{"id":8110,"date":"2026-06-10T11:14:26","date_gmt":"2026-06-10T08:14:26","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=8110"},"modified":"2026-06-10T11:14:28","modified_gmt":"2026-06-10T08:14:28","slug":"gen1e-lifesciences-gen-1123-medicine-for-duchenne-muscular-dystrophy-dmd","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/ar\/gen1e-lifesciences-gen-1123-medicine-for-duchenne-muscular-dystrophy-dmd\/","title":{"rendered":"GEn1E Lifesciences \u0648 GEn-1123: \u0646\u0647\u062c \u062c\u062f\u064a\u062f \u0644\u0644\u0637\u0628 \u0627\u0644\u062f\u0642\u064a\u0642 \u0644\u0639\u0644\u0627\u062c \u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a (DMD)"},"content":{"rendered":"<p class=\"wp-block-paragraph\">\u0645\u0646\u062d\u062a \u0625\u062f\u0627\u0631\u0629 \u0627\u0644\u063a\u0630\u0627\u0621 \u0648\u0627\u0644\u062f\u0648\u0627\u0621 \u0627\u0644\u0623\u0645\u0631\u064a\u0643\u064a\u0629 (FDA) \u0643\u0644\u0627\u064b \u0645\u0646 \u062a\u0635\u0646\u064a\u0641 \u062f\u0648\u0627\u0621 \u0627\u0644\u064a\u062a\u064a\u0645 (ODD) \u0648\u062a\u0635\u0646\u064a\u0641 \u0645\u0631\u0636 \u0627\u0644\u0623\u0637\u0641\u0627\u0644 \u0627\u0644\u0646\u0627\u062f\u0631 (RPDD) \u0625\u0644\u0649 GEn-1123\u060c \u0648\u0647\u0648 \u0639\u0644\u0627\u062c \u062a\u062c\u0631\u064a\u0628\u064a \u0644\u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a (DMD) \u064a\u062a\u0645 \u062a\u0637\u0648\u064a\u0631\u0647 \u0628\u0648\u0627\u0633\u0637\u0629 GEn1E Lifesciences\u060c \u0648\u0647\u064a \u0634\u0631\u0643\u0629 \u0644\u0644\u062a\u0643\u0646\u0648\u0644\u0648\u062c\u064a\u0627 \u0627\u0644\u062d\u064a\u0648\u064a\u0629 \u0641\u064a \u0627\u0644\u0645\u0631\u062d\u0644\u0629 \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629 \u0627\u0644\u062b\u0627\u0646\u064a\u0629 \u0645\u062a\u062e\u0635\u0635\u0629 \u0641\u064a \u0627\u0644\u0637\u0628 \u0627\u0644\u062f\u0642\u064a\u0642 \u0627\u0644\u0645\u062f\u0639\u0648\u0645 \u0628\u0627\u0644\u0630\u0643\u0627\u0621 \u0627\u0644\u0627\u0635\u0637\u0646\u0627\u0639\u064a.<\/p>\n\n\n\n<div class=\"wp-block-rank-math-toc-block\" id=\"rank-math-toc\"><h2>\u062c\u062f\u0648\u0644 \u0627\u0644\u0645\u062d\u062a\u0648\u064a\u0627\u062a<\/h2><nav><ul><li><a href=\"#what-is-g-en-1-e-lifesciences\">\u0645\u0627 \u0647\u0648 GEn1E Lifesciences\u061f<\/a><\/li><li><a href=\"#understanding-duchenne-muscular-dystrophy-dmd\">\u0641\u0647\u0645 \u0645\u0631\u0636 \u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a (DMD)<\/a><ul><\/ul><\/li><li><a href=\"#what-is-g-en-1123\">\u0645\u0627 \u0647\u0648 GEn-1123\u061f<\/a><ul><li><a href=\"#a-novel-oral-precision-therapy\">\u0639\u0644\u0627\u062c \u0641\u0645\u0648\u064a \u062f\u0642\u064a\u0642 \u062c\u062f\u064a\u062f<\/a><\/li><\/ul><\/li><li><a href=\"#how-does-g-en-1123-work\">\u0643\u064a\u0641 \u064a\u0639\u0645\u0644 \u062c\u0647\u0627\u0632 GEn-1123\u061f<\/a><ul><li><a href=\"#targeting-inflammation-and-muscle-degeneration\">\u0627\u0633\u062a\u0647\u062f\u0627\u0641 \u0627\u0644\u0627\u0644\u062a\u0647\u0627\u0628 \u0648\u062a\u062f\u0647\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a<\/a><ul><li><a href=\"#reduce-harmful-inflammation\">\u0627\u0644\u062d\u062f \u0645\u0646 \u0627\u0644\u0627\u0644\u062a\u0647\u0627\u0628\u0627\u062a \u0627\u0644\u0636\u0627\u0631\u0629<\/a><\/li><li><a href=\"#promote-muscle-survival\">\u062a\u0639\u0632\u064a\u0632 \u0628\u0642\u0627\u0621 \u0627\u0644\u0639\u0636\u0644\u0627\u062a<\/a><\/li><li><a href=\"#support-regenerative-processes\">\u062f\u0639\u0645 \u0627\u0644\u0639\u0645\u0644\u064a\u0627\u062a \u0627\u0644\u062a\u062c\u062f\u064a\u062f\u064a\u0629<\/a><\/li><li><a href=\"#potentially-reduce-fibrosis\">\u0642\u062f \u064a\u0642\u0644\u0644 \u0645\u0646 \u0627\u0644\u062a\u0644\u064a\u0641<\/a><\/li><\/ul><\/li><\/ul><\/li><li><a href=\"#why-is-g-en-1123-different\">\u0644\u0645\u0627\u0630\u0627 \u064a\u062e\u062a\u0644\u0641 GEn-1123\u061f<\/a><ul><li><a href=\"#mutation-independent-potential\">\u0627\u0644\u0642\u062f\u0631\u0629 \u063a\u064a\u0631 \u0627\u0644\u0645\u0639\u062a\u0645\u062f\u0629 \u0639\u0644\u0649 \u0627\u0644\u0637\u0641\u0631\u0629<\/a><\/li><li><a href=\"#oral-administration\">\u0627\u0644\u0625\u062f\u0627\u0631\u0629 \u0639\u0646 \u0637\u0631\u064a\u0642 \u0627\u0644\u0641\u0645<\/a><\/li><\/ul><\/li><li><a href=\"#fda-recognition-why-it-matters\">\u0627\u0644\u062a\u0639\u0631\u0641 \u0639\u0644\u0649 FDA: \u0644\u0645\u0627\u0630\u0627 \u0647\u0648 \u0645\u0647\u0645<\/a><ul><li><a href=\"#orphan-drug-designation-odd\">\u062a\u0635\u0646\u064a\u0641 \u0627\u0644\u0623\u062f\u0648\u064a\u0629 \u0627\u0644\u064a\u062a\u064a\u0645\u0629 (ODD)<\/a><\/li><li><a href=\"#rare-pediatric-disease-designation-rpdd\">\u062a\u0635\u0646\u064a\u0641 \u0627\u0644\u0623\u0645\u0631\u0627\u0636 \u0627\u0644\u0646\u0627\u062f\u0631\u0629 \u0644\u062f\u0649 \u0627\u0644\u0623\u0637\u0641\u0627\u0644 (RPDD)<\/a><\/li><\/ul><\/li><li><a href=\"#current-development-status\">\u0627\u0644\u0648\u0636\u0639 \u0627\u0644\u062d\u0627\u0644\u064a \u0644\u0644\u062a\u0637\u0648\u064a\u0631<\/a><ul><li><a href=\"#is-g-en-1123-approved\">\u0647\u0644 \u0627\u0644\u0645\u0646\u062a\u062c GEn-1123 \u0645\u0639\u062a\u0645\u062f\u061f<\/a><\/li><\/ul><\/li><li><a href=\"#what-could-g-en-1123-mean-for-the-dmd-community\">\u0645\u0627\u0630\u0627 \u0642\u062f \u064a\u0639\u0646\u064a GEn-1123 \u0644\u0645\u062c\u062a\u0645\u0639 \u0645\u0631\u0636\u0649 \u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0627\u0644\u062f\u0648\u0634\u064a\u0646\u064a\u061f<\/a><\/li><li><a href=\"#key-takeaways\">\u0627\u0644\u0646\u0642\u0627\u0637 \u0627\u0644\u0631\u0626\u064a\u0633\u064a\u0629<\/a><\/li><\/ul><\/nav><\/div>\n\n\n\n<h2 id=\"what-is-g-en-1-e-lifesciences\" class=\"wp-block-heading\">\u0645\u0627 \u0647\u0648 GEn1E Lifesciences\u061f<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u0634\u0631\u0643\u0629 GEn1E Lifesciences \u0647\u064a \u0634\u0631\u0643\u0629 \u0644\u0644\u062a\u0643\u0646\u0648\u0644\u0648\u062c\u064a\u0627 \u0627\u0644\u062d\u064a\u0648\u064a\u0629 \u0645\u0642\u0631\u0647\u0627 \u0628\u0627\u0644\u0648 \u0623\u0644\u062a\u0648\u060c \u0643\u0627\u0644\u064a\u0641\u0648\u0631\u0646\u064a\u0627\u060c \u062a\u0631\u0643\u0632 \u0639\u0644\u0649 \u062a\u0637\u0648\u064a\u0631 \u0639\u0644\u0627\u062c\u0627\u062a \u062f\u0642\u064a\u0642\u0629 \u0644\u0644\u0623\u0645\u0631\u0627\u0636 \u0627\u0644\u0627\u0644\u062a\u0647\u0627\u0628\u064a\u0629 \u0648\u0627\u0644\u0645\u0646\u0627\u0639\u064a\u0629 \u0648\u0627\u0644\u0646\u0627\u062f\u0631\u0629. \u062a\u062c\u0645\u0639 \u0627\u0644\u0634\u0631\u0643\u0629 \u0628\u064a\u0646 \u0627\u0644\u0630\u0643\u0627\u0621 \u0627\u0644\u0627\u0635\u0637\u0646\u0627\u0639\u064a \u0648\u062a\u062d\u0644\u064a\u0644 \u0627\u0644\u0645\u0624\u0634\u0631\u0627\u062a \u0627\u0644\u062d\u064a\u0648\u064a\u0629 \u0648\u0628\u064a\u0627\u0646\u0627\u062a \u0639\u0644\u0645 \u0627\u0644\u062c\u064a\u0646\u0648\u0645 \u0627\u0644\u0645\u062a\u0639\u062f\u062f \u0648\u062a\u0648\u0635\u064a\u0641 \u0627\u0644\u0623\u0645\u0631\u0627\u0636 \u0627\u0644\u062e\u0627\u0635 \u0628\u0643\u0644 \u0645\u0631\u064a\u0636 \u0644\u062a\u062d\u062f\u064a\u062f \u0641\u0631\u0635 \u0639\u0644\u0627\u062c\u064a\u0629 \u062c\u062f\u064a\u062f\u0629.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u062a\u0645 \u062a\u0635\u0645\u064a\u0645 \u0645\u0646\u0635\u0629 GRID \u0627\u0644\u062e\u0627\u0635\u0629 \u0628\u0647\u0627 \u0644\u062a\u062d\u0644\u064a\u0644 \u0627\u0644\u0628\u064a\u0627\u0646\u0627\u062a \u0627\u0644\u0628\u064a\u0648\u0644\u0648\u062c\u064a\u0629 \u0627\u0644\u0645\u0639\u0642\u062f\u0629 \u0648\u0645\u0633\u0627\u0639\u062f\u0629 \u0627\u0644\u0628\u0627\u062d\u062b\u064a\u0646 \u0639\u0644\u0649 \u062a\u0637\u0648\u064a\u0631 \u0639\u0644\u0627\u062c\u0627\u062a \u0645\u0648\u062c\u0647\u0629 \u062a\u0639\u0627\u0644\u062c \u0627\u0644\u0622\u0644\u064a\u0627\u062a \u0627\u0644\u0643\u0627\u0645\u0646\u0629 \u0648\u0631\u0627\u0621 \u0627\u0644\u0645\u0631\u0636 \u0628\u062f\u0644\u0627\u064b \u0645\u0646 \u0645\u062c\u0631\u062f \u0625\u062f\u0627\u0631\u0629 \u0627\u0644\u0623\u0639\u0631\u0627\u0636.<\/p>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 id=\"understanding-duchenne-muscular-dystrophy-dmd\" class=\"wp-block-heading\">\u0641\u0647\u0645 \u0645\u0631\u0636 \u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a (DMD)<\/h2>\n\n\n\n<h3 id=\"what-is-dmd\" class=\"wp-block-heading\">\u0645\u0627 \u0647\u0648 \u0645\u0631\u0636 \u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0627\u0644\u062f\u0648\u0634\u064a\u0646\u064a\u061f<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a (DMD) \u0647\u0648 \u0627\u0636\u0637\u0631\u0627\u0628 \u0648\u0631\u0627\u062b\u064a \u0646\u0627\u062f\u0631 \u0646\u0627\u062a\u062c \u0639\u0646 \u0637\u0641\u0631\u0627\u062a \u0641\u064a \u062c\u064a\u0646 \u0627\u0644\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646. \u0648\u0628\u062f\u0648\u0646 \u0628\u0631\u0648\u062a\u064a\u0646 \u0627\u0644\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0627\u0644\u0648\u0638\u064a\u0641\u064a\u060c \u062a\u062a\u0636\u0631\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0648\u062a\u0636\u0639\u0641 \u062a\u062f\u0631\u064a\u062c\u064a\u064b\u0627 \u0645\u0639 \u0645\u0631\u0648\u0631 \u0627\u0644\u0648\u0642\u062a. \u0627\u0642\u0631\u0623 \u0627\u0644\u0645\u0632\u064a\u062f:\u00a0<a href=\"https:\/\/dmdwarrior.com\/ar\/what-is-duchenne\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u0645\u0627 \u0647\u0648 \u062f\u0648\u0634\u064a\u0646\u061f<\/a><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u064a\u0624\u062b\u0631 \u0645\u0631\u0636 \u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0627\u0644\u062f\u0648\u0634\u064a\u0646\u064a \u0639\u0644\u0649 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0627\u0644\u0647\u064a\u0643\u0644\u064a\u0629 \u0648\u0627\u0644\u0642\u0644\u0628 \u0648\u0639\u0636\u0644\u0627\u062a \u0627\u0644\u062c\u0647\u0627\u0632 \u0627\u0644\u062a\u0646\u0641\u0633\u064a\u060c \u0645\u0645\u0627 \u064a\u0624\u062f\u064a \u0625\u0644\u0649 \u0632\u064a\u0627\u062f\u0629 \u0627\u0644\u0625\u0639\u0627\u0642\u0629 \u0648\u0645\u0636\u0627\u0639\u0641\u0627\u062a \u0635\u062d\u064a\u0629 \u062e\u0637\u064a\u0631\u0629.