{"id":6720,"date":"2026-03-11T13:24:08","date_gmt":"2026-03-11T10:24:08","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=6720"},"modified":"2026-03-11T13:31:48","modified_gmt":"2026-03-11T10:31:48","slug":"genethon-gnt0004-creatine-kinase-ck-levels-and-nsaa-scores","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/ar\/genethon-gnt0004-creatine-kinase-ck-levels-and-nsaa-scores\/","title":{"rendered":"\u064a\u0624\u0643\u062f Genethon \u0641\u0639\u0627\u0644\u064a\u0629 \u0627\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u062c\u064a\u0646\u064a GNT0004 \u0644\u0645\u062f\u0629 \u0639\u0627\u0645\u064a\u0646 \u0645\u0639 \u062a\u062d\u0633\u0646 \u0641\u064a \u0645\u0633\u062a\u0648\u064a\u0627\u062a \u0627\u0644\u0643\u0631\u064a\u0627\u062a\u064a\u0646 \u0643\u064a\u0646\u0627\u0632 (CK) \u0648\u062f\u0631\u062c\u0627\u062a NSAA"},"content":{"rendered":"<p class=\"wp-block-paragraph\">\u064a\u0633\u062a\u0645\u0631 \u0627\u0644\u0628\u062d\u062b \u0641\u064a \u0645\u062c\u0627\u0644 \u0627\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u062c\u064a\u0646\u064a \u0644\u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a (DMD) \u0641\u064a \u0627\u0644\u062a\u0642\u062f\u0645. <strong>\u0641\u064a \u0627\u0644\u0645\u0624\u062a\u0645\u0631 \u0627\u0644\u0633\u0631\u064a\u0631\u064a \u0648\u0627\u0644\u0639\u0644\u0645\u064a \u0644\u062c\u0645\u0639\u064a\u0629 \u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0641\u064a \u0623\u0648\u0631\u0644\u0627\u0646\u062f\u0648\u060c \u0642\u062f\u0645\u062a \u0645\u0646\u0638\u0645\u0629 \u0627\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u062c\u064a\u0646\u064a \u0627\u0644\u0641\u0631\u0646\u0633\u064a\u0629 Genethon \u0628\u064a\u0627\u0646\u0627\u062a \u062c\u062f\u064a\u062f\u0629 \u0637\u0648\u064a\u0644\u0629 \u0627\u0644\u0623\u062c\u0644 \u062a\u064f\u0638\u0647\u0631 \u0623\u0646 \u0639\u0644\u0627\u062c\u0647\u0627 \u0627\u0644\u062a\u062c\u0631\u064a\u0628\u064a GNT0004 \u064a\u062d\u0627\u0641\u0638 \u0639\u0644\u0649 \u0641\u0648\u0627\u0626\u062f\u0647 \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629 \u0644\u0645\u062f\u0629 \u0639\u0627\u0645\u064a\u0646 \u0628\u0639\u062f \u0627\u0644\u0639\u0644\u0627\u062c.<\/strong><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0648\u062a\u0633\u0644\u0637 \u0627\u0644\u0646\u062a\u0627\u0626\u062c \u0627\u0644\u0636\u0648\u0621 \u0639\u0644\u0649 \u0627\u0644\u062a\u062d\u0633\u064a\u0646\u0627\u062a \u0641\u064a \u0627\u0644\u0648\u0638\u0627\u0626\u0641 \u0627\u0644\u062d\u0631\u0643\u064a\u0629\u060c \u0648\u0627\u0646\u062e\u0641\u0627\u0636 \u0627\u0644\u0645\u0624\u0634\u0631\u0627\u062a \u0627\u0644\u062d\u064a\u0648\u064a\u0629 \u0644\u062a\u0644\u0641 \u0627\u0644\u0639\u0636\u0644\u0627\u062a\u060c \u0648\u0645\u0644\u0641 \u0627\u0644\u0633\u0644\u0627\u0645\u0629 \u0627\u0644\u0645\u0648\u0627\u062a\u064a \u0644\u062f\u0649 \u0627\u0644\u0623\u0648\u0644\u0627\u062f \u0627\u0644\u0645\u0635\u0627\u0628\u064a\u0646 \u0628\u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a \u0627\u0644\u0630\u064a\u0646 \u062a\u0644\u0642\u0648\u0627 \u0627\u0644\u0639\u0644\u0627\u062c \u062e\u0644\u0627\u0644 \u0627\u0644\u0645\u0631\u062d\u0644\u0629 \u0627\u0644\u0623\u0648\u0644\u0649 \u0645\u0646 \u0627\u0644\u062a\u062c\u0631\u0628\u0629 \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629.