{"id":4964,"date":"2025-10-30T15:41:35","date_gmt":"2025-10-30T12:41:35","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=4964"},"modified":"2025-11-03T19:56:20","modified_gmt":"2025-11-03T16:56:20","slug":"regenxbio-announces-completion-pivotal-enrollment-and-initiates","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/ar\/regenxbio-announces-completion-pivotal-enrollment-and-initiates\/","title":{"rendered":"\u0623\u0639\u0644\u0646\u062a \u0634\u0631\u0643\u0629 REGENXBIO \u0639\u0646 \u0627\u0643\u062a\u0645\u0627\u0644 \u0627\u0644\u062a\u0633\u062c\u064a\u0644 \u0627\u0644\u0645\u062d\u0648\u0631\u064a \u0644\u0640 RGX-202 \u0648\u0628\u062f\u0621 \u0627\u0644\u0625\u0646\u062a\u0627\u062c \u0627\u0644\u062a\u062c\u0627\u0631\u064a \u0641\u064a \u0628\u0631\u0646\u0627\u0645\u062c \u0627\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u062c\u064a\u0646\u064a \u0644\u062f\u0648\u0634\u064a\u0646"},"content":{"rendered":"<p class=\"wp-block-paragraph\">\u0623\u0639\u0644\u0646\u062a \u0634\u0631\u0643\u0629 REGENXBIO \u0639\u0646 \u0627\u0643\u062a\u0645\u0627\u0644 \u0627\u0644\u062a\u0633\u062c\u064a\u0644 \u0641\u064a \u062a\u062c\u0631\u0628\u0629 AFFINITY DUCHENNE \u0627\u0644\u0645\u062d\u0648\u0631\u064a\u0629 \u0644\u0640 RGX-202\u060c \u0648\u0647\u0648 \u0639\u0644\u0627\u062c \u062c\u064a\u0646\u064a \u062a\u062c\u0631\u064a\u0628\u064a \u0644\u0639\u0644\u0627\u062c \u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u062f\u0648\u0634\u064a\u0646\u060c \u0628\u0627\u0644\u0625\u0636\u0627\u0641\u0629 \u0625\u0644\u0649 \u0627\u0644\u0625\u0646\u062a\u0627\u062c \u0627\u0644\u0646\u0627\u062c\u062d \u0644\u0644\u062f\u0641\u0639\u0627\u062a \u0627\u0644\u0623\u0648\u0644\u0649 \u0627\u0644\u0645\u062e\u0635\u0635\u0629 \u0644\u0644\u062a\u0648\u0631\u064a\u062f \u0627\u0644\u062a\u062c\u0627\u0631\u064a. <strong>\u0627\u0642\u0631\u0623 \u0627\u0644\u0645\u0632\u064a\u062f<\/strong>: <a href=\"https:\/\/clinicaltrials.gov\/study\/NCT05693142\" target=\"_blank\" rel=\"noreferrer noopener\">NCT05693142<\/a>.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u201c&quot;\u064a\u062d\u062a\u0627\u062c \u0645\u062c\u062a\u0645\u0639 \u062f\u0648\u0634\u064a\u0646 \u0628\u0634\u0643\u0644 \u0639\u0627\u062c\u0644 \u0625\u0644\u0649 \u062e\u064a\u0627\u0631\u0627\u062a \u0639\u0644\u0627\u062c\u064a\u0629 \u062c\u062f\u064a\u062f\u0629 \u062a\u0648\u0641\u0631 \u0646\u062a\u0627\u0626\u062c \u062f\u0627\u0626\u0645\u0629 \u0648\u0622\u0645\u0646\u0629 \u0648\u064a\u0645\u0643\u0646\u0647\u0627 \u062a\u063a\u064a\u064a\u0631 \u0645\u0633\u0627\u0631 \u0647\u0630\u0627 \u0627\u0644\u0645\u0631\u0636 \u0627\u0644\u062a\u0646\u0643\u0633\u064a \u0628\u0634\u0643\u0644 \u0645\u0644\u0645\u0648\u0633. <strong>\u0648\u0642\u0627\u0644 \u0643\u0648\u0631\u0627\u0646 \u0633\u064a\u0645\u0628\u0633\u0648\u0646\u060c \u0627\u0644\u0631\u0626\u064a\u0633 \u0648\u0627\u0644\u0645\u062f\u064a\u0631 \u0627\u0644\u062a\u0646\u0641\u064a\u0630\u064a \u0644\u0634\u0631\u0643\u0629 REGENXBIO: &quot;\u0625\u0646 \u0625\u0643\u0645\u0627\u0644 \u0647\u0630\u0647 \u0627\u0644\u062a\u062c\u0631\u0628\u0629 \u0627\u0644\u0645\u062d\u0648\u0631\u064a\u0629 \u0648\u062a\u0635\u0646\u064a\u0639 \u0627\u0644\u062c\u0631\u0639\u0627\u062a \u0627\u0644\u0623\u0648\u0644\u0649 \u0627\u0644\u0645\u062e\u0635\u0635\u0629 \u0644\u0644\u0627\u0633\u062a\u062e\u062f\u0627\u0645 \u0627\u0644\u062a\u062c\u0627\u0631\u064a \u062f\u0627\u062e\u0644 \u0627\u0644\u0634\u0631\u0643\u0629 \u064a\u0642\u0631\u0628\u0646\u0627 \u0623\u0643\u062b\u0631 \u0645\u0646 \u062a\u0642\u062f\u064a\u0645 RGX-202 \u0643\u0623\u0641\u0636\u0644 \u0639\u0644\u0627\u062c \u062c\u064a\u0646\u064a \u0645\u062d\u062a\u0645\u0644 \u0641\u064a \u0641\u0626\u062a\u0647 \u0644\u0645\u0631\u0636\u0649 \u062f\u0648\u0634\u064a\u0646 \u0630\u0648\u064a \u0627\u0644\u062e\u064a\u0627\u0631\u0627\u062a \u0627\u0644\u0645\u062d\u062f\u0648\u062f\u0629&quot;.<\/strong> \u201c&quot;\u0625\u0646 \u0627\u0644\u0646\u0647\u062c \u0627\u0644\u0639\u0644\u0627\u062c\u064a \u0627\u0644\u0645\u062a\u0645\u0627\u064a\u0632 \u0648\u0631\u0627\u0621 RGX-202\u060c \u0628\u0645\u0627 \u0641\u064a \u0630\u0644\u0643 \u0645\u0633\u062a\u0648\u064a\u0627\u062a \u0646\u0642\u0627\u0621 \u0627\u0644\u0645\u0646\u062a\u062c \u0627\u0644\u0631\u0627\u0626\u062f\u0629 \u0641\u064a \u0627\u0644\u0635\u0646\u0627\u0639\u0629 \u0648\u0627\u0644\u0628\u0646\u064a\u0629 \u0627\u0644\u062c\u062f\u064a\u062f\u0629 \u0645\u0639 \u0627\u0644\u0645\u062c\u0627\u0644 \u0627\u0644\u0637\u0631\u0641\u064a C\u060c \u0623\u062f\u0649 \u0625\u0644\u0649 \u0645\u0644\u0641 \u062a\u0639\u0631\u064a\u0641 \u0625\u064a\u062c\u0627\u0628\u064a \u0644\u0644\u0633\u0644\u0627\u0645\u0629 \u0648\u0627\u0644\u0641\u0639\u0627\u0644\u064a\u0629\u060c \u0645\u0639 \u0641\u0627\u0626\u062f\u0629 \u0648\u0638\u064a\u0641\u064a\u0629 \u0645\u062a\u0633\u0642\u0629 \u0634\u0648\u0647\u062f\u062a \u0641\u064a \u0627\u0644\u0645\u0631\u062d\u0644\u0629 \u0627\u0644\u0623\u0648\u0644\u0649 \/ \u0627\u0644\u062b\u0627\u0646\u064a\u0629. <strong>\u0648\u0645\u0639 \u0647\u0630\u0647 \u0627\u0644\u0646\u062a\u0627\u0626\u062c \u0627\u0644\u0645\u0634\u062c\u0639\u0629 \u0644\u0644\u063a\u0627\u064a\u0629\u060c \u0641\u0625\u0646\u0646\u0627 \u0645\u0644\u062a\u0632\u0645\u0648\u0646 \u0628\u062a\u0648\u0633\u064a\u0639 \u0625\u0645\u062f\u0627\u062f\u0627\u062a\u0646\u0627 \u0627\u0644\u062a\u062c\u0627\u0631\u064a\u0629 \u0648\u0645\u0634\u0627\u0631\u0643\u0629 \u0627\u0644\u0628\u064a\u0627\u0646\u0627\u062a \u0627\u0644\u0645\u062d\u0648\u0631\u064a\u0629 \u0641\u064a \u0623\u0648\u0627\u0626\u0644 \u0627\u0644\u0631\u0628\u0639 \u0627\u0644\u062b\u0627\u0646\u064a \u0645\u0646 \u0627\u0644\u0639\u0627\u0645 \u0627\u0644\u0645\u0642\u0628\u0644&quot;.