{"id":5315,"date":"2025-12-12T17:44:59","date_gmt":"2025-12-12T14:44:59","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=5315"},"modified":"2025-12-12T17:51:07","modified_gmt":"2025-12-12T14:51:07","slug":"ractigen-therapeutics-study-of-rag-18-sarna-for-duchenne-muscular-dystrophy","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/ar\/ractigen-therapeutics-study-of-rag-18-sarna-for-duchenne-muscular-dystrophy\/","title":{"rendered":"Ractigen Therapeutics \u064a\u064f\u0639\u0637\u064a \u0627\u0644\u062c\u0631\u0639\u0629 \u0627\u0644\u0623\u0648\u0644\u0649 \u0644\u0645\u0631\u064a\u0636 \u0641\u064a \u062f\u0631\u0627\u0633\u0629 IIT \u0644\u0640 RAG-18\u060c \u0648\u0647\u0648 \u0639\u0644\u0627\u062c \u0645\u062d\u062a\u0645\u0644 \u0628\u062a\u0642\u0646\u064a\u0629 saRNA \u064a\u064f\u062d\u062f\u062b \u0646\u0642\u0644\u0629 \u0646\u0648\u0639\u064a\u0629 \u0641\u064a \u0639\u0644\u0627\u062c \u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a."},"content":{"rendered":"<p class=\"wp-block-paragraph\">\u0623\u0639\u0644\u0646\u062a \u0634\u0631\u0643\u0629 Ractigen Therapeutics\u060c \u0648\u0647\u064a \u0634\u0631\u0643\u0629 \u0631\u0627\u0626\u062f\u0629 \u0641\u064a \u062a\u0637\u0648\u064a\u0631 \u0639\u0644\u0627\u062c\u0627\u062a \u0627\u0644\u062d\u0645\u0636 \u0627\u0644\u0646\u0648\u0648\u064a \u0627\u0644\u0631\u064a\u0628\u064a \u0627\u0644\u0645\u0646\u0634\u0637 \u0627\u0644\u0635\u063a\u064a\u0631 (saRNA)\u060c \u0627\u0644\u064a\u0648\u0645 \u0639\u0646 \u0646\u062c\u0627\u062d \u0625\u0639\u0637\u0627\u0621 \u0627\u0644\u062c\u0631\u0639\u0629 \u0644\u0623\u0648\u0644 \u0645\u0631\u064a\u0636 \u0641\u064a \u062a\u062c\u0631\u0628\u062a\u0647\u0627 \u0627\u0644\u062a\u064a \u0628\u062f\u0623\u0647\u0627 \u0627\u0644\u0628\u0627\u062d\u062b\u0648\u0646 (IIT) \u0644\u0640 RAG-18 \u0641\u064a \u0645\u0633\u062a\u0634\u0641\u0649 \u0643\u0644\u064a\u0629 \u0627\u0644\u0637\u0628 \u0628\u062c\u0627\u0645\u0639\u0629 \u0628\u0643\u064a\u0646 (PUMCH)\u060c \u0627\u0644\u0623\u0643\u0627\u062f\u064a\u0645\u064a\u0629 \u0627\u0644\u0635\u064a\u0646\u064a\u0629 \u0644\u0644\u0639\u0644\u0648\u0645 \u0627\u0644\u0637\u0628\u064a\u0629 \u0641\u064a \u0628\u0643\u064a\u0646.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u064a\u0645\u062b\u0644 \u0647\u0630\u0627 \u0627\u0644\u0625\u0646\u062c\u0627\u0632 \u0644\u062d\u0638\u0629 \u062a\u062d\u0648\u0644\u064a\u0629 \u0641\u064a \u0645\u0643\u0627\u0641\u062d\u0629 \u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a (DMD)\u060c \u0645\u0645\u0627 \u064a\u062c\u0639\u0644 RAG-18 \u0628\u0645\u062b\u0627\u0628\u0629 \u0639\u0627\u0645\u0644 \u062a\u063a\u064a\u064a\u0631 \u0645\u062d\u062a\u0645\u0644 \u0641\u064a \u0647\u0630\u0627 \u0627\u0644\u0645\u062c\u0627\u0644.