644\u0627\u0644 \u0627\u0644\u0646\u0635\u0641 \u0627\u0644\u062b\u0627\u0646\u064a \u0645\u0646 \u0639\u0627\u0645 2027.<\/p>\n\n\n\n<h2 class=\"wp-block-heading\">\u0627\u0644\u0646\u062a\u0627\u0626\u062c \u0627\u0644\u0631\u0626\u064a\u0633\u064a\u0629 \u0644\u0644\u062f\u0631\u0627\u0633\u0629 \u0627\u0644\u0645\u062d\u0648\u0631\u064a\u0629 RGX-202<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u0623\u0638\u0647\u0631\u062a \u0628\u064a\u0627\u0646\u0627\u062a \u0627\u0644\u062f\u0631\u0627\u0633\u0629 \u0627\u0644\u0645\u062d\u0648\u0631\u064a\u0629 \u0627\u0644\u062a\u064a \u062a\u0645 \u0627\u0644\u0625\u0628\u0644\u0627\u063a \u0639\u0646\u0647\u0627 \u0645\u0624\u062e\u0631\u064b\u0627 \u0646\u062a\u0627\u0626\u062c \u0645\u0634\u062c\u0639\u0629 \u0644\u0640 RGX-202.<\/p>\n\n\n\n<h3 class=\"wp-block-heading\">\u062a\u0645 \u062a\u062d\u0642\u064a\u0642 \u0627\u0644\u0647\u062f\u0641 \u0627\u0644\u0631\u0626\u064a\u0633\u064a \u0628\u0646\u062c\u0627\u062d<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u062d\u0642\u0642 \u062f\u0648\u0627\u0621 RGX-202 \u0647\u062f\u0641\u0647 \u0627\u0644\u0631\u0626\u064a\u0633\u064a\u060c \u062d\u064a\u062b \u0628\u0644\u063a \u0645\u0639\u062f\u0644 \u0627\u0644\u062a\u0639\u0628\u064a\u0631 \u0639\u0646 \u0628\u0631\u0648\u062a\u064a\u0646 \u0627\u0644\u0645\u064a\u0643\u0631\u0648\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0644\u062f\u0649 \u0623\u0643\u062b\u0631 \u0645\u0646 93% \u0645\u0646 \u0627\u0644\u0645\u0631\u0636\u0649 10% \u0639\u0644\u0649 \u0627\u0644\u0623\u0642\u0644 \u0641\u064a \u0627\u0644\u0623\u0633\u0628\u0648\u0639 \u0627\u0644\u062b\u0627\u0646\u064a \u0639\u0634\u0631 \u0628\u0639\u062f \u0627\u0644\u0639\u0644\u0627\u062c. \u0627\u0642\u0631\u0623 \u0627\u0644\u0645\u0632\u064a\u062f: <a href=\"https:\/\/dmdwarrior.com\/ar\/rgx-202-phase-3-affinity-duchenne-results-released-by-regenxbio\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u0623\u0638\u0647\u0631 RGX-202 \u062a\u062d\u0633\u0646\u0627\u064b \u0641\u064a \u0645\u0633\u062a\u0648\u064a\u0627\u062a \u0645\u0636\u0627\u062f\u0627\u062a \u0627\u0644\u0627\u0644\u062a\u0647\u0627\u0628 \u063a\u064a\u0631 \u0627\u0644\u0633\u062a\u064a\u0631\u0648\u064a\u062f\u064a\u0629\u060c \u0644\u0643\u0646 \u0628\u064a\u0627\u0646\u0627\u062a \u0627\u0644\u0645\u0624\u0634\u0631\u0627\u062a \u0627\u0644\u062d\u064a\u0648\u064a\u0629 \u0627\u0644\u0631\u0626\u064a\u0633\u064a\u0629 \u0645\u0641\u0642\u0648\u062f\u0629.