{"id":6196,"date":"2026-02-09T17:21:36","date_gmt":"2026-02-09T14:21:36","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=6196"},"modified":"2026-02-09T17:21:38","modified_gmt":"2026-02-09T14:21:38","slug":"solid-biosciences-aligns-with-fda-on-sgt-003-phase-3-trial-design-for-duchenne-muscular-dystrophy-gene-therapy","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/ar\/solid-biosciences-aligns-with-fda-on-sgt-003-phase-3-trial-design-for-duchenne-muscular-dystrophy-gene-therapy\/","title":{"rendered":"\u064a\u062a\u0648\u0627\u0641\u0642 Solid Biosciences \u0645\u0639 FDA \u0641\u064a \u062a\u0635\u0645\u064a\u0645 \u0627\u0644\u0645\u0631\u062d\u0644\u0629 \u0627\u0644\u062b\u0627\u0644\u062b\u0629 \u0645\u0646 \u062a\u062c\u0631\u0628\u0629 SGT-003 \u0644\u0639\u0644\u0627\u062c \u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a \u0628\u0627\u0644\u062c\u064a\u0646\u0627\u062a"},"content":{"rendered":"<p class=\"wp-block-paragraph\">\u0623\u0639\u0644\u0646\u062a \u0634\u0631\u0643\u0629 Solid Biosciences \u0639\u0646 \u062a\u062d\u062f\u064a\u062b \u062a\u0646\u0638\u064a\u0645\u064a \u0625\u064a\u062c\u0627\u0628\u064a \u0645\u0646 \u0627\u062c\u062a\u0645\u0627\u0639\u0647\u0627 \u0627\u0644\u0623\u062e\u064a\u0631 \u0645\u0646 \u0627\u0644\u0646\u0648\u0639 C \u0645\u0639 \u0625\u062f\u0627\u0631\u0629 \u0627\u0644\u063a\u0630\u0627\u0621 \u0648\u0627\u0644\u062f\u0648\u0627\u0621 \u0627\u0644\u0623\u0645\u0631\u064a\u0643\u064a\u0629 (FDA) \u0648\u0627\u0644\u0630\u064a \u064a\u062f\u0639\u0645 \u0627\u0644\u062a\u0642\u062f\u0645 \u0627\u0644\u0645\u0633\u062a\u0645\u0631 \u0644\u0640 SGT-003 \u0643\u0639\u0644\u0627\u062c \u0645\u062d\u062a\u0645\u0644 \u0644\u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a.<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u0634\u0631\u0643\u0629 \u0625\u0645\u0628\u0627\u0643\u062a \u062f\u0648\u0634\u064a\u0646: \u0627\u0644\u0634\u0631\u0643\u0629 \u062a\u062a\u0641\u0642 \u0645\u0639 \u0634\u0631\u0643\u0629 FDA \u0628\u0634\u0623\u0646 \u062a\u0635\u0645\u064a\u0645 \u0627\u0644\u0645\u0631\u062d\u0644\u0629 \u0627\u0644\u062b\u0627\u0644\u062b\u0629 \u0645\u0646 \u0627\u0644\u062a\u062c\u0627\u0631\u0628 \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629 \u0627\u0644\u0639\u0634\u0648\u0627\u0626\u064a\u0629\u060c \u0645\u0632\u062f\u0648\u062c\u0629 \u0627\u0644\u062a\u0639\u0645\u064a\u0629\u060c \u0648\u0627\u0644\u0645\u0636\u0628\u0648\u0637\u0629 \u0628\u0627\u0644\u063a\u0641\u0644 \u2013<\/li>\n\n\n\n<li>\u062a\u0623\u062b\u064a\u0631 \u062f\u0648\u0634\u064a\u0646: \u062a\u062a\u0648\u0642\u0639 \u0627\u0644\u0634\u0631\u0643\u0629 \u0625\u0639\u0637\u0627\u0621 \u0627\u0644\u062c\u0631\u0639\u0629 \u0627\u0644\u0623\u0648\u0644\u0649 \u0644\u0644\u0645\u0634\u0627\u0631\u0643\u064a\u0646 \u0641\u064a \u0627\u0644\u0631\u0628\u0639 \u0627\u0644\u0623\u0648\u0644 \u0645\u0646 \u0639\u0627\u0645 2026 \u2013<\/li>\n\n\n\n<li>\u062a\u062e\u0637\u0637 \u0627\u0644\u0634\u0631\u0643\u0629 \u0644\u0639\u0642\u062f \u0627\u062c\u062a\u0645\u0627\u0639\u0627\u062a \u0625\u0636\u0627\u0641\u064a\u0629 \u0645\u0639 FDA \u0641\u064a \u0627\u0644\u0646\u0635\u0641 \u0627\u0644\u0623\u0648\u0644 \u0645\u0646 \u0639\u0627\u0645 2026 \u0644\u0644\u0627\u062a\u0641\u0627\u0642 \u0639\u0644\u0649 \u0645\u0633\u0627\u0631 \u0645\u0648\u0627\u0641\u0642\u0629 \u0645\u064f\u0639\u062c\u0651\u0644 \u0645\u062d\u062a\u0645\u0644 \u0644\u0640 SGT-003 \u2013<\/li>\n\n\n\n<li>INSPIRE DUCHENNE: \u0644\u0627 \u064a\u0632\u0627\u0644 \u062f\u0648\u0627\u0621 SGT-003 \u064a\u064f\u062a\u062d\u0645\u0651\u0644 \u0628\u0634\u0643\u0644 \u0639\u0627\u0645 \u062c\u064a\u062f\u0627\u064b\u060c \u062d\u064a\u062b \u062a\u0645 \u0625\u0639\u0637\u0627\u0621 \u0627\u0644\u062c\u0631\u0639\u0629 \u0644\u0640 