<\/p>\n\n\n\n<h3 id=\"why-does-dmd-progress\" class=\"wp-block-heading\">\u0644\u0645\u0627\u0630\u0627 \u064a\u062a\u0637\u0648\u0631 \u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0627\u0644\u062f\u0648\u0634\u064a\u0646\u064a\u061f<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u0644\u0627 \u064a\u0642\u062a\u0635\u0631 \u062a\u0637\u0648\u0631 \u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0627\u0644\u062f\u0648\u0634\u064a\u0646\u064a \u0639\u0644\u0649 \u0646\u0642\u0635 \u0627\u0644\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0641\u0642\u0637\u060c \u0628\u0644 \u062a\u0633\u0627\u0647\u0645 \u0639\u062f\u0629 \u0639\u0645\u0644\u064a\u0627\u062a \u0628\u064a\u0648\u0644\u0648\u062c\u064a\u0629 \u0641\u064a \u0627\u0633\u062a\u0645\u0631\u0627\u0631 \u062a\u0644\u0641 \u0627\u0644\u0639\u0636\u0644\u0627\u062a\u060c \u0628\u0645\u0627 \u0641\u064a \u0630\u0644\u0643:<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u0627\u0644\u0627\u0644\u062a\u0647\u0627\u0628 \u0627\u0644\u0645\u0632\u0645\u0646<\/li>\n\n\n\n<li>\u062a\u0633\u0644\u0644 \u0627\u0644\u062e\u0644\u0627\u064a\u0627 \u0627\u0644\u0645\u0646\u0627\u0639\u064a\u0629<\/li>\n\n\n\n<li>\u0645\u0648\u062a \u0623\u0644\u064a\u0627\u0641 \u0627\u0644\u0639\u0636\u0644\u0627\u062a<\/li>\n\n\n\n<li>\u0636\u0639\u0641 \u062a\u062c\u062f\u062f \u0627\u0644\u0639\u0636\u0644\u0627\u062a<\/li>\n\n\n\n<li>\u0627\u0644\u062a\u0644\u064a\u0641 (\u062a\u0643\u0648\u0651\u0646 \u0627\u0644\u0646\u0633\u064a\u062c \u0627\u0644\u0646\u062f\u0628\u064a)<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\">\u062a\u0639\u0645\u0644 \u0647\u0630\u0647 \u0627\u0644\u0622\u0644\u064a\u0627\u062a \u0645\u062c\u062a\u0645\u0639\u0629 \u0639\u0644\u0649 \u062a\u0633\u0631\u064a\u0639 \u062a\u062f\u0647\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0648\u0627\u0644\u062a\u0631\u0627\u062c\u0639 \u0627\u0644\u0648\u0638\u064a\u0641\u064a.<\/p>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<figure class=\"wp-block-image size-large\"><img loading=\"lazy\" decoding=\"async\" width=\"1024\" height=\"576\" src=\"https:\/\/dmdwarrior.com\/wp-content\/uploads\/2026\/06\/gen-1123-duchenne-muscular-dystrophy-1-1024x576.jpg\" alt=\"\u0627\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u0641\u0645\u0648\u064a \u0627\u0644\u062a\u062c\u0631\u064a\u0628\u064a GEn-1123 \u0644\u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a\u060c \u0648\u0627\u0644\u0630\u064a \u0637\u0648\u0631\u0647 GEn1E Lifesciences\" class=\"wp-image-8114\" title=\"\" srcset=\"https:\/\/dmdwarrior.com\/wp-content\/uploads\/2026\/06\/gen-1123-duchenne-muscular-dystrophy-1-1024x576.jpg 1024w, https:\/\/dmdwarrior.com\/wp-content\/uploads\/2026\/06\/gen-1123-duchenne-muscular-dystrophy-1-300x169.jpg 300w, https:\/\/dmdwarrior.com\/wp-content\/uploads\/2026\/06\/gen-1123-duchenne-muscular-dystrophy-1-768x432.jpg 768w, https:\/\/dmdwarrior.com\/wp-content\/uploads\/2026\/06\/gen-1123-duchenne-muscular-dystrophy-1-1536x864.jpg 1536w, https:\/\/dmdwarrior.com\/wp-content\/uploads\/2026\/06\/gen-1123-duchenne-muscular-dystrophy-1-18x10.jpg 18w, https:\/\/dmdwarrior.com\/wp-content\/uploads\/2026\/06\/gen-1123-duchenne-muscular-dystrophy-1-747x420.jpg 747w, https:\/\/dmdwarrior.com\/wp-content\/uploads\/2026\/06\/gen-1123-duchenne-muscular-dystrophy-1-150x84.jpg 150w, https:\/\/dmdwarrior.com\/wp-content\/uploads\/2026\/06\/gen-1123-duchenne-muscular-dystrophy-1-696x392.jpg 696w, https:\/\/dmdwarrior.com\/wp-content\/uploads\/2026\/06\/gen-1123-duchenne-muscular-dystrophy-1-1068x601.jpg 1068w, https:\/\/dmdwarrior.com\/wp-content\/uploads\/2026\/06\/gen-1123-duchenne-muscular-dystrophy-1.jpg 1920w\" sizes=\"auto, (max-width: 1024px) 100vw, 1024px\" \/><figcaption class=\"wp-element-caption\">GEn-1123 \u0647\u0648 \u0639\u0644\u0627\u062c \u0641\u0645\u0648\u064a \u062a\u062c\u0631\u064a\u0628\u064a \u064a\u062a\u0645 \u062a\u0637\u0648\u064a\u0631\u0647 \u0628\u0648\u0627\u0633\u0637\u0629 GEn1E Lifesciences \u0644\u0639\u0644\u0627\u062c \u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a.