{"id":5673,"date":"2026-02-05T04:47:49","date_gmt":"2026-02-05T01:47:49","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=5673"},"modified":"2026-02-07T09:41:46","modified_gmt":"2026-02-07T06:41:46","slug":"elevidys-gene-therapy-efficacy-in-dmd","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/ar\/elevidys-gene-therapy-efficacy-in-dmd\/","title":{"rendered":"\u0645\u0642\u0627\u0631\u0646\u0629 \u0628\u0633\u0639\u0631\u0647\u0627 \u0627\u0644\u0628\u0627\u0644\u063a \u0645\u0644\u064a\u0648\u0646 \u062f\u0648\u0644\u0627\u0631\u060c \u0645\u0627 \u0645\u062f\u0649 \u062a\u062d\u0633\u0646 \u062d\u0627\u0644\u0629 \u0627\u0644\u0623\u0637\u0641\u0627\u0644 \u0627\u0644\u0645\u0635\u0627\u0628\u064a\u0646 \u0628\u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0627\u0644\u062f\u0648\u0634\u064a\u0646\u064a (DMD) \u0628\u0641\u0636\u0644 \u0627\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u062c\u064a\u0646\u064a Elevidys\u061f"},"content":{"rendered":"<p class=\"wp-block-paragraph\">\u0623\u062b\u0627\u0631 \u0627\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u062c\u064a\u0646\u064a Elevidys\u060c \u0648\u0647\u0648 \u0627\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u0648\u062d\u064a\u062f \u0627\u0644\u0645\u0639\u062a\u0645\u062f \u0644\u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a (DMD)\u060c \u062e\u064a\u0628\u0629 \u0623\u0645\u0644 \u0645\u062c\u062a\u0645\u0639\u0627\u062a \u0645\u0631\u0636\u0649 \u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a \u0648\u0627\u0644\u0645\u0633\u062a\u062b\u0645\u0631\u064a\u0646 \u0628\u0639\u062f \u0646\u0634\u0631 \u0628\u064a\u0627\u0646\u0627\u062a \u062b\u0644\u0627\u062b \u0633\u0646\u0648\u0627\u062a \u0645\u0646 \u062a\u062c\u0627\u0631\u0628 \u0627\u0644\u0645\u0631\u0636\u0649. \u0648\u0642\u062f \u0623\u062b\u0627\u0631 \u0647\u0630\u0627 \u0627\u0644\u0645\u0646\u062a\u062c\u060c \u0627\u0644\u0630\u064a \u064a\u064f\u0633\u0648\u0651\u0642 \u0628\u0633\u0639\u0631 2.9 \u0645\u0644\u064a\u0648\u0646 \u062f\u0648\u0644\u0627\u0631 \u0623\u0645\u0631\u064a\u0643\u064a\u060c \u0627\u0644\u0639\u062f\u064a\u062f \u0645\u0646 \u0627\u0644\u062a\u0633\u0627\u0624\u0644\u0627\u062a \u0644\u062f\u0649 \u0639\u0627\u0626\u0644\u0627\u062a \u0627\u0644\u0623\u0637\u0641\u0627\u0644 \u0627\u0644\u0645\u0635\u0627\u0628\u064a\u0646 \u0628\u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a\u060c \u0645\u0646\u0647\u0627: &quot;\u0645\u0627 \u0645\u062f\u0649 \u0641\u0639\u0627\u0644\u064a\u0629 \u0627\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u062c\u064a\u0646\u064a Elevidys\u061f \u0648\u0645\u0627 \u0645\u0642\u062f\u0627\u0631 \u0627\u0644\u0632\u064a\u0627\u062f\u0629 \u0627\u0644\u062a\u064a \u064a\u064f\u062d\u062f\u062b\u0647\u0627 \u0641\u064a \u0645\u062a\u0648\u0633\u0637 \u0639\u0645\u0631 \u0627\u0644\u0623\u0637\u0641\u0627\u0644\u061f \u0648\u0647\u0644 \u0645\u0646 \u0627\u0644\u062f\u0642\u064a\u0642 \u0627\u0644\u062d\u0643\u0645 \u0639\u0644\u0649 \u0641\u0639\u0627\u0644\u064a\u0629 \u0627\u0644\u0639\u0644\u0627\u062c \u0628\u0646\u0627\u0621\u064b \u0639\u0644\u0649 \u0646\u062a\u0627\u0626\u062c \u0645\u0642\u064a\u0627\u0633 NSAA \u0641\u0642\u0637\u061f&quot; <strong>\u064a\u062a\u0639\u0644\u0645 \u0623\u0643\u062b\u0631:<\/strong> <a href=\"https:\/\/dmdwarrior.com\/ar\/north-star-ambulatory-assessment-nsaa-in-duchenne-dmd\/\" data-type=\"post\" data-id=\"4959\" target=\"_blank\" rel=\"noreferrer noopener\">\u0645\u0627 \u0647\u064a NSAA\u061f<\/a><\/p>\n\n\n\n<div class=\"wp-block-rank-math-toc-block\" id=\"rank-math-toc\"><h2>\u062c\u062f\u0648\u0644 \u0627\u0644\u0645\u062d\u062a\u0648\u064a\u0627\u062a<\/h2><nav><ul><li><a href=\"#sarepta-really-needs-something-to-freshen-up-the-story\">\u062a\u062d\u062a\u0627\u062c \u0633\u0627\u0631\u064a\u0628\u062a\u0627 \u062d\u0642\u064b\u0627 \u0625\u0644\u0649 \u0634\u064a\u0621 \u0644\u062a\u062c\u062f\u064a\u062f \u0627\u0644\u0642\u0635\u0629<\/a><\/li><li><a href=\"#i-dont-know-if-elevidys-works\">\u0647\u0644 \u064a\u0639\u0645\u0644 \u062c\u0647\u0627\u0632 Elevidys \u0623\u0645 \u0644\u0627\u061f<\/a><\/li><li><a href=\"#questions-from-families-organizing-the-campaign\">\u0623\u0633\u0626\u0644\u0629 \u0645\u0646 \u0639\u0627\u0626\u0644\u0627\u062a \u062a\u0646\u0638\u0645 \u0641\u0639\u0627\u0644\u064a\u0627\u062a \u0644\u062c\u0645\u0639 \u0627\u0644\u062a\u0628\u0631\u0639\u0627\u062a<\/a><\/li><li><a href=\"#which-dmd-gene-therapy-should-you-choose\">\u0623\u064a \u0639\u0644\u0627\u062c \u062c\u064a\u0646\u064a \u0644\u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0627\u0644\u062f\u0648\u0634\u064a\u0646\u064a \u064a\u062c\u0628 \u0623\u0646 \u062a\u062e\u062a\u0627\u0631\u061f<\/a><\/li><li><a href=\"#sareptas-1-year-share-price\">\u0633\u0639\u0631 \u0633\u0647\u0645 \u0633\u0627\u0631\u064a\u0628\u062a\u0627 \u0628\u0639\u062f \u0639\u0627\u0645<\/a><\/li><\/ul><\/nav><\/div>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"sarepta-really-needs-something-to-freshen-up-the-story\">\u062a\u062d\u062a\u0627\u062c \u0633\u0627\u0631\u064a\u0628\u062a\u0627 \u062d\u0642\u064b\u0627 \u0625\u0644\u0649 \u0634\u064a\u0621 \u0644\u062a\u062c\u062f\u064a\u062f \u0627\u0644\u0642\u0635\u0629<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u0646\u0634\u0631\u062a \u0634\u0631\u0643\u0629 \u0633\u0627\u0631\u064a\u0628\u062a\u0627 \u0645\u0624\u062e\u0631\u064b\u0627 \u0628\u064a\u0627\u0646\u0627\u062a \u0644\u0645 \u062a\u062a\u0636\u0645\u0646 \u0645\u0633\u062a\u0648\u064a\u0627\u062a \u0625\u0646\u0632\u064a\u0645 \u0627\u0644\u0643\u0631\u064a\u0627\u062a\u064a\u0646 \u0643\u064a\u0646\u0627\u0632\u060c \u0648\u0647\u0648 \u0623\u062d\u062f \u0623\u0647\u0645 \u0627\u0644\u0645\u0624\u0634\u0631\u0627\u062a \u0627\u0644\u062d\u064a\u0648\u064a\u0629 \u0644\u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a. \u0648\u0642\u062f \u0623\u0639\u0631\u0628\u062a \u0627\u0644\u0639\u0627\u0626\u0644\u0627\u062a \u0627\u0644\u062a\u064a \u062a\u064f\u0637\u0627\u0644\u0628 \u0628\u062a\u0648\u0641\u064a\u0631 \u0627\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u062c\u064a\u0646\u064a Elevidys \u0639\u0646 \u063a\u0636\u0628\u0647\u0627 \u0644\u0639\u062f\u0645 \u0645\u0634\u0627\u0631\u0643\u0629 \u0647\u0630\u0647 \u0627\u0644\u0645\u0639\u0644\u0648\u0645\u0627\u062a \u0627\u0644\u062a\u0642\u0646\u064a\u0629. \u0648\u062a\u0642\u0648\u0644 \u0627\u0644\u063a\u0627\u0644\u0628\u064a\u0629 \u0627\u0644\u0639\u0638\u0645\u0649 \u0645\u0646 \u0627\u0644\u0639\u0627\u0626\u0644\u0627\u062a \u0627\u0644\u062a\u064a \u062c\u0645\u0639\u062a \u0627\u0644\u062a\u0628\u0631\u0639\u0627\u062a \u0628\u0644\u0627 \u0643\u0644\u0644 \u0645\u0646 \u062e\u0644\u0627\u0644 \u062d\u0645\u0644\u0627\u062a \u0644\u062a\u0648\u0641\u064a\u0631 \u0647\u0630\u0627 \u0627\u0644\u0639\u0644\u0627\u062c: &quot;\u0646\u062d\u0646 \u0645\u0646 \u0646\u062a\u0628\u0631\u0639 \u0644\u0643\u0645 \u0628\u0645\u0644\u0627\u064a\u064a\u0646 \u0627\u0644\u062f\u0648\u0644\u0627\u0631\u0627\u062a\u060c \u0644\u0643\u0646\u0643\u0645 \u0644\u0627 \u062a\u0642\u062f\u0645\u0648\u0646 \u0644\u0646\u0627 \u0634\u064a\u0626\u064b\u0627 \u0641\u064a \u0627\u0644\u0645\u0642\u0627\u0628\u0644\u061b \u0644\u0627 \u0627\u0644\u062d\u0642\u0627\u0626\u0642 \u0648\u0644\u0627 \u0627\u0644\u0628\u064a\u0627\u0646\u0627\u062a \u0648\u0644\u0627 \u0627\u0644\u0639\u0644\u0645. \u0623\u0646\u062a\u0645 \u062a\u0623\u062e\u0630\u0648\u0646 \u0623\u0645\u0648\u0627\u0644\u0646\u0627 \u0641\u0642\u0637.&quot; <strong>\u064a\u062a\u0639\u0644\u0645 \u0623\u0643\u062b\u0631:<\/strong> <a href=\"https:\/\/dmdwarrior.com\/ar\/sarepta-3-year-topline-data-of-elevidys-gene-therapy\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u0623\u0639\u0644\u0646\u062a \u0634\u0631\u0643\u0629 \u0633\u0627\u0631\u064a\u0628\u062a\u0627 \u0639\u0646 \u0627\u0644\u0628\u064a\u0627\u0646\u0627\u062a \u0627\u0644\u0631\u0626\u064a\u0633\u064a\u0629 \u0644\u0645\u062f\u0629 3 \u0633\u0646\u0648\u0627\u062a \u0644\u0639\u0642\u0627\u0631 \u0625\u064a\u0644\u064a\u0641\u064a\u062f\u064a\u0633<\/a><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0639\u0646\u062f\u0645\u0627 \u0648\u0642\u0639\u062a \u062d\u0627\u0644\u062a\u0627 \u0648\u0641\u0627\u0629 \u0645\u0631\u062a\u0628\u0637\u062a\u0627\u0646 \u0628\u0639\u0644\u0627\u062c Elevidys \u0641\u064a \u0631\u0628\u064a\u0639 \u0639\u0627\u0645 2025\u060c \u0628\u062f\u0623 \u0633\u0647\u0645 \u0634\u0631\u0643\u0629 \u0633\u0627\u0631\u064a\u0628\u062a\u0627 \u0628\u0627\u0644\u0627\u0646\u062e\u0641\u0627\u0636. \u0648\u062e\u0644\u0627\u0644 \u0627\u0644\u0635\u064a\u0641\u060c \u0638\u0647\u0631\u062a \u0623\u0646\u0628\u0627\u0621 \u0639\u0646 \u062d\u0627\u0644\u0629 \u0648\u0641\u0627\u0629 \u062b\u0627\u0644\u062b\u0629\u060c \u0645\u0631\u062a\u0628\u0637\u0629 \u0628\u0639\u0644\u0627\u062c \u062c\u064a\u0646\u064a \u062a\u062c\u0631\u064a\u0628\u064a \u0644\u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0627\u0644\u062d\u0632\u0627\u0645\u064a\u0629 \u0627\u0644\u0637\u0631\u0641\u064a\u0629\u060c \u064a\u0633\u062a\u062e\u062f\u0645 \u0646\u0641\u0633 \u0646\u0627\u0642\u0644 \u0627\u0644\u0641\u064a\u0631\u0648\u0633 \u0627\u0644\u063a\u062f\u064a \u0627\u0644\u0645\u0631\u062a\u0628\u0637 (AAV) \u0627\u0644\u0645\u0633\u062a\u062e\u062f\u0645 \u0641\u064a \u0639\u0644\u0627\u062c Elevidys. \u0648\u0628\u0634\u0643\u0644 \u0639\u0627\u0645\u060c \u0627\u0646\u062e\u0641\u0636 \u0633\u0639\u0631 \u0633\u0647\u0645 \u0627\u0644\u0634\u0631\u0643\u0629 \u0628\u0645\u0642\u062f\u0627\u0631 80% \u0645\u0646\u0630 \u0628\u062f\u0627\u064a\u0629 \u0627\u0644\u0639\u0627\u0645 \u0625\u0644\u0649 \u0623\u062f\u0646\u0649 \u0645\u0633\u062a\u0648\u0649 \u0644\u0647 \u0645\u0646\u0630 \u0645\u0627 \u064a\u0642\u0631\u0628 \u0645\u0646 \u0639\u0634\u0631 \u0633\u0646\u0648\u0627\u062a.<\/p>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"i-dont-know-if-elevidys-works\">\u0647\u0644 \u064a\u0639\u0645\u0644 \u062c\u0647\u0627\u0632 Elevidys \u0623\u0645 \u0644\u0627\u061f<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u0642\u062f \u062a\u0634\u0639\u0631 \u0625\u062f\u0627\u0631\u0629 \u0627\u0644\u0634\u0631\u0643\u0629 \u0628\u062e\u064a\u0628\u0629 \u0623\u0645\u0644\u060c \u0638\u0646\u064b\u0627 \u0645\u0646\u0647\u0627 \u0623\u0646 \u0627\u0644\u0628\u064a\u0627\u0646\u0627\u062a \u0627\u0644\u0645\u0627\u0644\u064a\u0629 \u0627\u0644\u062c\u062f\u064a\u062f\u0629 \u0644\u0639\u0627\u0645 2025 \u0648\u0627\u0644\u0625\u062d\u0635\u0627\u0621\u0627\u062a \u0627\u0644\u0645\u062d\u062f\u062b\u0629 \u0644\u062b\u0644\u0627\u062b \u0633\u0646\u0648\u0627\u062a \u062d\u0648\u0644 Elevidys \u0633\u062a\u064f\u062e\u0641\u0641 \u0645\u0646 \u062d\u062f\u0629 \u0627\u0644\u0645\u0648\u0642\u0641. \u0641\u0639\u0644\u0649 \u0627\u0644\u0631\u063a\u0645 \u0645\u0646 \u0623\u0646 \u0634\u0631\u0643\u0629 \u0633\u0627\u0631\u064a\u0628\u062a\u0627 \u062a\u0631\u0649 \u0641\u064a \u0632\u064a\u0627\u062f\u0629 4 \u0646\u0642\u0627\u0637 \u0641\u064a \u0645\u0624\u0634\u0631 NSAA \u062f\u0644\u0627\u0644\u0629 \u0639\u0644\u0649 \u0641\u0627\u0626\u062f\u0629 \u0627\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u062c\u064a\u0646\u064a\u060c \u0625\u0644\u0627 \u0623\u0646 \u062a\u0643\u0644\u0641\u0629 \u0627\u0644\u0639\u0644\u0627\u062c \u0648\u062f\u0631\u062c\u0629 NSAA \u0627\u0644\u0628\u0627\u0644\u063a\u0629 4 \u0646\u0642\u0627\u0637 \u062a\u064f\u062b\u064a\u0631\u0627\u0646 \u0645\u062e\u0627\u0648\u0641\u0647\u0627. <strong>\u062a\u0646\u062a\u0638\u0631 \u0639\u0627\u0626\u0644\u0627\u062a \u0627\u0644\u0623\u0637\u0641\u0627\u0644 \u0627\u0644\u0645\u0635\u0627\u0628\u064a\u0646 \u0628\u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0627\u0644\u062f\u0648\u0634\u064a\u0646\u064a \u0631\u062f\u0648\u062f\u064b\u0627 \u0645\u0646 \u0634\u0631\u0643\u0629 \u0633\u0627\u0631\u064a\u0628\u062a\u0627 \u0639\u0644\u0649 \u0647\u0630\u0647 \u0627\u0644\u0623\u0633\u0626\u0644\u0629:<\/strong><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0627\u0643\u062a\u0634\u0641 \u0627\u0644\u0645\u0632\u064a\u062f: <a href=\"https:\/\/dmdwarrior.com\/ar\/what-is-creatine-kinase-ck\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u0645\u0627 \u0647\u0648 \u0627\u0644\u0643\u0631\u064a\u0627\u062a\u064a\u0646 \u0643\u064a\u0646\u0627\u0632 (CK)\u061f<\/a><\/p>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"questions-from-families-organizing-the-campaign\">\u0623\u0633\u0626\u0644\u0629 \u0645\u0646 \u0639\u0627\u0626\u0644\u0627\u062a \u062a\u0646\u0638\u0645 \u0641\u0639\u0627\u0644\u064a\u0627\u062a \u0644\u062c\u0645\u0639 \u0627\u0644\u062a\u0628\u0631\u0639\u0627\u062a<\/h2>\n\n\n\n<ol class=\"wp-block-list\">\n<li>\u0647\u0644 \u062a\u0643\u0644\u0641 \u0627\u0644\u0632\u064a\u0627\u062f\u0629 \u0628\u0645\u0642\u062f\u0627\u0631 4 \u0646\u0642\u0627\u0637 \u0641\u064a NSAA \u062d\u0642\u064b\u0627 2.9 \u0645\u0644\u064a\u0648\u0646\u061f<\/li>\n\n\n\n<li>\u0642\u0628\u0644 \u062b\u0644\u0627\u062b \u0633\u0646\u0648\u0627\u062a\u060c \u0645\u0627 \u0647\u0648 \u0645\u0633\u062a\u0648\u0649 \u0627\u0644\u0643\u0631\u064a\u0627\u062a\u064a\u0646 \u0643\u064a\u0646\u0627\u0632 \u0644\u062f\u0649 \u0637\u0641\u0644 \u0645\u0635\u0627\u0628 \u0628\u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0627\u0644\u062f\u0648\u0634\u064a\u0646\u064a \u0648\u0643\u0627\u0646 \u0645\u0631\u0634\u062d\u064b\u0627 \u0644\u0644\u0639\u0644\u0627\u062c \u0628\u0640 Elevidys\u060c \u0648\u0645\u0627 \u0647\u0648 \u0645\u0633\u062a\u0648\u0649 \u0627\u0644\u0643\u0631\u064a\u0627\u062a\u064a\u0646 \u0643\u064a\u0646\u0627\u0632 \u0628\u0639\u062f 3 \u0633\u0646\u0648\u0627\u062a \u0645\u0646 \u062a\u0644\u0642\u064a \u0627\u0644\u0639\u0644\u0627\u062c \u0628\u0640 Elevidys\u061f<\/li>\n\n\n\n<li>\u0625\u0630\u0627 \u0644\u0645 \u062a\u0646\u062e\u0641\u0636 \u0645\u0633\u062a\u0648\u064a\u0627\u062a \u0627\u0644\u0643\u0631\u064a\u0627\u062a\u064a\u0646 \u0643\u064a\u0646\u0627\u0632 \u0628\u0639\u062f \u062a\u0646\u0627\u0648\u0644 Elevidys\u060c \u0623\u0644\u0627 \u064a\u0639\u0646\u064a \u0630\u0644\u0643 \u0623\u0646 \u062a\u0644\u0641 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0645\u0633\u062a\u0645\u0631\u061f<\/li>\n\n\n\n<li>\u0647\u0644 \u0642\u0645\u062a \u0628\u0623\u062e\u0630 \u0639\u064a\u0646\u0627\u062a \u062e\u0632\u0639\u0629 \u0639\u0636\u0644\u064a\u0629 \u0644\u0642\u064a\u0627\u0633 \u0645\u0633\u062a\u0648\u064a\u0627\u062a \u0627\u0644\u0643\u0631\u064a\u0627\u062a\u064a\u0646 \u0643\u064a\u0646\u0627\u0632 \u0644\u062f\u0649 \u0627\u0644\u0623\u0637\u0641\u0627\u0644 \u0627\u0644\u0630\u064a\u0646 \u064a\u062a\u0644\u0642\u0648\u0646 \u0627\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u062c\u064a\u0646\u064a Elevidys\u061f<\/li>\n<\/ol>\n\n\n\n<p class=\"wp-block-paragraph\">\u064a\u0648\u0627\u062c\u0647 \u0627\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u062c\u064a\u0646\u064a Elevidys\u060c \u0648\u0647\u0648 \u0623\u0648\u0644 \u0639\u0644\u0627\u062c \u062c\u064a\u0646\u064a \u0644\u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a \u0627\u0644\u0630\u064a \u062d\u0635\u0644 \u0639\u0644\u0649 \u0645\u0648\u0627\u0641\u0642\u0629 FDA (\u0648\u0644\u0643\u0646 \u0644\u064a\u0633 EMA)\u060c \u0645\u0646\u0627\u0641\u0633\u0629\u064b \u062c\u062f\u064a\u062f\u0629\u064b \u0642\u0631\u064a\u0628\u064b\u0627. \u0623\u0642\u0631\u0628 \u0647\u0630\u0647 \u0627\u0644\u0645\u0646\u0627\u0641\u0633\u0627\u062a \u0625\u0644\u0649 \u062f\u062e\u0648\u0644 \u0627\u0644\u0633\u0648\u0642 \u0647\u064a \u0634\u0631\u0643\u0629 REGENXBIO\u060c \u0627\u0644\u062a\u064a \u0623\u0639\u0644\u0646\u062a \u0627\u0644\u0634\u0647\u0631 \u0627\u0644\u0645\u0627\u0636\u064a \u0639\u0646 \u0646\u064a\u062a\u0647\u0627 \u0627\u0644\u062a\u0642\u062f\u0645 \u0628\u0637\u0644\u0628 \u0644\u0644\u062d\u0635\u0648\u0644 \u0639\u0644\u0649 \u0645\u0648\u0627\u0641\u0642\u0629 \u0644\u0639\u0644\u0627\u062c\u0647\u0627 \u0627\u0644\u062c\u064a\u0646\u064a RGX-202 \u0628\u062d\u0644\u0648\u0644 \u0645\u0646\u062a\u0635\u0641 \u0639\u0627\u0645 2026. \u0643\u0645\u0627 \u064a\u064f\u0639\u062f \u0627\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u062c\u064a\u0646\u064a SGT-003 \u0645\u0646 \u0634\u0631\u0643\u0629 SolidBio \u0628\u062f\u064a\u0644\u0627\u064b \u0637\u0645\u0648\u062d\u064b\u0627\u060c \u0648\u0625\u0630\u0627 \u062f\u062e\u0644\u062a \u0647\u0630\u0647 \u0627\u0644\u062e\u064a\u0627\u0631\u0627\u062a \u0627\u0644\u0633\u0648\u0642\u060c \u0641\u0644\u0646 \u064a\u0643\u0648\u0646 \u0645\u0646 \u0627\u0644\u0645\u0633\u062a\u063a\u0631\u0628 \u0623\u0646 \u064a\u062e\u062a\u0627\u0631 \u0645\u0631\u0636\u0649 \u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a \u0648\u0639\u0627\u0626\u0644\u0627\u062a\u0647\u0645 \u0627\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u062c\u064a\u0646\u064a Elevidys \u0628\u062f\u0644\u0627\u064b \u0645\u0646 Elevidys. <strong>\u0627\u0642\u0631\u0623 \u0627\u0644\u0645\u0632\u064a\u062f:<\/strong> <a href=\"https:\/\/dmdwarrior.com\/ar\/creatine-kinase-ck-dystrophin-level-nsaa-score-in-elevidys-gene-therapy\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u0643\u064a\u0646\u0627\u0632 \u0627\u0644\u0643\u0631\u064a\u0627\u062a\u064a\u0646 (CK)\u060c \u0648\u0645\u0633\u062a\u0648\u0649 \u0627\u0644\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0648\u062f\u0631\u062c\u0629 NSAA \u0641\u064a \u0627\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u062c\u064a\u0646\u064a Elevidys<\/a><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0642\u062f \u062a\u0648\u0627\u062c\u0647 \u0634\u0631\u0643\u0629 \u0633\u0627\u0631\u064a\u0628\u062a\u0627 \u0623\u0648\u0642\u0627\u062a\u064b\u0627 \u0639\u0635\u064a\u0628\u0629 \u0641\u064a \u0627\u0644\u0645\u0633\u062a\u0642\u0628\u0644 \u0646\u0638\u0631\u064b\u0627 \u0644\u0627\u0646\u062e\u0641\u0627\u0636 \u0627\u0644\u0645\u0628\u064a\u0639\u0627\u062a\u060c \u0648\u0627\u0634\u062a\u062f\u0627\u062f \u0627\u0644\u0645\u0646\u0627\u0641\u0633\u0629\u060c \u0648\u0646\u0642\u0635 \u0627\u0644\u0628\u064a\u0627\u0646\u0627\u062a \u0627\u0644\u0639\u0644\u0645\u064a\u0629 \u0627\u0644\u0648\u0627\u0636\u062d\u0629 \u0648\u0627\u0644\u0645\u0637\u0645\u0626\u0646\u0629. \u0648\u064a\u0631\u0649 \u0627\u0644\u0645\u0645\u062b\u0644 \u0627\u0644\u0623\u0644\u0645\u0627\u0646\u064a \u0644\u0645\u0646\u0638\u0645\u0629 DMDWarrior \u0623\u0646 \u0634\u0631\u0643\u0629 \u0627\u0644\u062a\u0643\u0646\u0648\u0644\u0648\u062c\u064a\u0627 \u0627\u0644\u062d\u064a\u0648\u064a\u0629 \u062a\u0641\u0642\u062f \u062c\u0627\u0630\u0628\u064a\u062a\u0647\u0627 \u0643\u0647\u062f\u0641 \u0645\u062d\u062a\u0645\u0644 \u0644\u0644\u0627\u0633\u062a\u062d\u0648\u0627\u0630\u060c \u062d\u062a\u0649 \u0628\u0627\u0644\u0646\u0633\u0628\u0629 \u0644\u0634\u0631\u0643\u0627\u062a \u0627\u0644\u0623\u062f\u0648\u064a\u0629 \u0627\u0644\u0643\u0628\u0631\u0649\u060c \u0628\u0633\u0628\u0628 \u062a\u0636\u0631\u0631 \u0633\u0645\u0639\u062a\u0647\u0627 \u0648\u0639\u062f\u0645 \u0631\u0636\u0627 \u0645\u0631\u0636\u0627\u0647\u0627. <strong>\u0627\u0633\u0623\u0644\u0648\u0627 \u0623\u0646\u0641\u0633\u0643\u0645:<\/strong> <a href=\"https:\/\/dmdwarrior.com\/ar\/one-time-gene-therapies-or-exon-skipping-therapies-which-may-be-better-for-duchenne-muscular-dystrophy-dmd-today\/\">\u2018\u0627\u0644\u0639\u0644\u0627\u062c\u0627\u062a \u0627\u0644\u062c\u064a\u0646\u064a\u0629 &quot;\u0644\u0644\u0645\u0631\u0629 \u0627\u0644\u0648\u0627\u062d\u062f\u0629&quot; \u0623\u0648 \u0639\u0644\u0627\u062c\u0627\u062a \u062a\u062e\u0637\u064a \u0627\u0644\u0625\u0643\u0633\u0648\u0646<\/a><\/p>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"which-dmd-gene-therapy-should-you-choose\">\u0623\u064a \u0639\u0644\u0627\u062c \u062c\u064a\u0646\u064a \u0644\u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0627\u0644\u062f\u0648\u0634\u064a\u0646\u064a \u064a\u062c\u0628 \u0623\u0646 \u062a\u062e\u062a\u0627\u0631\u061f<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u0642\u062f \u064a\u0636\u0637\u0631 \u0645\u0631\u0636\u0649 \u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0627\u0644\u062f\u0648\u0634\u064a\u0646\u064a \u0648\u0639\u0627\u0626\u0644\u0627\u062a\u0647\u0645 \u0642\u0631\u064a\u0628\u064b\u0627 \u0625\u0644\u0649 \u0627\u062a\u062e\u0627\u0630 \u062e\u064a\u0627\u0631\u0627\u062a \u0635\u0639\u0628\u0629 \u0644\u0623\u0646 Elevidys \u064a\u0633\u062a\u062e\u062f\u0645 \u0646\u0641\u0633 \u0627\u0644\u0646\u0627\u0642\u0644 \u0627\u0644\u0645\u0633\u062a\u062e\u062f\u0645 \u0641\u064a \u0627\u0644\u0639\u0644\u0627\u062c\u0627\u062a \u0627\u0644\u0623\u062d\u062f\u062b \u0645\u062b\u0644 RGX-202 \u0645\u0646 REGENXBIO \u0648 SGT-003 \u0645\u0646 Solid Biosciences.