{"id":4942,"date":"2025-11-20T19:30:28","date_gmt":"2025-11-20T16:30:28","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=4942"},"modified":"2026-03-17T10:55:13","modified_gmt":"2026-03-17T07:55:13","slug":"creatine-kinase-ck-dystrophin-level-nsaa-score-in-elevidys-gene-therapy","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/ar\/creatine-kinase-ck-dystrophin-level-nsaa-score-in-elevidys-gene-therapy\/","title":{"rendered":"\u0643\u064a\u0646\u0627\u0632 \u0627\u0644\u0643\u0631\u064a\u0627\u062a\u064a\u0646 (CK)\u060c \u0648\u0645\u0633\u062a\u0648\u0649 \u0627\u0644\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0648\u062f\u0631\u062c\u0629 NSAA \u0641\u064a \u0627\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u062c\u064a\u0646\u064a Elevidys"},"content":{"rendered":"<p class=\"wp-block-paragraph\">\u0644\u0627 \u064a\u0632\u0627\u0644 \u0645\u0646 \u0627\u0644\u0645\u062b\u064a\u0631 \u0644\u0644\u0641\u0636\u0648\u0644 \u0645\u0639\u0631\u0641\u0629 \u0645\u0642\u062f\u0627\u0631 \u0627\u0646\u062e\u0641\u0627\u0636 \u0645\u0633\u062a\u0648\u064a\u0627\u062a \u0643\u064a\u0646\u0627\u0632 \u0627\u0644\u0643\u0631\u064a\u0627\u062a\u064a\u0646 (CK)\u060c \u0648\u062f\u0631\u062c\u0629 NSAA\u060c \u0648\u0632\u064a\u0627\u062f\u0629 \u0645\u0633\u062a\u0648\u064a\u0627\u062a \u0627\u0644\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0627\u0644\u0637\u0628\u064a\u0639\u064a\u0629 \u0644\u062f\u0649 \u0627\u0644\u0623\u0637\u0641\u0627\u0644 \u0627\u0644\u0645\u0635\u0627\u0628\u064a\u0646 \u0628\u0645\u0631\u0636 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a \u0627\u0644\u0630\u064a\u0646 \u064a\u062a\u0644\u0642\u0648\u0646 ELEVIDYS (delandistrogene moxeparvovec-rokl)\u060c \u0648\u0647\u0648 \u0623\u062d\u062f \u0623\u063a\u0644\u0649 \u0627\u0644\u0639\u0644\u0627\u062c\u0627\u062a \u0641\u064a \u0627\u0644\u0639\u0627\u0644\u0645 \u0627\u0644\u062a\u064a \u0637\u0648\u0631\u0647\u0627 Sarepta Therapeutics \u0644\u0639\u0644\u0627\u062c \u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u062f\u0648\u0634\u064a\u0646.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">ELEVIDYS (delandistrogene moxeparvovec-rokl)\u060c \u0627\u0644\u0630\u064a \u0637\u0648\u0631\u062a\u0647 Sarepta Therapeutics\u060c \u0647\u0648 \u0639\u0644\u0627\u062c \u062c\u064a\u0646\u064a \u0644\u0645\u0631\u0629 \u0648\u0627\u062d\u062f\u0629 \u0644\u0641\u064a\u0631\u0648\u0633 \u0627\u0644\u063a\u062f\u0629 \u0627\u0644\u062f\u0631\u0642\u064a\u0629 \u0627\u0644\u0645\u0631\u062a\u0628\u0637 \u0628\u0627\u0644\u062c\u064a\u0646 AAV (Adeno-associated virus) \u062a\u0645\u062a \u0627\u0644\u0645\u0648\u0627\u0641\u0642\u0629 \u0639\u0644\u064a\u0647 \u0641\u064a \u064a\u0648\u0646\u064a\u0648 2023 \u0641\u064a \u0627\u0644\u0648\u0644\u0627\u064a\u0627\u062a \u0627\u0644\u0645\u062a\u062d\u062f\u0629 \u0644\u0645\u0631\u0636\u0649 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0623\u0637\u0641\u0627\u0644 \u0627\u0644\u0645\u062a\u0646\u0642\u0644\u064a\u0646 \u0627\u0644\u0630\u064a\u0646 \u062a\u062a\u0631\u0627\u0648\u062d \u0623\u0639\u0645\u0627\u0631\u0647\u0645 \u0628\u064a\u0646 4 \u06485 \u0633\u0646\u0648\u0627\u062a\u060c \u0648\u062a\u0645 \u062a\u0648\u0633\u064a\u0639 \u0646\u0637\u0627\u0642\u0647 \u0644\u0627\u062d\u0642\u064b\u0627. &gt;&gt;&gt; <a href=\"https:\/\/investorrelations.sarepta.com\/news-releases\/news-release-details\/sarepta-therapeutics-announces-fda-approval-elevidys-first-gene\" target=\"_blank\" rel=\"noreferrer noopener\">investorrelations.sarepta.com<\/a><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u062a\u0645 \u062a\u0635\u0645\u064a\u0645\u0647 \u0644\u062a\u0648\u0635\u064a\u0644 \u0627\u0644\u062c\u064a\u0646 \u0627\u0644\u0630\u064a \u064a\u0634\u0641\u0631 \u0628\u0631\u0648\u062a\u064a\u0646 \u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0627\u0644\u062f\u0642\u064a\u0642 (\u062d\u0648\u0627\u0644\u064a 138 \u0643\u064a\u0644\u0648 \u062f\u0627\u0644\u062a\u0648\u0646 \u0645\u0642\u0627\u0628\u0644 \u0627\u0644\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0627\u0644\u0637\u0628\u064a\u0639\u064a \u0627\u0644\u0630\u064a \u064a\u0628\u0644\u063a \u0648\u0632\u0646\u0647 \u062d\u0648\u0627\u0644\u064a 427 \u0643\u064a\u0644\u0648 \u062f\u0627\u0644\u062a\u0648\u0646) \u0625\u0644\u0649 \u062e\u0644\u0627\u064a\u0627 \u0627\u0644\u0639\u0636\u0644\u0627\u062a. &gt;&gt;&gt; <a href=\"https:\/\/pubmed.ncbi.nlm.nih.gov\/37566211\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u0628\u0628\u0645\u062f<\/a><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0641\u064a \u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a\u060c \u064a\u0624\u062f\u064a \u063a\u064a\u0627\u0628 \u0627\u0644\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0623\u0648 \u0646\u0642\u0635\u0647 \u0627\u0644\u0634\u062f\u064a\u062f \u0625\u0644\u0649 \u062a\u0644\u0641 \u062e\u0644\u0627\u064a\u0627 \u0627\u0644\u0639\u0636\u0644\u0627\u062a\u061b \u0648\u062a\u0631\u062a\u0641\u0639 \u0645\u0624\u0634\u0631\u0627\u062a \u0645\u062b\u0644 \u0643\u064a\u0646\u0627\u0632 \u0627\u0644\u0643\u0631\u064a\u0627\u062a\u064a\u0646 (CK) \u0645\u0639 \u062a\u062f\u0647\u0648\u0631 \u0623\u0644\u064a\u0627\u0641 \u0627\u0644\u0639\u0636\u0644\u0627\u062a. \u0644\u0630\u0644\u0643\u060c \u064a\u064f\u0646\u0638\u0631 \u0641\u064a \u0645\u0624\u0634\u0631\u064a\u0646 \u062d\u064a\u0648\u064a\u064a\u0646 \u0628\u062f\u064a\u0644\u064a\u0646 \u0641\u064a \u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a:<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u0645\u0633\u062a\u0648\u064a\u0627\u062a CK\u060c \u0643\u0645\u0624\u0634\u0631 \u0639\u0644\u0649 \u062a\u0644\u0641 \u0627\u0644\u0639\u0636\u0644\u0627\u062a\/\u062a\u0633\u0631\u0628\u0647\u0627 \u0625\u0644\u0649 \u0627\u0644\u062f\u0645 &gt; <a href=\"https:\/\/dmdwarrior.com\/ar\/what-is-creatine-kinase-ck\/\" target=\"_blank\" data-type=\"post\" data-id=\"2167\" rel=\"noreferrer noopener\">\u0645\u0627 \u0647\u0648 \u0627\u0644\u0643\u0631\u064a\u0627\u062a\u064a\u0646 \u0643\u064a\u0646\u0627\u0632\u061f<\/a><\/li>\n\n\n\n<li>\u0645\u0633\u062a\u0648\u064a\u0627\u062a \u0627\u0644\u062a\u0639\u0628\u064a\u0631 \u0639\u0646 \u0627\u0644\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 (\u0623\u0648 \u0641\u064a \u0647\u0630\u0647 \u0627\u0644\u062d\u0627\u0644\u0629 \u0627\u0644\u0645\u064a\u0643\u0631\u0648\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646) \u0641\u064a \u0623\u0646\u0633\u062c\u0629 \u0627\u0644\u0639\u0636\u0644\u0627\u062a<\/li>\n<\/ul>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"the-core-questions-about-creatine-kinase-ck-dystrophin-level-and-nsaa-score-in-elevidys-gene-therapy\"><strong>\u0627\u0644\u0623\u0633\u0626\u0644\u0629 \u0627\u0644\u0623\u0633\u0627\u0633\u064a\u0629 \u062d\u0648\u0644 \u0627\u0644\u0643\u0631\u064a\u0627\u062a\u064a\u0646 \u0643\u064a\u0646\u0627\u0632 (CK)\u060c \u0648\u0645\u0633\u062a\u0648\u0649 \u0627\u0644\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0648\u062f\u0631\u062c\u0629 NSAA \u0641\u064a \u0627\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u062c\u064a\u0646\u064a Elevidys:<\/strong><\/h2>\n\n\n\n<ul class=\"wp-block-list\">\n<li><strong>\u0628\u0639\u062f \u0627\u0644\u0639\u0644\u0627\u062c \u0628\u0627\u0633\u062a\u062e\u062f\u0627\u0645 ELEVIDYS \u0639\u0646\u062f \u0627\u0644\u0623\u0637\u0641\u0627\u0644 \u0627\u0644\u0645\u0635\u0627\u0628\u064a\u0646 \u0628\u0645\u0631\u0636 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a\u060c \u0645\u0627 \u0645\u0642\u062f\u0627\u0631 \u0627\u0646\u062e\u0641\u0627\u0636 \u0645\u0633\u062a\u0648\u064a\u0627\u062a CK\u060c \u0648\u0645\u0627 \u0645\u0642\u062f\u0627\u0631 \u0632\u064a\u0627\u062f\u0629 \u0627\u0644\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646\/\u0627\u0644\u0645\u064a\u0643\u0631\u0648\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646\u061f<\/strong><\/li>\n<\/ul>\n\n\n\n<ul class=\"wp-block-list\">\n<li><strong>\u0645\u0627 \u0647\u064a \u0646\u0633\u0628\u0629 \u0627\u0644\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0627\u0644\u0628\u0634\u0631\u064a \u0627\u0644\u0637\u0628\u064a\u0639\u064a \u0627\u0644\u062a\u064a \u064a\u0645\u062b\u0644\u0647\u0627 \u0645\u0633\u062a\u0648\u0649 \u0627\u0644\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0627\u0644\u0635\u063a\u064a\u0631 \u0627\u0644\u0630\u064a \u062a\u0645 \u062a\u062d\u0642\u064a\u0642\u0647 \u0628\u0639\u062f \u0627\u0644\u0639\u0644\u0627\u062c\u061f<\/strong><\/li>\n<\/ul>\n\n\n\n<div class=\"wp-block-rank-math-toc-block\" id=\"rank-math-toc\"><h2>\u062c\u062f\u0648\u0644 \u0627\u0644\u0645\u062d\u062a\u0648\u064a\u0627\u062a<\/h2><nav><ul><li><a href=\"#the-core-questions-about-creatine-kinase-ck-dystrophin-level-and-nsaa-score-in-elevidys-gene-therapy\">\u0627\u0644\u0623\u0633\u0626\u0644\u0629 \u0627\u0644\u0623\u0633\u0627\u0633\u064a\u0629 \u062d\u0648\u0644 \u0627\u0644\u0643\u0631\u064a\u0627\u062a\u064a\u0646 \u0643\u064a\u0646\u0627\u0632 (CK)\u060c \u0648\u0645\u0633\u062a\u0648\u0649 \u0627\u0644\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0648\u062f\u0631\u062c\u0629 NSAA \u0641\u064a \u0627\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u062c\u064a\u0646\u064a Elevidys:<\/a><\/li><li><a href=\"#how-much-micro-dystrophin-is-produced-by-elevidys\">\u0645\u0627 \u0647\u064a \u0643\u0645\u064a\u0629 \u0627\u0644\u0645\u064a\u0643\u0631\u0648 \u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0627\u0644\u062a\u064a \u064a\u0646\u062a\u062c\u0647\u0627 Elevidys\u061f<\/a><\/li><li><a href=\"#elevidys-alan-cocuklarda-north-star-ambulatuvar-degerlendirmesi-bazen-nsaa-veya-north-star-olarak-da-adlandirilir-puani-ne-kadar-artti\">\u0645\u0627 \u0647\u0648 \u0645\u0642\u062f\u0627\u0631 \u0627\u0644\u0632\u064a\u0627\u062f\u0629 \u0641\u064a \u062f\u0631\u062c\u0629 NSAA \u0644\u062f\u0649 \u0627\u0644\u0623\u0637\u0641\u0627\u0644 \u0627\u0644\u0630\u064a\u0646 \u062d\u0635\u0644\u0648\u0627 \u0639\u0644\u0649 Elevidys\u061f<\/a><ul><li><a href=\"#what-is-north-star-ambulatory-assessment-nsaa\">\u0645\u0627 \u0647\u0648 \u062a\u0642\u064a\u064a\u0645 \u0646\u0648\u0631\u062b \u0633\u062a\u0627\u0631 \u0644\u0644\u0645\u0634\u064a (NSAA)<\/a><\/li><\/ul><\/li><li><a href=\"#what-level-of-improvement-was-observed-in-children-who-were-administered-elevidys\">\u0645\u0627 \u0647\u0648 \u0645\u0633\u062a\u0648\u0649 \u0627\u0644\u062a\u062d\u0633\u0646 \u0627\u0644\u0630\u064a \u062a\u0645 \u0645\u0644\u0627\u062d\u0638\u062a\u0647 \u0644\u062f\u0649 \u0627\u0644\u0623\u0637\u0641\u0627\u0644 \u0627\u0644\u0630\u064a\u0646 \u062a\u0645 \u0625\u0639\u0637\u0627\u0624\u0647\u0645 Elevidys\u061f<\/a><ul><li><a href=\"#what-we-do-know-about-micro-dystrophin-increase\">\u0645\u0627 \u0646\u0639\u0631\u0641\u0647 \u0639\u0646 \u0632\u064a\u0627\u062f\u0629 \u0627\u0644\u0645\u064a\u0643\u0631\u0648\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646<\/a><\/li><li><a href=\"#what-we-do-not-yet-know-clearly-about-ck-decrease\">\u0645\u0627 \u0644\u0627 \u0646\u0639\u0631\u0641\u0647 \u0628\u0648\u0636\u0648\u062d \u062d\u062a\u0649 \u0627\u0644\u0622\u0646 \u0639\u0646 \u0627\u0646\u062e\u0641\u0627\u0636 CK<\/a><\/li><li><a href=\"#why-the-data-gap-matters\">\u0644\u0645\u0627\u0630\u0627 \u062a\u0639\u062a\u0628\u0631 \u0641\u062c\u0648\u0629 \u0627\u0644\u0628\u064a\u0627\u0646\u0627\u062a \u0645\u0647\u0645\u0629\u061f<\/a><\/li><li><a href=\"#what-this-means-for-children-families-and-clinicians\">\u0645\u0627\u0630\u0627 \u064a\u0639\u0646\u064a \u0647\u0630\u0627 \u0628\u0627\u0644\u0646\u0633\u0628\u0629 \u0644\u0644\u0623\u0637\u0641\u0627\u0644\/\u0627\u0644\u0639\u0627\u0626\u0644\u0627\u062a \u0648\u0627\u0644\u0623\u0637\u0628\u0627\u0621<\/a><\/li><\/ul><\/li><li><a href=\"#n\">\u0628\u062d\u062b \u062c\u062f\u064a\u062f \u062d\u0648\u0644 \u062a\u0644\u0641 \u0627\u0644\u0644\u064a\u0633\u0648\u0633\u0648\u0645\u0627\u062a \u0641\u064a \u0645\u0631\u0636 \u062f\u0648\u0634\u064a\u0646<\/a><\/li><li><a href=\"#real-world-experience-with-elevidys-gene-therapy-report-from-qatar\">\u062a\u062c\u0631\u0628\u0629 \u0648\u0627\u0642\u0639\u064a\u0629 \u0645\u0639 \u062a\u0642\u0631\u064a\u0631 \u0627\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u062c\u064a\u0646\u064a Elevidys \u0645\u0646 \u0642\u0637\u0631<\/a><ul><li><a href=\"#alt-and-ast-levels\">\u0645\u0633\u062a\u0648\u064a\u0627\u062a ALT \u0648AST<\/a><\/li><li><a href=\"#creatine-kinase-ck-levels\">\u0645\u0633\u062a\u0648\u064a\u0627\u062a \u0627\u0644\u0643\u0631\u064a\u0627\u062a\u064a\u0646 \u0643\u064a\u0646\u0627\u0632 (CK)<\/a><\/li><li><a href=\"#n-1\">\u0646\u062a\u064a\u062c\u0629 NSAA<\/a><\/li><\/ul><\/li><li><a href=\"#conclusion\">\u062e\u0627\u062a\u0645\u0629<\/a><\/li><\/ul><\/nav><\/div>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"how-much-micro-dystrophin-is-produced-by-elevidys\">\u0645\u0627 \u0647\u064a \u0643\u0645\u064a\u0629 \u0627\u0644\u0645\u064a\u0643\u0631\u0648 \u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0627\u0644\u062a\u064a \u064a\u0646\u062a\u062c\u0647\u0627 Elevidys\u061f<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u0648\u0641\u0642\u064b\u0627 \u0644\u0644\u0645\u0639\u0644\u0648\u0645\u0627\u062a \u0627\u0644\u0645\u0646\u0634\u0648\u0631\u0629 \u0639\u0644\u0649 \u0627\u0644\u0645\u0648\u0642\u0639 \u0627\u0644\u0631\u0633\u0645\u064a \u0644\u0640 Elevidys\u060c \u0641\u064a \u062c\u0645\u064a\u0639 \u0627\u0644\u062a\u062c\u0627\u0631\u0628 \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629\u060c \u0623\u0646\u062a\u062c \u0627\u0644\u0645\u0634\u0627\u0631\u0643\u0648\u0646 \u0645\u0627 \u0645\u0639\u062f\u0644\u0647 34% \u0625\u0644\u0649 51% \u0645\u0646 \u0645\u064a\u0643\u0631\u0648 \u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 ELEVIDYS \u0628\u0639\u062f 3 \u0623\u0634\u0647\u0631 \u0645\u0646 \u0627\u0644\u0639\u0644\u0627\u062c. \u0644\u0643\u0646 \u0647\u0630\u0647 \u0627\u0644\u0645\u0639\u0644\u0648\u0645\u0627\u062a \u0644\u0627 \u062a\u062d\u062f\u062f \u0643\u0645\u064a\u0629 \u0627\u0644\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0627\u0644\u0637\u0628\u064a\u0639\u064a\u0629 \u0627\u0644\u062a\u064a \u062a\u0639\u0627\u062f\u0644 \u0647\u0630\u0647 \u0627\u0644\u0643\u0645\u064a\u0629.