<\/figcaption><\/figure>\n\n\n\n<h2 id=\"what-is-g-en-1123\" class=\"wp-block-heading\">\u0645\u0627 \u0647\u0648 GEn-1123\u061f<\/h2>\n\n\n\n<h3 id=\"a-novel-oral-precision-therapy\" class=\"wp-block-heading\">\u0639\u0644\u0627\u062c \u0641\u0645\u0648\u064a \u062f\u0642\u064a\u0642 \u062c\u062f\u064a\u062f<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">GEn-1123 \u0647\u0648 \u0639\u0644\u0627\u062c \u062a\u062c\u0631\u064a\u0628\u064a \u0639\u0646 \u0637\u0631\u064a\u0642 \u0627\u0644\u0641\u0645 \u0628\u062c\u0632\u064a\u0626\u0627\u062a \u0635\u063a\u064a\u0631\u0629 \u064a\u062a\u0645 \u062a\u0637\u0648\u064a\u0631\u0647 \u0628\u0648\u0627\u0633\u0637\u0629 GEn1E Lifesciences \u0644\u0639\u0644\u0627\u062c \u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0628\u062e\u0644\u0627\u0641 \u0627\u0644\u0639\u0644\u0627\u062c\u0627\u062a \u0627\u0644\u062a\u064a \u062a\u0631\u0643\u0632 \u0628\u0634\u0643\u0644 \u0645\u0628\u0627\u0634\u0631 \u0639\u0644\u0649 \u0627\u0633\u062a\u0639\u0627\u062f\u0629 \u0625\u0646\u062a\u0627\u062c \u0627\u0644\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646\u060c \u064a\u0647\u062f\u0641 GEn-1123 \u0625\u0644\u0649 \u0645\u0639\u0627\u0644\u062c\u0629 \u0627\u0644\u0639\u0645\u0644\u064a\u0627\u062a \u0627\u0644\u0628\u064a\u0648\u0644\u0648\u062c\u064a\u0629 \u0627\u0644\u0631\u0626\u064a\u0633\u064a\u0629 \u0627\u0644\u062a\u064a \u062a\u062f\u0641\u0639 \u062a\u0637\u0648\u0631 \u0627\u0644\u0645\u0631\u0636.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0627\u0644\u0639\u0644\u0627\u062c \u0642\u064a\u062f \u0627\u0644\u062a\u0637\u0648\u064a\u0631 \u062d\u0627\u0644\u064a\u064b\u0627 \u0648\u0642\u062f \u062d\u0635\u0644 \u0639\u0644\u0649 \u0643\u0644 \u0645\u0646 \u062a\u0635\u0646\u064a\u0641 \u062f\u0648\u0627\u0621 \u0627\u0644\u064a\u062a\u064a\u0645 FDA \u0648\u062a\u0635\u0646\u064a\u0641 \u0645\u0631\u0636 \u0627\u0644\u0623\u0637\u0641\u0627\u0644 \u0627\u0644\u0646\u0627\u062f\u0631.<\/p>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 id=\"how-does-g-en-1123-work\" class=\"wp-block-heading\">\u0643\u064a\u0641 \u064a\u0639\u0645\u0644 \u062c\u0647\u0627\u0632 GEn-1123\u061f<\/h2>\n\n\n\n<h3 id=\"targeting-inflammation-and-muscle-degeneration\" class=\"wp-block-heading\">\u0627\u0633\u062a\u0647\u062f\u0627\u0641 \u0627\u0644\u0627\u0644\u062a\u0647\u0627\u0628 \u0648\u062a\u062f\u0647\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u064a\u0648\u0635\u0641 GEn-1123 \u0628\u0623\u0646\u0647 &quot;\u0645\u0639\u062f\u0644 \u0625\u0634\u0627\u0631\u0629 \u0645\u0632\u062f\u0648\u062c&quot;.\u201c<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u064a\u0647\u062f\u0641 \u0647\u0630\u0627 \u0627\u0644\u0639\u0644\u0627\u062c \u0625\u0644\u0649 \u0627\u0644\u0645\u0633\u0627\u0639\u062f\u0629 \u0641\u064a \u0625\u0639\u0627\u062f\u0629 \u062a\u0648\u0627\u0632\u0646 \u0645\u0633\u0627\u0631\u0627\u062a \u0627\u0644\u0625\u0634\u0627\u0631\u0627\u062a \u0627\u0644\u0627\u0644\u062a\u0647\u0627\u0628\u064a\u0629 \u063a\u064a\u0631 \u0627\u0644\u0637\u0628\u064a\u0639\u064a\u0629 \u0627\u0644\u062a\u064a \u062a\u0633\u0627\u0647\u0645 \u0641\u064a \u062a\u0644\u0641 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0641\u064a \u0645\u0631\u0636 \u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0627\u0644\u062f\u0648\u0634\u064a\u0646\u064a.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0635\u064f\u0645\u0645 \u0627\u0644\u0639\u0644\u0627\u062c \u0645\u0646 \u0623\u062c\u0644:<\/p>\n\n\n\n<h4 id=\"reduce-harmful-inflammation\" class=\"wp-block-heading\">\u0627\u0644\u062d\u062f \u0645\u0646 \u0627\u0644\u0627\u0644\u062a\u0647\u0627\u0628\u0627\u062a \u0627\u0644\u0636\u0627\u0631\u0629<\/h4>\n\n\n\n<p class=\"wp-block-paragraph\">\u062a\u062a\u0645\u064a\u0632 \u0639\u0636\u0644\u0627\u062a \u0645\u0631\u0636\u0649 \u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0627\u0644\u062f\u0648\u0634\u064a\u0646\u064a \u0628\u0646\u0634\u0627\u0637 \u0627\u0644\u062a\u0647\u0627\u0628\u064a \u0645\u0641\u0631\u0637. \u0648\u064a\u0633\u0627\u0647\u0645 \u0627\u0644\u0627\u0644\u062a\u0647\u0627\u0628 \u0627\u0644\u0645\u0633\u062a\u0645\u0631 \u0641\u064a \u062a\u062d\u0644\u0644 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0648\u062a\u0644\u0641 \u0627\u0644\u0623\u0646\u0633\u062c\u0629.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u064a\u0647\u062f\u0641 GEn-1123 \u0625\u0644\u0649 \u062a\u0639\u062f\u064a\u0644 \u0627\u0644\u0645\u0633\u0627\u0631\u0627\u062a \u0627\u0644\u0645\u0624\u064a\u062f\u0629 \u0644\u0644\u0627\u0644\u062a\u0647\u0627\u0628\u0627\u062a \u0627\u0644\u062a\u064a \u0642\u062f \u062a\u0624\u062f\u064a \u0625\u0644\u0649 \u062a\u0641\u0627\u0642\u0645 \u062a\u0637\u0648\u0631 \u0627\u0644\u0645\u0631\u0636.<\/p>\n\n\n\n<h4 id=\"promote-muscle-survival\" class=\"wp-block-heading\">\u062a\u0639\u0632\u064a\u0632 \u0628\u0642\u0627\u0621 \u0627\u0644\u0639\u0636\u0644\u0627\u062a<\/h4>\n\n\n\n<p class=\"wp-block-paragraph\">\u0643\u0645\u0627 \u062a\u0645 \u062a\u0635\u0645\u064a\u0645 \u0627\u0644\u0639\u0644\u0627\u062c \u0644\u062f\u0639\u0645 \u0627\u0644\u0645\u0633\u0627\u0631\u0627\u062a \u0627\u0644\u0628\u064a\u0648\u0644\u0648\u062c\u064a\u0629 \u0627\u0644\u0645\u0624\u064a\u062f\u0629 \u0644\u0644\u0628\u0642\u0627\u0621 \u0648\u0627\u0644\u062a\u064a \u0642\u062f \u062a\u0633\u0627\u0639\u062f \u0641\u064a \u062d\u0645\u0627\u064a\u0629 \u062e\u0644\u0627\u064a\u0627 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0645\u0646 \u0627\u0644\u062a\u0644\u0641 \u0627\u0644\u0645\u0633\u062a\u0645\u0631.