<\/p>\n\n\n\n<div class=\"wp-block-rank-math-toc-block\" id=\"rank-math-toc\"><h2>\u062c\u062f\u0648\u0644 \u0627\u0644\u0645\u062d\u062a\u0648\u064a\u0627\u062a<\/h2><nav><ul><li><a href=\"#two-year-results-from-the-gnt-0004-clinical-trial\">\u0646\u062a\u0627\u0626\u062c \u0639\u0627\u0645\u064a\u0646 \u0645\u0646 \u0627\u0644\u062a\u062c\u0631\u0628\u0629 \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629 GNT0004<\/a><\/li><li><a href=\"#significant-improvement-in-nsaa-motor-function-scores\">\u062a\u062d\u0633\u0646 \u0645\u0644\u062d\u0648\u0638 \u0641\u064a \u0646\u062a\u0627\u0626\u062c \u0648\u0638\u0627\u0626\u0641 \u0627\u0644\u062d\u0631\u0643\u0629 \u0648\u0641\u0642\u064b\u0627 \u0644\u0645\u0642\u064a\u0627\u0633 NSAA<\/a><\/li><li><a href=\"#improvements-in-walking-tests\">\u062a\u062d\u0633\u064a\u0646\u0627\u062a \u0641\u064a \u0627\u062e\u062a\u0628\u0627\u0631\u0627\u062a \u0627\u0644\u0645\u0634\u064a<\/a><\/li><li><a href=\"#large-reduction-in-creatine-kinase-ck-levels\">\u0627\u0646\u062e\u0641\u0627\u0636 \u0643\u0628\u064a\u0631 \u0641\u064a \u0645\u0633\u062a\u0648\u064a\u0627\u062a \u0627\u0644\u0643\u0631\u064a\u0627\u062a\u064a\u0646 \u0643\u064a\u0646\u0627\u0632 (CK)<\/a><\/li><li><a href=\"#mri-imaging-shows-slower-disease-progression\">\u064a\u064f\u0638\u0647\u0631 \u0627\u0644\u062a\u0635\u0648\u064a\u0631 \u0628\u0627\u0644\u0631\u0646\u064a\u0646 \u0627\u0644\u0645\u063a\u0646\u0627\u0637\u064a\u0633\u064a \u062a\u0628\u0627\u0637\u0624\u064b\u0627 \u0641\u064a \u062a\u0637\u0648\u0631 \u0627\u0644\u0645\u0631\u0636.<\/a><\/li><li><a href=\"#favorable-safety-profile\">\u0645\u0644\u0641 \u0623\u0645\u0627\u0646 \u062c\u064a\u062f<\/a><\/li><li><a href=\"#pivotal-phase-of-the-trial-now-underway\">\u0627\u0644\u0645\u0631\u062d\u0644\u0629 \u0627\u0644\u0645\u062d\u0648\u0631\u064a\u0629 \u0645\u0646 \u0627\u0644\u0628\u062d\u062b \u062c\u0627\u0631\u064a\u0629 \u0627\u0644\u0622\u0646<\/a><\/li><li><a href=\"#why-these-results-matter\">\u0644\u0645\u0627\u0630\u0627 \u0647\u0630\u0647 \u0627\u0644\u0646\u062a\u0627\u0626\u062c \u0645\u0647\u0645\u0629\u061f<\/a><\/li><\/ul><\/nav><\/div>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"two-year-results-from-the-gnt-0004-clinical-trial\">\u0646\u062a\u0627\u0626\u062c \u0639\u0627\u0645\u064a\u0646 \u0645\u0646 \u0627\u0644\u062a\u062c\u0631\u0628\u0629 \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629 GNT0004<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u0634\u0645\u0644\u062a \u0627\u0644\u062f\u0631\u0627\u0633\u0629 \u0627\u0644\u062f\u0648\u0644\u064a\u0629 \u0645\u062a\u0639\u062f\u062f\u0629 \u0627\u0644\u0645\u0631\u0627\u0643\u0632 \u0623\u0648\u0644\u0627\u062f\u064b\u0627 \u0642\u0627\u062f\u0631\u064a\u0646 \u0639\u0644\u0649 \u0627\u0644\u0645\u0634\u064a \u062a\u062a\u0631\u0627\u0648\u062d \u0623\u0639\u0645\u0627\u0631\u0647\u0645 \u0628\u064a\u0646 6 \u0648 10 \u0633\u0646\u0648\u0627\u062a \u062a\u0645 \u062a\u0634\u062e\u064a\u0635 \u0625\u0635\u0627\u0628\u062a\u0647\u0645 \u0628\u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a.<\/strong><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u062e\u0644\u0627\u0644 \u0645\u0631\u062d\u0644\u0629 \u0632\u064a\u0627\u062f\u0629 \u0627\u0644\u062c\u0631\u0639\u0629\u060c \u062a\u0644\u0642\u0649 \u062e\u0645\u0633\u0629 \u0645\u0631\u0636\u0649 \u0627\u0644\u0639\u0644\u0627\u062c:<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u0623\u0631\u0628\u0639\u0629 \u0645\u0631\u0636\u0649 \u0641\u064a \u0641\u0631\u0646\u0633\u0627<\/li>\n\n\n\n<li>\u0645\u0631\u064a\u0636 \u0648\u0627\u062d\u062f \u0641\u064a \u0627\u0644\u0645\u0645\u0644\u0643\u0629 \u0627\u0644\u0645\u062a\u062d\u062f\u0629<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u062a\u0644\u0642\u0649 \u062b\u0644\u0627\u062b\u0629 \u0645\u0631\u0636\u0649 \u0627\u0644\u062c\u0631\u0639\u0629 \u0627\u0644\u0639\u0644\u0627\u062c\u064a\u0629 \u0627\u0644\u0628\u0627\u0644\u063a\u0629 3\u00d710\u00b9\u00b3 vg\/kg\u060c \u0648\u062a\u0634\u0643\u0644 \u0628\u064a\u0627\u0646\u0627\u062a \u0627\u0644\u0645\u062a\u0627\u0628\u0639\u0629 \u0637\u0648\u064a\u0644\u0629 \u0627\u0644\u0645\u062f\u0649 \u0627\u0644\u062e\u0627\u0635\u0629 \u0628\u0647\u0645 \u0623\u0633\u0627\u0633 \u0627\u0644\u062a\u062d\u0644\u064a\u0644 \u0627\u0644\u062c\u062f\u064a\u062f.