{"id":5183,"date":"2025-11-19T18:44:39","date_gmt":"2025-11-19T15:44:39","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=5183"},"modified":"2025-11-19T19:06:37","modified_gmt":"2025-11-19T16:06:37","slug":"avidity-biosciences-announces-u-s-managed-access-program-map-for-investigational-therapy-del-zota-in-dmd44","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/ar\/avidity-biosciences-announces-u-s-managed-access-program-map-for-investigational-therapy-del-zota-in-dmd44\/","title":{"rendered":"Avidity Biosciences \u064a\u0639\u0644\u0646 \u0639\u0646 \u0628\u0631\u0646\u0627\u0645\u062c \u0627\u0644\u0648\u0635\u0648\u0644 \u0627\u0644\u0645\u064f\u062f\u0627\u0631 \u0641\u064a \u0627\u0644\u0648\u0644\u0627\u064a\u0627\u062a \u0627\u0644\u0645\u062a\u062d\u062f\u0629 (MAP) \u0644\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u062a\u062c\u0631\u064a\u0628\u064a del-zota (\u062a\u062e\u0637\u064a \u0627\u0644\u0625\u0643\u0633\u0648\u0646 44)"},"content":{"rendered":"

\u0623\u0639\u0644\u0646\u062a \u0634\u0631\u0643\u0629 Avidity Biosciences \u0639\u0646 \u0628\u0631\u0646\u0627\u0645\u062c \u0627\u0644\u0648\u0635\u0648\u0644 \u0627\u0644\u0645\u064f\u062f\u0627\u0631 (MAP) \u0644\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u062a\u062c\u0631\u064a\u0628\u064a delpacibart zotadirsen (del-zota) \u0644\u0644\u0623\u0634\u062e\u0627\u0635 \u0627\u0644\u0645\u0624\u0647\u0644\u064a\u0646 \u0627\u0644\u0645\u0635\u0627\u0628\u064a\u0646 \u0628\u0637\u0641\u0631\u0627\u062a \u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0642\u0627\u0628\u0644\u0629 \u0644\u062a\u062e\u0637\u064a \u0627\u0644\u0625\u0643\u0633\u0648\u0646 44 (DMD44) \u0641\u064a \u0627\u0644\u0648\u0644\u0627\u064a\u0627\u062a \u0627\u0644\u0645\u062a\u062d\u062f\u0629.<\/p>\n\n\n\n

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\u0628\u0645\u0648\u062c\u0628 \u0628\u0631\u0648\u062a\u0648\u0643\u0648\u0644 \u0639\u0644\u0627\u062c\u064a \u0645\u0639\u062a\u0645\u062f \u0645\u0646 FDA\u060c \u0633\u062a\u0648\u0641\u0631 \u0623\u0641\u064a\u062f\u064a\u062a\u064a \u0639\u0644\u0627\u062c del-zota \u0644\u0644\u0641\u062a\u064a\u0627\u0646 \u0648\u0627\u0644\u0631\u062c\u0627\u0644 \u0627\u0644\u0645\u0624\u0647\u0644\u064a\u0646 \u0627\u0644\u0645\u0635\u0627\u0628\u064a\u0646 \u0628\u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0627\u0644\u0647\u064a\u0643\u0644\u064a 44 \u0645\u0646 \u062e\u0644\u0627\u0644 \u0645\u0642\u062f\u0645\u064a \u0627\u0644\u0631\u0639\u0627\u064a\u0629 \u0627\u0644\u0635\u062d\u064a\u0629 \u0627\u0644\u0645\u0634\u0627\u0631\u0643\u064a\u0646. \u0645\u0646 \u0627\u0644\u0645\u062a\u0648\u0642\u0639 \u0623\u0646 \u064a\u0628\u062f\u0623 \u0627\u0644\u062a\u0633\u062c\u064a\u0644 \u0628\u0646\u0647\u0627\u064a\u0629 \u0627\u0644\u0639\u0627\u0645\u060c \u0648\u0633\u064a\u062a\u0627\u062d \u0644\u0644\u0645\u0634\u0627\u0631\u0643\u064a\u0646 \u0641\u064a \u0628\u0631\u0646\u0627\u0645\u062c EXPLORE44-OLE \u062e\u064a\u0627\u0631 \u0627\u0644\u0627\u0646\u062a\u0642\u0627\u0644 \u0625\u0644\u0649 \u0628\u0631\u0646\u0627\u0645\u062c MAP \u0628\u0639\u062f \u0625\u0643\u0645\u0627\u0644 \u0639\u0627\u0645\u064a\u0646 \u0645\u0646 \u0627\u0644\u0639\u0644\u0627\u062c.<\/p>\n\n\n\n