<\/p>\n\n\n\n<h4 id=\"support-regenerative-processes\" class=\"wp-block-heading\">\u062f\u0639\u0645 \u0627\u0644\u0639\u0645\u0644\u064a\u0627\u062a \u0627\u0644\u062a\u062c\u062f\u064a\u062f\u064a\u0629<\/h4>\n\n\n\n<p class=\"wp-block-paragraph\">\u062a\u062a\u0645\u062a\u0639 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0627\u0644\u0645\u0635\u0627\u0628\u0629 \u0628\u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0627\u0644\u062f\u0648\u0634\u064a\u0646\u064a \u0628\u0642\u062f\u0631\u0629 \u0645\u062d\u062f\u0648\u062f\u0629 \u0639\u0644\u0649 \u0625\u0635\u0644\u0627\u062d \u0646\u0641\u0633\u0647\u0627 \u0628\u0645\u0631\u0648\u0631 \u0627\u0644\u0648\u0642\u062a.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u064a\u0633\u0639\u0649 \u0627\u0644\u0645\u0631\u0643\u0628 GEn-1123 \u0625\u0644\u0649 \u062a\u0639\u0632\u064a\u0632 \u0622\u0644\u064a\u0627\u062a \u0627\u0644\u062a\u062c\u062f\u064a\u062f \u0627\u0644\u062a\u064a \u0642\u062f \u062a\u062d\u0633\u0646 \u0627\u0633\u062a\u062c\u0627\u0628\u0629 \u0627\u0644\u062c\u0633\u0645 \u0627\u0644\u0637\u0628\u064a\u0639\u064a\u0629 \u0644\u0644\u0625\u0635\u0644\u0627\u062d.<\/p>\n\n\n\n<h4 id=\"potentially-reduce-fibrosis\" class=\"wp-block-heading\">\u0642\u062f \u064a\u0642\u0644\u0644 \u0645\u0646 \u0627\u0644\u062a\u0644\u064a\u0641<\/h4>\n\n\n\n<p class=\"wp-block-paragraph\">\u064a\u0624\u062f\u064a \u0627\u0644\u062a\u0644\u064a\u0641 \u0625\u0644\u0649 \u0627\u0633\u062a\u0628\u062f\u0627\u0644 \u0623\u0646\u0633\u062c\u0629 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0627\u0644\u0633\u0644\u064a\u0645\u0629 \u0628\u0623\u0646\u0633\u062c\u0629 \u0646\u062f\u0628\u064a\u0629\u060c \u0645\u0645\u0627 \u064a\u0642\u0644\u0644 \u0645\u0646 \u0648\u0638\u064a\u0641\u0629 \u0627\u0644\u0639\u0636\u0644\u0627\u062a.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0645\u0646 \u062e\u0644\u0627\u0644 \u0627\u0633\u062a\u0647\u062f\u0627\u0641 \u0627\u0644\u0645\u0633\u0627\u0631\u0627\u062a \u0627\u0644\u0645\u0634\u0627\u0631\u0643\u0629 \u0641\u064a \u0627\u0644\u062a\u0646\u0643\u0633 \u0648\u0627\u0644\u0627\u0644\u062a\u0647\u0627\u0628\u060c \u0642\u062f \u064a\u0633\u0627\u0639\u062f GEn-1123 \u0641\u064a \u0627\u0644\u062d\u062f \u0645\u0646 \u062a\u0637\u0648\u0631 \u0627\u0644\u062a\u0644\u064a\u0641.<\/p>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 id=\"why-is-g-en-1123-different\" class=\"wp-block-heading\">\u0644\u0645\u0627\u0630\u0627 \u064a\u062e\u062a\u0644\u0641 GEn-1123\u061f<\/h2>\n\n\n\n<h3 id=\"mutation-independent-potential\" class=\"wp-block-heading\">\u0627\u0644\u0642\u062f\u0631\u0629 \u063a\u064a\u0631 \u0627\u0644\u0645\u0639\u062a\u0645\u062f\u0629 \u0639\u0644\u0649 \u0627\u0644\u0637\u0641\u0631\u0629<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u062a\u0633\u062a\u0647\u062f\u0641 \u0627\u0644\u0639\u062f\u064a\u062f \u0645\u0646 \u0627\u0644\u0639\u0644\u0627\u062c\u0627\u062a \u0627\u0644\u062d\u0627\u0644\u064a\u0629 \u0644\u0645\u0631\u0636 \u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0627\u0644\u062f\u0648\u0634\u064a\u0646\u064a \u0637\u0641\u0631\u0627\u062a \u062c\u064a\u0646\u064a\u0629 \u0645\u062d\u062f\u062f\u0629.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u064a\u0631\u0643\u0632 GEn-1123 \u0639\u0644\u0649 \u0627\u0644\u0639\u0645\u0644\u064a\u0627\u062a \u0627\u0644\u0627\u0644\u062a\u0647\u0627\u0628\u064a\u0629 \u0648\u0627\u0644\u062a\u0646\u0643\u0633\u064a\u0629 \u0627\u0644\u0634\u0627\u0626\u0639\u0629 \u0628\u064a\u0646 \u0627\u0644\u0639\u062f\u064a\u062f \u0645\u0646 \u0645\u0631\u0636\u0649 \u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0627\u0644\u062f\u0648\u0634\u064a\u0646\u064a\u060c \u0645\u0645\u0627 \u064a\u062c\u0639\u0644\u0647 \u0630\u0627 \u0635\u0644\u0629 \u0628\u063a\u0636 \u0627\u0644\u0646\u0638\u0631 \u0639\u0646 \u0646\u0648\u0639 \u0627\u0644\u0637\u0641\u0631\u0629 \u0644\u062f\u0649 \u0627\u0644\u0645\u0631\u064a\u0636.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0642\u062f \u064a\u0624\u062f\u064a \u0647\u0630\u0627 \u0627\u0644\u0646\u0647\u062c \u0625\u0644\u0649 \u062a\u0648\u0633\u064a\u0639 \u0646\u0637\u0627\u0642 \u0639\u062f\u062f \u0627\u0644\u0645\u0631\u0636\u0649 \u0627\u0644\u0630\u064a\u0646 \u0642\u062f \u064a\u0633\u062a\u0641\u064a\u062f\u0648\u0646 \u0645\u0646\u0647 \u0625\u0630\u0627 \u0623\u0643\u062f\u062a \u0627\u0644\u062f\u0631\u0627\u0633\u0627\u062a \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629 \u0627\u0644\u0645\u0633\u062a\u0642\u0628\u0644\u064a\u0629 \u0633\u0644\u0627\u0645\u062a\u0647 \u0648\u0641\u0639\u0627\u0644\u064a\u062a\u0647.