<\/strong><\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u0648\u0628\u0639\u062f \u0639\u0627\u0645\u064a\u0646\u060c \u0623\u0638\u0647\u0631\u062a \u0627\u0644\u062f\u0631\u0627\u0633\u0629 \u0645\u0627 \u064a\u0644\u064a:<\/strong><\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u062a\u062d\u0633\u0646 \u0645\u0633\u062a\u0645\u0631 \u0641\u064a \u0627\u0644\u0648\u0638\u0627\u0626\u0641 \u0627\u0644\u062d\u0631\u0643\u064a\u0629<\/li>\n\n\n\n<li>\u0627\u0646\u062e\u0641\u0627\u0636 \u0627\u0644\u0645\u0624\u0634\u0631\u0627\u062a \u0627\u0644\u062d\u064a\u0648\u064a\u0629 \u0644\u062a\u0644\u0641 \u0627\u0644\u0639\u0636\u0644\u0627\u062a<\/li>\n\n\n\n<li>\u062a\u0637\u0648\u0631 \u0627\u0644\u0645\u0631\u0636 \u0628\u0634\u0643\u0644 \u0623\u0628\u0637\u0623<\/li>\n\n\n\n<li>\u0644\u0627 \u062a\u0648\u062c\u062f \u0645\u062e\u0627\u0648\u0641 \u0623\u0645\u0646\u064a\u0629 \u062e\u0637\u064a\u0631\u0629<\/li>\n<\/ul>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"significant-improvement-in-nsaa-motor-function-scores\">\u062a\u062d\u0633\u0646 \u0645\u0644\u062d\u0648\u0638 \u0641\u064a \u0646\u062a\u0627\u0626\u062c \u0648\u0638\u0627\u0626\u0641 \u0627\u0644\u062d\u0631\u0643\u0629 \u0648\u0641\u0642\u064b\u0627 \u0644\u0645\u0642\u064a\u0627\u0633 NSAA<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u062a\u0645 \u062a\u0642\u064a\u064a\u0645 \u0627\u0644\u0648\u0638\u0627\u0626\u0641 \u0627\u0644\u062d\u0631\u0643\u064a\u0629 \u0628\u0627\u0633\u062a\u062e\u062f\u0627\u0645 \u0645\u0642\u064a\u0627\u0633 \u0646\u0648\u0631\u062b \u0633\u062a\u0627\u0631 \u0644\u062a\u0642\u064a\u064a\u0645 \u0627\u0644\u0642\u062f\u0631\u0629 \u0639\u0644\u0649 \u0627\u0644\u0645\u0634\u064a (NSAA)\u060c \u0648\u0647\u0648 \u0645\u0642\u064a\u0627\u0633 \u0633\u0631\u064a\u0631\u064a \u0634\u0627\u0626\u0639 \u0627\u0644\u0627\u0633\u062a\u062e\u062f\u0627\u0645 \u0644\u0645\u0631\u0636\u0649 \u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0627\u0644\u062f\u0648\u0634\u064a\u0646\u064a \u0627\u0644\u0642\u0627\u062f\u0631\u064a\u0646 \u0639\u0644\u0649 \u0627\u0644\u0645\u0634\u064a. \u0644\u0644\u0645\u0632\u064a\u062f \u0645\u0646 \u0627\u0644\u0645\u0639\u0644\u0648\u0645\u0627\u062a: <a href=\"https:\/\/dmdwarrior.com\/ar\/north-star-ambulatory-assessment-nsaa-in-duchenne-dmd\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u062a\u0642\u064a\u064a\u0645 \u0646\u0648\u0631\u062b \u0633\u062a\u0627\u0631 \u0644\u0644\u0639\u064a\u0627\u062f\u0627\u062a \u0627\u0644\u062e\u0627\u0631\u062c\u064a\u0629 (NSAA) \u0641\u064a \u062f\u0648\u0634\u064a\u0646<\/a><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u062a\u0634\u0645\u0644 \u0627\u0644\u0646\u062a\u0627\u0626\u062c \u0627\u0644\u0631\u0626\u064a\u0633\u064a\u0629 \u0645\u0627 \u064a\u0644\u064a:<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li><strong>\u062a\u062d\u0633\u0646 \u0628\u0645\u0642\u062f\u0627\u0631 9 \u0646\u0642\u0627\u0637 \u0641\u064a \u0646\u062a\u064a\u062c\u0629 \u0627\u062e\u062a\u0628\u0627\u0631 NSAA \u0628\u0639\u062f \u0639\u0627\u0645\u064a\u0646<\/strong><\/li>\n\n\n\n<li>\u0628\u0627\u0644\u0645\u0642\u0627\u0631\u0646\u0629 \u0645\u0639 \u0627\u0644\u0645\u0631\u0636\u0649 \u063a\u064a\u0631 \u0627\u0644\u0645\u0639\u0627\u0644\u062c\u064a\u0646 \u0627\u0644\u0630\u064a\u0646 \u062a\u0645\u062a \u0645\u0637\u0627\u0628\u0642\u062a\u0647\u0645 \u0645\u0646 \u062e\u0644\u0627\u0644 \u062a\u062d\u0644\u064a\u0644 \u062f\u0631\u062c\u0629 \u0627\u0644\u0645\u064a\u0644<\/li>\n\n\n\n<li><strong>\u0623\u0639\u0644\u0649 \u0628\u0643\u062b\u064a\u0631 \u0645\u0646 \u0639\u062a\u0628\u0629 2.5 \u0646\u0642\u0637\u0629 \u0627\u0644\u062a\u064a \u062a\u0639\u062a\u0628\u0631 \u0630\u0627\u062a \u062f\u0644\u0627\u0644\u0629 \u0633\u0631\u064a\u0631\u064a\u0629<\/strong><\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\">\u062a\u0634\u064a\u0631 \u0647\u0630\u0647 \u0627\u0644\u0646\u062a\u0627\u0626\u062c \u0625\u0644\u0649 \u0623\u0646 GNT0004 \u0642\u062f \u064a\u062d\u0633\u0646 \u0623\u0648 \u064a\u062b\u0628\u062a \u0627\u0644\u0642\u062f\u0631\u0627\u062a \u0627\u0644\u062d\u0631\u0643\u064a\u0629 \u0628\u0634\u0643\u0644 \u0643\u0628\u064a\u0631 \u0644\u062f\u0649 \u0627\u0644\u0645\u0631\u0636\u0649 \u0627\u0644\u0645\u0639\u0627\u0644\u062c\u064a\u0646.<\/p>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"improvements-in-walking-tests\">\u062a\u062d\u0633\u064a\u0646\u0627\u062a \u0641\u064a \u0627\u062e\u062a\u0628\u0627\u0631\u0627\u062a \u0627\u0644\u0645\u0634\u064a<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u0623\u0638\u0647\u0631 \u0627\u0644\u0645\u0631\u0636\u0649 \u0627\u0644\u0630\u064a\u0646 \u0639\u0648\u0644\u062c\u0648\u0627 \u0628\u0640 GNT0004 \u0623\u064a\u0636\u064b\u0627 \u0645\u0643\u0627\u0633\u0628 \u0642\u0627\u0628\u0644\u0629 \u0644\u0644\u0642\u064a\u0627\u0633 \u0641\u064a \u062a\u0642\u064a\u064a\u0645\u0627\u062a \u0627\u0644\u0645\u0634\u064a \u0627\u0644\u0645\u062d\u062f\u062f\u0629 \u0628\u0648\u0642\u062a:<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li><strong>\u0641\u0631\u0642 +173 \u0645\u062a\u0631\u064b\u0627 \u0641\u064a \u0627\u062e\u062a\u0628\u0627\u0631 \u0627\u0644\u0645\u0634\u064a \u0644\u0645\u062f\u0629 6 \u062f\u0642\u0627\u0626\u0642 \u0645\u0642\u0627\u0631\u0646\u0629 \u0628\u0627\u0644\u0645\u0631\u0636\u0649 \u063a\u064a\u0631 \u0627\u0644\u0645\u0639\u0627\u0644\u062c\u064a\u0646<\/strong><\/li>\n\n\n\n<li><strong>\u0632\u064a\u0627\u062f\u0629 \u0642\u062f\u0631\u0647\u0627 0.95 \u0645\u062a\u0631\/\u062b\u0627\u0646\u064a\u0629 \u0641\u064a \u0633\u0631\u0639\u0629 \u0627\u062e\u062a\u0628\u0627\u0631 \u0627\u0644\u0645\u0634\u064a \u0644\u0645\u0633\u0627\u0641\u0629 10 \u0623\u0645\u062a\u0627\u0631<\/strong><\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\">\u062a\u0634\u064a\u0631 \u0647\u0630\u0647 \u0627\u0644\u062a\u062d\u0633\u064a\u0646\u0627\u062a \u0627\u0644\u0648\u0638\u064a\u0641\u064a\u0629 \u0625\u0644\u0649 \u0623\u0646 \u0627\u0644\u0623\u0637\u0641\u0627\u0644 \u0627\u0644\u0630\u064a\u0646 \u062e\u0636\u0639\u0648\u0627 \u0644\u0644\u0639\u0644\u0627\u062c \u062d\u0627\u0641\u0638\u0648\u0627 \u0639\u0644\u0649 \u0642\u062f\u0631\u0629 \u0623\u0641\u0636\u0644 \u0639\u0644\u0649 \u0627\u0644\u062d\u0631\u0643\u0629 \u0645\u0639 \u0645\u0631\u0648\u0631 \u0627\u0644\u0648\u0642\u062a.