{"id":7683,"date":"2026-04-21T17:37:11","date_gmt":"2026-04-21T14:37:11","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=7683"},"modified":"2026-04-21T17:37:12","modified_gmt":"2026-04-21T14:37:12","slug":"elevidys-phase-4-enhance-clinical-trial-nct07542314","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/ar\/elevidys-phase-4-enhance-clinical-trial-nct07542314\/","title":{"rendered":"\u062f\u0631\u0627\u0633\u0629 ELEVIDYS ENHANCE: \u0628\u062f\u0621 \u062a\u062c\u0631\u0628\u0629 \u0627\u0644\u0645\u0631\u062d\u0644\u0629 \u0627\u0644\u0631\u0627\u0628\u0639\u0629 \u0644\u062a\u0642\u064a\u064a\u0645 \u0627\u0644\u0633\u0644\u0627\u0645\u0629 \u0648\u0627\u0644\u0641\u0639\u0627\u0644\u064a\u0629 \u0641\u064a \u0639\u0644\u0627\u062c \u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a"},"content":{"rendered":"<p class=\"wp-block-paragraph\"><strong>\u062a\u064f\u0639\u062f \u062f\u0631\u0627\u0633\u0629 ENHANCE \u062a\u062c\u0631\u0628\u0629 \u0633\u0631\u064a\u0631\u064a\u0629 \u0645\u0646 \u0627\u0644\u0645\u0631\u062d\u0644\u0629 \u0627\u0644\u0631\u0627\u0628\u0639\u0629 \u0645\u0635\u0645\u0645\u0629 \u0644\u062a\u0642\u064a\u064a\u0645 \u0627\u0644\u0633\u0644\u0627\u0645\u0629 \u0648\u0627\u0644\u0641\u0639\u0627\u0644\u064a\u0629 \u0627\u0644\u0648\u0627\u0642\u0639\u064a\u0629 \u0644\u0640 ELEVIDYS \u0644\u062f\u0649 \u0627\u0644\u0645\u0631\u0636\u0649 \u0627\u0644\u0630\u064a\u0646 \u064a\u0639\u0627\u0646\u0648\u0646 \u0645\u0646 \u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a (DMD).<\/strong><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u062a\u064f\u0639\u062f \u0647\u0630\u0647 \u0627\u0644\u062f\u0631\u0627\u0633\u0629 \u0630\u0627\u062a \u0623\u0647\u0645\u064a\u0629 \u062e\u0627\u0635\u0629 \u0644\u0623\u0646\u0647\u0627 \u062a\u0631\u0643\u0632 \u0639\u0644\u0649 \u0627\u0644\u0645\u0631\u0636\u0649 \u0627\u0644\u0630\u064a\u0646 \u0639\u0648\u0644\u062c\u0648\u0627 \u0641\u064a \u0628\u064a\u0626\u0629 \u0645\u0627 \u0628\u0639\u062f \u0627\u0644\u062a\u0633\u0648\u064a\u0642\u060c \u0623\u064a \u0628\u0639\u062f \u0623\u0646 \u062a\u0645\u062a \u0627\u0644\u0645\u0648\u0627\u0641\u0642\u0629 \u0639\u0644\u0649 \u0627\u0644\u0639\u0644\u0627\u062c \u0628\u0627\u0644\u0641\u0639\u0644 \u0648\u064a\u062a\u0645 \u0627\u0633\u062a\u062e\u062f\u0627\u0645\u0647 \u0641\u064a \u0627\u0644\u0645\u0645\u0627\u0631\u0633\u0629 \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u062a\u0645 \u062a\u0645\u0648\u064a\u0644 \u0647\u0630\u0647 \u0627\u0644\u062a\u062c\u0631\u0628\u0629 \u0645\u0646 \u0642\u0628\u0644 Sarepta Therapeutics \u0648\u062a\u062d\u0645\u0644 \u0631\u0642\u0645 \u062a\u0639\u0631\u064a\u0641 \u0627\u0644\u062f\u0631\u0627\u0633\u0629 SRP-9001-402.