<\/p>\n\n\n\n<h3 id=\"oral-administration\" class=\"wp-block-heading\">\u0627\u0644\u0625\u062f\u0627\u0631\u0629 \u0639\u0646 \u0637\u0631\u064a\u0642 \u0627\u0644\u0641\u0645<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u0648\u0645\u0646 \u0627\u0644\u0633\u0645\u0627\u062a \u0627\u0644\u0645\u0645\u064a\u0632\u0629 \u0627\u0644\u0623\u062e\u0631\u0649 \u0623\u0646 GEn-1123 \u064a\u062a\u0645 \u062a\u0637\u0648\u064a\u0631\u0647 \u0643\u0639\u0644\u0627\u062c \u0641\u0645\u0648\u064a.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0642\u062f \u062a\u0648\u0641\u0631 \u0627\u0644\u0639\u0644\u0627\u062c\u0627\u062a \u0627\u0644\u0641\u0645\u0648\u064a\u0629 \u0645\u0632\u0627\u064a\u0627 \u0639\u0645\u0644\u064a\u0629 \u0644\u0644\u0645\u0631\u0636\u0649 \u0648\u0639\u0627\u0626\u0644\u0627\u062a\u0647\u0645 \u0645\u0642\u0627\u0631\u0646\u0629 \u0628\u0627\u0644\u0639\u0644\u0627\u062c\u0627\u062a \u0627\u0644\u062a\u064a \u062a\u062a\u0637\u0644\u0628 \u0625\u0639\u0637\u0627\u0621\u0647\u0627 \u0639\u0646 \u0637\u0631\u064a\u0642 \u0627\u0644\u0648\u0631\u064a\u062f.<\/p>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 id=\"fda-recognition-why-it-matters\" class=\"wp-block-heading\">\u0627\u0644\u062a\u0639\u0631\u0641 \u0639\u0644\u0649 FDA: \u0644\u0645\u0627\u0630\u0627 \u0647\u0648 \u0645\u0647\u0645<\/h2>\n\n\n\n<h3 id=\"orphan-drug-designation-odd\" class=\"wp-block-heading\">\u062a\u0635\u0646\u064a\u0641 \u0627\u0644\u0623\u062f\u0648\u064a\u0629 \u0627\u0644\u064a\u062a\u064a\u0645\u0629 (ODD)<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u062a\u0645\u0646\u062d \u0625\u062f\u0627\u0631\u0629 \u0627\u0644\u063a\u0630\u0627\u0621 \u0648\u0627\u0644\u062f\u0648\u0627\u0621 \u0627\u0644\u0623\u0645\u0631\u064a\u0643\u064a\u0629 (FDA) \u062a\u0635\u0646\u064a\u0641 \u0627\u0644\u0623\u062f\u0648\u064a\u0629 \u0627\u0644\u064a\u062a\u064a\u0645\u0629 \u0644\u0644\u0639\u0644\u0627\u062c\u0627\u062a \u0627\u0644\u062a\u064a \u062a\u0647\u062f\u0641 \u0625\u0644\u0649 \u0639\u0644\u0627\u062c \u0627\u0644\u0623\u0645\u0631\u0627\u0636 \u0627\u0644\u0646\u0627\u062f\u0631\u0629 \u0627\u0644\u062a\u064a \u062a\u0635\u064a\u0628 \u0623\u0642\u0644 \u0645\u0646 200000 \u0634\u062e\u0635 \u0641\u064a \u0627\u0644\u0648\u0644\u0627\u064a\u0627\u062a \u0627\u0644\u0645\u062a\u062d\u062f\u0629.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0642\u062f \u062a\u0634\u0645\u0644 \u0627\u0644\u0645\u0632\u0627\u064a\u0627 \u0645\u0627 \u064a\u0644\u064a:<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u062d\u0648\u0627\u0641\u0632 \u0627\u0644\u062a\u0646\u0645\u064a\u0629<\/li>\n\n\n\n<li>\u0627\u0644\u0625\u0639\u0641\u0627\u0621\u0627\u062a \u0627\u0644\u0636\u0631\u064a\u0628\u064a\u0629 \u0627\u0644\u0645\u062d\u062a\u0645\u0644\u0629<\/li>\n\n\n\n<li>\u0631\u0633\u0648\u0645 \u062a\u0646\u0638\u064a\u0645\u064a\u0629 \u0645\u062e\u0641\u0636\u0629<\/li>\n\n\n\n<li>\u0641\u062a\u0631\u0629 \u062d\u0635\u0631\u064a\u0629 \u0641\u064a \u0627\u0644\u0633\u0648\u0642 \u062a\u0635\u0644 \u0625\u0644\u0649 \u0633\u0628\u0639 \u0633\u0646\u0648\u0627\u062a \u0628\u0639\u062f \u0627\u0644\u0645\u0648\u0627\u0641\u0642\u0629<\/li>\n<\/ul>\n\n\n\n<h3 id=\"rare-pediatric-disease-designation-rpdd\" class=\"wp-block-heading\">\u062a\u0635\u0646\u064a\u0641 \u0627\u0644\u0623\u0645\u0631\u0627\u0636 \u0627\u0644\u0646\u0627\u062f\u0631\u0629 \u0644\u062f\u0649 \u0627\u0644\u0623\u0637\u0641\u0627\u0644 (RPDD)<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u0643\u0645\u0627 \u0645\u0646\u062d FDA \u062a\u0635\u0646\u064a\u0641 GEn-1123 \u0644\u0644\u0623\u0645\u0631\u0627\u0636 \u0627\u0644\u0646\u0627\u062f\u0631\u0629 \u0644\u062f\u0649 \u0627\u0644\u0623\u0637\u0641\u0627\u0644.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0647\u0630\u0627 \u0627\u0644\u062a\u0635\u0646\u064a\u0641 \u0645\u062e\u0635\u0635 \u0644\u0644\u0623\u0645\u0631\u0627\u0636 \u0627\u0644\u062e\u0637\u064a\u0631\u0629 \u0627\u0644\u062a\u064a \u062a\u0635\u064a\u0628 \u0627\u0644\u0623\u0637\u0641\u0627\u0644 \u0628\u0634\u0643\u0644 \u0623\u0633\u0627\u0633\u064a.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0625\u0630\u0627 \u062d\u0635\u0644 \u0627\u0644\u0639\u0644\u0627\u062c \u0641\u064a \u0646\u0647\u0627\u064a\u0629 \u0627\u0644\u0645\u0637\u0627\u0641 \u0639\u0644\u0649 \u0627\u0644\u0645\u0648\u0627\u0641\u0642\u0629 \u0627\u0644\u062a\u0646\u0638\u064a\u0645\u064a\u0629 \u0648\u0627\u0633\u062a\u0648\u0641\u0649 \u0645\u062a\u0637\u0644\u0628\u0627\u062a FDA\u060c \u0641\u0642\u062f \u064a\u0635\u0628\u062d GEn1E \u0645\u0624\u0647\u0644\u0627\u064b \u0644\u0644\u062d\u0635\u0648\u0644 \u0639\u0644\u0649 \u0642\u0633\u064a\u0645\u0629 \u0645\u0631\u0627\u062c\u0639\u0629 \u0630\u0627\u062a \u0623\u0648\u0644\u0648\u064a\u0629 (PRV)\u060c \u0648\u0627\u0644\u062a\u064a \u064a\u0645\u0643\u0646 \u0623\u0646 \u062a\u0633\u0627\u0639\u062f \u0641\u064a \u062a\u0633\u0631\u064a\u0639 \u0628\u0631\u0627\u0645\u062c \u062a\u0637\u0648\u064a\u0631 \u0627\u0644\u0623\u062f\u0648\u064a\u0629 \u0627\u0644\u0645\u0633\u062a\u0642\u0628\u0644\u064a\u0629.