<\/a><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0627\u0644\u0645\u064a\u0643\u0631\u0648\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0647\u0648 \u0634\u0643\u0644 \u0645\u062e\u062a\u0635\u0631 \u0645\u0646 \u0628\u0631\u0648\u062a\u064a\u0646 \u0627\u0644\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0627\u0644\u0630\u064a \u062a\u0647\u062f\u0641 \u0627\u0644\u0639\u0644\u0627\u062c\u0627\u062a \u0627\u0644\u062c\u064a\u0646\u064a\u0629 \u0625\u0644\u0649 \u0625\u0646\u062a\u0627\u062c\u0647 \u0641\u064a \u062e\u0644\u0627\u064a\u0627 \u0627\u0644\u0639\u0636\u0644\u0627\u062a. \u0648\u064a\u064f\u0639\u062f \u0646\u0642\u0635 \u0627\u0644\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0627\u0644\u0633\u0628\u0628 \u0627\u0644\u0631\u0626\u064a\u0633\u064a \u0644\u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a.<\/p>\n\n\n\n<h3 class=\"wp-block-heading\">\u062a\u062d\u0633\u064a\u0646\u0627\u062a \u0641\u064a \u0627\u0644\u0646\u062a\u0627\u0626\u062c \u0627\u0644\u0648\u0638\u064a\u0641\u064a\u0629<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u0644\u0627\u062d\u0638 \u0627\u0644\u0628\u0627\u062d\u062b\u0648\u0646 \u062a\u062d\u0633\u0646\u0627\u062a \u0645\u0644\u062d\u0648\u0638\u0629 \u0641\u064a \u0627\u0644\u0639\u062f\u064a\u062f \u0645\u0646 \u0627\u0644\u0645\u0642\u0627\u064a\u064a\u0633 \u0627\u0644\u0648\u0638\u064a\u0641\u064a\u0629 \u0644\u062f\u0649 \u0627\u0644\u0645\u0631\u0636\u0649 \u0627\u0644\u0630\u064a\u0646 \u0623\u0643\u0645\u0644\u0648\u0627 \u062a\u0642\u064a\u064a\u0645\u0627\u062a \u0627\u0644\u0645\u062a\u0627\u0628\u0639\u0629 \u0644\u0645\u062f\u0629 12 \u0634\u0647\u0631\u064b\u0627.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0648\u0634\u0645\u0644\u062a \u0647\u0630\u0647:<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u0627\u062e\u062a\u0628\u0627\u0631\u0627\u062a \u0627\u0644\u0648\u0638\u0627\u0626\u0641 \u0627\u0644\u0645\u0648\u0642\u0648\u062a\u0629<\/li>\n\n\n\n<li><a href=\"https:\/\/dmdwarrior.com\/ar\/north-star-ambulatory-assessment-nsaa-in-duchenne-dmd\/\" target=\"_blank\" data-type=\"post\" data-id=\"4959\" rel=\"noreferrer noopener\">\u0646\u062a\u0627\u0626\u062c \u062a\u0642\u064a\u064a\u0645 \u0646\u0648\u0631\u062b \u0633\u062a\u0627\u0631 \u0644\u0644\u0645\u0634\u064a (NSAA)<\/a><\/li>\n\n\n\n<li>\u0645\u0624\u0634\u0631\u0627\u062a \u0627\u0644\u0623\u062f\u0627\u0621 \u0627\u0644\u0628\u062f\u0646\u064a \u0627\u0644\u0639\u0627\u0645<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\">\u0623\u0639\u0644\u0646\u062a \u0627\u0644\u0634\u0631\u0643\u0629 \u0639\u0646 \u062a\u062d\u0633\u0646 \u0643\u0628\u064a\u0631 \u0645\u0642\u0627\u0631\u0646\u0629 \u0628\u0627\u0644\u0642\u064a\u0627\u0633\u0627\u062a \u0627\u0644\u0623\u0633\u0627\u0633\u064a\u0629.