<\/strong> \u0645\u0646 \u062e\u0644\u0627\u0644 \u0627\u0633\u062a\u062e\u062f\u0627\u0645 \u0622\u0644\u064a\u0629 saRNA \u062c\u062f\u064a\u062f\u0629 \u0644\u0632\u064a\u0627\u062f\u0629 \u0627\u0644\u062a\u0639\u0628\u064a\u0631 \u0639\u0646 UTRN\u060c \u064a\u0645\u062b\u0644 RAG-18 \u0646\u0647\u062c\u064b\u0627 \u0639\u0644\u0627\u062c\u064a\u064b\u0627 \u062b\u0648\u0631\u064a\u064b\u0627 \u064a\u0647\u062f\u0641 \u0625\u0644\u0649 \u0627\u0644\u062a\u063a\u0644\u0628 \u0639\u0644\u0649 \u0642\u064a\u0648\u062f \u0627\u0644\u0639\u0644\u0627\u062c\u0627\u062a \u0627\u0644\u062d\u0627\u0644\u064a\u0629 \u0648\u064a\u0645\u0643\u0646 \u0623\u0646 \u064a\u0648\u0641\u0631 \u062d\u0644\u0627\u064b \u0639\u0627\u0644\u0645\u064a\u064b\u0627 \u064a\u0641\u064a\u062f \u062c\u0645\u064a\u0639 \u0627\u0644\u0645\u0631\u0636\u0649 \u0627\u0644\u0645\u062a\u0636\u0631\u0631\u064a\u0646 \u0645\u0646 \u0647\u0630\u0647 \u0627\u0644\u062d\u0627\u0644\u0629 \u0627\u0644\u0645\u062f\u0645\u0631\u0629.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u064a\u0642\u0648\u062f \u0645\u0639\u0647\u062f IIT \u0627\u0644\u0628\u0631\u0648\u0641\u064a\u0633\u0648\u0631 \u062f\u0627\u064a \u064a\u064a\u060c \u0627\u0644\u062e\u0628\u064a\u0631 \u0627\u0644\u0645\u062a\u0645\u064a\u0632 \u0641\u064a \u0627\u0636\u0637\u0631\u0627\u0628\u0627\u062a \u0627\u0644\u062c\u0647\u0627\u0632 \u0627\u0644\u0639\u0635\u0628\u064a \u0627\u0644\u0639\u0636\u0644\u064a \u0648\u0646\u0627\u0626\u0628 \u0645\u062f\u064a\u0631 \u0642\u0633\u0645 \u0637\u0628 \u0627\u0644\u0623\u0639\u0635\u0627\u0628 \u0641\u064a \u0645\u0633\u062a\u0634\u0641\u0649 \u0628\u0643\u064a\u0646 \u0627\u0644\u0637\u0628\u064a \u0627\u0644\u062c\u0627\u0645\u0639\u064a. \u062a\u0647\u062f\u0641 \u0627\u0644\u062f\u0631\u0627\u0633\u0629 \u0625\u0644\u0649 \u062a\u0642\u064a\u064a\u0645 \u0633\u0644\u0627\u0645\u0629 \u0648\u062e\u0635\u0627\u0626\u0635 \u062d\u0631\u0643\u064a\u0629 \u062f\u0648\u0627\u0621 RAG-18\u060c \u0628\u0627\u0644\u0625\u0636\u0627\u0641\u0629 \u0625\u0644\u0649 \u0627\u0633\u062a\u0643\u0634\u0627\u0641 \u0625\u0645\u0643\u0627\u0646\u064a\u0629 \u062a\u062d\u0633\u064a\u0646 \u0648\u0638\u0627\u0626\u0641 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0644\u062f\u0649 \u0645\u0631\u0636\u0649 \u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0627\u0644\u062f\u0648\u0634\u064a\u0646\u064a. <strong>\u0635\u0631\u062d \u0627\u0644\u0628\u0631\u0648\u0641\u064a\u0633\u0648\u0631 \u062f\u0627\u064a \u0642\u0627\u0626\u0644\u0627\u064b: &quot;\u0646\u062d\u0646 \u0645\u062a\u062d\u0645\u0633\u0648\u0646 \u0644\u0628\u062f\u0621 \u0647\u0630\u0647 \u0627\u0644\u062a\u062c\u0631\u0628\u0629 \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629 \u0628\u0627\u0633\u062a\u062e\u062f\u0627\u0645 RAG-18\u060c \u0648\u0647\u0648 \u0646\u0647\u062c \u0639\u0644\u0627\u062c\u064a \u0645\u062a\u0637\u0648\u0631 \u0644\u0639\u0644\u0627\u062c \u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0627\u0644\u062f\u0648\u0634\u064a\u0646\u064a. \u0646\u062a\u0648\u0642\u0639 \u0646\u062a\u0627\u0626\u062c \u0633\u0631\u064a\u0631\u064a\u0629 \u0625\u064a\u062c\u0627\u0628\u064a\u0629 \u0642\u062f \u062a\u0641\u062a\u062d \u0622\u0641\u0627\u0642\u0627\u064b \u062c\u062f\u064a\u062f\u0629 \u0648\u0645\u0628\u062a\u0643\u0631\u0629 \u0644\u0644\u0639\u0644\u0627\u062c \u0623\u0645\u0627\u0645 \u0627\u0644\u0645\u0631\u0636\u0649 \u0648\u062a\u062d\u0633\u0646 \u062c\u0648\u062f\u0629 \u062d\u064a\u0627\u062a\u0647\u0645 \u0628\u0634\u0643\u0644 \u0645\u0644\u062d\u0648\u0638.&quot;\u201c<\/strong><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0623\u0639\u0631\u0628 \u0627\u0644\u062f\u0643\u062a\u0648\u0631 \u0644\u0648\u0646\u063a \u062a\u0634\u0646\u063a \u0644\u064a\u060c \u0627\u0644\u0645\u0624\u0633\u0633 \u0648\u0627\u0644\u0631\u0626\u064a\u0633 \u0627\u0644\u062a\u0646\u0641\u064a\u0630\u064a \u0644\u0634\u0631\u0643\u0629 Ractigen Therapeutics\u060c \u0639\u0646 \u062d\u0645\u0627\u0633\u0647 \u0644\u0644\u062a\u062c\u0631\u0628\u0629\u060c \u0642\u0627\u0626\u0644\u0627\u064b: &quot;\u064a\u0645\u062b\u0644 \u0628\u062f\u0621 \u0647\u0630\u0647 \u0627\u0644\u062f\u0631\u0627\u0633\u0629 \u062e\u0637\u0648\u0629 \u062d\u0627\u0633\u0645\u0629 \u0644\u0644\u0623\u0645\u0627\u0645 \u0628\u0627\u0644\u0646\u0633\u0628\u0629 \u0644\u0639\u0642\u0627\u0631 RAG-18\u060c \u0645\u0645\u0627 \u064a\u0624\u0643\u062f \u062f\u0648\u0631\u0647 \u0627\u0644\u0641\u0631\u064a\u062f \u0641\u064a \u0627\u0644\u062a\u063a\u0644\u0628 \u0639\u0644\u0649 \u062a\u062d\u062f\u064a\u0627\u062a \u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0627\u0644\u062f\u0648\u0634\u064a\u0646\u064a. \u064a\u062a\u0645\u062a\u0639 \u0647\u0630\u0627 \u0627\u0644\u0639\u0644\u0627\u062c \u0628\u0625\u0645\u0643\u0627\u0646\u064a\u0629 \u0645\u0639\u0627\u0644\u062c\u0629 \u062c\u0645\u064a\u0639 \u0627\u0644\u0637\u0641\u0631\u0627\u062a \u0627\u0644\u062c\u064a\u0646\u064a\u0629 \u0627\u0644\u0645\u0631\u062a\u0628\u0637\u0629 \u0628\u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0627\u0644\u062f\u0648\u0634\u064a\u0646\u064a\u060c \u0645\u0645\u0627 \u064a\u064f\u0638\u0647\u0631 \u062a\u0642\u0646\u064a\u0629 \u062a\u0646\u0634\u064a\u0637 \u0627\u0644\u062d\u0645\u0636 \u0627\u0644\u0646\u0648\u0648\u064a \u0627\u0644\u0631\u064a\u0628\u0648\u0632\u064a (RNAa) \u0643\u0637\u0631\u064a\u0642\u0629 \u062b\u0648\u0631\u064a\u0629 \u0641\u064a \u0627\u0644\u0645\u0645\u0627\u0631\u0633\u0629 \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629\u060c \u0648\u064a\u064f\u0642\u062f\u0645 \u0627\u0644\u0623\u0645\u0644 \u0644\u062d\u0627\u0644\u0627\u062a \u0643\u0627\u0646\u062a \u062a\u064f\u0639\u062a\u0628\u0631 \u0633\u0627\u0628\u0642\u064b\u0627 \u063a\u064a\u0631 \u0642\u0627\u0628\u0644\u0629 \u0644\u0644\u0639\u0644\u0627\u062c.