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><a href=\"https:\/\/dmdwarrior.com\/ar\/fda-rejection-letter-vyondys-53-golodirsen\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u062a\u0639\u0631\u0641 \u0639\u0644\u0649 \u0632\u064a\u0627\u062f\u0629 \u0627\u0644\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0641\u064a \u0639\u0644\u0627\u062c \u062a\u062e\u0637\u064a \u0625\u0643\u0633\u0648\u0646 \u0641\u064a\u0648\u0646\u062f\u064a\u0632 53.<\/a><\/p>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"elevidys-alan-cocuklarda-north-star-ambulatuvar-degerlendirmesi-bazen-nsaa-veya-north-star-olarak-da-adlandirilir-puani-ne-kadar-artti\">\u0645\u0627 \u0647\u0648 \u0645\u0642\u062f\u0627\u0631 \u0627\u0644\u0632\u064a\u0627\u062f\u0629 \u0641\u064a \u062f\u0631\u062c\u0629 NSAA \u0644\u062f\u0649 \u0627\u0644\u0623\u0637\u0641\u0627\u0644 \u0627\u0644\u0630\u064a\u0646 \u062d\u0635\u0644\u0648\u0627 \u0639\u0644\u0649 Elevidys\u061f<\/h2>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"what-is-north-star-ambulatory-assessment-nsaa\">\u0645\u0627 \u0647\u0648 \u062a\u0642\u064a\u064a\u0645 \u0646\u0648\u0631\u062b \u0633\u062a\u0627\u0631 \u0644\u0644\u0645\u0634\u064a (NSAA)<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u0645\u062c\u0645\u0648\u0639 \u0627\u0644\u062f\u0631\u062c\u0627\u062a \u0645\u0646 \u0660 \u0625\u0644\u0649 \u0663\u0664\u060c \u0648\u062a\u0634\u064a\u0631 \u0627\u0644\u062f\u0631\u062c\u0629 \u0627\u0644\u0623\u0639\u0644\u0649 \u0625\u0644\u0649 \u0645\u0633\u062a\u0648\u0649 \u0623\u062f\u0627\u0621 \u0623\u0639\u0644\u0649. \u064a\u062a\u0636\u0645\u0646 \u0627\u0644\u0627\u062e\u062a\u0628\u0627\u0631 \u0627\u062e\u062a\u0628\u0627\u0631\u064a\u0646 \u0645\u064f\u0648\u0642\u064e\u0651\u062a\u064a\u0646: \u0627\u062e\u062a\u0628\u0627\u0631 \u0627\u0644\u0646\u0647\u0648\u0636 \u0645\u0646 \u0627\u0644\u0623\u0631\u0636 (RFF) \u0648\u0627\u062e\u062a\u0628\u0627\u0631 \u0627\u0644\u0645\u0634\u064a\/\u0627\u0644\u062c\u0631\u064a \u0644\u0645\u0633\u0627\u0641\u0629 \u0661\u0660 \u0623\u0645\u062a\u0627\u0631 (\u0661\u0660 \u0623\u0645\u062a\u0627\u0631 \u0648\u0648\u0631). \u0645\u064f\u0639\u062a\u0645\u062f \u0648\u064a\u064f\u0633\u062a\u062e\u062f\u0645 \u0628\u0627\u0646\u062a\u0638\u0627\u0645 \u0641\u064a \u0627\u0644\u062a\u062c\u0627\u0631\u0628 \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629 \u0648\u0627\u0644\u0639\u064a\u0627\u062f\u0627\u062a. <strong>\u0627\u0642\u0631\u0623 \u0627\u0644\u0645\u0632\u064a\u062f<\/strong>: <a href=\"https:\/\/dmdwarrior.com\/ar\/north-star-ambulatory-assessment-nsaa-in-duchenne-dmd\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u0648\u0643\u0627\u0644\u0629 \u0627\u0644\u0623\u0645\u0646 \u0627\u0644\u0642\u0648\u0645\u064a<\/a><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0648\u0628\u062d\u0633\u0628 \u0627\u0644\u0645\u0639\u0644\u0648\u0645\u0627\u062a \u0627\u0644\u0645\u0646\u0634\u0648\u0631\u0629 \u0639\u0644\u0649 \u0627\u0644\u0645\u0648\u0642\u0639 \u0627\u0644\u0631\u0633\u0645\u064a \u0644\u0640 Elevidys\u060c \u0643\u0627\u0646 \u0647\u0646\u0627\u0643 \u0632\u064a\u0627\u062f\u0629 \u0628\u0645\u0642\u062f\u0627\u0631 2.6 \u0646\u0642\u0637\u0629 \u0641\u064a \u0627\u062e\u062a\u0628\u0627\u0631 NSAA \u0627\u0644\u0645\u0643\u0648\u0646 \u0645\u0646 34 \u0646\u0642\u0637\u0629 \u0644\u062f\u0649 \u0627\u0644\u0623\u0637\u0641\u0627\u0644 \u0627\u0644\u0630\u064a\u0646 \u062a\u0644\u0642\u0648\u0627 \u0627\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u062c\u064a\u0646\u064a \u0648\u0632\u064a\u0627\u062f\u0629 \u0628\u0645\u0642\u062f\u0627\u0631 1.9 \u0646\u0642\u0637\u0629 \u0644\u062f\u0649 \u0627\u0644\u0623\u0637\u0641\u0627\u0644 \u0627\u0644\u0630\u064a\u0646 \u0644\u0645 \u064a\u062a\u0644\u0642\u0648\u0627 \u0627\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u062c\u064a\u0646\u064a. <strong>\u0648\u064a\u0639\u0646\u064a \u0647\u0630\u0627 \u0623\u0646 \u0627\u0644\u0623\u0637\u0641\u0627\u0644 \u0627\u0644\u0630\u064a\u0646 \u0644\u0645 \u064a\u062a\u0644\u0642\u0648\u0627 \u0627\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u062c\u064a\u0646\u064a Elevidys \u0634\u0647\u062f\u0648\u0627 \u0623\u064a\u0636\u064b\u0627 \u062a\u062d\u0633\u0646\u064b\u0627.<\/strong> &gt;&gt;&gt; <a href=\"https:\/\/www.elevidys.com\/about-elevidys\/results-ambulatory\" target=\"_blank\" rel=\"noreferrer noopener\">Elevidys<\/a><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0648\u0628\u062d\u0633\u0628 \u062a\u0642\u0631\u064a\u0631 EMA\u060c \u0641\u0625\u0646 \u0647\u0630\u0647 \u0627\u0644\u0632\u064a\u0627\u062f\u0629 \u0628\u0644\u063a\u062a 0.65 \u0646\u0642\u0637\u0629 \u0641\u0642\u0637. &gt;&gt;&gt; <a href=\"https:\/\/dmdwarrior.com\/ar\/why-elevidys-was-not-approved-by-the-european-medicines-agency-ema\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u062f\u064a \u0625\u0645 \u062f\u064a \u0648\u0627\u0631\u064a\u0648\u0631<\/a><\/p>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"what-level-of-improvement-was-observed-in-children-who-were-administered-elevidys\">\u0645\u0627 \u0647\u0648 \u0645\u0633\u062a\u0648\u0649 \u0627\u0644\u062a\u062d\u0633\u0646 \u0627\u0644\u0630\u064a \u062a\u0645 \u0645\u0644\u0627\u062d\u0638\u062a\u0647 \u0644\u062f\u0649 \u0627\u0644\u0623\u0637\u0641\u0627\u0644 \u0627\u0644\u0630\u064a\u0646 \u062a\u0645 \u0625\u0639\u0637\u0627\u0624\u0647\u0645 Elevidys\u061f<\/h2>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u0643\u0627\u0646 \u0623\u0648\u0644\u0626\u0643 \u0627\u0644\u0630\u064a\u0646 \u062a\u0644\u0642\u0648\u0627 ELEVIDYS \u0642\u0627\u062f\u0631\u064a\u0646 \u0639\u0644\u0649 \u0627\u0644\u0646\u0647\u0648\u0636 \u0645\u0646 \u0627\u0644\u0623\u0631\u0636 \u0623\u0633\u0631\u0639 \u0628\u0645\u0642\u062f\u0627\u0631 0.64 \u062b\u0627\u0646\u064a\u0629 \u0645\u0646 \u0623\u0648\u0644\u0626\u0643 \u0627\u0644\u0630\u064a\u0646 \u062a\u0646\u0627\u0648\u0644\u0648\u0627 \u0627\u0644\u062f\u0648\u0627\u0621 \u0627\u0644\u0648\u0647\u0645\u064a (\u0644\u0627 \u064a\u062a\u0646\u0627\u0648\u0644\u0648\u0646 ELEVIDYS) \u0628\u0639\u062f \u0639\u0627\u0645 \u0648\u0627\u062d\u062f (\u0641\u064a \u0627\u0644\u0645\u062a\u0648\u0633\u0637) &gt;&gt;&gt; <a href=\"https:\/\/www.institut-myologie.org\/en\/2023\/11\/20\/mixed-efficacy-results-for-srp-9001-elevidys-a-gene-therapy-approved-in-the-usa-for-dmd\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u0646\u062a\u0627\u0626\u062c \u0641\u0639\u0627\u0644\u064a\u0629 SRP-9001 (Elevidys)<\/a><\/li>\n<\/ul>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u0643\u0627\u0646 \u0627\u0644\u0623\u0634\u062e\u0627\u0635 \u0627\u0644\u0630\u064a\u0646 \u062a\u0644\u0642\u0648\u0627 ELEVIDYS \u0642\u0627\u062f\u0631\u064a\u0646 \u0639\u0644\u0649 \u0627\u0644\u0645\u0634\u064a\/\u0627\u0644\u062c\u0631\u064a \u0644\u0645\u0633\u0627\u0641\u0629 10 \u0623\u0645\u062a\u0627\u0631 \u0623\u0633\u0631\u0639 \u0628\u0640 0.42 \u062b\u0627\u0646\u064a\u0629 \u0645\u0646 \u0623\u0648\u0644\u0626\u0643 \u0627\u0644\u0630\u064a\u0646 \u062a\u0646\u0627\u0648\u0644\u0648\u0627 \u0627\u0644\u062f\u0648\u0627\u0621 \u0627\u0644\u0648\u0647\u0645\u064a (\u0628\u062f\u0648\u0646 ELEVIDYS) \u0628\u0639\u062f \u0639\u0627\u0645 \u0648\u0627\u062d\u062f (\u0641\u064a \u0627\u0644\u0645\u062a\u0648\u0633\u0637) &gt;&gt;&gt; <a href=\"https:\/\/www.elevidys.com\/about-elevidys\/results-ambulatory\" target=\"_blank\" rel=\"noreferrer noopener\">\u0627\u0644\u0646\u062a\u0627\u0626\u062c \u0641\u064a \u0627\u0644\u0639\u064a\u0627\u062f\u0627\u062a \u0627\u0644\u062e\u0627\u0631\u062c\u064a\u0629<\/a><\/li>\n<\/ul>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"what-we-do-know-about-micro-dystrophin-increase\">\u0645\u0627 \u0646\u0639\u0631\u0641\u0647 \u0639\u0646 \u0632\u064a\u0627\u062f\u0629 \u0627\u0644\u0645\u064a\u0643\u0631\u0648\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646<\/h3>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u0648\u0641\u0642\u064b\u0627 \u0644\u0645\u0644\u062e\u0635 \u0627\u0644\u0645\u0648\u0627\u0641\u0642\u0629\u060c \u0648\u062c\u062f FDA \u0623\u0646 ELEVIDYS \u0632\u0627\u062f \u0645\u0646 \u0627\u0644\u062a\u0639\u0628\u064a\u0631 \u0639\u0646 \u0628\u0631\u0648\u062a\u064a\u0646 \u0645\u064a\u0643\u0631\u0648 \u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0641\u064a \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0627\u0644\u0647\u064a\u0643\u0644\u064a\u0629 \u0644\u0644\u0645\u0631\u0636\u0649 \u0627\u0644\u0630\u064a\u0646 \u0639\u0648\u0644\u062c\u0648\u0627. &gt;&gt;&gt; <a href=\"https:\/\/investorrelations.sarepta.com\/news-releases\/news-release-details\/sarepta-therapeutics-announces-fda-approval-elevidys-first-gene\" target=\"_blank\" rel=\"noreferrer noopener\">investorrelations.sarepta.com<\/a><\/li>\n\n\n\n<li>\u062a\u0646\u0635 \u0645\u0642\u0627\u0644\u0629 \u0645\u0631\u0627\u062c\u0639\u0629 (\u0646\u0633\u062e\u0629 \u0623\u0648\u0644\u064a\u0629) \u0639\u0644\u0649 \u0645\u0627 \u064a\u0644\u064a: &quot;\u0628\u0639\u062f 48 \u0623\u0633\u0628\u0648\u0639\u064b\u0627\u060c \u0623\u0638\u0647\u0631 \u0627\u0644\u0645\u0631\u0636\u0649 \u0627\u0644\u0630\u064a\u0646 \u0639\u0648\u0644\u062c\u0648\u0627 \u0645\u062a\u0648\u0633\u0637 \u062a\u0639\u0628\u064a\u0631 \u0639\u0646 \u0645\u064a\u0643\u0631\u0648\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u064a\u0628\u0644\u063a \u062d\u0648\u0627\u0644\u064a 28 % \u0641\u064a \u0627\u062e\u062a\u0628\u0627\u0631 \u0648\u064a\u0633\u062a\u0631\u0646 \u0628\u0644\u0648\u062a&quot;. &gt;&gt;&gt; <a href=\"https:\/\/www.preprints.org\/manuscript\/202506.2161\/download\/final_file\" target=\"_blank\" rel=\"noreferrer noopener\">preprints.org<\/a><\/li>\n\n\n\n<li>\u064a\u0646\u0635 \u0625\u0639\u0644\u0627\u0646 \u0639\u0646 \u062f\u0631\u0627\u0633\u0629 \u0625\u0645\u0628\u0627\u0631\u0643 \u0639\u0644\u0649 \u0645\u0627 \u064a\u0644\u064a: &quot;\u0641\u064a \u0627\u0644\u0645\u0631\u0636\u0649 \u0627\u0644\u0630\u064a\u0646 \u0639\u0648\u0644\u062c\u0648\u0627 \u0641\u064a \u0627\u0644\u062c\u0632\u0621 \u0627\u0644\u0623\u0648\u0644\u060c \u0623\u0638\u0647\u0631\u062a \u0627\u0644\u062e\u0632\u0639\u0627\u062a \u0627\u0644\u0645\u0623\u062e\u0648\u0630\u0629 \u0628\u0639\u062f 64 \u0623\u0633\u0628\u0648\u0639\u064b\u0627 \u0645\u0646 \u0627\u0644\u062c\u0631\u0639\u0629 \u062a\u0639\u0628\u064a\u0631\u064b\u0627 \u062b\u0627\u0628\u062a\u064b\u0627 \u0648\u0645\u0633\u062a\u062f\u0627\u0645\u064b\u0627 \u0639\u0646 \u0645\u064a\u0643\u0631\u0648 \u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0625\u0644\u064a\u0641\u064a\u062f\u064a\u0633\u060c \u0645\u0642\u0627\u0631\u0646\u0629\u064b \u0628\u062e\u0632\u0639\u0627\u062a \u0627\u0644\u0623\u0633\u0628\u0648\u0639 \u0627\u0644\u062b\u0627\u0646\u064a \u0639\u0634\u0631\u060c \u0643\u0645\u0627 \u062a\u0645 \u0642\u064a\u0627\u0633\u0647\u0627 \u0628\u0627\u0633\u062a\u062e\u062f\u0627\u0645 \u062a\u0642\u0646\u064a\u0629 \u0648\u064a\u0633\u062a\u0631\u0646 \u0628\u0644\u0648\u062a\u060c \u0648\u062a\u0648\u0641\u0631 \u062f\u0639\u0645\u064b\u0627 \u0628\u064a\u0648\u0644\u0648\u062c\u064a\u064b\u0627 \u0644\u0644\u0646\u062a\u0627\u0626\u062c \u0627\u0644\u0648\u0638\u064a\u0641\u064a\u0629 \u0627\u0644\u0645\u0644\u062d\u0648\u0638\u0629&quot;. \u0645\u0639 \u0630\u0644\u0643\u060c \u0644\u0645 \u064a\u0643\u0634\u0641 \u0627\u0644\u0625\u0639\u0644\u0627\u0646 \u0639\u0646 \u0623\u0631\u0642\u0627\u0645 \u0643\u0645\u064a\u0629 \u0645\u064a\u0643\u0631\u0648 \u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0627\u0644\u0645\u064f\u0646\u062a\u062c\u0629 \u0648\u0645\u062f\u0649 \u0627\u0644\u062d\u0641\u0627\u0638 \u0639\u0644\u0649 \u0645\u0633\u062a\u0648\u0627\u0647\u0627 \u0645\u0639 \u0645\u0631\u0648\u0631 \u0627\u0644\u0648\u0642\u062a. &gt;&gt;&gt; <a href=\"https:\/\/sarepta.gcs-web.com\/news-releases\/news-release-details\/sarepta-therapeutics-announces-results-part-2-embark-study\" target=\"_blank\" rel=\"noreferrer noopener\">sarepta.gcs-web.com<\/a><\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\">\u0648\u0628\u0627\u0644\u062a\u0627\u0644\u064a\u060c \u0641\u0625\u0646 \u0623\u062d\u062f \u0627\u0644\u0623\u0631\u0642\u0627\u0645 \u0627\u0644\u0645\u062a\u0627\u062d\u0629 \u0647\u0648 \u062a\u0639\u0628\u064a\u0631 28% \u062a\u0642\u0631\u064a\u0628\u064b\u0627 \u0645\u0642\u0627\u0631\u0646\u0629\u064b \u0628\u0627\u0644\u0645\u0633\u062a\u0648\u0649 \u0627\u0644\u0637\u0628\u064a\u0639\u064a (\u0639\u0644\u0649 \u0627\u062e\u062a\u0628\u0627\u0631 \u0648\u064a\u0633\u062a\u0631\u0646 \u0628\u0644\u0648\u062a) \u0639\u0646\u062f \u062d\u0648\u0627\u0644\u064a 48 \u0623\u0633\u0628\u0648\u0639\u064b\u0627 \u0641\u064a \u0627\u0644\u0645\u062c\u0645\u0648\u0639\u0629 \u0627\u0644\u0645\u0639\u0627\u0644\u062c\u0629 (\u0641\u064a \u062a\u0644\u0643 \u0627\u0644\u062f\u0631\u0627\u0633\u0629 \u0627\u0644\u0635\u063a\u064a\u0631\u0629). \u0648\u0645\u0639 \u0630\u0644\u0643:<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u0644\u064a\u0633 \u0645\u0646 \u0627\u0644\u0648\u0627\u0636\u062d \u062f\u0627\u0626\u0645\u064b\u0627 \u0645\u0627 \u064a\u0639\u0646\u064a\u0647 &quot;100%&quot; (\u0645\u0633\u062a\u0648\u064a\u0627\u062a \u0627\u0644\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0627\u0644\u0635\u062d\u064a\u0629 \u0627\u0644\u0637\u0628\u064a\u0639\u064a\u0629) \u0641\u064a \u0647\u0630\u0627 \u0627\u0644\u0642\u064a\u0627\u0633.