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong><em>\u064a\u062c\u0628 \u062a\u0630\u0643\u064a\u0631 \u0627\u0644\u0639\u0627\u0626\u0644\u0627\u062a \u0627\u0644\u062a\u064a \u062a\u0646\u0638\u0645 \u062d\u0645\u0644\u0627\u062a \u0627\u0644\u062a\u0637\u0639\u064a\u0645 \u0645\u0631\u0629 \u0623\u062e\u0631\u0649: &quot;\u0644\u0627 \u064a\u0645\u0643\u0646 \u0627\u0633\u062a\u062e\u062f\u0627\u0645 \u0627\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u062c\u064a\u0646\u064a AAV \u0625\u0644\u0627 \u0645\u0631\u0629 \u0648\u0627\u062d\u062f\u0629!&quot; &quot;\u0644\u0630\u0627\u060c \u0625\u0630\u0627 \u0627\u062e\u062a\u0631\u062a\u0645 \u0627\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u062c\u064a\u0646\u064a Elevidys\u060c \u0641\u0642\u062f \u062a\u0641\u0648\u062a\u0643\u0645 \u062e\u064a\u0627\u0631\u0627\u062a \u0623\u062e\u0631\u0649.&quot; \u0644\u0647\u0630\u0627 \u0627\u0644\u0633\u0628\u0628\u060c \u0642\u062f \u064a\u0643\u0648\u0646 \u0645\u0646 \u0627\u0644\u0623\u0641\u0636\u0644 \u0644\u0644\u0639\u0627\u0626\u0644\u0627\u062a \u0627\u0644\u062a\u064a \u0644\u0627 \u064a\u0632\u0627\u0644 \u0644\u062f\u064a\u0647\u0627 \u0645\u062a\u0633\u0639 \u0645\u0646 \u0627\u0644\u0648\u0642\u062a \u0623\u0646 \u062a\u064f\u0628\u0637\u0626 \u062d\u0645\u0644\u0627\u062a\u0647\u0627 \u0623\u0648 \u062d\u062a\u0649 \u062a\u0624\u062c\u0644\u0647\u0627 \u0644\u0641\u062a\u0631\u0629.<\/em><\/strong><\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u0627\u0643\u062a\u0634\u0641 \u0627\u0644\u0645\u0632\u064a\u062f:<\/strong> <a href=\"https:\/\/dmdwarrior.com\/ar\/frequently-asked-questions-about-elevidys-used-for-duchenne-muscular-dystrophy\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u0627\u0644\u0623\u0633\u0626\u0644\u0629 \u0627\u0644\u0634\u0627\u0626\u0639\u0629 \u062d\u0648\u0644 Elevidys<\/a><\/p>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"sareptas-1-year-share-price\">\u0633\u0639\u0631 \u0633\u0647\u0645 \u0633\u0627\u0631\u064a\u0628\u062a\u0627 \u0628\u0639\u062f \u0639\u0627\u0645<\/h2>\n\n\n\n<div><a href=\"https:\/\/dmdwarrior.com\/wp-content\/uploads\/2026\/02\/Sarepta-1-Year-Share-Price-1024x534.jpg\" class=\"td-modal-image\"><figure class=\"wp-block-image size-large\"><img loading=\"lazy\" decoding=\"async\" width=\"1024\" height=\"534\" src=\"https:\/\/dmdwarrior.com\/wp-content\/uploads\/2026\/02\/Sarepta-1-Year-Share-Price-1024x534.jpg\" alt=\"Sarepta Therapeutics \u0633\u0639\u0631 \u0627\u0644\u0633\u0647\u0645 \u0644\u0645\u062f\u0629 \u0639\u0627\u0645 \u0648\u0627\u062d\u062f\" class=\"wp-image-6177\" title=\"\" srcset=\"https:\/\/dmdwarrior.com\/wp-content\/uploads\/2026\/02\/Sarepta-1-Year-Share-Price-1024x534.jpg 1024w, https:\/\/dmdwarrior.com\/wp-content\/uploads\/2026\/02\/Sarepta-1-Year-Share-Price-300x157.jpg 300w, https:\/\/dmdwarrior.com\/wp-content\/uploads\/2026\/02\/Sarepta-1-Year-Share-Price-768x401.jpg 768w, https:\/\/dmdwarrior.com\/wp-content\/uploads\/2026\/02\/Sarepta-1-Year-Share-Price-18x9.jpg 18w, https:\/\/dmdwarrior.com\/wp-content\/uploads\/2026\/02\/Sarepta-1-Year-Share-Price-805x420.jpg 805w, https:\/\/dmdwarrior.com\/wp-content\/uploads\/2026\/02\/Sarepta-1-Year-Share-Price-150x78.jpg 150w, https:\/\/dmdwarrior.com\/wp-content\/uploads\/2026\/02\/Sarepta-1-Year-Share-Price-696x363.jpg 696w, https:\/\/dmdwarrior.com\/wp-content\/uploads\/2026\/02\/Sarepta-1-Year-Share-Price-1068x557.jpg 1068w, https:\/\/dmdwarrior.com\/wp-content\/uploads\/2026\/02\/Sarepta-1-Year-Share-Price.jpg 