&quot;\u201c<\/p>\n\n\n\n<h2 class=\"wp-block-heading\">\u0645\u0627 \u0647\u0648 RAG-18 saRNA\u061f<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>RAG-18 \u0647\u0648 \u0623\u0648\u0644 \u0645\u0631\u0634\u062d \u0645\u0646 \u0646\u0648\u0639\u0647 \u0645\u0646 \u0646\u0648\u0639 saRNA \u0645\u0635\u0645\u0645 \u0644\u0627\u0633\u062a\u0647\u062f\u0627\u0641 \u0648\u062a\u0646\u0634\u064a\u0637 \u0627\u0644\u062a\u0639\u0628\u064a\u0631 \u0627\u0644\u062c\u064a\u0646\u064a UTRN \u0641\u064a \u0627\u0644\u062e\u0644\u0627\u064a\u0627 \u0627\u0644\u0639\u0636\u0644\u064a\u0629 \u0639\u0644\u0649 \u0648\u062c\u0647 \u0627\u0644\u062a\u062d\u062f\u064a\u062f \u0639\u0628\u0631 \u0622\u0644\u064a\u0629 RNAa.<\/strong> \u0625\u0646 \u0628\u0631\u0648\u062a\u064a\u0646 \u0627\u0644\u064a\u0648\u062a\u0631\u0648\u0641\u064a\u0646 \u0627\u0644\u0645\u0634\u0641\u0631 \u0628\u0648\u0627\u0633\u0637\u0629 \u062c\u064a\u0646 UTRN \u064a\u0634\u0628\u0647 \u0645\u0646 \u0627\u0644\u0646\u0627\u062d\u064a\u0629 \u0627\u0644\u0647\u064a\u0643\u0644\u064a\u0629 \u0648\u0627\u0644\u0648\u0638\u064a\u0641\u064a\u0629 \u0628\u0631\u0648\u062a\u064a\u0646 \u0627\u0644\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646\u060c \u0648\u064a\u0645\u0643\u0646 \u0623\u0646 \u064a\u0624\u062f\u064a \u062a\u0646\u0638\u064a\u0645\u0647 \u0625\u0644\u0649 \u0627\u0633\u062a\u0628\u062f\u0627\u0644 \u0648\u0638\u064a\u0641\u064a \u0644\u0644\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0627\u0644\u0645\u0641\u0642\u0648\u062f \u0641\u064a \u062e\u0644\u0627\u064a\u0627 \u0627\u0644\u0639\u0636\u0644\u0627\u062a DMD\u060c \u0645\u0645\u0627 \u064a\u0648\u0641\u0631 \u0639\u0644\u0627\u062c\u064b\u0627 \u0644\u062c\u0645\u064a\u0639 \u0645\u0631\u0636\u0649 DMD \u0628\u063a\u0636 \u0627\u0644\u0646\u0638\u0631 \u0639\u0646 \u0645\u0648\u0642\u0639 \u0627\u0644\u0637\u0641\u0631\u0629 \u0627\u0644\u0645\u062d\u062f\u062f.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u062a\u0634\u064a\u0631 \u0627\u0644\u0628\u064a\u0627\u0646\u0627\u062a \u0645\u0627 \u0642\u0628\u0644 \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629 \u0625\u0644\u0649 \u0623\u0646 RAG-18\u060c \u0627\u0644\u0630\u064a \u062a\u0645 \u062a\u0648\u0635\u064a\u0644\u0647 \u0628\u0627\u0633\u062a\u062e\u062f\u0627\u0645 \u062a\u0642\u0646\u064a\u0629 LiCO\u2122 (\u0627\u0644\u0623\u0648\u0644\u064a\u063a\u0648\u0646\u0648\u0643\u0644\u064a\u0648\u062a\u064a\u062f \u0627\u0644\u0645\u0631\u062a\u0628\u0637 \u0628\u0627\u0644\u062f\u0647\u0648\u0646) \u0627\u0644\u062e\u0627\u0635\u0629 \u0628\u0634\u0631\u0643\u0629 Ractigen\u060c \u0642\u062f \u0631\u0641\u0639 \u0628\u0634\u0643\u0644 \u0641\u0639\u0627\u0644 \u0645\u0646 \u062a\u0639\u0628\u064a\u0631 UTRN\u060c \u0648\u062e\u0641\u0641 \u0645\u0646 \u062a\u0644\u0641 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0648\u062d\u0633\u0646 \u0648\u0638\u064a\u0641\u0629 \u0627\u0644\u0639\u0636\u0644\u0627\u062a\u060c \u0645\u0645\u0627 \u064a\u062f\u0644 \u0639\u0644\u0649 \u0625\u0645\u0643\u0627\u0646\u0627\u062a \u0643\u0628\u064a\u0631\u0629 \u0641\u064a \u0639\u0644\u0627\u062c \u0645\u0631\u0636\u0649 \u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0627\u0644\u062f\u0648\u0634\u064a\u0646\u064a. <strong>\u062d\u0635\u0644 RAG-18 \u0639\u0644\u0649 \u062a\u0635\u0646\u064a\u0641 \u062f\u0648\u0627\u0621 \u0627\u0644\u064a\u062a\u064a\u0645 (ODD) \u0648\u062a\u0635\u0646\u064a\u0641 \u0645\u0631\u0636 \u0627\u0644\u0623\u0637\u0641\u0627\u0644 \u0627\u0644\u0646\u0627\u062f\u0631 (RPDD) \u0645\u0646 \u0625\u062f\u0627\u0631\u0629 \u0627\u0644\u063a\u0630\u0627\u0621 \u0648\u0627\u0644\u062f\u0648\u0627\u0621 \u0627\u0644\u0623\u0645\u0631\u064a\u0643\u064a\u0629 (FDA) \u0641\u064a \u0639\u0627\u0645 2024\u060c \u0645\u0645\u0627 \u064a\u0624\u0643\u062f \u0648\u0639\u062f\u0647 \u0643\u062e\u064a\u0627\u0631 \u0639\u0644\u0627\u062c\u064a \u0644\u0644\u0645\u0631\u0636\u0649 \u0627\u0644\u0630\u064a\u0646 \u064a\u0639\u0627\u0646\u0648\u0646 \u0645\u0646 \u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0627\u0644\u062f\u0648\u0634\u064a\u0646\u064a.<\/strong><\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u062a\u0627\u0628\u0639 \u0647\u0630\u0647 \u0627\u0644\u0635\u0641\u062d\u0629<\/strong>&nbsp;&gt;&gt;&gt;&nbsp;<a href=\"https:\/\/dmdwarrior.com\/ar\/dmd-therapies\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u062c\u0645\u064a\u0639 \u0627\u0644\u062a\u062c\u0627\u0631\u0628 \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629 \u0644\u0645\u0631\u0636 \u062f\u0648\u0634\u064a\u0646<\/a><\/p>","protected":false},"excerpt":{"rendered":"<p>Ractigen Therapeutics, a pioneering developer of small activating RNA (saRNA) therapeutics, today announced the successful dosing of the first patient in its investigator-initiated trial (IIT) of RAG-18 at Peking Union Medical College Hospital (PUMCH), Chinese Academy of Medical Sciences in Beijing. This milestone marks a transformative moment in the fight against Duchenne Muscular Dystrophy (DMD), [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":5316,"comment_status":"open","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[27],"tags":[123,466,467,465,468],"class_list":["post-5315","post","type-post","status-publish","format-standard","has-post-thumbnail","category-research","tag-china","tag-ractigen-therapeutics","tag-rag-18","tag-sarna","tag-utrn-expression"],"_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/posts\/5315","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/comments?post=5315"}],"version-history":[{"count":0,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/posts\/5315\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/media\/5316"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/media?parent=5315"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/categories?post=5315"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/tags?post=5315"}],"curies":[{"name":"\u0648\u0648\u0631\u062f\u0628\u0631\u064a\u0633","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}