{"id":6742,"date":"2026-03-11T21:55:54","date_gmt":"2026-03-11T18:55:54","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=6742"},"modified":"2026-03-11T21:59:30","modified_gmt":"2026-03-11T18:59:30","slug":"regenxbio-phase-1-2-affinity-duchenne-trial-of-rgx-202","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/ar\/regenxbio-phase-1-2-affinity-duchenne-trial-of-rgx-202\/","title":{"rendered":"\u0623\u0639\u0644\u0646\u062a \u0634\u0631\u0643\u0629 Regenxbio \u0639\u0646 \u0628\u064a\u0627\u0646\u0627\u062a \u0623\u0648\u0644\u064a\u0629 \u0625\u064a\u062c\u0627\u0628\u064a\u0629 \u062c\u062f\u064a\u062f\u0629 \u0645\u0646 \u0627\u0644\u0645\u0631\u062d\u0644\u0629 \u0627\u0644\u0623\u0648\u0644\u0649\/\u0627\u0644\u062b\u0627\u0646\u064a\u0629 \u0645\u0646 \u062a\u062c\u0631\u0628\u0629 Affinity Duchenne \u0644\u0639\u0642\u0627\u0631 Rgx-202"},"content":{"rendered":"<p class=\"wp-block-paragraph\"><strong>\u0623\u0639\u0644\u0646\u062a \u0634\u0631\u0643\u0629 REGENXBIO \u0639\u0646 \u0628\u064a\u0627\u0646\u0627\u062a \u0645\u0624\u0642\u062a\u0629 \u0625\u064a\u062c\u0627\u0628\u064a\u0629 \u062c\u062f\u064a\u062f\u0629 \u0645\u0646 \u0627\u0644\u0645\u0631\u062d\u0644\u0629 \u0627\u0644\u0623\u0648\u0644\u0649\/\u0627\u0644\u062b\u0627\u0646\u064a\u0629 \u0645\u0646 \u062a\u062c\u0631\u0628\u0629 AFFINITY DUCHENNE \u0644\u0640 RGX-202\u060c \u0648\u0647\u0648 \u0639\u0644\u0627\u062c \u062c\u064a\u0646\u064a \u0645\u062d\u062a\u0645\u0644 \u0647\u0648 \u0627\u0644\u0623\u0641\u0636\u0644 \u0641\u064a \u0641\u0626\u062a\u0647 \u0644\u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a.<\/strong> \u062a\u0642\u062f\u0645 \u0627\u0644\u062f\u0643\u062a\u0648\u0631\u0629 \u0643\u0627\u0631\u0648\u0644\u064a\u0646\u0627 \u062a\u064a\u0633\u064a-\u0631\u0648\u0634\u0627\u060c \u0623\u0633\u062a\u0627\u0630\u0629 \u0639\u0644\u0645 \u0627\u0644\u0623\u0639\u0635\u0627\u0628 \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629 \u0641\u064a \u0643\u0644\u064a\u0629 \u0627\u0644\u0637\u0628 \u0628\u062c\u0627\u0645\u0639\u0629 \u0633\u062a\u0627\u0646\u0641\u0648\u0631\u062f\u060c \u0648\u0645\u0624\u0633\u0633\u0629 \u0633\u062a\u0627\u0646\u0641\u0648\u0631\u062f \u0644\u0635\u062d\u0629 \u0627\u0644\u0623\u0637\u0641\u0627\u0644\u060c \u0647\u0630\u0647 \u0627\u0644\u0628\u064a\u0627\u0646\u0627\u062a\u060c \u0628\u0645\u0627 \u0641\u064a \u0630\u0644\u0643 \u0645\u0642\u0627\u064a\u064a\u0633 \u062c\u062f\u064a\u062f\u0629 \u0644\u0644\u0648\u0638\u0627\u0626\u0641 \u0648\u0627\u0644\u0633\u0644\u0627\u0645\u0629 \u0648\u0627\u0644\u0645\u0624\u0634\u0631\u0627\u062a \u0627\u0644\u062d\u064a\u0648\u064a\u0629 \u0648\u0627\u0644\u062a\u0635\u0648\u064a\u0631 \u0628\u0627\u0644\u0631\u0646\u064a\u0646 \u0627\u0644\u0645\u063a\u0646\u0627\u0637\u064a\u0633\u064a \u0644\u0644\u0642\u0644\u0628\u060c \u0641\u064a \u0627\u0644\u0645\u0624\u062a\u0645\u0631 \u0627\u0644\u0633\u0631\u064a\u0631\u064a \u0648\u0627\u0644\u0639\u0644\u0645\u064a \u0644\u062c\u0645\u0639\u064a\u0629 \u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a (MDA). \u0644\u0644\u0645\u0632\u064a\u062f \u0645\u0646 \u0627\u0644\u0645\u0639\u0644\u0648\u0645\u0627\u062a:\u00a0<a href=\"https:\/\/dmdwarrior.com\/ar\/biomarkers-in-duchenne-muscular-dystrophy\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u0627\u0644\u0645\u0624\u0634\u0631\u0627\u062a \u0627\u0644\u062d\u064a\u0648\u064a\u0629<\/a><\/p>\n\n\n\n<div class=\"wp-block-rank-math-toc-block\" id=\"rank-math-toc\"><h2>\u062c\u062f\u0648\u0644 \u0627\u0644\u0645\u062d\u062a\u0648\u064a\u0627\u062a<\/h2><nav><ul><li><a href=\"#affinity-duchenne-phase-i-ii-interim-data-updates-data-cut-january-5-2026\">\u062a\u062d\u062f\u064a\u062b\u0627\u062a \u0627\u0644\u0628\u064a\u0627\u0646\u0627\u062a \u0627\u0644\u0645\u0624\u0642\u062a\u0629 \u0644\u0644\u0645\u0631\u062d\u0644\u062a\u064a\u0646 \u0627\u0644\u0623\u0648\u0644\u0649 \u0648\u0627\u0644\u062b\u0627\u0646\u064a\u0629 \u0645\u0646 \u062f\u0631\u0627\u0633\u0629 AFFINITY DUCHENN (\u062a\u0627\u0631\u064a\u062e \u0642\u0637\u0639 \u0627\u0644\u0628\u064a\u0627\u0646\u0627\u062a: 5 \u064a\u0646\u0627\u064a\u0631 2026)<\/a><ul><li><a