<\/p>\n\n\n\n<h3 class=\"wp-block-heading\">\u0627\u0631\u062a\u0628\u0627\u0637 \u0642\u0648\u064a \u0628\u064a\u0646 \u0627\u0644\u0645\u064a\u0643\u0631\u0648\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0648\u0627\u0644\u0648\u0638\u064a\u0641\u0629<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u0643\u0645\u0627 \u0623\u0641\u0627\u062f\u062a \u0634\u0631\u0643\u0629 REGENXBIO \u0628\u0648\u062c\u0648\u062f \u0639\u0644\u0627\u0642\u0629 \u0642\u0648\u064a\u0629 \u0628\u064a\u0646 \u0627\u0644\u062a\u0639\u0628\u064a\u0631 \u0639\u0646 \u0627\u0644\u0645\u064a\u0643\u0631\u0648\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0641\u064a \u0627\u0644\u0623\u0633\u0628\u0648\u0639 12 \u0648\u0627\u0644\u062a\u062d\u0633\u064a\u0646\u0627\u062a \u0627\u0644\u0648\u0638\u064a\u0641\u064a\u0629 \u0627\u0644\u062a\u064a \u0644\u0648\u062d\u0638\u062a \u0628\u0639\u062f \u0639\u0627\u0645 \u0648\u0627\u062d\u062f \u0645\u0646 \u0627\u0644\u0639\u0644\u0627\u062c.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u062a\u062f\u0639\u0645 \u0647\u0630\u0647 \u0627\u0644\u0646\u062a\u064a\u062c\u0629 \u0627\u0633\u062a\u062e\u062f\u0627\u0645 \u0627\u0644\u0645\u064a\u0643\u0631\u0648\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0643\u0646\u0642\u0637\u0629 \u0646\u0647\u0627\u064a\u0629 \u0628\u062f\u064a\u0644\u0629 \u0642\u062f \u062a\u0633\u0627\u0639\u062f \u0641\u064a \u0627\u0644\u062a\u0646\u0628\u0624 \u0628\u0627\u0644\u0641\u0627\u0626\u062f\u0629 \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629 \u0637\u0648\u064a\u0644\u0629 \u0627\u0644\u0645\u062f\u0649 \u0644\u0645\u0631\u0636\u0649 \u062f\u0648\u0634\u064a\u0646.<\/p>\n\n\n\n<h2 class=\"wp-block-heading\">\u0645\u0644\u0641 \u0627\u0644\u0633\u0644\u0627\u0645\u0629 \u0627\u0644\u062e\u0627\u0635 \u0628\u0640 RGX-202<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u0648\u0630\u0643\u0631\u062a \u0627\u0644\u0634\u0631\u0643\u0629 \u0623\u0646 \u062f\u0648\u0627\u0621 RGX-202 \u0643\u0627\u0646 \u062c\u064a\u062f \u0627\u0644\u062a\u062d\u0645\u0644 \u0628\u0634\u0643\u0644 \u0639\u0627\u0645 \u0637\u0648\u0627\u0644 \u0641\u062a\u0631\u0629 \u0627\u0644\u062f\u0631\u0627\u0633\u0629.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0623\u0641\u0627\u062f \u0627\u0644\u0628\u0627\u062d\u062b\u0648\u0646 \u0628\u0648\u062c\u0648\u062f \u0645\u0644\u0641 \u0623\u0645\u0627\u0646 \u0625\u064a\u062c\u0627\u0628\u064a\u060c \u0648\u0647\u0648 \u0645\u0627 \u062a\u0639\u062a\u0642\u062f \u0634\u0631\u0643\u0629 REGENXBIO \u0623\u0646\u0647 \u064a\u0645\u064a\u0632 RGX-202 \u0639\u0646 \u062e\u064a\u0627\u0631\u0627\u062a \u0627\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u0645\u062d\u062a\u0645\u0644\u0629 \u0627\u0644\u0623\u062e\u0631\u0649 \u0642\u064a\u062f \u0627\u0644\u062a\u0637\u0648\u064a\u0631 \u062d\u0627\u0644\u064a\u064b\u0627.