<\/li>\n\n\n\n<li>\u0644\u0645 \u064a\u062d\u0642\u0642 \u0627\u0644\u062a\u062d\u0633\u0646 \u0627\u0644\u0648\u0638\u064a\u0641\u064a (\u0646\u0642\u0627\u0637 \u0627\u0644\u0646\u0647\u0627\u064a\u0629 \u0627\u0644\u062d\u0631\u0643\u064a\u0629) \u0641\u064a \u0627\u0644\u062a\u062c\u0631\u0628\u0629 \u0627\u0644\u0623\u0643\u0628\u0631 \u0646\u0642\u0637\u0629 \u0627\u0644\u0646\u0647\u0627\u064a\u0629 \u0627\u0644\u0623\u0633\u0627\u0633\u064a\u0629. &gt;&gt;&gt; <a href=\"https:\/\/www.medscape.com\/viewarticle\/ema-says-no-duchenne-gene-therapyelevidys-2025a1000jqs\" target=\"_blank\" rel=\"noreferrer noopener\">\u0645\u064a\u062f\u0633\u0643\u064a\u0628<\/a><\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\">\u0644\u0630\u0627\u060c \u0641\u0628\u064a\u0646\u0645\u0627 \u062a\u0631\u062a\u0641\u0639 \u0645\u0633\u062a\u0648\u064a\u0627\u062a \u0627\u0644\u0645\u064a\u0643\u0631\u0648\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646\u060c \u0641\u0625\u0646 \u0627\u0644\u062d\u062c\u0645 \u0627\u0644\u062f\u0642\u064a\u0642 \u064a\u062e\u062a\u0644\u0641\u060c \u0648\u0645\u0627 \u0632\u0627\u0644\u062a \u0627\u0644\u0645\u062a\u0627\u0646\u0629 \u0639\u0644\u0649 \u0627\u0644\u0645\u062f\u0649 \u0627\u0644\u0637\u0648\u064a\u0644 \u0642\u064a\u062f \u0627\u0644\u062f\u0631\u0627\u0633\u0629\u060c \u0648\u0645\u0627 \u0632\u0627\u0644\u062a \u0627\u0644\u062a\u0631\u062c\u0645\u0629 \u0625\u0644\u0649 \u0641\u0627\u0626\u062f\u0629 \u0633\u0631\u064a\u0631\u064a\u0629 \u063a\u064a\u0631 \u0645\u0624\u0643\u062f\u0629.<\/p>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"what-we-do-not-yet-know-clearly-about-ck-decrease\">\u0645\u0627 \u0644\u0627 \u0646\u0639\u0631\u0641\u0647 \u0628\u0648\u0636\u0648\u062d \u062d\u062a\u0649 \u0627\u0644\u0622\u0646 \u0639\u0646 \u0627\u0646\u062e\u0641\u0627\u0636 CK<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u0641\u064a \u0627\u0644\u0648\u062b\u0627\u0626\u0642 \u0648\u0627\u0644\u0645\u0646\u0634\u0648\u0631\u0627\u062a \u0627\u0644\u062a\u0646\u0638\u064a\u0645\u064a\u0629 \u0627\u0644\u0639\u0627\u0645\u0629 \u0627\u0644\u062a\u064a \u0631\u0627\u062c\u0639\u0646\u0627\u0647\u0627\u060c \u0644\u0627 \u062a\u0648\u062c\u062f \u0642\u064a\u0645\u0629 \u0648\u0627\u0636\u062d\u0629 \u0648\u062b\u0627\u0628\u062a\u0629 \u0644\u0645\u062f\u0649 \u0627\u0646\u062e\u0641\u0627\u0636 \u0645\u0633\u062a\u0648\u064a\u0627\u062a \u0643\u064a\u0646\u0627\u0632 \u0627\u0644\u0643\u0631\u064a\u0627\u062a\u064a\u0646 (CK) \u0628\u0639\u062f \u0627\u0633\u062a\u062e\u062f\u0627\u0645 \u062f\u0648\u0627\u0621 \u0625\u064a\u0644\u064a\u0641\u064a\u062f\u064a\u0633 \u0644\u062f\u0649 \u0627\u0644\u0623\u0637\u0641\u0627\u0644 \u0627\u0644\u0645\u0635\u0627\u0628\u064a\u0646 \u0628\u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0627\u0644\u062f\u0648\u0634\u064a\u0646\u064a. \u0627\u0644\u0646\u0642\u0627\u0637 \u0627\u0644\u0631\u0626\u064a\u0633\u064a\u0629:<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u064a\u0630\u0643\u0631 \u0628\u064a\u0627\u0646 \u0627\u0644\u0645\u0648\u0627\u0641\u0642\u0629 \u0639\u0644\u0649 \u062a\u0648\u0633\u064a\u0639 \u0646\u0637\u0627\u0642 FDA \u0623\u0646\u0647 \u0645\u0646 \u0628\u064a\u0646 \u0625\u062c\u0645\u0627\u0644\u064a \u0627\u0644\u0623\u062f\u0644\u0629 \u0627\u0644\u062a\u064a \u062a\u0645 \u0627\u0644\u0646\u0638\u0631 \u0641\u064a\u0647\u0627 &quot;\u0627\u0644\u062a\u062d\u0633\u0646 \u0641\u064a ... \u0645\u0633\u062a\u0648\u064a\u0627\u062a \u0643\u064a\u0646\u0627\u0632 \u0627\u0644\u0643\u0631\u064a\u0627\u062a\u064a\u0646&quot; \u0645\u0646 \u0628\u064a\u0646 \u0646\u0642\u0627\u0637 \u0627\u0644\u0646\u0647\u0627\u064a\u0629 \u0627\u0644\u0623\u062e\u0631\u0649. &gt;&gt;&gt; <a href=\"https:\/\/www.fda.gov\/news-events\/press-announcements\/fda-expands-approval-gene-therapy-patients-duchenne-muscular-dystrophy\" target=\"_blank\" rel=\"noreferrer noopener\">\u0625\u062f\u0627\u0631\u0629 \u0627\u0644\u063a\u0630\u0627\u0621 \u0648\u0627\u0644\u062f\u0648\u0627\u0621 \u0627\u0644\u0623\u0645\u0631\u064a\u0643\u064a\u0629<\/a><\/li>\n\n\n\n<li>\u0648\u0645\u0639 \u0630\u0644\u0643\u060c \u0644\u0645 \u0646\u0639\u062b\u0631 \u0639\u0644\u0649 \u0631\u0642\u0645 \u0645\u0646\u0634\u0648\u0631 \u0645\u062b\u0644 &quot;\u0627\u0646\u062e\u0641\u0636 CK \u0628\u0645\u0642\u062f\u0627\u0631 X% \u0641\u064a \u0627\u0644\u0645\u062a\u0648\u0633\u0637 \u0639\u0646\u062f Y \u0623\u0633\u0627\u0628\u064a\u0639\/\u0623\u0634\u0647\u0631&quot; \u0641\u064a \u0627\u0644\u0623\u062f\u0628\u064a\u0627\u062a \u0627\u0644\u062a\u064a \u062a\u0645\u062a \u0645\u0631\u0627\u062c\u0639\u062a\u0647\u0627 \u0645\u0646 \u0642\u0628\u0644 \u0627\u0644\u0623\u0642\u0631\u0627\u0646 (\u0639\u0644\u0649 \u0627\u0644\u0623\u0642\u0644 \u0641\u064a \u0627\u0644\u0645\u0635\u0627\u062f\u0631 \u0627\u0644\u0645\u062a\u0627\u062d\u0629).<\/li>\n\n\n\n<li>\u062a\u0638\u0644 \u0627\u0644\u0639\u062f\u064a\u062f \u0645\u0646 \u0627\u0644\u0646\u062a\u0627\u0626\u062c \u0645\u062c\u0631\u062f \u0646\u0642\u0627\u0637 \u0646\u0647\u0627\u064a\u0629 \u0627\u0633\u062a\u0643\u0634\u0627\u0641\u064a\u0629 \u0623\u0648 \u062b\u0627\u0646\u0648\u064a\u0629\u061b \u0648\u0644\u0645 \u062a\u0635\u0644 \u0646\u0642\u0637\u0629 \u0627\u0644\u0646\u0647\u0627\u064a\u0629 \u0627\u0644\u0648\u0638\u064a\u0641\u064a\u0629 \u0627\u0644\u0623\u0633\u0627\u0633\u064a\u0629 (NSAA) \u0641\u064a \u062a\u062c\u0631\u0628\u0629 EMBARK \u0625\u0644\u0649 \u062f\u0644\u0627\u0644\u0629 \u0625\u062d\u0635\u0627\u0626\u064a\u0629 (\u0641\u0631\u0642 \u062d\u0648\u0627\u0644\u064a 0.65 \u0646\u0642\u0637\u0629) \u0639\u0646\u062f 52 \u0623\u0633\u0628\u0648\u0639\u064b\u0627. &gt;&gt;&gt; <a href=\"https:\/\/www.medscape.com\/viewarticle\/ema-says-no-duchenne-gene-therapyelevidys-2025a1000jqs\" target=\"_blank\" rel=\"noreferrer noopener\">\u0645\u064a\u062f\u0633\u0643\u064a\u0628<\/a><\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\">\u0648\u0647\u0643\u0630\u0627\u060c \u0641\u064a \u062d\u064a\u0646 \u0623\u0646 \u0647\u0646\u0627\u0643 \u0645\u0624\u0634\u0631\u0627\u062a \u0639\u0644\u0649 \u0623\u0646 \u0645\u0633\u062a\u0648\u064a\u0627\u062a CK \u0642\u062f \u062a\u0646\u062e\u0641\u0636\u060c \u0641\u0625\u0646 \u062f\u0631\u062c\u0629 \u0627\u0644\u0627\u0646\u062e\u0641\u0627\u0636 (\u0639\u0644\u0649 \u0633\u0628\u064a\u0644 \u0627\u0644\u0645\u062b\u0627\u0644\u060c \u0627\u0644\u0646\u0633\u0628\u0629 \u0627\u0644\u0645\u0626\u0648\u064a\u0629 \u0644\u0644\u0627\u0646\u062e\u0641\u0627\u0636\u060c \u0627\u0644\u0648\u062d\u062f\u0627\u062a \u0627\u0644\u0645\u0637\u0644\u0642\u0629) \u0644\u0645 \u064a\u062a\u0645 \u062a\u062d\u062f\u064a\u062f\u0647\u0627 \u0628\u0634\u0643\u0644 \u062c\u064a\u062f \u0639\u0644\u0646\u064b\u0627 \u0641\u064a \u0627\u0644\u0639\u062f\u064a\u062f \u0645\u0646 \u0627\u0644\u062f\u0631\u0627\u0633\u0627\u062a \u0627\u0644\u0643\u0628\u064a\u0631\u0629 (\u0623\u0648 \u0639\u0644\u0649 \u0627\u0644\u0623\u0642\u0644 \u0644\u0645 \u064a\u062a\u0645 \u0646\u0634\u0631\u0647\u0627 \u0628\u0639\u062f \u0641\u064a \u0634\u0643\u0644 \u064a\u0645\u0643\u0646 \u0627\u0644\u0648\u0635\u0648\u0644 \u0625\u0644\u064a\u0647 \u0628\u0633\u0647\u0648\u0644\u0629).