href=\"#functional-data\">\u0627\u0644\u0628\u064a\u0627\u0646\u0627\u062a \u0627\u0644\u0648\u0638\u064a\u0641\u064a\u0629<\/a><\/li><li><a href=\"#cardiac-function\">\u0648\u0638\u0627\u0626\u0641 \u0627\u0644\u0642\u0644\u0628<\/a><\/li><li><a href=\"#biomarker-data\">\u0628\u064a\u0627\u0646\u0627\u062a \u0627\u0644\u0645\u0624\u0634\u0631\u0627\u062a \u0627\u0644\u062d\u064a\u0648\u064a\u0629<\/a><\/li><li><a href=\"#safety-and-tolerability-data\">\u0628\u064a\u0627\u0646\u0627\u062a \u0627\u0644\u0633\u0644\u0627\u0645\u0629 \u0648\u0627\u0644\u062a\u062d\u0645\u0644<\/a><\/li><li><a href=\"#affinity-duchenne-trial\">\u0645\u062d\u0627\u0643\u0645\u0629 \u0623\u0641\u064a\u0646\u064a\u062a\u064a \u062f\u0648\u0634\u064a\u0646<\/a><\/li><\/ul><\/li><\/ul><\/nav><\/div>\n\n\n\n<p class=\"wp-block-paragraph\">\u201c&quot;\u062a\u064f\u0638\u0647\u0631 \u0627\u0644\u0628\u064a\u0627\u0646\u0627\u062a \u0627\u0644\u0645\u0624\u0642\u062a\u0629 \u0627\u0644\u062c\u062f\u064a\u062f\u0629 \u0644\u0644\u0645\u0631\u062d\u0644\u062a\u064a\u0646 \u0627\u0644\u0623\u0648\u0644\u0649 \u0648\u0627\u0644\u062b\u0627\u0646\u064a\u0629 \u0627\u0644\u064a\u0648\u0645 \u0627\u0633\u062a\u0645\u0631\u0627\u0631 \u0627\u0644\u062a\u0623\u062b\u064a\u0631 \u0627\u0644\u0625\u064a\u062c\u0627\u0628\u064a \u0639\u0644\u0649 \u0648\u0638\u0627\u0626\u0641 \u0627\u0644\u0642\u0644\u0628\u060c \u0648\u0627\u0633\u062a\u0642\u0631\u0627\u0631 \u0635\u062d\u0629 \u0627\u0644\u0642\u0644\u0628\u060c \u0648\u0645\u0644\u0641 \u0623\u0645\u0627\u0646 \u0645\u064f\u0631\u0636\u064d\u060c \u0645\u0645\u0627 \u064a\u064f\u0628\u0631\u0632 \u0625\u0645\u0643\u0627\u0646\u064a\u0629 \u0627\u0639\u062a\u0628\u0627\u0631 RGX-202 \u062e\u064a\u0627\u0631\u064b\u0627 \u0639\u0644\u0627\u062c\u064a\u064b\u0627 \u062c\u064a\u0646\u064a\u064b\u0627 \u0645\u062a\u0645\u064a\u0632\u064b\u0627 \u0644\u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a&quot;\u060c \u0635\u0631\u0651\u062d \u0628\u0630\u0644\u0643 \u0627\u0644\u062f\u0643\u062a\u0648\u0631 \u0633\u062a\u064a\u0641 \u0628\u0627\u0643\u0648\u0644\u0627\u060c \u0643\u0628\u064a\u0631 \u0627\u0644\u0645\u0633\u0624\u0648\u0644\u064a\u0646 \u0627\u0644\u0637\u0628\u064a\u064a\u0646 \u0641\u064a \u0634\u0631\u0643\u0629 REGENXBIO. \u0648\u0623\u0636\u0627\u0641: &quot;\u0625\u0646 \u0646\u0647\u062c\u0646\u0627 \u0627\u0644\u0627\u0633\u062a\u0628\u0627\u0642\u064a \u0648\u0627\u0644\u0634\u0627\u0645\u0644 \u0641\u064a \u0645\u062c\u0627\u0644 \u0627\u0644\u0633\u0644\u0627\u0645\u0629\u060c \u0628\u0627\u0644\u0625\u0636\u0627\u0641\u0629 \u0625\u0644\u0649 \u062a\u0631\u0643\u064a\u0628\u062a\u0646\u0627 \u0627\u0644\u0645\u0628\u062a\u0643\u0631\u0629 \u0645\u0646 \u0627\u0644\u0645\u064a\u0643\u0631\u0648\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646\u060c \u0645\u062f\u0639\u0648\u0645\u064c \u0628\u0627\u0644\u0633\u0644\u0627\u0645\u0629 \u0627\u0644\u0645\u0633\u062a\u062f\u0627\u0645\u0629 \u0648\u0627\u0644\u0646\u062a\u0627\u0626\u062c \u0627\u0644\u0648\u0638\u064a\u0641\u064a\u0629 \u0627\u0644\u062f\u0627\u0626\u0645\u0629 \u0639\u0644\u0649 \u0645\u062f\u0627\u0631 \u0639\u0627\u0645\u064a\u0646 \u0628\u0639\u062f \u0627\u0644\u0639\u0644\u0627\u062c. \u0648\u0645\u0639 \u0627\u0642\u062a\u0631\u0627\u0628\u0646\u0627 \u0645\u0646 \u0646\u0634\u0631 \u0646\u062a\u0627\u0626\u062c\u0646\u0627 \u0627\u0644\u0645\u062d\u0648\u0631\u064a\u0629 \u0627\u0644\u0631\u0626\u064a\u0633\u064a\u0629 \u0641\u064a \u0623\u0648\u0627\u0626\u0644 \u0627\u0644\u0631\u0628\u0639 \u0627\u0644\u062b\u0627\u0646\u064a\u060c \u0641\u0625\u0646\u0646\u0627 \u0646\u0634\u0639\u0631 \u0628\u062a\u0641\u0627\u0624\u0644 \u0643\u0628\u064a\u0631 \u0625\u0632\u0627\u0621 \u0647\u0630\u0647 \u0627\u0644\u0628\u064a\u0627\u0646\u0627\u062a \u0627\u0644\u062c\u062f\u064a\u062f\u0629 \u0627\u0644\u0634\u0627\u0645\u0644\u0629 \u0648\u0641\u0631\u0635\u0629 \u062a\u0637\u0648\u064a\u0631 RGX-202 \u0643\u062e\u064a\u0627\u0631 \u0639\u0644\u0627\u062c\u064a \u0641\u0639\u0651\u0627\u0644 \u0644\u0644\u0645\u0631\u0636\u0649&quot;.