36 \u0645\u0634\u0627\u0631\u0643\u0627\u064b \u062d\u062a\u0649 9 \u0641\u0628\u0631\u0627\u064a\u0631 2026\u060c \u0641\u064a \u0627\u0644\u0645\u0631\u062d\u0644\u0629 \u0627\u0644\u0623\u0648\u0644\u0649\/\u0627\u0644\u062b\u0627\u0646\u064a\u0629 \u0645\u0646 \u0627\u0644\u062a\u062c\u0631\u0628\u0629 \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629 \u2013<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\">\u0648\u0627\u0641\u0642 \u0641\u0631\u064a\u0642 FDA \u0639\u0644\u0649 \u0623\u0646 \u062a\u0635\u0645\u064a\u0645 \u0627\u0644\u062a\u062c\u0631\u0628\u0629 \u0643\u0627\u0646 \u0645\u0639\u0642\u0648\u0644\u0627\u064b \u0628\u0645\u0627 \u0641\u064a \u0630\u0644\u0643: \u0645\u062c\u0645\u0648\u0639\u0629 \u0627\u0644\u0645\u0631\u0636\u0649 \u0645\u0646 \u0627\u0644\u0645\u0634\u0627\u0631\u0643\u064a\u0646 \u0627\u0644\u0642\u0627\u062f\u0631\u064a\u0646 \u0639\u0644\u0649 \u0627\u0644\u0645\u0634\u064a \u0627\u0644\u0630\u064a\u0646 \u062a\u062a\u0631\u0627\u0648\u062d \u0623\u0639\u0645\u0627\u0631\u0647\u0645 \u0628\u064a\u0646 7 \u0648 &lt;12 \u0639\u0627\u0645\u064b\u0627\u060c \u0648\u0646\u0642\u0637\u0629 \u0627\u0644\u0646\u0647\u0627\u064a\u0629 \u0627\u0644\u0623\u0648\u0644\u064a\u0629 \u0627\u0644\u0645\u062a\u0645\u062b\u0644\u0629 \u0641\u064a \u0627\u0644\u062a\u063a\u064a\u0631 \u0639\u0646 \u062e\u0637 \u0627\u0644\u0623\u0633\u0627\u0633 \u0641\u064a \u0633\u0631\u0639\u0629 \u0648\u0642\u062a \u0627\u0644\u0646\u0647\u0648\u0636 (TTR) \u0645\u0646 \u0648\u0636\u0639 \u0627\u0644\u0627\u0633\u062a\u0644\u0642\u0627\u0621 \u0627\u0644\u0630\u064a \u062a\u0645 \u062a\u0642\u064a\u064a\u0645\u0647 \u0639\u0646\u062f 18 \u0634\u0647\u0631\u064b\u0627 \u0648\u0646\u0642\u0627\u0637 \u0627\u0644\u0646\u0647\u0627\u064a\u0629 \u0627\u0644\u062b\u0627\u0646\u0648\u064a\u0629 \u0627\u0644\u0631\u0626\u064a\u0633\u064a\u0629 \u0627\u0644\u0623\u062e\u0631\u0649.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u062a\u0627\u0628\u0639 \u0647\u0630\u0647 \u0627\u0644\u0635\u0641\u062d\u0629<\/strong>&nbsp;&gt;&gt;&gt;&nbsp;<a href=\"https:\/\/dmdwarrior.com\/ar\/dmd-therapies\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u062c\u0645\u064a\u0639 \u0627\u0644\u062a\u062c\u0627\u0631\u0628 \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629 \u0644\u0645\u0631\u0636 \u062f\u0648\u0634\u064a\u0646<\/a><\/p>","protected":false},"excerpt":{"rendered":"<p>Solid Biosciences announced a positive regulatory update from its recent Type C meeting with the U.S. Food and Drug Administration (FDA) that supports the continued advancement of SGT-003 as a potential treatment for Duchenne muscular dystrophy. The FDA agreed that the trial design was reasonable including: the patient population of ambulant participants 7 to &lt;12 [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":6197,"comment_status":"open","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[281],"tags":[88,110,170,109],"class_list":["post-6196","post","type-post","status-publish","format-standard","has-post-thumbnail","category-press-releases","tag-fda","tag-sgt-003","tag-sgt-003-gene-therapy","tag-solid-biosciences"],"_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/posts\/6196","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/comments?post=6196"}],"version-history":[{"count":0,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/posts\/6196\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/media\/6197"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/media?parent=6196"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/categories?post=6196"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/tags?post=6196"}],"curies":[{"name":"\u0648\u0648\u0631\u062f\u0628\u0631\u064a\u0633","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}