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\u0627\u0646\u0636\u0645\u062a \u0623\u0641\u064a\u062f\u064a\u062a\u064a \u0625\u0644\u0649 FDA \u0641\u064a \u0645\u0633\u0627\u0631 \u0627\u0644\u062a\u0642\u062f\u0645 \u0628\u0637\u0644\u0628 \u0627\u0644\u062d\u0635\u0648\u0644 \u0639\u0644\u0649 \u062a\u0631\u062e\u064a\u0635 \u0628\u064a\u0648\u0644\u0648\u062c\u064a \u062c\u062f\u064a\u062f (BLA) \u0644\u0640 del-zota \u0628\u0639\u062f \u0627\u062c\u062a\u0645\u0627\u0639 \u0645\u0627 \u0642\u0628\u0644 \u0627\u0644\u062d\u0635\u0648\u0644 \u0639\u0644\u0649 \u062a\u0631\u062e\u064a\u0635 \u0628\u064a\u0648\u0644\u0648\u062c\u064a \u062c\u062f\u064a\u062f (BLA) \u0641\u064a \u0623\u0643\u062a\u0648\u0628\u0631 2025\u060c \u0648\u0645\u0646 \u0627\u0644\u0645\u0642\u0631\u0631 \u062a\u0642\u062f\u064a\u0645 \u0627\u0644\u0637\u0644\u0628 \u0641\u064a \u0639\u0627\u0645 2026 \u0644\u0644\u062d\u0635\u0648\u0644 \u0639\u0644\u0649 \u0645\u0648\u0627\u0641\u0642\u0629 \u0633\u0631\u064a\u0639\u0629. \u0633\u064a\u0646\u062a\u0642\u0644 \u0627\u0644\u0645\u0634\u0627\u0631\u0643\u0648\u0646 \u0625\u0644\u0649 \u062a\u0648\u0631\u064a\u062f \u0627\u0644\u0623\u062f\u0648\u064a\u0629 \u0627\u0644\u062a\u062c\u0627\u0631\u064a\u0629 \u0639\u0646\u062f \u0627\u0644\u0645\u0648\u0627\u0641\u0642\u0629 \u0627\u0644\u0645\u062d\u062a\u0645\u0644\u0629 \u0639\u0644\u0649 FDA \u0648\u062a\u0648\u0627\u0641\u0631 \u0627\u0644\u0645\u0646\u062a\u062c \u0645\u0633\u062a\u0642\u0628\u0644\u064b\u0627.<\/a><\/p>\n\n\n\n

\u062a\u0627\u0628\u0639 \u0647\u0630\u0647 \u0627\u0644\u0635\u0641\u062d\u0629<\/strong> >>> \u062c\u0645\u064a\u0639 \u0627\u0644\u062a\u062c\u0627\u0631\u0628 \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629 \u0644\u0645\u0631\u0636 \u062f\u0648\u0634\u064a\u0646<\/a><\/p>","protected":false},"excerpt":{"rendered":"

Avidity Biosciences announced its Managed Access Program (MAP) for investigational therapy delpacibart zotadirsen (del-zota) for eligible people with Duchenne muscular dystrophy mutations amenable to exon 44 skipping (DMD44) in the United States. “We recognize the considerable needs facing the DMD44 community given there are no approved exon skipping therapies for this disease as well as […]<\/p>\n","protected":false},"author":1,"featured_media":5185,"comment_status":"open","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[281],"tags":[126,298,397,129,141,127,246],"class_list":["post-5183","post","type-post","status-publish","format-standard","has-post-thumbnail","category-press-releases","tag-avidity-biosciences","tag-del-zota","tag-delpacibart-zotadirsen","tag-dmd44","tag-exon-44","tag-exon-44-skipping","tag-exon-44-skipping-therapies"],"_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/posts\/5183","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/comments?post=5183"}],"version-history":[{"count":0,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/posts\/5183\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/media\/5185"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/media?parent=5183"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/categories?post=5183"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/tags?post=5183"}],"curies":[{"name":"\u0648\u0648\u0631\u062f\u0628\u0631\u064a\u0633","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}