\u201d<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u201c&quot;\u0645\u0631\u0636 \u062f\u0648\u0634\u064a\u0646 \u0645\u0631\u0636\u064c \u0645\u064f\u0646\u0647\u0643\u064c \u0648\u0645\u064f\u062a\u064e\u0646\u064e\u0643\u0650\u0651\u0633\u064c \u064a\u064f\u0641\u0642\u062f \u0627\u0644\u0623\u0637\u0641\u0627\u0644 \u0642\u0648\u0629 \u0639\u0636\u0644\u0627\u062a\u0647\u0645 \u0648\u0627\u0633\u062a\u0642\u0644\u0627\u0644\u064a\u062a\u0647\u0645 \u0645\u0639 \u0645\u0631\u0648\u0631 \u0627\u0644\u0648\u0642\u062a\u060c \u0648\u064a\u0633\u0631\u0646\u064a \u0623\u0646 \u0623\u0631\u0649 \u0627\u0633\u062a\u0645\u0631\u0627\u0631 \u0633\u0644\u0627\u0645\u0629 \u062f\u0648\u0627\u0621 RGX-202 \u0648\u0641\u0639\u0627\u0644\u064a\u062a\u0647 \u0627\u0644\u0645\u064f\u0634\u062c\u0650\u0651\u0639\u0629&quot;\u060c \u0635\u0631\u064e\u0651\u062d\u062a \u0627\u0644\u062f\u0643\u062a\u0648\u0631\u0629 \u062a\u064a\u0633\u064a-\u0631\u0648\u0634\u0627. &quot;\u062a\u064f\u0642\u062f\u0650\u0651\u0645 \u0647\u0630\u0647 \u0627\u0644\u0628\u064a\u0627\u0646\u0627\u062a \u0627\u0644\u0625\u064a\u062c\u0627\u0628\u064a\u0629 \u0645\u0646 \u0627\u0644\u0645\u0631\u062d\u0644\u062a\u064a\u0646 \u0627\u0644\u0623\u0648\u0644\u0649 \u0648\u0627\u0644\u062b\u0627\u0646\u064a\u0629\u060c \u0628\u0645\u0627 \u0641\u064a \u0630\u0644\u0643 \u0646\u062a\u0627\u0626\u062c \u0627\u0644\u0645\u0624\u0634\u0631\u0627\u062a \u0627\u0644\u062d\u064a\u0648\u064a\u0629\u060c \u0648\u0627\u0644\u062a\u062d\u0633\u064f\u0651\u0646 \u0627\u0644\u0648\u0638\u064a\u0641\u064a\u060c \u0648\u0627\u0633\u062a\u0642\u0631\u0627\u0631 \u0627\u0644\u0642\u0644\u0628\u060c \u0648\u0633\u0644\u0627\u0645\u0629 \u0627\u0644\u0643\u0628\u062f\u060c \u0635\u0648\u0631\u0629\u064b \u0623\u0648\u0636\u062d \u0639\u0646 \u0627\u0644\u062a\u0623\u062b\u064a\u0631 \u0627\u0644\u0645\u064f\u062d\u062a\u0645\u0644 \u0644\u062f\u0648\u0627\u0621 RGX-202 \u0639\u0644\u0649 \u0627\u0644\u0645\u0624\u0634\u0631\u0627\u062a \u0627\u0644\u0635\u062d\u064a\u0629 \u0627\u0644\u0631\u0626\u064a\u0633\u064a\u0629 \u0641\u064a \u0645\u0631\u0636 \u062f\u0648\u0634\u064a\u0646.&quot;\u201d<\/p>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"affinity-duchenne-phase-i-ii-interim-data-updates-data-cut-january-5-2026\">\u062a\u062d\u062f\u064a\u062b\u0627\u062a \u0627\u0644\u0628\u064a\u0627\u0646\u0627\u062a \u0627\u0644\u0645\u0624\u0642\u062a\u0629 \u0644\u0644\u0645\u0631\u062d\u0644\u062a\u064a\u0646 \u0627\u0644\u0623\u0648\u0644\u0649 \u0648\u0627\u0644\u062b\u0627\u0646\u064a\u0629 \u0645\u0646 \u062f\u0631\u0627\u0633\u0629 AFFINITY DUCHENN (\u062a\u0627\u0631\u064a\u062e \u0642\u0637\u0639 \u0627\u0644\u0628\u064a\u0627\u0646\u0627\u062a: 5 \u064a\u0646\u0627\u064a\u0631 2026)<\/h2>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"functional-data\">\u0627\u0644\u0628\u064a\u0627\u0646\u0627\u062a \u0627\u0644\u0648\u0638\u064a\u0641\u064a\u0629<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u0641\u064a \u0627\u0644\u0646\u062a\u0627\u0626\u062c \u0627\u0644\u0648\u0638\u064a\u0641\u064a\u0629 \u0627\u0644\u0645\u0624\u0642\u062a\u0629 \u0645\u0646 \u0633\u0628\u0639\u0629 \u0645\u0634\u0627\u0631\u0643\u064a\u0646 \u0639\u0648\u0644\u062c\u0648\u0627 \u0628\u0645\u0633\u062a\u0648\u0649 \u0627\u0644\u062c\u0631\u0639\u0629 \u0627\u0644\u0645\u062d\u0648\u0631\u064a\u0629 (2\u00d71014 GC\/kg)\u060c \u0648\u0627\u0644\u0630\u064a\u0646 \u062a\u062a\u0631\u0627\u0648\u062d \u0623\u0639\u0645\u0627\u0631\u0647\u0645 \u0628\u064a\u0646 6 \u0648 12 \u0639\u0627\u0645\u064b\u0627 \u062a\u0642\u0631\u064a\u0628\u064b\u0627 \u0639\u0646\u062f \u0625\u0639\u0637\u0627\u0621 \u0627\u0644\u062c\u0631\u0639\u0629\u060c \u064a\u0633\u062a\u0645\u0631 RGX-202 \u0641\u064a \u0625\u0638\u0647\u0627\u0631 \u062f\u0644\u064a\u0644 \u0639\u0644\u0649 \u0627\u0644\u062a\u0623\u062b\u064a\u0631 \u0627\u0644\u0625\u064a\u062c\u0627\u0628\u064a \u0639\u0644\u0649 \u0645\u0633\u0627\u0631 \u0627\u0644\u0645\u0631\u0636 \u0641\u064a \u062a\u0642\u064a\u064a\u0645 \u0646\u0648\u0631\u062b \u0633\u062a\u0627\u0631 \u0644\u0644\u0645\u0634\u064a (NSAA) \u0648\u062c\u0645\u064a\u0639 \u0627\u062e\u062a\u0628\u0627\u0631\u0627\u062a \u0627\u0644\u0648\u0638\u0627\u0626\u0641 \u0627\u0644\u0645\u062d\u062f\u062f\u0629 \u0628\u0648\u0642\u062a (\u0648\u0642\u062a \u0627\u0644\u0648\u0642\u0648\u0641\u060c \u0648\u0627\u0644\u0645\u0634\u064a \u0648\u0627\u0644\u062c\u0631\u064a \u0644\u0645\u0633\u0627\u0641\u0629 10 \u0623\u0645\u062a\u0627\u0631\u060c \u0648\u0648\u0642\u062a \u0627\u0644\u062a\u0633\u0644\u0642) \u0628\u0639\u062f \u0639\u0627\u0645 \u0648\u0627\u062d\u062f.