<\/p>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"large-reduction-in-creatine-kinase-ck-levels\">\u0627\u0646\u062e\u0641\u0627\u0636 \u0643\u0628\u064a\u0631 \u0641\u064a \u0645\u0633\u062a\u0648\u064a\u0627\u062a \u0627\u0644\u0643\u0631\u064a\u0627\u062a\u064a\u0646 \u0643\u064a\u0646\u0627\u0632 (CK)<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u0643\u0645\u0627 \u0623\u0628\u0644\u063a \u0627\u0644\u0628\u0627\u062d\u062b\u0648\u0646 \u0639\u0646 \u0627\u0646\u062e\u0641\u0627\u0636 \u0643\u0628\u064a\u0631 \u0641\u064a \u0645\u0633\u062a\u0648\u064a\u0627\u062a \u0627\u0644\u0643\u0631\u064a\u0627\u062a\u064a\u0646 \u0643\u064a\u0646\u0627\u0632 (CK)\u060c \u0648\u0647\u0648 \u0645\u0624\u0634\u0631 \u062d\u064a\u0648\u064a \u0645\u0647\u0645 \u0644\u062a\u0644\u0641 \u0627\u0644\u0639\u0636\u0644\u0627\u062a.<\/strong> \u0627\u0642\u0631\u0623 \u0627\u0644\u0645\u0632\u064a\u062f: <a href=\"https:\/\/dmdwarrior.com\/ar\/what-is-creatine-kinase-ck\/\" data-type=\"post\" data-id=\"2167\" target=\"_blank\" rel=\"noreferrer noopener\">\u0645\u0627 \u0647\u0648 \u0627\u0644\u0643\u0631\u064a\u0627\u062a\u064a\u0646 \u0643\u064a\u0646\u0627\u0632 (CK)\u061f<\/a><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0623\u0638\u0647\u0631\u062a \u0627\u0644\u0646\u062a\u0627\u0626\u062c \u0645\u0627 \u064a\u0644\u064a:<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li><strong>\u0645\u062a\u0648\u0633\u0637 \u0627\u0646\u062e\u0641\u0627\u0636 \u0645\u0633\u062a\u0648\u0649 \u0627\u0644\u0643\u0631\u064a\u0627\u062a\u064a\u0646 \u0643\u064a\u0646\u0627\u0632 (CK) \u062d\u0648\u0627\u0644\u064a 70% \u0628\u0639\u062f \u0639\u0627\u0645\u064a\u0646<\/strong><\/li>\n\n\n\n<li>\u0628\u0627\u0644\u0645\u0642\u0627\u0631\u0646\u0629 \u0645\u0639 \u062e\u0637 \u0627\u0644\u0623\u0633\u0627\u0633 \u0644\u0643\u0644 \u0645\u0631\u064a\u0636 \u0642\u0628\u0644 \u0627\u0644\u0639\u0644\u0627\u062c<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u0623\u0638\u0647\u0631 \u0623\u062d\u062f \u0627\u0644\u0645\u0631\u0636\u0649 \u0627\u0644\u0630\u064a\u0646 \u062a\u0645\u062a \u0645\u062a\u0627\u0628\u0639\u062a\u0647\u0645 \u0644\u0645\u062f\u0629 \u062b\u0644\u0627\u062b \u0633\u0646\u0648\u0627\u062a \u0645\u0633\u062a\u0648\u064a\u0627\u062a \u0645\u0633\u062a\u0642\u0631\u0629 \u0645\u0646 \u0625\u0646\u0632\u064a\u0645 \u0627\u0644\u0643\u0631\u064a\u0627\u062a\u064a\u0646 \u0643\u064a\u0646\u0627\u0632\u060c \u0645\u0645\u0627 \u064a\u0634\u064a\u0631 \u0625\u0644\u0649 \u0623\u0646 \u0627\u0644\u0639\u0644\u0627\u062c \u0642\u062f \u064a\u0643\u0648\u0646 \u0644\u0647 \u062a\u0623\u062b\u064a\u0631 \u0637\u0648\u064a\u0644 \u0627\u0644\u0623\u0645\u062f \u0639\u0644\u0649 \u0627\u0633\u062a\u0642\u0631\u0627\u0631 \u063a\u0634\u0627\u0621 \u0627\u0644\u062e\u0644\u064a\u0629 \u0627\u0644\u0639\u0636\u0644\u064a\u0629.<\/strong><\/p>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"mri-imaging-shows-slower-disease-progression\">\u064a\u064f\u0638\u0647\u0631 \u0627\u0644\u062a\u0635\u0648\u064a\u0631 \u0628\u0627\u0644\u0631\u0646\u064a\u0646 \u0627\u0644\u0645\u063a\u0646\u0627\u0637\u064a\u0633\u064a \u062a\u0628\u0627\u0637\u0624\u064b\u0627 \u0641\u064a \u062a\u0637\u0648\u0631 \u0627\u0644\u0645\u0631\u0636.<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u0623\u0638\u0647\u0631 \u0627\u0644\u062a\u0635\u0648\u064a\u0631 \u0628\u0627\u0644\u0631\u0646\u064a\u0646 \u0627\u0644\u0645\u063a\u0646\u0627\u0637\u064a\u0633\u064a \u0627\u0644\u0643\u0645\u064a \u062a\u0628\u0627\u0637\u0624\u064b\u0627 \u0641\u064a \u062a\u062f\u0647\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0644\u062f\u0649 \u0627\u0644\u0645\u0631\u0636\u0649 \u0627\u0644\u0630\u064a\u0646 \u062e\u0636\u0639\u0648\u0627 \u0644\u0644\u0639\u0644\u0627\u062c.