<\/p>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 id=\"current-development-status\" class=\"wp-block-heading\">\u0627\u0644\u0648\u0636\u0639 \u0627\u0644\u062d\u0627\u0644\u064a \u0644\u0644\u062a\u0637\u0648\u064a\u0631<\/h2>\n\n\n\n<h3 id=\"is-g-en-1123-approved\" class=\"wp-block-heading\">\u0647\u0644 \u0627\u0644\u0645\u0646\u062a\u062c GEn-1123 \u0645\u0639\u062a\u0645\u062f\u061f<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u0644\u0627.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0644\u0627 \u064a\u0632\u0627\u0644 \u0627\u0644\u0639\u0644\u0627\u062c GEn-1123 \u0639\u0644\u0627\u062c\u064b\u0627 \u062a\u062c\u0631\u064a\u0628\u064a\u064b\u0627 \u0648\u0644\u0645 \u062a\u062a\u0645 \u0627\u0644\u0645\u0648\u0627\u0641\u0642\u0629 \u0639\u0644\u064a\u0647 \u0628\u0639\u062f \u0645\u0646 \u0642\u0628\u0644 FDA \u0623\u0648 \u063a\u064a\u0631\u0647\u0627 \u0645\u0646 \u0627\u0644\u0647\u064a\u0626\u0627\u062a \u0627\u0644\u062a\u0646\u0638\u064a\u0645\u064a\u0629 \u0644\u0639\u0644\u0627\u062c \u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0633\u062a\u0643\u0648\u0646 \u0647\u0646\u0627\u0643 \u062d\u0627\u062c\u0629 \u0625\u0644\u0649 \u062f\u0631\u0627\u0633\u0627\u062a \u0633\u0631\u064a\u0631\u064a\u0629 \u0625\u0636\u0627\u0641\u064a\u0629 \u0644\u062a\u062d\u062f\u064a\u062f \u0645\u0627 \u064a\u0644\u064a:<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u0623\u0645\u0627\u0646<\/li>\n\n\n\n<li>\u0641\u0639\u0627\u0644\u064a\u0629<\/li>\n\n\n\n<li>\u0627\u0644\u062c\u0631\u0639\u0629 \u0627\u0644\u0645\u062b\u0644\u0649<\/li>\n\n\n\n<li>\u0627\u0644\u0641\u0648\u0627\u0626\u062f \u0648\u0627\u0644\u0645\u062e\u0627\u0637\u0631 \u0639\u0644\u0649 \u0627\u0644\u0645\u062f\u0649 \u0627\u0644\u0637\u0648\u064a\u0644<\/li>\n<\/ul>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 id=\"what-could-g-en-1123-mean-for-the-dmd-community\" class=\"wp-block-heading\">\u0645\u0627\u0630\u0627 \u0642\u062f \u064a\u0639\u0646\u064a GEn-1123 \u0644\u0645\u062c\u062a\u0645\u0639 \u0645\u0631\u0636\u0649 \u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0627\u0644\u062f\u0648\u0634\u064a\u0646\u064a\u061f<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u0644\u0627 \u064a\u0632\u0627\u0644 \u0645\u0631\u0636 \u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0627\u0644\u062f\u0648\u0634\u064a\u0646\u064a \u0645\u0631\u0636\u0627\u064b \u0645\u062a\u0641\u0627\u0642\u0645\u0627\u064b \u0645\u0639 \u0648\u062c\u0648\u062f \u0627\u062d\u062a\u064a\u0627\u062c\u0627\u062a \u0637\u0628\u064a\u0629 \u0643\u0628\u064a\u0631\u0629 \u063a\u064a\u0631 \u0645\u0644\u0628\u0627\u0629.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0641\u064a \u062d\u064a\u0646 \u0623\u0646 \u0627\u0644\u0639\u0644\u0627\u062c\u0627\u062a \u0627\u0644\u062c\u064a\u0646\u064a\u0629 \u0648\u0639\u0644\u0627\u062c\u0627\u062a \u062a\u062e\u0637\u064a \u0627\u0644\u0625\u0643\u0633\u0648\u0646 \u0642\u062f \u0648\u0633\u0639\u062a \u0627\u0644\u062e\u064a\u0627\u0631\u0627\u062a \u0627\u0644\u0639\u0644\u0627\u062c\u064a\u0629 \u0644\u0628\u0639\u0636 \u0627\u0644\u0645\u0631\u0636\u0649\u060c \u0625\u0644\u0627 \u0623\u0646 \u0627\u0644\u0639\u062f\u064a\u062f \u0645\u0646 \u0627\u0644\u0623\u0641\u0631\u0627\u062f \u0645\u0627 \u0632\u0627\u0644\u0648\u0627 \u064a\u0639\u0627\u0646\u0648\u0646 \u0645\u0646 \u062a\u0641\u0627\u0642\u0645 \u0627\u0644\u0645\u0631\u0636.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u064a\u0645\u062b\u0644 GEn-1123 \u0627\u0633\u062a\u0631\u0627\u062a\u064a\u062c\u064a\u0629 \u0639\u0644\u0627\u062c\u064a\u0629 \u0645\u062e\u062a\u0644\u0641\u0629 \u0645\u0646 \u062e\u0644\u0627\u0644 \u0627\u0633\u062a\u0647\u062f\u0627\u0641 \u0627\u0644\u0627\u0644\u062a\u0647\u0627\u0628 \u0648\u0627\u0644\u062a\u0646\u0643\u0633 \u0648\u0636\u0639\u0641 \u0627\u0644\u062a\u062c\u062f\u064a\u062f - \u0648\u0647\u064a \u0639\u0645\u0644\u064a\u0627\u062a \u0628\u064a\u0648\u0644\u0648\u062c\u064a\u0629 \u062a\u0633\u0627\u0647\u0645 \u0641\u064a \u0641\u0642\u062f\u0627\u0646 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0637\u0648\u0627\u0644 \u0645\u0633\u0627\u0631 \u0627\u0644\u0645\u0631\u0636.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0625\u0630\u0627 \u0623\u0638\u0647\u0631\u062a \u0627\u0644\u062a\u062c\u0627\u0631\u0628 \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629 \u0627\u0644\u0645\u0633\u062a\u0642\u0628\u0644\u064a\u0629 \u0646\u062a\u0627\u0626\u062c \u0625\u064a\u062c\u0627\u0628\u064a\u0629\u060c \u0641\u0642\u062f \u064a\u0635\u0628\u062d GEn-1123 \u0625\u0636\u0627\u0641\u0629 \u0645\u0647\u0645\u0629 \u0625\u0644\u0649 \u0627\u0644\u0645\u0634\u0647\u062f \u0627\u0644\u0639\u0644\u0627\u062c\u064a \u0627\u0644\u0645\u062a\u0637\u0648\u0631 \u0644\u0645\u0631\u0636 \u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0627\u0644\u062f\u0648\u0634\u064a\u0646\u064a.