1290w\" sizes=\"auto, (max-width: 1024px) 100vw, 1024px\" \/><\/figure><\/a><\/div>\n\n\n\n<p class=\"wp-block-paragraph\">\u0639\u0644\u0649 \u0627\u0644\u0631\u063a\u0645 \u0645\u0646 \u0627\u0644\u062a\u062d\u062f\u064a\u062b \u0627\u0644\u0645\u0634\u062c\u0639 \u0644\u0640 EMBARK\u060c \u0625\u0644\u0627 \u0623\u0646 \u0623\u062f\u0627\u0621 \u0633\u0639\u0631 \u0633\u0647\u0645 Sarepta Therapeutics \u0643\u0627\u0646 \u0636\u0639\u064a\u0641\u064b\u0627 \u0645\u0624\u062e\u0631\u064b\u0627\u060c \u062d\u064a\u062b \u0628\u0644\u063a \u0639\u0627\u0626\u062f \u0627\u0644\u0633\u0647\u0645 \u062e\u0644\u0627\u0644 7 \u0623\u064a\u0627\u0645 8.53%\u060c \u0628\u064a\u0646\u0645\u0627 \u0627\u0646\u062e\u0641\u0636 \u0639\u0627\u0626\u062f \u0627\u0644\u0633\u0647\u0645 \u0645\u0646\u0630 \u0628\u062f\u0627\u064a\u0629 \u0627\u0644\u0639\u0627\u0645 \u0628\u0645\u0642\u062f\u0627\u0631 4.83%. \u0641\u064a \u0627\u0644\u0648\u0642\u062a \u0646\u0641\u0633\u0647\u060c \u064a\u064f\u0638\u0647\u0631 \u0627\u0646\u062e\u0641\u0627\u0636 \u0625\u062c\u0645\u0627\u0644\u064a \u0639\u0627\u0626\u062f \u0627\u0644\u0645\u0633\u0627\u0647\u0645\u064a\u0646 \u062e\u0644\u0627\u0644 \u0639\u0627\u0645 \u0648\u0627\u062d\u062f \u0625\u0644\u0649 82.22%\u060c \u0648\u0627\u0646\u062e\u0641\u0627\u0636\u0647 \u062e\u0644\u0627\u0644 3 \u0633\u0646\u0648\u0627\u062a \u0625\u0644\u0649 83.21%\u060c \u0645\u062f\u0649 \u0641\u062a\u0648\u0631 \u0627\u0644\u0645\u0639\u0646\u0648\u064a\u0627\u062a\u060c \u062d\u062a\u0649 \u0628\u0639\u062f \u0623\u0646 \u064a\u0634\u064a\u0631 \u0639\u0627\u0626\u062f \u0627\u0644\u0633\u0647\u0645 \u062e\u0644\u0627\u0644 90 \u064a\u0648\u0645\u064b\u0627 \u0627\u0644\u0628\u0627\u0644\u063a 8.62% \u0625\u0644\u0649 \u0645\u062d\u0627\u0648\u0644\u0629 \u0627\u0633\u062a\u0639\u0627\u062f\u0629 \u0628\u0639\u0636 \u0627\u0644\u0632\u062e\u0645 \u0639\u0644\u0649 \u0627\u0644\u0645\u062f\u0649 \u0627\u0644\u0642\u0635\u064a\u0631.<\/p>","protected":false},"excerpt":{"rendered":"<p>Elevidys, the only gene therapy approved by the FDA for Duchenne muscular dystrophy (DMD), has disappointed DMD communities and investors following the release of three years of data from patients. Marketed at a price of $2.9 million American dollars, the product has raised several questions for families of children with DMD: &#8216;How effective is Elevidys [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":6174,"comment_status":"open","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[282],"tags":[33,179,61,107,108,65,110,109],"class_list":["post-5673","post","type-post","status-publish","format-standard","has-post-thumbnail","category-editorials","tag-elevidys","tag-elevidys-gene-therapy","tag-gene-therapy","tag-regenxbio","tag-rgx-202","tag-sarepta","tag-sgt-003","tag-solid-biosciences"],"_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/posts\/5673","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/comments?post=5673"}],"version-history":[{"count":0,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/posts\/5673\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/media\/6174"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/media?parent=5673"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/categories?post=5673"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/tags?post=5673"}],"curies":[{"name":"\u0648\u0648\u0631\u062f\u0628\u0631\u064a\u0633","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}