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0644\u0627\u062d\u0638 \u0627\u0644\u0628\u0627\u062d\u062b\u0648\u0646 \u0645\u0627 \u064a\u0644\u064a:<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li><strong>\u0641\u0631\u0642 \u064a\u0632\u064a\u062f \u0639\u0646 18% \u0641\u064a \u0646\u0633\u0628\u0629 \u0627\u0644\u062f\u0647\u0648\u0646 \u0627\u0644\u0639\u0636\u0644\u064a\u0629<\/strong><\/li>\n\n\n\n<li>\u0628\u0627\u0644\u0645\u0642\u0627\u0631\u0646\u0629 \u0645\u0639 \u0627\u0644\u0645\u0631\u0636\u0649 \u063a\u064a\u0631 \u0627\u0644\u0645\u0639\u0627\u0644\u062c\u064a\u0646 \u0641\u064a \u0645\u062c\u0645\u0648\u0639\u0627\u062a \u0627\u0644\u062a\u0627\u0631\u064a\u062e \u0627\u0644\u0637\u0628\u064a\u0639\u064a \u0644\u0644\u0645\u0631\u0636<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\">\u0641\u064a \u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a\u060c \u064a\u0634\u064a\u0631 \u0627\u0631\u062a\u0641\u0627\u0639 \u0646\u0633\u0628\u0629 \u0627\u0644\u062f\u0647\u0648\u0646 \u0627\u0644\u0645\u062a\u0631\u0627\u0643\u0645\u0629 \u0639\u0627\u062f\u0629\u064b \u0625\u0644\u0649 \u062a\u0637\u0648\u0631 \u0627\u0644\u0645\u0631\u0636. \u0623\u0645\u0627 \u0627\u0644\u0645\u0633\u062a\u0648\u064a\u0627\u062a \u0627\u0644\u0645\u0646\u062e\u0641\u0636\u0629 \u0641\u062a\u0634\u064a\u0631 \u0625\u0644\u0649 \u0633\u0644\u0627\u0645\u0629 \u0623\u0646\u0633\u062c\u0629 \u0627\u0644\u0639\u0636\u0644\u0627\u062a.<\/p>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"favorable-safety-profile\">\u0645\u0644\u0641 \u0623\u0645\u0627\u0646 \u062c\u064a\u062f<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u0644\u0645 \u062a\u0633\u062c\u0644 \u0627\u0644\u062f\u0631\u0627\u0633\u0629 \u0623\u064a \u0623\u062d\u062f\u0627\u062b \u0636\u0627\u0626\u0631\u0629 \u062e\u0637\u064a\u0631\u0629\u060c \u0645\u0645\u0627 \u064a\u0624\u0643\u062f \u0623\u0646 \u0627\u0644\u0639\u0644\u0627\u062c \u0643\u0627\u0646 \u062c\u064a\u062f \u0627\u0644\u062a\u062d\u0645\u0644.<\/strong><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u062a\u0644\u0642\u0649 \u0627\u0644\u0645\u0631\u0636\u0649 \u062a\u062b\u0628\u064a\u0637\u064b\u0627 \u0645\u0646\u0627\u0639\u064a\u064b\u0627 \u0648\u0642\u0627\u0626\u064a\u064b\u0627 \u0645\u0624\u0642\u062a\u064b\u0627\u060c \u0645\u0645\u0627 \u0633\u0627\u0639\u062f \u0639\u0644\u0649 \u062a\u0642\u0644\u064a\u0644 \u0631\u062f\u0648\u062f \u0627\u0644\u0641\u0639\u0644 \u0627\u0644\u0645\u0646\u0627\u0639\u064a\u0629 \u062a\u062c\u0627\u0647 \u0646\u0627\u0642\u0644 \u0627\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u062c\u064a\u0646\u064a.<\/p>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"pivotal-phase-of-the-trial-now-underway\">\u0627\u0644\u0645\u0631\u062d\u0644\u0629 \u0627\u0644\u0645\u062d\u0648\u0631\u064a\u0629 \u0645\u0646 \u0627\u0644\u0628\u062d\u062b \u062c\u0627\u0631\u064a\u0629 \u0627\u0644\u0622\u0646<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u062a\u0645\u062a \u0627\u0644\u0645\u0648\u0627\u0641\u0642\u0629 \u0639\u0644\u0649 \u0627\u0644\u0645\u0631\u062d\u0644\u0629 \u0627\u0644\u0645\u062d\u0648\u0631\u064a\u0629 \u0627\u0644\u062c\u0627\u0631\u064a\u0629 \u0645\u0646 \u0627\u0644\u062a\u062c\u0631\u0628\u0629 \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629 \u0645\u0646 \u0642\u0628\u0644:<\/strong><\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u0627\u0644\u0648\u0643\u0627\u0644\u0629 \u0627\u0644\u0623\u0648\u0631\u0648\u0628\u064a\u0629 \u0644\u0644\u0623\u062f\u0648\u064a\u0629 (EMA)<\/li>\n\n\n\n<li>\u0648\u0643\u0627\u0644\u0629 \u062a\u0646\u0638\u064a\u0645 \u0627\u0644\u0623\u062f\u0648\u064a\u0629 \u0648\u0645\u0646\u062a\u062c\u0627\u062a \u0627\u0644\u0631\u0639\u0627\u064a\u0629 \u0627\u0644\u0635\u062d\u064a\u0629 (MHRA)<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\">\u0633\u062a\u0634\u0645\u0644 \u0647\u0630\u0647 \u0627\u0644\u0645\u0631\u062d\u0644\u0629 \u0645\u0627 \u064a\u0644\u064a:<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li><strong>\u062a\u0633\u062c\u064a\u0644 64 \u0635\u0628\u064a\u064b\u0627 \u0642\u0627\u062f\u0631\u064a\u0646 \u0639\u0644\u0649 \u0627\u0644\u0645\u0634\u064a \u062a\u062a\u0631\u0627\u0648\u062d \u0623\u0639\u0645\u0627\u0631\u0647\u0645 \u0628\u064a\u0646 6 \u064810 \u0633\u0646\u0648\u0627\u062a<\/strong><\/li>\n\n\n\n<li>\u0627\u0633\u062a\u062e\u062f\u0645 \u062a\u0635\u0645\u064a\u0645\u064b\u0627 \u0639\u0634\u0648\u0627\u0626\u064a\u064b\u0627 \u0645\u0632\u062f\u0648\u062c \u0627\u0644\u062a\u0639\u0645\u064a\u0629 \u0648\u0645\u0636\u0628\u0648\u0637\u064b\u0627 \u0628\u0627\u0644\u063a\u0641\u0644<\/li>\n\n\n\n<li><strong>\u0627\u062e\u062a\u0628\u0631 \u0627\u0644\u062c\u0631\u0639\u0629 \u0627\u0644\u0645\u062e\u062a\u0627\u0631\u0629 \u0627\u0644\u0628\u0627\u0644\u063a\u0629 3\u00d710\u00b9\u00b3 \u0648\u062d\u062f\u0629 \u062d\u062c\u0645\u064a\u0629\/\u0643\u062c\u0645<\/strong><\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\">\u0648\u0627\u0644\u062c\u062f\u064a\u0631 \u0628\u0627\u0644\u0630\u0643\u0631 \u0623\u0646 \u0647\u0630\u0647 \u0627\u0644\u062c\u0631\u0639\u0629 \u0623\u0642\u0644 \u0645\u0646 \u0627\u0644\u062c\u0631\u0639\u0627\u062a \u0627\u0644\u0645\u0633\u062a\u062e\u062f\u0645\u0629 \u0641\u064a \u0628\u0639\u0636 \u0627\u0644\u062a\u062c\u0627\u0631\u0628 \u0627\u0644\u0623\u062e\u0631\u0649 \u0644\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u062c\u064a\u0646\u064a \u0644\u0645\u0631\u0636 \u062f\u0648\u0634\u064a\u0646\u060c \u0645\u0645\u0627 \u0642\u062f \u064a\u0648\u0641\u0631 \u0645\u0632\u0627\u064a\u0627 \u062a\u062a\u0639\u0644\u0642 \u0628\u0627\u0644\u0633\u0644\u0627\u0645\u0629.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0627\u0643\u062a\u0634\u0641 \u0627\u0644\u0645\u0632\u064a\u062f: <a href=\"https:\/\/dmdwarrior.com\/ar\/new-gene-therapies-for-duchenne-muscular-dystrophy\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u0639\u0644\u0627\u062c\u0627\u062a \u062c\u064a\u0646\u064a\u0629 \u062c\u062f\u064a\u062f\u0629 \u0645\u062d\u062a\u0645\u0644\u0629 \u0644\u0645\u0631\u0636 \u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u062f\u0648\u0634\u064a\u0646<\/a><\/p>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"why-these-results-matter\">\u0644\u0645\u0627\u0630\u0627 \u0647\u0630\u0647 \u0627\u0644\u0646\u062a\u0627\u0626\u062c \u0645\u0647\u0645\u0629\u061f<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a \u0647\u0648 \u0627\u0636\u0637\u0631\u0627\u0628 \u0648\u0631\u0627\u062b\u064a \u062d\u0627\u062f \u0646\u0627\u062a\u062c \u0639\u0646 \u0637\u0641\u0631\u0627\u062a \u0641\u064a \u062c\u064a\u0646 \u0627\u0644\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646. \u064a\u0624\u062f\u064a \u0647\u0630\u0627 \u0627\u0644\u0645\u0631\u0636 \u0625\u0644\u0649 \u0636\u0645\u0648\u0631 \u0639\u0636\u0644\u064a \u062a\u062f\u0631\u064a\u062c\u064a \u0648\u0641\u0642\u062f\u0627\u0646 \u0627\u0644\u0642\u062f\u0631\u0629 \u0639\u0644\u0649 \u0627\u0644\u062d\u0631\u0643\u0629.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u062a\u0647\u062f\u0641 \u0627\u0644\u0639\u0644\u0627\u062c\u0627\u062a \u0627\u0644\u062c\u064a\u0646\u064a\u0629 \u0645\u062b\u0644 GNT0004 \u0625\u0644\u0649 \u062a\u0648\u0635\u064a\u0644 \u0627\u0644\u0645\u0648\u0627\u062f \u0627\u0644\u0648\u0631\u0627\u062b\u064a\u0629 \u0627\u0644\u0648\u0638\u064a\u0641\u064a\u0629 \u0625\u0644\u0649 \u062e\u0644\u0627\u064a\u0627 \u0627\u0644\u0639\u0636\u0644\u0627\u062a\u060c \u0645\u0645\u0627 \u0642\u062f \u064a\u0639\u0627\u0644\u062c \u0627\u0644\u0633\u0628\u0628 \u0627\u0644\u062c\u0630\u0631\u064a \u0644\u0644\u0645\u0631\u0636.