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0633\u062a\u0648\u0641\u0631 \u0627\u0644\u0645\u0631\u0627\u0642\u0628\u0629 \u0627\u0644\u0645\u0633\u062a\u0645\u0631\u0629 \u0645\u0639\u0644\u0648\u0645\u0627\u062a \u0625\u0636\u0627\u0641\u064a\u0629 \u062d\u0648\u0644 \u0627\u0644\u0633\u0644\u0627\u0645\u0629 \u0639\u0644\u0649 \u0627\u0644\u0645\u062f\u0649 \u0627\u0644\u0637\u0648\u064a\u0644 \u0645\u0639 \u0627\u0633\u062a\u0645\u0631\u0627\u0631 \u0645\u062a\u0627\u0628\u0639\u0629 \u0627\u0644\u0645\u0631\u0636\u0649.<\/p>\n\n\n\n<h2 class=\"wp-block-heading\">\u0634\u0631\u0643\u0629 REGENXBIO \u062a\u0633\u062a\u0639\u062f \u0644\u0625\u0637\u0644\u0627\u0642 \u062a\u062c\u0627\u0631\u064a \u0645\u062d\u062a\u0645\u0644<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u062a\u062d\u0633\u0628\u0627\u064b \u0644\u0645\u0648\u0627\u0641\u0642\u0629 \u0645\u062d\u062a\u0645\u0644\u0629 \u0639\u0644\u0649 FDA\u060c \u0628\u062f\u0623\u062a \u0634\u0631\u0643\u0629 REGENXBIO \u0628\u0627\u0644\u0641\u0639\u0644 \u0641\u064a \u0625\u0639\u062f\u0627\u062f \u0628\u0646\u064a\u062a\u0647\u0627 \u0627\u0644\u062a\u062d\u062a\u064a\u0629 \u0644\u0644\u062a\u0635\u0646\u064a\u0639 \u0648\u0627\u0644\u062a\u062c\u0627\u0631\u0629.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u062a\u0633\u062a\u062e\u062f\u0645 \u0627\u0644\u0634\u0631\u0643\u0629 \u0645\u0631\u0643\u0632 \u0627\u0644\u0627\u0628\u062a\u0643\u0627\u0631 \u0627\u0644\u062a\u0635\u0646\u064a\u0639\u064a \u0627\u0644\u062a\u0627\u0628\u0639 \u0644\u0647\u0627 \u0641\u064a \u0631\u0648\u0643\u0641\u064a\u0644 \u0628\u0648\u0644\u0627\u064a\u0629 \u0645\u0627\u0631\u064a\u0644\u0627\u0646\u062f\u060c \u062d\u064a\u062b \u0628\u062f\u0623 \u0627\u0644\u0625\u0646\u062a\u0627\u062c \u0627\u0644\u0645\u062e\u0635\u0635 \u0644\u0644\u0625\u0645\u062f\u0627\u062f \u0627\u0644\u062a\u062c\u0627\u0631\u064a \u0627\u0644\u0645\u0633\u062a\u0642\u0628\u0644\u064a \u0641\u064a \u0627\u0644\u0639\u0627\u0645 \u0627\u0644\u0645\u0627\u0636\u064a.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0642\u062f \u064a\u0633\u0627\u0639\u062f \u0647\u0630\u0627 \u0627\u0644\u0627\u0633\u062a\u0639\u062f\u0627\u062f \u0627\u0644\u062a\u0635\u0646\u064a\u0639\u064a \u0641\u064a \u062f\u0639\u0645 \u0648\u0635\u0648\u0644 \u0627\u0644\u0645\u0631\u0636\u0649 \u0639\u0644\u0649 \u0646\u0637\u0627\u0642 \u0623\u0648\u0633\u0639 \u0625\u0630\u0627 \u062d\u0635\u0644 RGX-202 \u0639\u0644\u0649 \u0627\u0644\u0645\u0648\u0627\u0641\u0642\u0629 \u0627\u0644\u062a\u0646\u0638\u064a\u0645\u064a\u0629.