\u201d<\/strong><\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u064a\u062a\u0639\u0644\u0645 \u0623\u0643\u062b\u0631<\/strong>: <a href=\"https:\/\/dmdwarrior.com\/ar\/rgx-202-gene-therapy-phase-3-clinical-trial-nct05693142\/\">\u0628\u062f\u0623\u062a \u0627\u0644\u0645\u0631\u062d\u0644\u0629 \u0627\u0644\u062b\u0627\u0644\u062b\u0629 \u0645\u0646 \u0627\u0644\u062a\u062c\u0627\u0631\u0628 \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629 \u0644\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u062c\u064a\u0646\u064a RGX-202<\/a><\/p>\n\n\n\n<h2 class=\"wp-block-heading\">\u0627\u0644\u0646\u062a\u0627\u0626\u062c \u0627\u0644\u0631\u0626\u064a\u0633\u064a\u0629 \u062d\u0648\u0644 RGX-202<\/h2>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u0623\u0638\u0647\u0631 \u0627\u0644\u0645\u0631\u0636\u0649 \u0627\u0644\u0630\u064a\u0646 \u0639\u0648\u0644\u062c\u0648\u0627 \u0628\u0627\u0633\u062a\u062e\u062f\u0627\u0645 RGX-202 \u062a\u0639\u0628\u064a\u0631\u064b\u0627 \u062b\u0627\u0628\u062a\u064b\u0627 \u0648\u0642\u0648\u064a\u064b\u0627 \u0639\u0646 \u0627\u0644\u0645\u064a\u0643\u0631\u0648\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0648\u062a\u062d\u0633\u0646\u064b\u0627 \u0648\u0638\u064a\u0641\u064a\u064b\u0627 \u0645\u0642\u0627\u0631\u0646\u0629 \u0628\u0627\u0644\u062a\u0627\u0631\u064a\u062e \u0627\u0644\u0637\u0628\u064a\u0639\u064a \u0641\u064a \u0627\u0644\u062c\u0632\u0621 \u0627\u0644\u0623\u0648\u0644 \/ \u0627\u0644\u062b\u0627\u0646\u064a \u0645\u0646 \u062a\u062c\u0631\u0628\u0629 AFFINITY DUCHENNE \u0627\u0644\u062a\u064a \u062a\u062f\u0639\u0645 \u0627\u0644\u0645\u0648\u0627\u0641\u0642\u0629 \u0627\u0644\u0645\u062d\u062a\u0645\u0644\u0629 \u0645\u0646 \u062e\u0644\u0627\u0644 \u0645\u0633\u0627\u0631 \u0627\u0644\u0645\u0648\u0627\u0641\u0642\u0629 \u0627\u0644\u0633\u0631\u064a\u0639\u0629<\/li>\n\n\n\n<li>\u062a\u0633\u062a\u0645\u0631 REGENXBIO \u0641\u064a \u062a\u0633\u062c\u064a\u0644 \u0627\u0644\u0645\u0631\u0636\u0649 \u0641\u064a \u0627\u0644\u062a\u062c\u0631\u0628\u0629 \u0627\u0644\u062a\u0623\u0643\u064a\u062f\u064a\u0629<\/li>\n\n\n\n<li>\u0627\u0644\u062f\u0641\u0639\u0627\u062a \u0627\u0644\u0623\u0648\u0644\u0649 \u0627\u0644\u0645\u062e\u0635\u0635\u0629 \u0644\u0644\u062a\u0648\u0631\u064a\u062f \u0627\u0644\u062a\u062c\u0627\u0631\u064a \u062a\u0645 \u062a\u0635\u0646\u064a\u0639\u0647\u0627 \u0641\u064a \u0645\u0631\u0643\u0632 \u0627\u0628\u062a\u0643\u0627\u0631 \u0627\u0644\u062a\u0635\u0646\u064a\u0639 \u0627\u0644\u062f\u0627\u062e\u0644\u064a\n<ul class=\"wp-block-list\">\n<li>\u0627\u0644\u0642\u062f\u0631\u0629 \u0639\u0644\u0649 \u0625\u0646\u062a\u0627\u062c \u0645\u0627 \u064a\u0635\u0644 \u0625\u0644\u0649 2500 \u062c\u0631\u0639\u0629 \u0645\u0646 RGX-202 \u0633\u0646\u0648\u064a\u064b\u0627<\/li>\n<\/ul>\n<\/li>\n\n\n\n<li>\u0645\u0646 \u0627\u0644\u0645\u062a\u0648\u0642\u0639 \u0627\u0644\u0622\u0646 \u0635\u062f\u0648\u0631 \u0627\u0644\u0628\u064a\u0627\u0646\u0627\u062a \u0627\u0644\u0645\u062d\u0648\u0631\u064a\u0629 \u0627\u0644\u0631\u0626\u064a\u0633\u064a\u0629 \u0641\u064a \u0623\u0648\u0627\u0626\u0644 \u0627\u0644\u0631\u0628\u0639 \u0627\u0644\u062b\u0627\u0646\u064a \u0645\u0646 \u0639\u0627\u0645 2026 \u0648\u062a\u0642\u062f\u064a\u0645 \u0637\u0644\u0628 BLA \u0641\u064a \u0645\u0646\u062a\u0635\u0641 \u0639\u0627\u0645 2026<\/li>\n<\/ul>\n\n\n\n<h2 class=\"wp-block-heading\">\u0622\u0644\u064a\u0629 \u0639\u0645\u0644 RGX-202<\/h2>\n\n\n\n<figure class=\"wp-block-embed is-type-video is-provider-vimeo wp-block-embed-vimeo\"><div class=\"wp-block-embed__wrapper\">\n<iframe loading=\"lazy\" title=\"\u0641\u064a\u062f\u064a\u0648 \u0627\u0644\u0645\u0631\u064a\u0636 \u0627\u0644\u0646\u0647\u0627\u0626\u064a 21 \u0645\u0627\u064a\u0648 2025 (1080 \u0628\u0643\u0633\u0644)\" src=\"https:\/\/player.vimeo.com\/video\/1092247292?dnt=1&amp;app_id=122963\" width=\"696\" height=\"392\" frameborder=\"0\" allow=\"autoplay; fullscreen; picture-in-picture; clipboard-write; encrypted-media; web-share\" referrerpolicy=\"strict-origin-when-cross-origin\"><\/iframe>\n<\/div><\/figure>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u0627\u0642\u0631\u0623 \u0627\u0644\u0645\u0632\u064a\u062f<\/strong>:\u00a0<a href=\"https:\/\/dmdwarrior.com\/ar\/dmd-therapies\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u0627\u0644\u062a\u062c\u0627\u0631\u0628 \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629 \u0644\u0645\u0631\u0636 \u062f\u0648\u0634\u064a\u0646 (\u0642\u0627\u0626\u0645\u0629 \u0628\u062c\u0645\u064a\u0639 \u0627\u0644\u0623\u0628\u062d\u0627\u062b)<\/a><\/p>","protected":false},"excerpt":{"rendered":"<p>REGENXBIO announced the completion of enrollment in the AFFINITY DUCHENNE pivotal trial of RGX-202, an investigational gene therapy for the treatment of Duchenne muscular dystrophy, as well as the successful production of the first batches intended for commercial supply. Read More: NCT05693142. &#8220;The Duchenne community urgently needs new treatment options that provide durable, safe outcomes [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":4965,"comment_status":"open","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[281],"tags":[61,107,108],"class_list":["post-4964","post","type-post","status-publish","format-standard","has-post-thumbnail","category-press-releases","tag-gene-therapy","tag-regenxbio","tag-rgx-202"],"_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/posts\/4964","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/comments?post=4964"}],"version-history":[{"count":0,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/posts\/4964\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/media\/4965"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/media?parent=4964"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/categories?post=4964"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/tags?post=4964"}],"curies":[{"name":"\u0648\u0648\u0631\u062f\u0628\u0631\u064a\u0633","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}