<\/p>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"why-the-data-gap-matters\">\u0644\u0645\u0627\u0630\u0627 \u062a\u0639\u062a\u0628\u0631 \u0641\u062c\u0648\u0629 \u0627\u0644\u0628\u064a\u0627\u0646\u0627\u062a \u0645\u0647\u0645\u0629\u061f<\/h3>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u064a\u064f\u0639\u062f\u0651 CK \u0645\u0624\u0634\u0631\u064b\u0627 \u062d\u064a\u0648\u064a\u064b\u0627 \u0634\u0627\u0626\u0639 \u0627\u0644\u0627\u0633\u062a\u062e\u062f\u0627\u0645 \u0641\u064a \u062f\u0648\u0634\u064a\u0646 (DMD) \u0644\u062a\u062a\u0628\u0639 \u062a\u0644\u0641\/\u062a\u0633\u0631\u0628 \u0627\u0644\u0639\u0636\u0644\u0627\u062a. \u0642\u062f \u064a\u0634\u064a\u0631 \u0627\u0644\u0627\u0646\u062e\u0641\u0627\u0636 \u0627\u0644\u0643\u0628\u064a\u0631 \u0641\u064a CK \u0625\u0644\u0649 \u0627\u0646\u062e\u0641\u0627\u0636 \u0625\u0635\u0627\u0628\u0629 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0627\u0644\u0645\u0633\u062a\u0645\u0631\u0629.<\/li>\n\n\n\n<li>\u064a\u0639\u062f \u0627\u0644\u062a\u0639\u0628\u064a\u0631 \u0639\u0646 \u0627\u0644\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 (\u0623\u0648 \u0627\u0644\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0627\u0644\u0635\u063a\u064a\u0631) \u0639\u0644\u0627\u0645\u0629 \u0645\u064a\u0643\u0627\u0646\u064a\u0643\u064a\u0629: \u062a\u064f\u0638\u0647\u0631 \u0623\u0646 \u0627\u0644\u0639\u0644\u0627\u062c \u064a\u0624\u062f\u064a \u0645\u0627 \u062a\u0645 \u062a\u0635\u0645\u064a\u0645\u0647 \u0645\u0646 \u0623\u062c\u0644\u0647.<\/li>\n\n\n\n<li>\u0648\u0644\u0643\u0646 \u062d\u062a\u0649 \u0644\u0648 \u0632\u0627\u062f \u0627\u0644\u0645\u064a\u0643\u0631\u0648\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0648\u0627\u0646\u062e\u0641\u0636 \u0627\u0644\u0643\u064a\u0646\u0627 CK\u060c \u0641\u0625\u0646 \u0627\u0644\u0633\u0624\u0627\u0644 \u0627\u0644\u0631\u0626\u064a\u0633\u064a \u064a\u0628\u0642\u0649: <strong>\u0647\u0644 \u064a\u062a\u0631\u062c\u0645 \u0647\u0630\u0627 \u0625\u0644\u0649 \u0641\u0648\u0627\u0626\u062f \u0648\u0638\u064a\u0641\u064a\u0629\/\u062d\u0631\u0643\u064a\u0629 \u0630\u0627\u062a \u0645\u0639\u0646\u0649\u060c \u0623\u0648 \u0642\u062f\u0631\u0629 \u0623\u0637\u0648\u0644 \u0639\u0644\u0649 \u0627\u0644\u0645\u0634\u064a\u060c \u0623\u0648 \u0646\u0648\u0639\u064a\u0629 \u062d\u064a\u0627\u0629 \u0623\u0641\u0636\u0644\u061f<\/strong><\/li>\n\n\n\n<li>\u0625\u0646 \u062d\u0642\u064a\u0642\u0629 \u0623\u0646 \u0627\u0644\u062a\u062c\u0631\u0628\u0629 \u0627\u0644\u0643\u0628\u064a\u0631\u0629 \u0641\u064a \u0627\u0644\u0645\u0631\u062d\u0644\u0629 \u0627\u0644\u062b\u0627\u0644\u062b\u0629 \u0644\u0645 \u062a\u062d\u0642\u0642 \u0647\u062f\u0641\u0647\u0627 \u0627\u0644\u062d\u0631\u0643\u064a \u0627\u0644\u0623\u0633\u0627\u0633\u064a \u062a\u062b\u064a\u0631 \u0627\u0644\u062d\u0630\u0631: \u0625\u0630 \u0625\u0646 \u0632\u064a\u0627\u062f\u0629 \u0627\u0644\u062a\u0639\u0628\u064a\u0631 \u0627\u0644\u0628\u0631\u0648\u062a\u064a\u0646\u064a \u0644\u0627 \u062a\u0636\u0645\u0646 \u062a\u0644\u0642\u0627\u0626\u064a\u064b\u0627 \u0645\u0643\u0627\u0633\u0628 \u0648\u0638\u064a\u0641\u064a\u0629 \u0643\u0628\u064a\u0631\u0629. &gt;&gt;&gt; <a href=\"https:\/\/www.medscape.com\/viewarticle\/ema-says-no-duchenne-gene-therapyelevidys-2025a1000jqs\" target=\"_blank\" rel=\"noreferrer noopener\">\u0645\u064a\u062f\u0633\u0643\u064a\u0628<\/a><\/li>\n\n\n\n<li>\u0643\u0627\u0646\u062a \u0627\u0644\u0647\u064a\u0626\u0627\u062a \u0627\u0644\u062a\u0646\u0638\u064a\u0645\u064a\u0629 \u0645\u062b\u0644 \u0648\u0643\u0627\u0644\u0629 \u0627\u0644\u0623\u062f\u0648\u064a\u0629 \u0627\u0644\u0623\u0648\u0631\u0648\u0628\u064a\u0629 (EMA) \u0623\u0643\u062b\u0631 \u062a\u0634\u0643\u0643\u0627: \u0623\u0648\u0635\u062a \u0644\u062c\u0646\u0629 \u0627\u0644\u0645\u0646\u062a\u062c\u0627\u062a \u0627\u0644\u0637\u0628\u064a\u0629 \u0644\u0644\u0627\u0633\u062a\u062e\u062f\u0627\u0645 \u0627\u0644\u0628\u0634\u0631\u064a (CHMP) \u0627\u0644\u062e\u0627\u0635\u0629 \u0628\u0640 EMA \u0628\u0639\u062f\u0645 \u0645\u0646\u062d \u062a\u0631\u062e\u064a\u0635 \u062a\u0633\u0648\u064a\u0642 Elevidys \u0641\u064a \u064a\u0648\u0644\u064a\u0648 2025\u060c \u0645\u0634\u064a\u0631\u0629 \u0625\u0644\u0649 \u0641\u0627\u0626\u062f\u0629 \u0648\u0638\u064a\u0641\u064a\u0629 \u063a\u064a\u0631 \u0643\u0627\u0641\u064a\u0629 \u0639\u0644\u0649 \u0627\u0644\u0631\u063a\u0645 \u0645\u0646 \u0625\u0646\u062a\u0627\u062c \u0645\u064a\u0643\u0631\u0648 \u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646. &gt;&gt;&gt; <a href=\"https:\/\/dmdwarrior.com\/ar\/why-elevidys-was-not-approved-by-the-european-medicines-agency-ema\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u062f\u064a \u0625\u0645 \u062f\u064a \u0648\u0627\u0631\u064a\u0648\u0631<\/a><\/li>\n<\/ul>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"what-this-means-for-children-families-and-clinicians\">\u0645\u0627\u0630\u0627 \u064a\u0639\u0646\u064a \u0647\u0630\u0627 \u0628\u0627\u0644\u0646\u0633\u0628\u0629 \u0644\u0644\u0623\u0637\u0641\u0627\u0644\/\u0627\u0644\u0639\u0627\u0626\u0644\u0627\u062a \u0648\u0627\u0644\u0623\u0637\u0628\u0627\u0621<\/h3>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u0625\u0630\u0627 \u0643\u0646\u062a \u0623\u062d\u062f \u0623\u0641\u0631\u0627\u062f \u0627\u0644\u0623\u0633\u0631\u0629 \u0623\u0648 \u0627\u0644\u0637\u0628\u064a\u0628 \u0627\u0644\u0630\u064a \u064a\u0641\u0643\u0631 \u0641\u064a \u0627\u0633\u062a\u062e\u062f\u0627\u0645 ELEVIDYS\u060c \u0641\u0645\u0646 \u0627\u0644\u0648\u0627\u0642\u0639\u064a \u0623\u0646 \u062a\u0639\u0631\u0641 \u0623\u0646 \u0627\u0644\u062a\u0639\u0628\u064a\u0631 \u0639\u0646 \u0645\u064a\u0643\u0631\u0648 \u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u064a\u0632\u062f\u0627\u062f (\u0639\u0644\u0649 \u0633\u0628\u064a\u0644 \u0627\u0644\u0645\u062b\u0627\u0644\u060c ~28% \u0641\u064a \u062f\u0631\u0627\u0633\u0629 \u0648\u0627\u062d\u062f\u0629) \u0648\u0644\u0643\u0646 \u0627\u0644\u062a\u0631\u062c\u0645\u0629 \u0625\u0644\u0649 \u0641\u0627\u0626\u062f\u0629 \u0648\u0638\u064a\u0641\u064a\u0629 \u0648\u0627\u0636\u062d\u0629 \u0648\u0630\u0627\u062a \u0645\u063a\u0632\u0649 \u0641\u064a \u0627\u0644\u0627\u0633\u062a\u062e\u062f\u0627\u0645 \u0637\u0648\u064a\u0644 \u0627\u0644\u0623\u0645\u062f \u0641\u064a \u0627\u0644\u0639\u0627\u0644\u0645 \u0627\u0644\u062d\u0642\u064a\u0642\u064a \u0644\u0627 \u062a\u0632\u0627\u0644 \u0642\u064a\u062f \u0627\u0644\u062a\u062d\u0642\u0642.