<\/p>\n\n\n\n<h2 class=\"wp-block-heading\">\u0645\u0627\u0630\u0627 \u064a\u0639\u0646\u064a \u0647\u0630\u0627 \u0644\u0639\u0627\u0626\u0644\u0627\u062a \u062f\u0648\u0634\u064a\u0646\u061f<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u064a\u0645\u062b\u0644 \u0625\u0643\u0645\u0627\u0644 \u0627\u0644\u062f\u0631\u0627\u0633\u0629 \u0627\u0644\u062a\u0623\u0643\u064a\u062f\u064a\u0629 \u062e\u0637\u0648\u0629 \u0645\u0647\u0645\u0629 \u0625\u0644\u0649 \u0627\u0644\u0623\u0645\u0627\u0645 \u0628\u0627\u0644\u0646\u0633\u0628\u0629 \u0644\u0640 RGX-202 \u0648\u0645\u062c\u062a\u0645\u0639 \u062f\u0648\u0634\u064a\u0646.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0645\u0639 \u062a\u0642\u062f\u064a\u0645 \u0637\u0644\u0628 FDA \u0627\u0644\u0645\u062e\u0637\u0637 \u0644\u0647 \u0641\u064a \u0627\u0644\u0631\u0628\u0639 \u0627\u0644\u062b\u0627\u0644\u062b \u0645\u0646 \u0639\u0627\u0645 2026 \u0648\u0642\u0631\u0627\u0631 \u0627\u0644\u0645\u0648\u0627\u0641\u0642\u0629 \u0627\u0644\u0645\u062d\u062a\u0645\u0644 \u0627\u0644\u0645\u062a\u0648\u0642\u0639 \u0641\u064a \u0627\u0644\u0646\u0635\u0641 \u0627\u0644\u062b\u0627\u0646\u064a \u0645\u0646 \u0639\u0627\u0645 2027\u060c \u0633\u062a\u0631\u0627\u0642\u0628 \u0639\u0627\u0626\u0644\u0627\u062a \u062f\u0648\u0634\u064a\u0646 \u0639\u0646 \u0643\u062b\u0628 \u0627\u0644\u062a\u0637\u0648\u0631\u0627\u062a \u0627\u0644\u062a\u0646\u0638\u064a\u0645\u064a\u0629 \u0627\u0644\u0642\u0627\u062f\u0645\u0629.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0641\u064a \u062d\u0627\u0644 \u0627\u0644\u0645\u0648\u0627\u0641\u0642\u0629\u060c \u064a\u0645\u0643\u0646 \u0623\u0646 \u064a\u0635\u0628\u062d RGX-202 \u062e\u064a\u0627\u0631\u064b\u0627 \u0625\u0636\u0627\u0641\u064a\u064b\u0627 \u0644\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u062c\u064a\u0646\u064a \u0644\u0644\u0645\u0631\u0636\u0649 \u0627\u0644\u0630\u064a\u0646 \u064a\u0639\u0627\u0646\u0648\u0646 \u0645\u0646 \u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a\u060c \u0645\u0645\u0627 \u064a\u0648\u0633\u0639 \u062e\u064a\u0627\u0631\u0627\u062a \u0627\u0644\u0639\u0644\u0627\u062c \u0648\u064a\u062d\u062a\u0645\u0644 \u0623\u0646 \u064a\u062d\u0633\u0646 \u0627\u0644\u0646\u062a\u0627\u0626\u062c \u0639\u0644\u0649 \u0627\u0644\u0645\u062f\u0649 \u0627\u0644\u0637\u0648\u064a\u0644.<\/p>\n\n\n\n<h2 class=\"wp-block-heading\">\u0627\u0644\u0623\u0633\u0626\u0644\u0629 \u0627\u0644\u0634\u0627\u0626\u0639\u0629 (FAQ)<\/h2>\n\n\n<div id=\"rank-math-faq\" class=\"rank-math-block\">\n<div class=\"rank-math-list\">\n<div id=\"faq-question-1782302007464\" class=\"rank-math-list-item\">\n<h3 class=\"rank-math-question\">\u0645\u0627 \u0647\u0648 RGX-202\u061f<\/h3>\n<div class=\"rank-math-answer\">\n\n<p>RGX-202 \u0647\u0648 \u0639\u0644\u0627\u062c \u062c\u064a\u0646\u064a \u062a\u062c\u0631\u064a\u0628\u064a \u064a\u062a\u0645 \u062a\u0637\u0648\u064a\u0631\u0647 \u0628\u0648\u0627\u0633\u0637\u0629 REGENXBIO \u0644\u0639\u0644\u0627\u062c \u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a (DMD).