<\/p>\n\n\n\n<div class=\"wp-block-rank-math-toc-block\" id=\"rank-math-toc\"><h2>\u062c\u062f\u0648\u0644 \u0627\u0644\u0645\u062d\u062a\u0648\u064a\u0627\u062a<\/h2><nav><ul><li><a href=\"#primary-goal-understanding-liver-safety-risks\">\u0627\u0644\u0647\u062f\u0641 \u0627\u0644\u0631\u0626\u064a\u0633\u064a: \u0641\u0647\u0645 \u0645\u062e\u0627\u0637\u0631 \u0633\u0644\u0627\u0645\u0629 \u0627\u0644\u0643\u0628\u062f<\/a><\/li><li><a href=\"#study-design-and-key-details\">\u062a\u0635\u0645\u064a\u0645 \u0627\u0644\u062f\u0631\u0627\u0633\u0629 \u0648\u0627\u0644\u062a\u0641\u0627\u0635\u064a\u0644 \u0627\u0644\u0631\u0626\u064a\u0633\u064a\u0629<\/a><\/li><li><a href=\"#who-can-participate\">\u0645\u0646 \u064a\u0645\u0643\u0646\u0647 \u0627\u0644\u0645\u0634\u0627\u0631\u0643\u0629\u061f<\/a><\/li><li><a href=\"#who-cannot-participate\">\u0645\u0646 \u0644\u0627 \u064a\u0633\u062a\u0637\u064a\u0639 \u0627\u0644\u0645\u0634\u0627\u0631\u0643\u0629\u061f<\/a><\/li><li><a href=\"#why-this-study-is-important-for-the-dmd-community\">\u0644\u0645\u0627\u0630\u0627 \u062a\u064f\u0639\u062f \u0647\u0630\u0647 \u0627\u0644\u062f\u0631\u0627\u0633\u0629 \u0645\u0647\u0645\u0629 \u0644\u0645\u062c\u062a\u0645\u0639 \u0645\u0631\u0636\u0649 \u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0627\u0644\u062f\u0648\u0634\u064a\u0646\u064a\u061f<\/a><\/li><li><a href=\"#contact-information\">\u0645\u0639\u0644\u0648\u0645\u0627\u062a \u0627\u0644\u0627\u062a\u0635\u0627\u0644<\/a><\/li><li><a href=\"#clinical-trial-locations-not-yet-announced\">\u0644\u0645 \u064a\u062a\u0645 \u0627\u0644\u0625\u0639\u0644\u0627\u0646 \u0628\u0639\u062f \u0639\u0646 \u0645\u0648\u0627\u0642\u0639 \u0627\u0644\u062a\u062c\u0627\u0631\u0628 \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629<\/a><\/li><\/ul><\/nav><\/div>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"primary-goal-understanding-liver-safety-risks\">\u0627\u0644\u0647\u062f\u0641 \u0627\u0644\u0631\u0626\u064a\u0633\u064a: \u0641\u0647\u0645 \u0645\u062e\u0627\u0637\u0631 \u0633\u0644\u0627\u0645\u0629 \u0627\u0644\u0643\u0628\u062f<\/h2>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"why-liver-safety-matters\">\u0644\u0645\u0627\u0630\u0627 \u062a\u064f\u0639\u062f \u0633\u0644\u0627\u0645\u0629 \u0627\u0644\u0643\u0628\u062f \u0645\u0647\u0645\u0629\u061f<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u0623\u062d\u062f \u0623\u0647\u0645 \u0627\u0644\u0645\u062e\u0627\u0648\u0641 \u0627\u0644\u0645\u062a\u0639\u0644\u0642\u0629 \u0628\u0627\u0644\u0639\u0644\u0627\u062c\u0627\u062a \u0627\u0644\u062c\u064a\u0646\u064a\u0629 \u0645\u062b\u0644 ELEVIDYS \u0647\u0648 \u062e\u0637\u0631 \u0627\u0644\u0625\u0635\u0627\u0628\u0629 \u0627\u0644\u062d\u0627\u062f\u0629 \u0628\u0627\u0644\u0643\u0628\u062f (ALI).