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u062a\u0645 \u062a\u062d\u0644\u064a\u0644 \u0627\u0644\u0646\u062a\u0627\u0626\u062c \u0627\u0644\u0648\u0638\u064a\u0641\u064a\u0629 \u0628\u0627\u0633\u062a\u062e\u062f\u0627\u0645 \u0639\u062f\u0629 \u0637\u0631\u0642 \u0645\u0639\u062a\u0645\u062f\u0629 \u0644\u062a\u0642\u062f\u064a\u0631 \u062a\u0637\u0648\u0631 \u0627\u0644\u0645\u0631\u0636 \u0627\u0644\u0645\u062a\u0648\u0642\u0639 \u0641\u064a \u062d\u0627\u0644 \u0639\u062f\u0645 \u062a\u0644\u0642\u064a \u0627\u0644\u0639\u0644\u0627\u062c\u060c \u0628\u0645\u0627 \u0641\u064a \u0630\u0644\u0643 \u0646\u0645\u0648\u0630\u062c \u062a\u0637\u0648\u0631 \u0627\u0644\u0645\u0631\u0636 cTAP \u0648\u0645\u0642\u0627\u0631\u0646\u0627\u062a \u0627\u0644\u062a\u062d\u0643\u0645 \u0627\u0644\u062e\u0627\u0631\u062c\u064a\u0629 \u0628\u0627\u0633\u062a\u062e\u062f\u0627\u0645 \u0627\u0644\u0645\u0637\u0627\u0628\u0642\u0629 \u0627\u0644\u062f\u0642\u064a\u0642\u0629 \u0627\u0644\u0645\u064f\u062d\u0633\u0651\u0646\u0629 \u0648\u062a\u0631\u062c\u064a\u062d \u062f\u0631\u062c\u0629 \u0627\u0644\u0645\u064a\u0644. \u064a\u064f\u0639\u062f \u062a\u0631\u062c\u064a\u062d \u062f\u0631\u062c\u0629 \u0627\u0644\u0645\u064a\u0644 \u0637\u0631\u064a\u0642\u0629 \u0627\u0644\u062a\u062d\u0644\u064a\u0644 \u0627\u0644\u0623\u0633\u0627\u0633\u064a\u0629 \u0627\u0644\u0645\u062d\u062f\u062f\u0629 \u0641\u064a \u062e\u0637\u0629 \u0627\u0644\u062a\u062d\u0644\u064a\u0644 \u0627\u0644\u062a\u0643\u0645\u064a\u0644\u064a\u0629 \u0644\u0644\u062a\u062c\u0631\u0628\u0629 \u0627\u0644\u0645\u062d\u0648\u0631\u064a\u0629.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0623\u0638\u0647\u0631 \u0627\u0644\u0645\u0634\u0627\u0631\u0643\u0648\u0646 \u0627\u0644\u0630\u064a\u0646 \u062a\u0644\u0642\u0648\u0627 \u0627\u0644\u062c\u0631\u0639\u0629 \u0627\u0644\u0645\u062d\u0648\u0631\u064a\u0629 \u062a\u062d\u0633\u0646\u0627\u064b \u0641\u064a \u0627\u0644\u0623\u062f\u0627\u0621 \u0641\u064a \u062c\u0645\u064a\u0639 \u0627\u062e\u062a\u0628\u0627\u0631\u0627\u062a \u0627\u0644\u0648\u0638\u0627\u0626\u0641 \u0627\u0644\u0645\u062d\u062f\u062f\u0629 \u0628\u0648\u0642\u062a \u0648\u0627\u062e\u062a\u0628\u0627\u0631 NSAA \u0645\u0642\u0627\u0631\u0646\u0629\u064b \u0628\u0627\u0644\u0645\u062c\u0645\u0648\u0639\u0629 \u0627\u0644\u0636\u0627\u0628\u0637\u0629 \u0627\u0644\u062e\u0627\u0631\u062c\u064a\u0629 \u0628\u0627\u0633\u062a\u062e\u062f\u0627\u0645 \u062a\u0631\u062c\u064a\u062d \u062f\u0631\u062c\u0629 \u0627\u0644\u0645\u064a\u0644. \u0648\u062a\u0634\u064a\u0631 \u0641\u062a\u0631\u0629 \u0627\u0644\u062b\u0642\u0629 95% \u0625\u0644\u0649 \u062a\u0641\u0636\u064a\u0644 RGX-202.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0641\u064a \u0645\u062c\u0645\u0648\u0639\u0629 NSAA\u060c \u062a\u062c\u0627\u0648\u0632\u062a \u0646\u062a\u0627\u0626\u062c \u0627\u0644\u0645\u0634\u0627\u0631\u0643\u064a\u0646 \u0627\u0644\u0630\u064a\u0646 \u062a\u0644\u0642\u0648\u0627 \u0627\u0644\u062c\u0631\u0639\u0629 \u0627\u0644\u0645\u062d\u0648\u0631\u064a\u0629 \u0645\u0633\u0627\u0631 \u0627\u0644\u0645\u0631\u0636 \u0627\u0644\u0645\u062a\u0648\u0642\u0639 \u0648\u0645\u062c\u0645\u0648\u0639\u0627\u062a \u0627\u0644\u0645\u0642\u0627\u0631\u0646\u0629 \u0627\u0644\u062e\u0627\u0631\u062c\u064a\u0629. \u0648\u0627\u0644\u062c\u062f\u064a\u0631 \u0628\u0627\u0644\u0630\u0643\u0631 \u0623\u0646 \u062e\u0645\u0633\u0629 \u0645\u0646 \u0627\u0644\u0645\u0634\u0627\u0631\u0643\u064a\u0646 \u0627\u0644\u0633\u0628\u0639\u0629 \u0643\u0627\u0646\u0648\u0627 \u0641\u064a \u0633\u0646 \u0627\u0644\u062b\u0627\u0645\u0646\u0629 \u0623\u0648 \u0623\u0643\u0628\u0631 \u0639\u0646\u062f \u0628\u062f\u0621 \u0627\u0644\u0639\u0644\u0627\u062c\u060c \u0648\u0647\u064a \u0627\u0644\u0641\u062a\u0631\u0629 \u0627\u0644\u062a\u064a \u064a\u064f\u062a\u0648\u0642\u0639 \u0641\u064a\u0647\u0627 \u062d\u062f\u0648\u062b \u062a\u062f\u0647\u0648\u0631 \u0648\u0638\u064a\u0641\u064a. \u0628\u0639\u062f \u0645\u0631\u0648\u0631 \u0639\u0627\u0645\u060c \u062a\u062d\u0633\u0646\u062a \u062d\u0627\u0644\u0629 \u0627\u0644\u0645\u0634\u0627\u0631\u0643\u064a\u0646 (\u0646=7) \u0628\u0645\u0639\u062f\u0644 4.9 \u0646\u0642\u0637\u0629 \u0645\u0642\u0627\u0631\u0646\u0629\u064b \u0628\u0645\u062c\u0645\u0648\u0639\u0629 cTAP. \u0623\u0645\u0627 \u0627\u0644\u0645\u0634\u0627\u0631\u0643\u0648\u0646 \u0627\u0644\u0623\u0643\u0628\u0631 \u0633\u0646\u064b\u0627 (\u0646=5) \u0641\u0642\u062f \u062a\u062d\u0633\u0646\u062a \u062d\u0627\u0644\u062a\u0647\u0645 \u0628\u0645\u0639\u062f\u0644 5.2 \u0646\u0642\u0637\u0629 \u0645\u0642\u0627\u0631\u0646\u0629\u064b \u0628\u0645\u062c\u0645\u0648\u0639\u0629 cTAP.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0628\u0627\u0644\u0625\u0636\u0627\u0641\u0629 \u0625\u0644\u0649 \u0630\u0644\u0643\u060c \u062a\u062c\u0627\u0648\u0632 \u0627\u0644\u0645\u0634\u0627\u0631\u0643\u0648\u0646 \u0641\u064a \u0645\u0633\u062a\u0648\u0649 \u0627\u0644\u062c\u0631\u0639\u0629 1 (1\u00d71014 GC\/kg) (\u0646 = 3) \u0645\u0633\u0627\u0631 \u0627\u0644\u0645\u0631\u0636 \u0627\u0644\u0645\u062a\u0648\u0642\u0639 \u0648\u062a\u062d\u0633\u0646\u0648\u0627 \u0628\u0645\u0639\u062f\u0644 +5.6 \u0646\u0642\u0637\u0629 \u0645\u0642\u0627\u0631\u0646\u0629 \u0628\u0640 cTAP \u0628\u0639\u062f \u0639\u0627\u0645\u064a\u0646.<\/p>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"cardiac-function\">\u0648\u0638\u0627\u0626\u0641 \u0627\u0644\u0642\u0644\u0628<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u0623\u0638\u0647\u0631 \u0627\u0644\u0645\u0634\u0627\u0631\u0643\u0648\u0646 \u0641\u064a \u0627\u0644\u062c\u0631\u0639\u0629 \u0627\u0644\u0645\u062d\u0648\u0631\u064a\u0629 \u0627\u0633\u062a\u0642\u0631\u0627\u0631\u064b\u0627 \u0642\u0644\u0628\u064a\u064b\u0627 \u0628\u0639\u062f \u0639\u0627\u0645 \u0648\u0627\u062d\u062f \u0645\u0646 \u0627\u0644\u0639\u0644\u0627\u062c \u0643\u0645\u0627 \u062a\u0645 \u0642\u064a\u0627\u0633\u0647 \u0628\u0648\u0627\u0633\u0637\u0629 \u0646\u0642\u0627\u0637 \u0646\u0647\u0627\u064a\u0629 \u0627\u0644\u062a\u0635\u0648\u064a\u0631 \u0628\u0627\u0644\u0631\u0646\u064a\u0646 \u0627\u0644\u0645\u063a\u0646\u0627\u0637\u064a\u0633\u064a\u060c \u0628\u0645\u0627 \u0641\u064a \u0630\u0644\u0643 \u0645\u062a\u0648\u0633\u0637 \u0627\u0644\u0643\u0633\u0631 \u0627\u0644\u0642\u0630\u0641\u064a \u0644\u0644\u0628\u0637\u064a\u0646 \u0627\u0644\u0623\u064a\u0633\u0631\u060c \u0648\u0627\u0644\u0625\u062c\u0647\u0627\u062f \u0627\u0644\u0645\u062d\u064a\u0637\u064a \u0627\u0644\u0639\u0627\u0644\u0645\u064a\u060c \u0648\u0627\u0644\u062a\u0644\u064a\u0641 \u0627\u0644\u0630\u064a \u062a\u0645 \u062a\u0642\u064a\u064a\u0645\u0647 \u0628\u0648\u0627\u0633\u0637\u0629 \u062a\u0639\u0632\u064a\u0632 \u0627\u0644\u063a\u0627\u062f\u0648\u0644\u064a\u0646\u064a\u0648\u0645 \u0627\u0644\u0645\u062a\u0623\u062e\u0631.<\/p>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"biomarker-data\">\u0628\u064a\u0627\u0646\u0627\u062a \u0627\u0644\u0645\u0624\u0634\u0631\u0627\u062a \u0627\u0644\u062d\u064a\u0648\u064a\u0629<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u0644\u0627 \u062a\u0632\u0627\u0644 \u0628\u064a\u0627\u0646\u0627\u062a \u0627\u0644\u0645\u0624\u0634\u0631\u0627\u062a \u0627\u0644\u062d\u064a\u0648\u064a\u0629 \u0645\u0646 \u062f\u0631\u0627\u0633\u0629 \u0627\u0644\u0645\u0631\u062d\u0644\u0629 \u0627\u0644\u0623\u0648\u0644\u0649\/\u0627\u0644\u062b\u0627\u0646\u064a\u0629 \u062a\u062f\u0639\u0645 \u0627\u0644\u062a\u0639\u0628\u064a\u0631 \u0627\u0644\u0639\u0627\u0644\u064a \u0648\u0627\u0644\u0645\u0633\u062a\u0645\u0631 \u0644\u0628\u0631\u0648\u062a\u064a\u0646 RGX-202 \u0645\u064a\u0643\u0631\u0648\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 (\u0646=13). \u0648\u0642\u062f \u0623\u0638\u0647\u0631\u062a \u0628\u064a\u0627\u0646\u0627\u062a \u062c\u062f\u064a\u062f\u0629 \u0645\u0646 \u0645\u0631\u064a\u0636 \u0625\u0636\u0627\u0641\u064a\u060c \u0643\u0627\u0646 \u0639\u0645\u0631\u0647 3.6 \u0633\u0646\u0648\u0627\u062a \u0639\u0646\u062f \u0628\u062f\u0621 \u0627\u0644\u0639\u0644\u0627\u062c\u060c \u0645\u0633\u062a\u0648\u0649 \u062a\u0639\u0628\u064a\u0631 \u0639\u0646 \u0628\u0631\u0648\u062a\u064a\u0646 RGX-202 \u0645\u064a\u0643\u0631\u0648\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0642\u062f\u0631\u0647 51.2% \u0641\u064a \u0627\u0644\u0623\u0633\u0628\u0648\u0639 12. \u0648\u062a\u062a\u0645\u062b\u0644 \u0646\u0642\u0637\u0629 \u0627\u0644\u0646\u0647\u0627\u064a\u0629 \u0627\u0644\u0623\u0648\u0644\u064a\u0629 \u0641\u064a \u0627\u0644\u0645\u0631\u062d\u0644\u0629 \u0627\u0644\u0645\u062d\u0648\u0631\u064a\u0629 \u0645\u0646 \u062f\u0631\u0627\u0633\u0629 AFFINITY DUCHENNE \u0641\u064a \u0646\u0633\u0628\u0629 \u0627\u0644\u0645\u0634\u0627\u0631\u0643\u064a\u0646 \u0627\u0644\u0630\u064a\u0646 \u064a\u0632\u064a\u062f \u0645\u0633\u062a\u0648\u0649 \u062a\u0639\u0628\u064a\u0631 \u0628\u0631\u0648\u062a\u064a\u0646 RGX-202 \u0645\u064a\u0643\u0631\u0648\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0644\u062f\u064a\u0647\u0645 \u0639\u0646 10% \u0641\u064a \u0627\u0644\u0623\u0633\u0628\u0648\u0639 12.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u062a\u0645 \u062a\u062d\u062f\u064a\u062f \u0645\u0648\u0642\u0639 RGX-202 \u0628\u0634\u0643\u0644 \u0645\u0646\u0627\u0633\u0628 \u0641\u064a \u063a\u0634\u0627\u0621 \u0627\u0644\u0644\u064a\u0641 \u0627\u0644\u0639\u0636\u0644\u064a\u060c \u0645\u0645\u0627 \u064a\u062f\u0644 \u0639\u0644\u0649 \u0623\u0646 \u0627\u0644\u062a\u0631\u0643\u064a\u0628 \u0627\u0644\u0645\u062a\u0645\u0627\u064a\u0632 \u0645\u0639 \u062a\u0636\u0645\u064a\u0646 \u0646\u0637\u0627\u0642 \u0627\u0644\u0637\u0631\u0641 \u0627\u0644\u0643\u0631\u0628\u0648\u0643\u0633\u064a\u0644\u064a (CT) \u064a\u0633\u062a\u0647\u062f\u0641 \u0627\u0644\u0639\u0636\u0644\u0629 \u0628\u0634\u0643\u0644 \u0645\u0646\u0627\u0633\u0628.<\/p>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"safety-and-tolerability-data\">\u0628\u064a\u0627\u0646\u0627\u062a \u0627\u0644\u0633\u0644\u0627\u0645\u0629 \u0648\u0627\u0644\u062a\u062d\u0645\u0644<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u0623\u0638\u0647\u0631\u062a \u0628\u064a\u0627\u0646\u0627\u062a \u0627\u0644\u0633\u0644\u0627\u0645\u0629 \u0627\u0644\u0645\u0624\u0642\u062a\u0629 \u0627\u0644\u062c\u062f\u064a\u062f\u0629\u060c \u0627\u0644\u0645\u0633\u062a\u0642\u0627\u0629 \u0645\u0646 \u062c\u0645\u064a\u0639 \u0627\u0644\u0645\u0634\u0627\u0631\u0643\u064a\u0646 \u0641\u064a \u0627\u0644\u0645\u0631\u062d\u0644\u0629 \u0627\u0644\u0623\u0648\u0644\u0649\/\u0627\u0644\u062b\u0627\u0646\u064a\u0629 \u0645\u0646 \u0627\u0644\u062a\u062c\u0627\u0631\u0628 \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629 \u0627\u0644\u0645\u062d\u0648\u0631\u064a\u0629\u060c \u0648\u0627\u0644\u0630\u064a\u0646 \u062a\u062a\u0631\u0627\u0648\u062d \u0623\u0639\u0645\u0627\u0631\u0647\u0645 \u0628\u064a\u0646 \u0633\u0646\u0629 \u0648\u0627\u062d\u062f\u0629 \u0648\u0623\u0642\u0644 \u0645\u0646 12 \u0633\u0646\u0629 \u0639\u0646\u062f \u062a\u0644\u0642\u064a\u0647\u0645 \u0627\u0644\u062c\u0631\u0639\u0629\u060c \u0639\u062f\u0645 \u0648\u062c\u0648\u062f \u0623\u064a \u062f\u0644\u064a\u0644 \u0639\u0644\u0649 \u0625\u0635\u0627\u0628\u0629 \u0627\u0644\u0643\u0628\u062f \u0648\u0641\u0642\u064b\u0627 \u0644\u0639\u062f\u0629 \u0645\u0642\u0627\u064a\u064a\u0633. \u0644\u0645 \u064a\u062a\u062c\u0627\u0648\u0632 \u0645\u062a\u0648\u0633\u0637 \u0625\u0646\u0632\u064a\u0645 \u063a\u0627\u0645\u0627 \u063a\u0644\u0648\u062a\u0627\u0645\u064a\u0644 \u062a\u0631\u0627\u0646\u0633\u0641\u064a\u0631\u0627\u0632 (GGT) \u0648\u0627\u0644\u0628\u064a\u0644\u064a\u0631\u0648\u0628\u064a\u0646 \u0627\u0644\u0643\u0644\u064a\u060c \u0648\u0647\u0645\u0627 \u0645\u0624\u0634\u0631\u0627\u0646 \u0645\u0639\u0631\u0648\u0641\u0627\u0646 \u0644\u0627\u0644\u062a\u0647\u0627\u0628 \u0627\u0644\u0643\u0628\u062f \u0641\u064a \u062f\u0648\u0634\u064a\u0646\u060c \u0627\u0644\u062d\u062f \u0627\u0644\u0623\u0639\u0644\u0649 \u0627\u0644\u0637\u0628\u064a\u0639\u064a \u062d\u062a\u0649 \u0633\u0646\u062a\u064a\u0646 \u0628\u0639\u062f \u0627\u0644\u0639\u0644\u0627\u062c. \u0644\u0648\u062d\u0638 \u0627\u0646\u062e\u0641\u0627\u0636 \u0645\u062a\u0648\u0633\u0637 \u0641\u064a \u0625\u0646\u0632\u064a\u0645 \u0643\u0631\u064a\u0627\u062a\u064a\u0646 \u0643\u064a\u0646\u0627\u0632 \u0628\u0639\u062f \u0633\u0646\u0629 \u0648\u0627\u062d\u062f\u0629 \u0645\u0646 \u0627\u0644\u0639\u0644\u0627\u062c (\u0646=8)\u060c \u0648\u062f\u064f\u0639\u0645 \u0630\u0644\u0643 \u0628\u0627\u0646\u062e\u0641\u0627\u0636\u0627\u062a \u0645\u062a\u0648\u0633\u0637\u0629 \u0641\u064a \u0625\u0646\u0632\u064a\u0645\u0627\u062a ALT (\u0646=7) \u0648AST (\u0646=7) \u0648LDH (\u0646=8).<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0623\u0638\u0647\u0631 RGX-202 \u062a\u062d\u0645\u0644\u0627\u064b \u062c\u064a\u062f\u0627\u064b\u060c \u062d\u064a\u062b \u0644\u0645 \u062a\u064f\u0633\u062c\u0651\u0644 \u0623\u064a \u0623\u062d\u062f\u0627\u062b \u0636\u0627\u0626\u0631\u0629 \u062e\u0637\u064a\u0631\u0629 \u0623\u0648 \u0623\u062d\u062f\u0627\u062b \u0636\u0627\u0626\u0631\u0629 \u0630\u0627\u062a \u0623\u0647\u0645\u064a\u0629 \u062e\u0627\u0635\u0629 \u0641\u064a \u062f\u0631\u0627\u0633\u0629 \u0627\u0644\u0645\u0631\u062d\u0644\u0629 \u0627\u0644\u0623\u0648\u0644\u0649\/\u0627\u0644\u062b\u0627\u0646\u064a\u0629 \u062d\u062a\u0649 \u062a\u0627\u0631\u064a\u062e \u062c\u0645\u0639 \u0627\u0644\u0628\u064a\u0627\u0646\u0627\u062a (\u0646=13). \u0634\u0645\u0644\u062a \u0627\u0644\u0623\u062d\u062f\u0627\u062b \u0627\u0644\u0636\u0627\u0626\u0631\u0629 \u0627\u0644\u0634\u0627\u0626\u0639\u0629 \u0627\u0644\u0645\u0631\u062a\u0628\u0637\u0629 \u0628\u0627\u0644\u062f\u0648\u0627\u0621 \u0627\u0644\u0642\u064a\u0621 \u0648\u0627\u0644\u062a\u0639\u0628 \u0648\u0627\u0644\u063a\u062b\u064a\u0627\u0646\u060c \u0648\u0647\u064a \u0623\u0639\u0631\u0627\u0636 \u0645\u062a\u0648\u0642\u0639\u0629 \u0639\u0627\u062f\u0629\u064b \u0645\u0639 \u0627\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u062c\u064a\u0646\u064a. \u0642\u062f \u064a\u064f\u0633\u0647\u0645 \u0646\u0638\u0627\u0645 \u062a\u0639\u062f\u064a\u0644 \u0627\u0644\u0645\u0646\u0627\u0639\u0629 \u0627\u0644\u0627\u0633\u062a\u0628\u0627\u0642\u064a \u0642\u0635\u064a\u0631 \u0627\u0644\u0623\u0645\u062f\u060c \u0628\u0627\u0644\u0625\u0636\u0627\u0641\u0629 \u0625\u0644\u0649 \u0627\u0644\u062a\u0631\u0643\u064a\u0628\u0629 \u0627\u0644\u0645\u062a\u0645\u064a\u0632\u0629 \u0648\u0645\u0633\u062a\u0648\u064a\u0627\u062a \u0646\u0642\u0627\u0621 \u0627\u0644\u0645\u0646\u062a\u062c \u0627\u0644\u0631\u0627\u0626\u062f\u0629 \u0641\u064a \u0627\u0644\u0635\u0646\u0627\u0639\u0629 \u0648\u0627\u0644\u062a\u064a \u062a\u062a\u062c\u0627\u0648\u0632 80% \u0645\u0646 \u0627\u0644\u0642\u0641\u064a\u0635\u0627\u062a \u0627\u0644\u0643\u0627\u0645\u0644\u0629\u060c \u0641\u064a \u062a\u0639\u0632\u064a\u0632 \u0633\u0644\u0627\u0645\u0629 RGX-202.<\/p>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"affinity-duchenne-trial\">\u0645\u062d\u0627\u0643\u0645\u0629 \u0623\u0641\u064a\u0646\u064a\u062a\u064a \u062f\u0648\u0634\u064a\u0646<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u062a\u062a\u0648\u0642\u0639 \u0634\u0631\u0643\u0629 REGENXBIO \u0645\u0634\u0627\u0631\u0643\u0629 \u0627\u0644\u0628\u064a\u0627\u0646\u0627\u062a \u0627\u0644\u0645\u062d\u0648\u0631\u064a\u0629 \u0627\u0644\u0631\u0626\u064a\u0633\u064a\u0629 \u0641\u064a \u0623\u0648\u0627\u0626\u0644 \u0627\u0644\u0631\u0628\u0639 \u0627\u0644\u062b\u0627\u0646\u064a \u0645\u0646 \u0639\u0627\u0645 2026 \u0648\u0637\u0644\u0628 \u0627\u062c\u062a\u0645\u0627\u0639 \u062a\u0645\u0647\u064a\u062f\u064a \u0642\u0628\u0644 \u062a\u0642\u062f\u064a\u0645 \u0637\u0644\u0628 \u062a\u0631\u062e\u064a\u0635 \u0627\u0644\u0645\u0646\u062a\u062c \u0627\u0644\u0628\u064a\u0648\u0644\u0648\u062c\u064a (BLA) \u0645\u0639 FDA \u0641\u064a \u0645\u0646\u062a\u0635\u0641 \u0639\u0627\u0645 2026. \u0648\u062a\u0648\u0627\u0635\u0644 \u0627\u0644\u0634\u0631\u0643\u0629 \u062a\u0633\u062c\u064a\u0644 \u062d\u0648\u0627\u0644\u064a 30 \u0645\u0634\u0627\u0631\u0643\u064b\u0627 \u0645\u0645\u0646 \u062a\u0628\u0644\u063a \u0623\u0639\u0645\u0627\u0631\u0647\u0645 \u0633\u0646\u0629 \u0648\u0627\u062d\u062f\u0629 \u0641\u0623\u0643\u062b\u0631 \u0641\u064a \u0627\u0644\u062a\u062c\u0631\u0628\u0629 \u0627\u0644\u062a\u0623\u0643\u064a\u062f\u064a\u0629 \u0644\u0640 RGX-202 \u0648\u062a\u062a\u0648\u0642\u0639 \u0623\u0646 \u064a\u0643\u0648\u0646 \u0645\u0639\u0638\u0645 \u0627\u0644\u0645\u0634\u0627\u0631\u0643\u064a\u0646 \u0641\u064a \u0647\u0630\u0647 \u0627\u0644\u062a\u062c\u0631\u0628\u0629 \u0645\u0633\u062c\u0644\u064a\u0646 \u0648\u0642\u062a \u062a\u0642\u062f\u064a\u0645 \u0637\u0644\u0628 \u062a\u0631\u062e\u064a\u0635 \u0627\u0644\u0645\u0646\u062a\u062c \u0627\u0644\u0628\u064a\u0648\u0644\u0648\u062c\u064a (BLA).<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u062a\u0627\u0628\u0639 \u0647\u0630\u0647 \u0627\u0644\u0635\u0641\u062d\u0629<\/strong>&nbsp;&gt;&gt;&gt;&nbsp;<a href=\"https:\/\/dmdwarrior.com\/ar\/dmd-therapies\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u062c\u0645\u064a\u0639 \u0627\u0644\u062a\u062c\u0627\u0631\u0628 \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629 \u0644\u0645\u0631\u0636 \u062f\u0648\u0634\u064a\u0646<\/a><\/p>","protected":false},"excerpt":{"rendered":"<p>REGENXBIO announced new positive interim data from the Phase I\/II AFFINITY DUCHENNE trial of RGX-202, a potential best-in-class gene therapy for Duchenne muscular dystrophy. Trial investigator Carolina Tesi-Rocha, M.D., Clinical Professor, Neurology, Stanford School of Medicine, Stanford Children&#8217;s Health, is presenting this data, including new functional, safety, biomarker, and cardiac MRI measures, at the Muscular [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":6744,"comment_status":"open","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[281],"tags":[525,61,107,108],"class_list":["post-6742","post","type-post","status-publish","format-standard","has-post-thumbnail","category-press-releases","tag-affinity-duchenne","tag-gene-therapy","tag-regenxbio","tag-rgx-202"],"subtitle":"\u062a\u0634\u064a\u0631 \u0628\u064a\u0627\u0646\u0627\u062a \u0623\u0648\u0644\u064a\u0629 \u062c\u062f\u064a\u062f\u0629 \u0645\u0646 \u062a\u062c\u0631\u0628\u0629 AFFINITY DUCHENNE \u0625\u0644\u0649 \u0623\u0646 \u0627\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u062c\u064a\u0646\u064a RGX-202 \u0645\u0646 \u0634\u0631\u0643\u0629 REGENXBIO \u0642\u062f \u064a\u064f\u062d\u0633\u0651\u0646 \u0628\u0634\u0643\u0644\u064d \u0645\u0644\u062d\u0648\u0638 \u0648\u0638\u0627\u0626\u0641 \u0627\u0644\u062c\u0633\u0645 \u0648\u0627\u0644\u0645\u0624\u0634\u0631\u0627\u062a \u0627\u0644\u062d\u064a\u0648\u064a\u0629 \u0644\u062f\u0649 \u0645\u0631\u0636\u0649 \u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a. \u0643\u0645\u0627 \u0623\u0641\u0627\u062f \u0627\u0644\u0628\u0627\u062d\u062b\u0648\u0646 \u0628\u0646\u062a\u0627\u0626\u062c \u0642\u0644\u0628\u064a\u0629 \u0645\u0633\u062a\u0642\u0631\u0629 \u0648\u0645\u0644\u0641 \u0623\u0645\u0627\u0646 \u062c\u064a\u062f. \u062a\u064f\u0639\u0632\u0632 \u0647\u0630\u0647 \u0627\u0644\u0646\u062a\u0627\u0626\u062c \u0627\u0644\u062a\u0648\u0642\u0639\u0627\u062a \u0644\u0628\u064a\u0627\u0646\u0627\u062a \u0627\u0644\u062a\u062c\u0627\u0631\u0628 \u0627\u0644\u0645\u062d\u0648\u0631\u064a\u0629 \u0627\u0644\u0645\u064f\u0646\u062a\u0638\u0631\u0629 \u0641\u064a \u0639\u0627\u0645 2026.","_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/posts\/6742","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/comments?post=6742"}],"version-history":[{"count":0,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/posts\/6742\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/media\/6744"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/media?parent=6742"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/categories?post=6742"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/tags?post=6742"}],"curies":[{"name":"\u0648\u0648\u0631\u062f\u0628\u0631\u064a\u0633","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}