<\/strong><\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u062a\u0634\u064a\u0631 \u0646\u062a\u0627\u0626\u062c \u0627\u0644\u0639\u0627\u0645\u064a\u0646 \u0625\u0644\u0649 \u0623\u0646 GNT0004 \u0642\u062f:<\/strong><\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u062a\u062d\u0633\u064a\u0646 \u0648\u0638\u0627\u0626\u0641 \u0627\u0644\u062d\u0631\u0643\u0629<\/li>\n\n\n\n<li>\u062a\u0642\u0644\u064a\u0644 \u062a\u0644\u0641 \u0627\u0644\u0639\u0636\u0644\u0627\u062a<\/li>\n\n\n\n<li>\u0625\u0628\u0637\u0627\u0621 \u062a\u0637\u0648\u0631 \u0627\u0644\u0645\u0631\u0636<\/li>\n\n\n\n<li>\u0627\u0644\u062d\u0641\u0627\u0638 \u0639\u0644\u0649 \u0645\u0633\u062a\u0648\u0649 \u0623\u0645\u0627\u0646 \u064a\u0645\u0643\u0646 \u0627\u0644\u062a\u062d\u0643\u0645 \u0641\u064a\u0647<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\">\u0633\u062a\u062d\u062f\u062f \u0627\u0644\u0646\u062a\u0627\u0626\u062c \u0627\u0644\u0625\u0636\u0627\u0641\u064a\u0629 \u0644\u0644\u062f\u0631\u0627\u0633\u0629 \u0627\u0644\u0645\u062d\u0648\u0631\u064a\u0629 \u0645\u0627 \u0625\u0630\u0627 \u0643\u0627\u0646 \u0627\u0644\u0639\u0644\u0627\u062c \u0633\u064a\u0635\u0628\u062d \u0641\u064a \u0646\u0647\u0627\u064a\u0629 \u0627\u0644\u0645\u0637\u0627\u0641 \u062e\u064a\u0627\u0631\u064b\u0627 \u0639\u0644\u0627\u062c\u064a\u064b\u0627 \u0645\u0639\u062a\u0645\u062f\u064b\u0627.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u062a\u0627\u0628\u0639 \u0647\u0630\u0647 \u0627\u0644\u0635\u0641\u062d\u0629<\/strong>&nbsp;&gt;&gt;&gt;&nbsp;<a href=\"https:\/\/dmdwarrior.com\/ar\/dmd-therapies\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u062c\u0645\u064a\u0639 \u0627\u0644\u062a\u062c\u0627\u0631\u0628 \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629 \u0644\u0645\u0631\u0636 \u062f\u0648\u0634\u064a\u0646<\/a><\/p>","protected":false},"excerpt":{"rendered":"<p>Gene therapy research for Duchenne muscular dystrophy (DMD) continues to advance. At the MDA Clinical &amp; Scientific Conference in Orlando, the French gene therapy organization Genethon presented new long-term data showing that its investigational therapy GNT0004 maintains clinical benefits two years after treatment. The findings highlight improvements in motor function, reductions in muscle damage biomarkers, [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":6722,"comment_status":"open","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[282],"tags":[68,61,105,220,434,449],"class_list":["post-6720","post","type-post","status-publish","format-standard","has-post-thumbnail","category-editorials","tag-creatine-kinase","tag-gene-therapy","tag-genethon","tag-gnt0004","tag-gnt0004-gene-therapy","tag-nsaa"],"_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/posts\/6720","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/comments?post=6720"}],"version-history":[{"count":0,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/posts\/6720\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/media\/6722"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/media?parent=6720"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/categories?post=6720"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/tags?post=6720"}],"curies":[{"name":"\u0648\u0648\u0631\u062f\u0628\u0631\u064a\u0633","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}