<\/p>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"role-of-sirolimus\">\u062f\u0648\u0631 \u0633\u064a\u0631\u0648\u0644\u064a\u0645\u0648\u0633<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u062a\u0642\u064a\u0651\u0645 \u0627\u0644\u062f\u0631\u0627\u0633\u0629 \u0645\u0627 \u0625\u0630\u0627 \u0643\u0627\u0646 \u0625\u0636\u0627\u0641\u0629 \u0633\u064a\u0631\u0648\u0644\u064a\u0645\u0648\u0633 \u0643\u0639\u0644\u0627\u062c \u0648\u0642\u0627\u0626\u064a (\u0648\u0642\u0627\u0626\u064a) \u0645\u062b\u0628\u0637 \u0644\u0644\u0645\u0646\u0627\u0639\u0629 \u064a\u0645\u0643\u0646 \u0623\u0646 \u064a\u0633\u0627\u0639\u062f \u0641\u064a \u062a\u0642\u0644\u064a\u0644 \u0627\u0644\u0645\u0636\u0627\u0639\u0641\u0627\u062a \u0627\u0644\u0645\u062a\u0639\u0644\u0642\u0629 \u0628\u0627\u0644\u0643\u0628\u062f.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0628\u0639\u0628\u0627\u0631\u0627\u062a \u0628\u0633\u064a\u0637\u0629:<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u064a\u0633\u0627\u0639\u062f ELEVIDYS \u0641\u064a \u062a\u0648\u0635\u064a\u0644 \u062c\u064a\u0646 \u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0648\u0638\u064a\u0641\u064a.<\/li>\n\n\n\n<li>\u064a\u0633\u0627\u0639\u062f \u062f\u0648\u0627\u0621 \u0633\u064a\u0631\u0648\u0644\u064a\u0645\u0648\u0633 \u0641\u064a \u0627\u0644\u0633\u064a\u0637\u0631\u0629 \u0639\u0644\u0649 \u0631\u062f \u0641\u0639\u0644 \u0627\u0644\u062c\u0647\u0627\u0632 \u0627\u0644\u0645\u0646\u0627\u0639\u064a \u062a\u062c\u0627\u0647 \u0627\u0644\u0639\u0644\u0627\u062c.<\/li>\n\n\n\n<li>\u0627\u0644\u0647\u062f\u0641 \u0647\u0648 \u062c\u0639\u0644 \u0627\u0644\u0639\u0644\u0627\u062c \u0623\u0643\u062b\u0631 \u0623\u0645\u0627\u0646\u0627\u064b \u062f\u0648\u0646 \u062a\u0642\u0644\u064a\u0644 \u0641\u0639\u0627\u0644\u064a\u062a\u0647.<\/li>\n<\/ul>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"study-design-and-key-details\">\u062a\u0635\u0645\u064a\u0645 \u0627\u0644\u062f\u0631\u0627\u0633\u0629 \u0648\u0627\u0644\u062a\u0641\u0627\u0635\u064a\u0644 \u0627\u0644\u0631\u0626\u064a\u0633\u064a\u0629<\/h2>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"trial-overview\">\u0646\u0638\u0631\u0629 \u0639\u0627\u0645\u0629 \u0639\u0644\u0649 \u0627\u0644\u062a\u062c\u0631\u0628\u0629<\/h3>\n\n\n\n<ul class=\"wp-block-list\">\n<li><strong>\u0646\u0648\u0639 \u0627\u0644\u062f\u0631\u0627\u0633\u0629:<\/strong> \u0627\u0644\u062a\u062f\u062e\u0644\u064a<\/li>\n\n\n\n<li><strong>\u0645\u0631\u062d\u0644\u0629:<\/strong> \u0627\u0644\u0645\u0631\u062d\u0644\u0629 \u0627\u0644\u0631\u0627\u0628\u0639\u0629<\/li>\n\n\n\n<li><strong>\u0639\u062f\u062f \u0627\u0644\u0637\u0644\u0627\u0628 \u0627\u0644\u0645\u062a\u0648\u0642\u0639:<\/strong> 20 \u0645\u0634\u0627\u0631\u0643\u064b\u0627<\/li>\n\n\n\n<li><strong>\u062a\u0627\u0631\u064a\u062e \u0627\u0644\u0628\u062f\u0621:<\/strong> 30 \u0623\u0628\u0631\u064a\u0644 2026<\/li>\n\n\n\n<li><strong>\u062a\u0627\u0631\u064a\u062e \u0627\u0644\u0625\u0646\u062c\u0627\u0632:<\/strong> 31 \u0645\u0627\u0631\u0633 2027<\/li>\n<\/ul>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"study-groups-cohorts\">\u0645\u062c\u0645\u0648\u0639\u0627\u062a \u0627\u0644\u062f\u0631\u0627\u0633\u0629 (\u0627\u0644\u0623\u0641\u0648\u0627\u062c)<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u062a\u062a\u0636\u0645\u0646 \u0627\u0644\u062a\u062c\u0631\u0628\u0629 \u0645\u062c\u0645\u0648\u0639\u062a\u064a\u0646 \u0645\u0646 \u0627\u0644\u0645\u0634\u0627\u0631\u0643\u064a\u0646:<\/p>\n\n\n\n<h4 class=\"wp-block-heading\" id=\"cohort-1\">\u0627\u0644\u0645\u062c\u0645\u0648\u0639\u0629 \u0627\u0644\u0623\u0648\u0644\u0649:<\/h4>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u0627\u0644\u0623\u0648\u0644\u0627\u062f \u0627\u0644\u0630\u064a\u0646 \u062a\u0628\u0644\u063a \u0623\u0639\u0645\u0627\u0631\u0647\u0645 4 \u0633\u0646\u0648\u0627\u062a \u0641\u0623\u0643\u062b\u0631<\/li>\n\n\n\n<li>\u064a\u062c\u0628 \u0623\u0646 \u064a\u0643\u0648\u0646 \u0642\u0627\u062f\u0631\u0627\u064b \u0639\u0644\u0649 \u0627\u0644\u0645\u0634\u064a (\u0627\u0644\u0642\u062f\u0631\u0629 \u0639\u0644\u0649 \u0627\u0644\u062d\u0631\u0643\u0629)<\/li>\n\n\n\n<li>\u0645\u0624\u0647\u0644 \u0644\u062a\u0644\u0642\u064a \u0639\u0644\u0627\u062c ELEVIDYS \u0627\u0644\u062a\u062c\u0627\u0631\u064a<\/li>\n<\/ul>\n\n\n\n<h4 class=\"wp-block-heading\" id=\"cohort-2\">\u0627\u0644\u0645\u062c\u0645\u0648\u0639\u0629 \u0627\u0644\u062b\u0627\u0646\u064a\u0629:<\/h4>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u0633\u0628\u0642 \u0639\u0644\u0627\u062c\u0647 \u0628\u0627\u0633\u062a\u062e\u062f\u0627\u0645 ELEVIDYS<\/li>\n\n\n\n<li>\u0633\u0628\u0642 \u0623\u0646 \u062a\u0644\u0642\u0649 \u0627\u0644\u0645\u0631\u064a\u0636 \u062f\u0648\u0627\u0621 \u0633\u064a\u0631\u0648\u0644\u064a\u0645\u0648\u0633 \u0648\u0627\u0644\u0643\u0648\u0631\u062a\u064a\u0643\u0648\u0633\u062a\u064a\u0631\u0648\u064a\u062f\u0627\u062a \u0642\u0628\u0644 \u0628\u062f\u0621 \u0627\u0644\u0639\u0644\u0627\u062c.