<\/p>\n\n<\/div>\n<\/div>\n<div id=\"faq-question-1782302015108\" class=\"rank-math-list-item\">\n<h3 class=\"rank-math-question\">\u0645\u062a\u0649 \u0633\u062a\u0642\u0648\u0645 \u0634\u0631\u0643\u0629 REGENXBIO \u0628\u062a\u0642\u062f\u064a\u0645 RGX-202 \u0625\u0644\u0649 FDA\u061f<\/h3>\n<div class=\"rank-math-answer\">\n\n<p>\u062a\u062e\u0637\u0637 \u0627\u0644\u0634\u0631\u0643\u0629 \u0644\u0628\u062f\u0621 \u062a\u0642\u062f\u064a\u0645 \u0637\u0644\u0628 \u062a\u0631\u062e\u064a\u0635 \u0627\u0644\u0645\u0646\u062a\u062c\u0627\u062a \u0627\u0644\u0628\u064a\u0648\u0644\u0648\u062c\u064a\u0629 (BLA) \u0641\u064a \u0627\u0644\u0631\u0628\u0639 \u0627\u0644\u062b\u0627\u0644\u062b \u0645\u0646 \u0639\u0627\u0645 2026.<\/p>\n\n<\/div>\n<\/div>\n<div id=\"faq-question-1782302022653\" class=\"rank-math-list-item\">\n<h3 class=\"rank-math-question\">\u0645\u0627 \u0647\u064a \u0627\u0644\u0646\u062a\u0627\u0626\u062c \u0627\u0644\u0631\u0626\u064a\u0633\u064a\u0629 \u0644\u0644\u062f\u0631\u0627\u0633\u0629\u061f<\/h3>\n<div class=\"rank-math-answer\">\n\n<p>\u062d\u0642\u0642 \u0623\u0643\u062b\u0631 \u0645\u0646 93 \u0628\u0627\u0644\u0645\u0627\u0626\u0629 \u0645\u0646 \u0627\u0644\u0645\u0631\u0636\u0649 \u062a\u0639\u0628\u064a\u0631\u064b\u0627 \u0639\u0646 \u0627\u0644\u0645\u064a\u0643\u0631\u0648\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0628\u0646\u0633\u0628\u0629 10 \u0628\u0627\u0644\u0645\u0627\u0626\u0629 \u0639\u0644\u0649 \u0627\u0644\u0623\u0642\u0644 \u0641\u064a \u0627\u0644\u0623\u0633\u0628\u0648\u0639 12\u060c \u0648\u0623\u0638\u0647\u0631\u062a \u0627\u0644\u0628\u064a\u0627\u0646\u0627\u062a \u0627\u0644\u0648\u0638\u064a\u0641\u064a\u0629 \u0627\u0644\u0645\u0628\u0643\u0631\u0629 \u062a\u062d\u0633\u064a\u0646\u0627\u062a \u0630\u0627\u062a \u0645\u063a\u0632\u0649 \u0628\u0639\u062f \u0639\u0627\u0645 \u0648\u0627\u062d\u062f.<\/p>\n\n<\/div>\n<\/div>\n<div id=\"faq-question-1782302027017\" class=\"rank-math-list-item\">\n<h3 class=\"rank-math-question\">\u0645\u062a\u0649 \u064a\u0645\u0643\u0646 \u0627\u0644\u0645\u0648\u0627\u0641\u0642\u0629 \u0639\u0644\u0649 RGX-202\u061f<\/h3>\n<div class=\"rank-math-answer\">\n\n<p>\u0625\u0630\u0627 \u0633\u0627\u0631\u062a \u0639\u0645\u0644\u064a\u0629 \u0645\u0631\u0627\u062c\u0639\u0629 FDA \u0643\u0645\u0627 \u0647\u0648 \u0645\u062a\u0648\u0642\u0639\u060c \u062a\u0639\u062a\u0642\u062f \u0634\u0631\u0643\u0629 REGENXBIO \u0623\u0646 RGX-202 \u0642\u062f \u064a\u062d\u0635\u0644 \u0639\u0644\u0649 \u0627\u0644\u0645\u0648\u0627\u0641\u0642\u0629 \u0641\u064a \u0627\u0644\u0646\u0635\u0641 \u0627\u0644\u062b\u0627\u0646\u064a \u0645\u0646 \u0639\u0627\u0645 2027.