<\/p>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 id=\"key-takeaways\" class=\"wp-block-heading\">\u0627\u0644\u0646\u0642\u0627\u0637 \u0627\u0644\u0631\u0626\u064a\u0633\u064a\u0629<\/h2>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u062a\u0642\u0648\u0645 \u0634\u0631\u0643\u0629 GEn1E Lifesciences \u0628\u062a\u0637\u0648\u064a\u0631 GEn-1123\u060c \u0648\u0647\u0648 \u0639\u0644\u0627\u062c \u0641\u0645\u0648\u064a \u062a\u062c\u0631\u064a\u0628\u064a \u0644\u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a.<\/li>\n\n\n\n<li>\u062a\u0645 \u062a\u0635\u0645\u064a\u0645 GEn-1123 \u0644\u062a\u0639\u062f\u064a\u0644 \u0627\u0644\u0627\u0644\u062a\u0647\u0627\u0628 \u0627\u0644\u0636\u0627\u0631 \u0645\u0639 \u062a\u0639\u0632\u064a\u0632 \u0628\u0642\u0627\u0621 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0648\u062a\u062c\u062f\u064a\u062f\u0647\u0627.<\/li>\n\n\n\n<li>\u064a\u0633\u062a\u0647\u062f\u0641 \u0627\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u0645\u0633\u0627\u0631\u0627\u062a \u0627\u0644\u0628\u064a\u0648\u0644\u0648\u062c\u064a\u0629 \u0627\u0644\u0645\u0633\u0628\u0628\u0629 \u0644\u0644\u0645\u0631\u0636 \u0628\u062f\u0644\u0627\u064b \u0645\u0646 \u0627\u0633\u062a\u0639\u0627\u062f\u0629 \u0627\u0644\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646.<\/li>\n\n\n\n<li>\u062d\u0635\u0644 \u0627\u0644\u0645\u0631\u0643\u0628 FDA \u0639\u0644\u0649 \u062a\u0635\u0646\u064a\u0641 \u062f\u0648\u0627\u0621 \u0627\u0644\u064a\u062a\u064a\u0645 \u0648\u062a\u0635\u0646\u064a\u0641 \u0627\u0644\u0623\u0645\u0631\u0627\u0636 \u0627\u0644\u0646\u0627\u062f\u0631\u0629 \u0644\u062f\u0649 \u0627\u0644\u0623\u0637\u0641\u0627\u0644.<\/li>\n\n\n\n<li>\u0644\u0627 \u064a\u0632\u0627\u0644 \u062f\u0648\u0627\u0621 GEn-1123 \u0642\u064a\u062f \u0627\u0644\u062a\u0637\u0648\u064a\u0631 \u0627\u0644\u0633\u0631\u064a\u0631\u064a \u0648\u0644\u0645 \u064a\u062d\u0635\u0644 \u0628\u0639\u062f \u0639\u0644\u0649 \u0627\u0644\u0645\u0648\u0627\u0641\u0642\u0629 \u0627\u0644\u062a\u0646\u0638\u064a\u0645\u064a\u0629.<\/li>\n\n\n\n<li>\u0642\u062f \u064a\u0643\u0648\u0646 \u0644\u0644\u0639\u0644\u0627\u062c \u0625\u0645\u0643\u0627\u0646\u0627\u062a \u0645\u0633\u062a\u0642\u0644\u0629 \u0639\u0646 \u0627\u0644\u0637\u0641\u0631\u0629\u060c \u0645\u0645\u0627 \u064a\u062c\u0639\u0644\u0647 \u0645\u0646\u0627\u0633\u0628\u064b\u0627 \u0644\u0645\u062c\u0645\u0648\u0639\u0629 \u0648\u0627\u0633\u0639\u0629 \u0645\u0646 \u0645\u0631\u0636\u0649 \u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0627\u0644\u062f\u0648\u0634\u064a\u0646\u064a.<\/li>\n<\/ul>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u062a\u0627\u0628\u0639 \u0647\u0630\u0647 \u0627\u0644\u0635\u0641\u062d\u0629<\/strong>&nbsp;&gt;&gt;&gt;&nbsp;<a href=\"https:\/\/dmdwarrior.com\/ar\/dmd-therapies\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u062c\u0645\u064a\u0639 \u0627\u0644\u062a\u062c\u0627\u0631\u0628 \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629 \u0644\u0645\u0631\u0636 \u062f\u0648\u0634\u064a\u0646<\/a><\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><\/p>","protected":false},"excerpt":{"rendered":"<p>The U.S. Food and Drug Administration (FDA) has granted both Orphan Drug Designation (ODD) and Rare Pediatric Disease Designation (RPDD) to GEn-1123, an investigational Duchenne Muscular Dystrophy (DMD) therapy being developed by GEn1E Lifesciences, a Phase 2 clinical-stage biotechnology company specializing in AI-driven precision medicine. What Is GEn1E Lifesciences? GEn1E Lifesciences is a biotechnology company [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":8113,"comment_status":"open","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[281],"tags":[819,680,817,815,816,820,195],"class_list":["post-8110","post","type-post","status-publish","format-standard","has-post-thumbnail","category-press-releases","tag-dmd-drug-development","tag-dmd-orphan-drugs","tag-dmd-treatment","tag-gen-1123","tag-gen1e-lifesciences","tag-oral-therapy","tag-orphan-drug"],"_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/posts\/8110","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/comments?post=8110"}],"version-history":[{"count":2,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/posts\/8110\/revisions"}],"predecessor-version":[{"id":8115,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/posts\/8110\/revisions\/8115"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/media\/8113"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/media?parent=8110"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/categories?post=8110"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/tags?post=8110"}],"curies":[{"name":"\u0648\u0648\u0631\u062f\u0628\u0631\u064a\u0633","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}