<\/li>\n<\/ul>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"who-can-participate\">\u0645\u0646 \u064a\u0645\u0643\u0646\u0647 \u0627\u0644\u0645\u0634\u0627\u0631\u0643\u0629\u061f<\/h2>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"key-inclusion-criteria\">\u0645\u0639\u0627\u064a\u064a\u0631 \u0627\u0644\u0625\u062f\u0631\u0627\u062c \u0627\u0644\u0631\u0626\u064a\u0633\u064a\u0629<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u064a\u062c\u0628 \u0639\u0644\u0649 \u0627\u0644\u0645\u0634\u0627\u0631\u0643\u064a\u0646:<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u0623\u0646 \u064a\u0643\u0648\u0646 \u0630\u0643\u0631\u0627\u064b \u0639\u0646\u062f \u0627\u0644\u0648\u0644\u0627\u062f\u0629<\/li>\n\n\n\n<li>\u0627\u0633\u062a\u064a\u0641\u0627\u0621 \u0645\u062a\u0637\u0644\u0628\u0627\u062a \u0627\u0644\u0633\u0646 \u0648\u0627\u0644\u0623\u0647\u0644\u064a\u0629 \u0644\u0644\u0639\u0644\u0627\u062c<\/li>\n\n\n\n<li>\u064a\u062c\u0628 \u0623\u0646 \u064a\u0643\u0648\u0646 \u0644\u062f\u064a\u0643 \u0645\u0642\u062f\u0645 \u0631\u0639\u0627\u064a\u0629 \u0623\u0648 \u0623\u0646 \u062a\u0643\u0648\u0646 \u0642\u0627\u062f\u0631\u0627\u064b \u0639\u0644\u0649 \u0627\u062a\u0628\u0627\u0639 \u0625\u062c\u0631\u0627\u0621\u0627\u062a \u0627\u0644\u062f\u0631\u0627\u0633\u0629<\/li>\n\n\n\n<li>\u062a\u0642\u062f\u064a\u0645 \u0627\u0644\u0645\u0648\u0627\u0641\u0642\u0629 \u0627\u0644\u0645\u0633\u062a\u0646\u064a\u0631\u0629 (\u0623\u0648 \u062a\u0643\u0644\u064a\u0641 \u0648\u0644\u064a \u0627\u0644\u0623\u0645\u0631 \u0627\u0644\u0642\u0627\u0646\u0648\u0646\u064a \u0628\u0630\u0644\u0643)<\/li>\n\n\n\n<li>\u0627\u0633\u062a\u062e\u062f\u0645\u064a \u0648\u0633\u0627\u0626\u0644 \u0645\u0646\u0639 \u0627\u0644\u062d\u0645\u0644 \u0627\u0644\u0645\u0646\u0627\u0633\u0628\u0629 \u0625\u0630\u0627 \u0643\u0646\u062a\u0650 \u0646\u0634\u0637\u0629 \u062c\u0646\u0633\u064a\u0627\u064b<\/li>\n<\/ul>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"who-cannot-participate\">\u0645\u0646 \u0644\u0627 \u064a\u0633\u062a\u0637\u064a\u0639 \u0627\u0644\u0645\u0634\u0627\u0631\u0643\u0629\u061f<\/h2>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"key-exclusion-criteria\">\u0645\u0639\u0627\u064a\u064a\u0631 \u0627\u0644\u0627\u0633\u062a\u0628\u0639\u0627\u062f \u0627\u0644\u0631\u0626\u064a\u0633\u064a\u0629<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u0644\u0627 \u064a\u062c\u0648\u0632 \u0644\u0644\u0645\u0634\u0627\u0631\u0643\u064a\u0646 \u0627\u0644\u0627\u0646\u0636\u0645\u0627\u0645 \u0625\u0630\u0627 \u0643\u0627\u0646\u0648\u0627:<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u0644\u0627 \u064a\u0645\u0643\u0646 \u062a\u0644\u0642\u064a ELEVIDYS \u0628\u0623\u0645\u0627\u0646<\/li>\n\n\n\n<li>\u064a\u064f\u0635\u0627\u0628 \u0628\u0639\u062f\u0648\u0649 \u0645\u062b\u0644:\n<ul class=\"wp-block-list\">\n<li>\u0641\u064a\u0631\u0648\u0633 \u0627\u0644\u0639\u0648\u0632 \u0627\u0644\u0645\u0646\u0627\u0639\u064a \u0627\u0644\u0628\u0634\u0631\u064a<\/li>\n\n\n\n<li>\u0627\u0644\u062a\u0647\u0627\u0628 \u0627\u0644\u0643\u0628\u062f \u0628 \u0623\u0648 \u062c<\/li>\n<\/ul>\n<\/li>\n\n\n\n<li>\u0647\u0644 \u0644\u062f\u064a\u0643 \u0625\u0635\u0627\u0628\u0627\u062a \u0623\u0648 \u062a\u0637\u0639\u064a\u0645\u0627\u062a \u062d\u062f\u064a\u062b\u0629\u061f<\/li>\n\n\n\n<li>\u062a\u0648\u062c\u062f \u0634\u0631\u0648\u0637 \u0642\u062f \u062a\u0624\u062b\u0631 \u0639\u0644\u0649 \u0627\u0644\u0633\u0644\u0627\u0645\u0629 \u0623\u0648 \u0646\u062a\u0627\u0626\u062c \u0627\u0644\u062f\u0631\u0627\u0633\u0629<\/li>\n\n\n\n<li>\u0644\u0627 \u064a\u062a\u062d\u0645\u0644 \u0627\u0644\u0633\u064a\u0631\u0648\u0644\u064a\u0645\u0648\u0633<\/li>\n\n\n\n<li>\u0647\u0644 \u062a\u0639\u0627\u0646\u064a \u0645\u0646 \u062c\u0631\u0648\u062d \u0623\u0648 \u0625\u0635\u0627\u0628\u0627\u062a \u0642\u062f \u062a\u0644\u062a\u0626\u0645 \u0628\u0634\u0643\u0644 \u0633\u064a\u0626 \u0641\u064a \u0638\u0644 \u062a\u062b\u0628\u064a\u0637 \u0627\u0644\u0645\u0646\u0627\u0639\u0629\u061f<\/li>\n<\/ul>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"why-this-study-is-important-for-the-dmd-community\">\u0644\u0645\u0627\u0630\u0627 \u062a\u064f\u0639\u062f \u0647\u0630\u0647 \u0627\u0644\u062f\u0631\u0627\u0633\u0629 \u0645\u0647\u0645\u0629 \u0644\u0645\u062c\u062a\u0645\u0639 \u0645\u0631\u0636\u0649 \u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0627\u0644\u062f\u0648\u0634\u064a\u0646\u064a\u061f<\/h2>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"real-world-evidence\">\u0623\u062f\u0644\u0629 \u0645\u0646 \u0627\u0644\u0648\u0627\u0642\u0639<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u0639\u0644\u0649 \u0639\u0643\u0633 \u0627\u0644\u062a\u062c\u0627\u0631\u0628 \u0627\u0644\u0633\u0627\u0628\u0642\u0629\u060c \u062a\u0639\u0643\u0633 \u0647\u0630\u0647 \u0627\u0644\u062f\u0631\u0627\u0633\u0629 \u0638\u0631\u0648\u0641 \u0627\u0644\u0639\u0644\u0627\u062c \u0641\u064a \u0627\u0644\u062d\u064a\u0627\u0629 \u0627\u0644\u0648\u0627\u0642\u0639\u064a\u0629\u060c \u0645\u0645\u0627 \u064a\u0633\u0627\u0639\u062f \u0627\u0644\u0623\u0637\u0628\u0627\u0621 \u0639\u0644\u0649 \u0641\u0647\u0645 \u0645\u0627 \u064a\u0644\u064a:<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u0645\u0627 \u0645\u062f\u0649 \u0623\u0645\u0627\u0646 \u062f\u0648\u0627\u0621 ELEVIDYS \u062e\u0627\u0631\u062c \u0627\u0644\u0628\u064a\u0626\u0627\u062a \u0627\u0644\u062e\u0627\u0636\u0639\u0629 \u0644\u0644\u0631\u0642\u0627\u0628\u0629\u061f<\/li>\n\n\n\n<li>\u0643\u064a\u0641 \u064a\u0633\u062a\u062c\u064a\u0628 \u0627\u0644\u0645\u0631\u0636\u0649 \u0628\u0645\u0631\u0648\u0631 \u0627\u0644\u0648\u0642\u062a<\/li>\n<\/ul>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"improving-treatment-safety\">\u062a\u062d\u0633\u064a\u0646 \u0633\u0644\u0627\u0645\u0629 \u0627\u0644\u0639\u0644\u0627\u062c<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u0641\u064a \u062d\u0627\u0644 \u0646\u062c\u0627\u062d \u0627\u0644\u062f\u0631\u0627\u0633\u0629\u060c \u0642\u062f:<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u062a\u0642\u0644\u064a\u0644 \u0627\u0644\u0645\u062e\u0627\u0637\u0631 \u0627\u0644\u0645\u062a\u0639\u0644\u0642\u0629 \u0628\u0627\u0644\u0643\u0628\u062f<\/li>\n\n\n\n<li>\u062a\u062d\u0633\u064a\u0646 \u0628\u0631\u0648\u062a\u0648\u0643\u0648\u0644\u0627\u062a \u0627\u0644\u0639\u0644\u0627\u062c<\/li>\n\n\n\n<li>\u0632\u064a\u0627\u062f\u0629 \u0627\u0644\u062b\u0642\u0629 \u0641\u064a \u0627\u0633\u062a\u062e\u062f\u0627\u0645 \u0627\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u062c\u064a\u0646\u064a<\/li>\n<\/ul>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"contact-information\">\u0645\u0639\u0644\u0648\u0645\u0627\u062a \u0627\u0644\u0627\u062a\u0635\u0627\u0644<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u0644\u0645\u0632\u064a\u062f \u0645\u0646 \u0627\u0644\u062a\u0641\u0627\u0635\u064a\u0644 \u062d\u0648\u0644 \u0627\u0644\u062f\u0631\u0627\u0633\u0629:<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li><strong>\u0645\u0646\u0638\u0645\u0629:<\/strong> \u0633\u0627\u0631\u064a\u0628\u062a\u0627 \u062b\u064a\u0631\u0627\u0628\u064a\u0648\u062a\u0643\u0633<\/li>\n\n\n\n<li><strong>\u0647\u0627\u062a\u0641:<\/strong> 1-888-\u0633\u0627\u0631\u064a\u0628\u062a\u0627 (1-888-727-3782)<\/li>\n\n\n\n<li><strong>\u0628\u0631\u064a\u062f \u0625\u0644\u0643\u062a\u0631\u0648\u0646\u064a:<\/strong> <a>SareptAlly@sarepta.com<\/a><\/li>\n<\/ul>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"clinical-trial-locations-not-yet-announced\">\u0644\u0645 \u064a\u062a\u0645 \u0627\u0644\u0625\u0639\u0644\u0627\u0646 \u0628\u0639\u062f \u0639\u0646 \u0645\u0648\u0627\u0642\u0639 \u0627\u0644\u062a\u062c\u0627\u0631\u0628 \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u0644\u0645 \u062a\u064f\u0639\u0644\u0646 \u0628\u0639\u062f \u0645\u0648\u0627\u0642\u0639 \u0627\u0644\u062a\u062c\u0627\u0631\u0628 \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629 ENHANCE. \u0648\u0645\u0646 \u0627\u0644\u0645\u062a\u0648\u0642\u0639 \u0623\u0646 \u062a\u064f\u0639\u0644\u0646 \u0627\u0644\u062c\u0647\u0629 \u0627\u0644\u0631\u0627\u0639\u064a\u0629 \u0644\u0644\u062f\u0631\u0627\u0633\u0629\u060c Sarepta Therapeutics\u060c \u0639\u0646 \u0627\u0644\u0645\u0648\u0627\u0642\u0639 \u0627\u0644\u0645\u0634\u0627\u0631\u0643\u0629 \u0644\u0627\u062d\u0642\u064b\u0627. \u0648\u0646\u0646\u0635\u062d \u0627\u0644\u0645\u0631\u0636\u0649 \u0648\u0645\u0642\u062f\u0645\u064a \u0627\u0644\u0631\u0639\u0627\u064a\u0629 \u0627\u0644\u0635\u062d\u064a\u0629 \u0648\u0627\u0644\u0639\u0627\u0645\u0644\u064a\u0646 \u0641\u064a \u0645\u062c\u0627\u0644 \u0627\u0644\u0631\u0639\u0627\u064a\u0629 \u0627\u0644\u0635\u062d\u064a\u0629 \u0628\u0645\u062a\u0627\u0628\u0639\u0629 \u0627\u0644\u062a\u062d\u062f\u064a\u062b\u0627\u062a \u0627\u0644\u0631\u0633\u0645\u064a\u0629 \u0641\u0648\u0631 \u062a\u0648\u0641\u0631 \u0645\u0639\u0644\u0648\u0645\u0627\u062a \u0627\u0644\u0645\u0648\u0627\u0642\u0639.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u062a\u0627\u0628\u0639 \u0647\u0630\u0647 \u0627\u0644\u0635\u0641\u062d\u0629<\/strong>&nbsp;&gt;&gt;&gt;&nbsp;<a href=\"https:\/\/dmdwarrior.com\/ar\/dmd-therapies\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u062c\u0645\u064a\u0639 \u0627\u0644\u062a\u062c\u0627\u0631\u0628 \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629 \u0644\u0645\u0631\u0636 \u062f\u0648\u0634\u064a\u0646<\/a><\/p>","protected":false},"excerpt":{"rendered":"<p>The ENHANCE study is a Phase 4 clinical trial designed to evaluate the real-world safety and effectiveness of ELEVIDYS in patients with Duchenne muscular dystrophy (DMD). This study is particularly important because it focuses on patients treated in a post-marketing setting, meaning after the therapy has already been approved and is being used in clinical [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":7684,"comment_status":"open","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[27],"tags":[137,33,179,702,61,65,703],"class_list":["post-7683","post","type-post","status-publish","format-standard","has-post-thumbnail","category-research","tag-clinical-trial","tag-elevidys","tag-elevidys-gene-therapy","tag-enhance","tag-gene-therapy","tag-sarepta","tag-sirolimus"],"_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/posts\/7683","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/comments?post=7683"}],"version-history":[{"count":1,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/posts\/7683\/revisions"}],"predecessor-version":[{"id":7685,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/posts\/7683\/revisions\/7685"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/media\/7684"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/media?parent=7683"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/categories?post=7683"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/tags?post=7683"}],"curies":[{"name":"\u0648\u0648\u0631\u062f\u0628\u0631\u064a\u0633","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}