<\/p>\n\n<\/div>\n<\/div>\n<div id=\"faq-question-1782302033436\" class=\"rank-math-list-item\">\n<h3 class=\"rank-math-question\">\u0643\u0645 \u0639\u062f\u062f \u0627\u0644\u0645\u0631\u0636\u0649 \u0627\u0644\u0645\u0634\u0645\u0648\u0644\u064a\u0646 \u0641\u064a \u062d\u0632\u0645\u0629 \u062a\u0631\u062e\u064a\u0635 \u0627\u0644\u0645\u0646\u062a\u062c \u0627\u0644\u0628\u064a\u0648\u0644\u0648\u062c\u064a\u061f<\/h3>\n<div class=\"rank-math-answer\">\n\n<p>\u0645\u0646 \u0627\u0644\u0645\u062a\u0648\u0642\u0639 \u0623\u0646 \u064a\u062a\u0636\u0645\u0646 \u0627\u0644\u0637\u0644\u0628 \u0627\u0644\u0645\u062e\u0637\u0637 \u0644\u0647 \u0628\u064a\u0627\u0646\u0627\u062a \u0627\u0644\u0633\u0644\u0627\u0645\u0629 \u0645\u0646 63 \u0645\u0634\u0627\u0631\u0643\u064b\u0627 \u0648\u0628\u064a\u0627\u0646\u0627\u062a \u0627\u0644\u0641\u0639\u0627\u0644\u064a\u0629 \u0645\u0646 30 \u0645\u0634\u0627\u0631\u0643\u064b\u0627 \u0641\u064a \u0627\u0644\u062f\u0631\u0627\u0633\u0629 \u0627\u0644\u0645\u062d\u0648\u0631\u064a\u0629.<\/p>\n\n<\/div>\n<\/div>\n<\/div>\n<\/div>\n\n\n<p class=\"wp-block-paragraph\"><\/p>","protected":false},"excerpt":{"rendered":"<p>REGENXBIO has announced the completion of patient dosing in the confirmatory study of RGX-202, its investigational gene therapy for Duchenne Muscular Dystrophy (DMD). This important milestone marks the completion of the company&#8217;s registrational development program and supports a planned Biologics License Application (BLA) submission to the U.S. Food and Drug Administration (FDA) in the third [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":8158,"comment_status":"open","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[281],"tags":[525,88,652,61,107,108],"class_list":["post-8153","post","type-post","status-publish","format-standard","has-post-thumbnail","category-press-releases","tag-affinity-duchenne","tag-fda","tag-fda-drug-approval","tag-gene-therapy","tag-regenxbio","tag-rgx-202"],"_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/posts\/8153","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/comments?post=8153"}],"version-history":[{"count":3,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/posts\/8153\/revisions"}],"predecessor-version":[{"id":8157,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/posts\/8153\/revisions\/8157"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/media\/8158"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/media?parent=8153"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/categories?post=8153"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/tags?post=8153"}],"curies":[{"name":"\u0648\u0648\u0631\u062f\u0628\u0631\u064a\u0633","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}