<\/li>\n\n\n\n<li>\u0646\u0638\u0631\u064b\u0627 \u0644\u0623\u0646 \u0623\u0631\u0642\u0627\u0645 \u0627\u0646\u062e\u0641\u0627\u0636 CK \u0644\u064a\u0633\u062a \u0645\u062d\u062f\u062f\u0629 \u0628\u0648\u0636\u0648\u062d\/\u0644\u0645 \u064a\u062a\u0645 \u0646\u0634\u0631\u0647\u0627 \u0628\u0627\u0633\u062a\u0645\u0631\u0627\u0631\u060c \u0641\u0644\u0627 \u064a\u0646\u0628\u063a\u064a \u0644\u0644\u0645\u0631\u0621 \u0623\u0646 \u064a\u0641\u062a\u0631\u0636 \u0623\u0646 CK \u0633\u0648\u0641 \u064a\u0646\u062e\u0641\u0636 \u0628\u0646\u0633\u0628\u0629 \u0645\u0639\u064a\u0646\u0629\u061b \u064a\u0638\u0644 \u0645\u0631\u0627\u0642\u0628\u0629 CK \u062c\u0632\u0621\u064b\u0627 \u0645\u0646 \u0627\u0644\u0628\u062d\u062b\/\u0627\u0644\u0645\u062a\u0627\u0628\u0639\u0629 \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629\u060c \u0648\u0644\u0643\u0646 \u064a\u062c\u0628 \u062a\u062e\u0641\u064a\u0641 \u0627\u0644\u062a\u0648\u0642\u0639\u0627\u062a.<\/li>\n\n\n\n<li>\u064a\u0638\u0644 \u0645\u0646 \u0627\u0644\u0645\u0647\u0645 \u0644\u0644\u063a\u0627\u064a\u0629 \u0627\u0644\u062a\u0633\u062c\u064a\u0644 \u0641\u064a \u0627\u0644\u062a\u062c\u0627\u0631\u0628 \u0627\u0644\u0645\u062a\u0627\u0628\u0639\u0629\/\u0627\u0644\u062a\u0623\u0643\u064a\u062f\u064a\u0629 (\u0645\u062b\u0644 EMBARK) \u0623\u0648 \u0645\u062a\u0627\u0628\u0639\u062a\u0647\u0627 \u0648\u0645\u0631\u0627\u0642\u0628\u0629 \u0643\u0644 \u0645\u0646 \u0627\u0644\u0645\u0624\u0634\u0631\u0627\u062a \u0627\u0644\u062d\u064a\u0648\u064a\u0629 \u0644\u0644\u0639\u0636\u0644\u0627\u062a (\u062a\u0639\u0628\u064a\u0631 \u0627\u0644\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646\u060c CK) \u0648\u0646\u0642\u0627\u0637 \u0627\u0644\u0646\u0647\u0627\u064a\u0629 \u0627\u0644\u0648\u0638\u064a\u0641\u064a\u0629 (\u0627\u0644\u0645\u0634\u064a\u060c \u0648\u0627\u0644\u0627\u062e\u062a\u0628\u0627\u0631\u0627\u062a \u0627\u0644\u0645\u062d\u062f\u062f\u0629 \u0627\u0644\u0648\u0642\u062a\u060c \u0648\u062d\u0627\u0644\u0629 \u0627\u0644\u062c\u0647\u0627\u0632 \u0627\u0644\u062a\u0646\u0641\u0633\u064a\/\u0627\u0644\u0642\u0644\u0628).<\/li>\n\n\n\n<li>\u0648\u0628\u0645\u0627 \u0623\u0646 \u0627\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u062c\u064a\u0646\u064a \u0647\u0648 \u0639\u0644\u0627\u062c \u0644\u0645\u0631\u0629 \u0648\u0627\u062d\u062f\u0629 \u0648\u0645\u0643\u0644\u0641 \u0644\u0644\u063a\u0627\u064a\u0629 (\u0648\u0642\u062f \u062a\u0645 \u0627\u0644\u0625\u0628\u0644\u0627\u063a \u0639\u0646 \u0627\u0644\u062a\u0633\u0639\u064a\u0631 \u0627\u0644\u0623\u0648\u0644\u064a \u0641\u064a \u0646\u0637\u0627\u0642 \u0645\u0644\u0627\u064a\u064a\u0646 \u0627\u0644\u062f\u0648\u0644\u0627\u0631\u0627\u062a \u0641\u064a \u0627\u0644\u0645\u0646\u0627\u0642\u0634\u0627\u062a) \u0648\u064a\u0646\u0637\u0648\u064a \u0639\u0644\u0649 \u0645\u062e\u0627\u0637\u0631 \u0645\u0639\u0631\u0648\u0641\u0629 \u062a\u062a\u0639\u0644\u0642 \u0628\u0627\u0644\u0633\u0644\u0627\u0645\u0629 (\u0639\u0644\u0649 \u0633\u0628\u064a\u0644 \u0627\u0644\u0645\u062b\u0627\u0644\u060c \u0625\u0635\u0627\u0628\u0629 \u0627\u0644\u0643\u0628\u062f)\u060c \u0641\u0625\u0646 \u0627\u0644\u0642\u0631\u0627\u0631 \u064a\u062c\u0628 \u0623\u0646 \u064a\u0632\u0646 \u0628\u064a\u0646 \u0627\u0644\u0645\u0639\u0631\u0648\u0641 \u0648\u0627\u0644\u0645\u062c\u0647\u0648\u0644.<\/li>\n<\/ul>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"n\">\u0628\u062d\u062b \u062c\u062f\u064a\u062f \u062d\u0648\u0644 \u062a\u0644\u0641 \u0627\u0644\u0644\u064a\u0633\u0648\u0633\u0648\u0645\u0627\u062a \u0641\u064a \u0645\u0631\u0636 \u062f\u0648\u0634\u064a\u0646<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u0639\u0644\u0649 \u0627\u0644\u0631\u063a\u0645 \u0645\u0646 \u062d\u0635\u0648\u0644 \u0627\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u062c\u064a\u0646\u064a (\u062f\u064a\u0644\u0627\u0646\u062f\u0633\u062a\u0631\u0648\u062c\u064a\u0646 \u0645\u0648\u0643\u0633\u064a\u0628\u0627\u0631\u0641\u0648\u0641\u064a\u0643) \u0639\u0644\u0649 \u0645\u0648\u0627\u0641\u0642\u0629 \u0625\u062f\u0627\u0631\u0629 \u0627\u0644\u063a\u0630\u0627\u0621 \u0648\u0627\u0644\u062f\u0648\u0627\u0621 \u0627\u0644\u0623\u0645\u0631\u064a\u0643\u064a\u0629 (FDA) \u0644\u0644\u0645\u0631\u0636\u0649 \u0627\u0644\u0645\u062a\u0646\u0642\u0644\u064a\u0646\u060c \u0625\u0644\u0627 \u0623\u0646 \u0627\u0644\u062a\u062d\u0633\u0646\u0627\u062a \u0627\u0644\u0648\u0638\u064a\u0641\u064a\u0629 \u0644\u0644\u0645\u0631\u0636\u0649 \u0644\u0645 \u062a\u0631\u0642 \u0625\u0644\u0649 \u0645\u0633\u062a\u0648\u0649 \u0627\u0644\u062a\u0648\u0642\u0639\u0627\u062a \u0642\u0628\u0644 \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629. \u0648\u064a\u0645\u0643\u0646 \u0625\u0631\u062c\u0627\u0639 \u0647\u0630\u0647 \u0627\u0644\u0641\u0627\u0626\u062f\u0629 \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629 \u0627\u0644\u0645\u062d\u062f\u0648\u062f\u0629 \u0625\u0644\u0649 \u0639\u062f\u0629 \u0639\u0648\u0627\u0645\u0644\u060c \u0645\u0646\u0647\u0627 \u0646\u0642\u0635 \u0628\u0639\u0636 \u0627\u0644\u0645\u062c\u0627\u0644\u0627\u062a \u0627\u0644\u0648\u0638\u064a\u0641\u064a\u0629 \u0627\u0644\u0645\u0648\u062c\u0648\u062f\u0629 \u0641\u064a \u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0643\u0627\u0645\u0644 \u0627\u0644\u0637\u0648\u0644. \u0644\u0630\u0644\u0643\u060c \u0642\u062f \u0644\u0627 \u064a\u062a\u0645\u0643\u0646 \u0646\u0642\u0644 \u0627\u0644\u062c\u064a\u0646\u0627\u062a \u0645\u0646 \u0639\u0643\u0633 \u062c\u0645\u064a\u0639 \u0627\u0644\u0622\u0644\u064a\u0627\u062a \u0627\u0644\u0645\u0631\u0636\u064a\u0629 \u0641\u064a \u0627\u0644\u0639\u0636\u0644\u0629. \u0644\u0630\u0627\u060c \u064a\u064f\u0639\u062f \u062a\u062d\u062f\u064a\u062f \u0627\u0644\u0622\u0644\u064a\u0627\u062a \u0627\u0644\u0645\u0631\u0636\u064a\u0629 \u0627\u0644\u0645\u062d\u062f\u062f\u0629 \u0627\u0644\u062a\u064a \u0644\u0645 \u064a\u064f\u0639\u0627\u0644\u062c\u0647\u0627 \u0627\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u062c\u064a\u0646\u064a\u060c \u0648\u0627\u0633\u062a\u0643\u0634\u0627\u0641 \u0645\u0646\u0627\u0647\u062c \u062a\u0631\u0643\u064a\u0628\u064a\u0629 \u0645\u0639 \u0639\u0644\u0627\u062c\u0627\u062a \u062a\u0643\u0645\u064a\u0644\u064a\u0629 \u062a\u0633\u062a\u0647\u062f\u0641 \u0647\u0630\u0647 \u0627\u0644\u0622\u0644\u064a\u0627\u062a\u060c \u0623\u0645\u0631\u064b\u0627 \u0628\u0627\u0644\u063a \u0627\u0644\u0623\u0647\u0645\u064a\u0629. &gt;&gt;&gt; \u0627\u0642\u0631\u0623 \u0627\u0644\u0645\u0632\u064a\u062f: <a href=\"https:\/\/www.science.org\/doi\/10.1126\/sciadv.adv6805\" target=\"_blank\" rel=\"noreferrer noopener\">\u064a\u0639\u062f \u062a\u0644\u0641 \u0627\u0644\u0644\u064a\u0633\u0648\u0633\u0648\u0645 \u0647\u062f\u0641\u064b\u0627 \u0639\u0644\u0627\u062c\u064a\u064b\u0627 \u0641\u064a \u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u062f\u0648\u0634\u064a\u0646<\/a><\/p>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"real-world-experience-with-elevidys-gene-therapy-report-from-qatar\">\u062a\u062c\u0631\u0628\u0629 \u0648\u0627\u0642\u0639\u064a\u0629 \u0645\u0639 \u062a\u0642\u0631\u064a\u0631 \u0627\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u062c\u064a\u0646\u064a Elevidys \u0645\u0646 \u0642\u0637\u0631<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u0641\u064a \u0647\u0630\u0647 \u0627\u0644\u062f\u0631\u0627\u0633\u0629 \u0627\u0644\u062a\u064a \u0623\u062c\u0631\u064a\u062a \u0641\u064a \u0642\u0637\u0631\u060c \u062a\u0645\u062a \u0645\u0631\u0627\u0642\u0628\u0629 \u0645\u0633\u062a\u0648\u064a\u0627\u062a \u0627\u0644\u0639\u062f\u064a\u062f \u0645\u0646 \u0627\u0644\u0645\u0624\u0634\u0631\u0627\u062a \u0627\u0644\u062d\u064a\u0648\u064a\u0629 (AST\u060c ALT\u060c CK\u060c Troponin I \u0648GGT) \u062e\u0644\u0627\u0644 \u0645\u062a\u0627\u0628\u0639\u0629 \u0644\u0645\u062f\u0629 30 \u0623\u0633\u0628\u0648\u0639\u064b\u0627 \u0644\u062f\u0649 \u062b\u0645\u0627\u0646\u064a\u0629 \u0645\u0631\u0636\u0649 \u064a\u062a\u0644\u0642\u0648\u0646 \u0627\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u062c\u064a\u0646\u064a \u0644\u0645\u0631\u0636 \u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u062f\u0648\u0634\u064a\u0646 (DMD). <strong>\u0645\u0635\u062f\u0631<\/strong>: <a href=\"https:\/\/www.nature.com\/articles\/s41434-025-00580-3\" target=\"_blank\" rel=\"noopener\">\u0646\u064a\u062a\u0634\u0631.\u0643\u0648\u0645<\/a><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0646\u0634\u0627\u0631\u0643 \u0645\u0639\u0643\u0645 \u0628\u0639\u0636 \u0627\u0644\u0646\u0642\u0627\u0637 \u0627\u0644\u0628\u0627\u0631\u0632\u0629 \u0641\u064a \u0627\u0644\u062f\u0631\u0627\u0633\u0629:<\/p>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"alt-and-ast-levels\">\u0645\u0633\u062a\u0648\u064a\u0627\u062a ALT \u0648AST<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u0623\u0638\u0647\u0631\u062a \u0645\u0633\u062a\u0648\u064a\u0627\u062a \u0625\u0646\u0632\u064a\u0645\u064a ALT \u0648AST \u0627\u0646\u062e\u0641\u0627\u0636\u064b\u0627 \u0641\u064a \u0627\u0644\u0623\u0633\u0628\u0648\u0639 \u0627\u0644\u0623\u0648\u0644\u060c \u062a\u0644\u0627\u0647 \u062a\u0642\u0644\u0628\u0627\u062a \u0637\u0641\u064a\u0641\u0629 \u0648\u0627\u0631\u062a\u0641\u0627\u0639 \u0637\u0641\u064a\u0641 \u0641\u064a \u0627\u0644\u0623\u0633\u0628\u0648\u0639\u064a\u0646 \u0627\u0644\u062b\u0627\u0646\u064a \u0648\u0627\u0644\u062b\u0627\u0644\u062b\u060c \u062b\u0645 \u0644\u0648\u062d\u0638 \u0627\u0633\u062a\u0642\u0631\u0627\u0631 \u062a\u062f\u0631\u064a\u062c\u064a \u0628\u062f\u0621\u064b\u0627 \u0645\u0646 \u0627\u0644\u0623\u0633\u0628\u0648\u0639 \u0627\u0644\u0631\u0627\u0628\u0639. \u0628\u062f\u0621\u064b\u0627 \u0645\u0646 \u0627\u0644\u0623\u0633\u0628\u0648\u0639 \u0627\u0644\u0631\u0627\u0628\u0639 \u0639\u0634\u0631\u060c \u0623\u0638\u0647\u0631 \u0627\u0644\u0645\u0631\u0636\u0649 \u0627\u0644\u0623\u0635\u063a\u0631 \u0633\u0646\u064b\u0627 \u0627\u0631\u062a\u0641\u0627\u0639\u064b\u0627 \u062a\u062f\u0631\u064a\u062c\u064a\u064b\u0627\u060c \u0648\u0628\u0644\u063a \u0630\u0631\u0648\u062a\u0647 \u0642\u0631\u0628 \u0627\u0644\u0623\u0633\u0628\u0648\u0639 \u0627\u0644\u0633\u0627\u062f\u0633 \u0648\u0627\u0644\u0639\u0634\u0631\u064a\u0646\u060c \u0642\u0628\u0644 \u0623\u0646 \u064a\u0639\u0648\u062f \u0625\u0644\u0649 \u0645\u0633\u062a\u0648\u064a\u0627\u062a\u0647 \u0627\u0644\u0623\u0648\u0644\u064a\u0629 \u0628\u0639\u062f \u0627\u0644\u062d\u0642\u0646 \u0641\u064a \u0627\u0644\u0623\u0633\u0628\u0648\u0639 \u0627\u0644\u062b\u0627\u0646\u064a \u062a\u0642\u0631\u064a\u0628\u064b\u0627.<\/p>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"creatine-kinase-ck-levels\">\u0645\u0633\u062a\u0648\u064a\u0627\u062a \u0627\u0644\u0643\u0631\u064a\u0627\u062a\u064a\u0646 \u0643\u064a\u0646\u0627\u0632 (CK)<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u062e\u0644\u0627\u0644 \u0639\u0645\u0644\u064a\u0627\u062a \u0627\u0644\u0645\u062a\u0627\u0628\u0639\u0629\u060c \u0623\u0638\u0647\u0631 CK \u0627\u0633\u062a\u062c\u0627\u0628\u0629 \u0623\u0648\u0644\u064a\u0629 \u0623\u0643\u062b\u0631 \u0648\u0636\u0648\u062d\u064b\u0627\u060c \u062d\u064a\u062b \u0623\u0638\u0647\u0631 \u0627\u0646\u062e\u0641\u0627\u0636\u064b\u0627 \u062d\u0627\u062f\u064b\u0627 \u0642\u062f\u0631\u0647 44.1% \u0641\u064a \u0627\u0644\u0623\u0633\u0628\u0648\u0639 \u0627\u0644\u0623\u0648\u0644. \u0627\u0633\u062a\u0645\u0631\u062a \u0627\u0644\u0645\u0633\u062a\u0648\u064a\u0627\u062a \u0641\u064a \u0627\u0644\u0627\u0646\u062e\u0641\u0627\u0636\u060c \u0644\u062a\u0635\u0644 \u0625\u0644\u0649 \u0623\u062f\u0646\u0649 \u0645\u0633\u062a\u0648\u0649 \u0644\u0647\u0627 \u0641\u064a \u0627\u0644\u0623\u0633\u0628\u0648\u0639 \u0627\u0644\u0631\u0627\u0628\u0639 \u062a\u0642\u0631\u064a\u0628\u064b\u0627. <strong>\u0648\u0645\u0639 \u0630\u0644\u0643\u060c \u0627\u0631\u062a\u0641\u0639\u062a \u0645\u0633\u062a\u0648\u064a\u0627\u062a CK \u0628\u0634\u0643\u0644 \u0645\u0644\u062d\u0648\u0638 \u0628\u0645\u0642\u062f\u0627\u0631 84.2% \u0628\u062d\u0644\u0648\u0644 \u0627\u0644\u0623\u0633\u0628\u0648\u0639 7.<\/strong> \u064a\u0634\u064a\u0631 \u0647\u0630\u0627 \u0627\u0644\u0646\u0645\u0637 \u0625\u0644\u0649 \u0627\u0633\u062a\u062c\u0627\u0628\u0629 \u0623\u0648\u0644\u064a\u0629 \u0642\u0648\u064a\u0629 \u0644\u0644\u0639\u0644\u0627\u062c\u060c \u0645\u0645\u0627 \u064a\u0639\u0643\u0633 \u0639\u0644\u0649 \u0627\u0644\u0623\u0631\u062c\u062d \u0625\u0635\u0644\u0627\u062d \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0623\u0648 \u062a\u0642\u0644\u064a\u0644 \u062a\u0644\u0641 \u0627\u0644\u0639\u0636\u0644\u0627\u062a\u060c \u064a\u062a\u0628\u0639\u0647 \u0645\u0631\u062d\u0644\u0629 \u0645\u062a\u0642\u0644\u0628\u0629 \u0645\u0639 \u062a\u0643\u064a\u0641 \u0627\u0644\u062c\u0633\u0645.<\/p>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"n-1\">\u0646\u062a\u064a\u062c\u0629 NSAA<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u0623\u0641\u0627\u062f \u062c\u0645\u064a\u0639 \u0627\u0644\u0622\u0628\u0627\u0621 \u0648\u0627\u0644\u0623\u0645\u0647\u0627\u062a \u0628\u062a\u063a\u064a\u0631\u0627\u062a \u0648\u0638\u064a\u0641\u064a\u0629 \u0625\u064a\u062c\u0627\u0628\u064a\u0629 \u062e\u0644\u0627\u0644 \u0634\u0647\u0631\u064a\u0646 \u0645\u0646 \u062a\u0644\u0642\u064a \u0627\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u062c\u064a\u0646\u064a\u060c \u0645\u0639 \u0623\u0646 \u0623\u0631\u0628\u0639\u0629 \u0645\u0646 \u0623\u0635\u0644 \u062e\u0645\u0633\u0629 \u0623\u0639\u0631\u0628\u0648\u0627 \u0639\u0646 \u0645\u062e\u0627\u0648\u0641\u0647\u0645 \u0628\u0634\u0623\u0646 \u0632\u064a\u0627\u062f\u0629 \u0627\u0644\u0648\u0632\u0646 \u0628\u0639\u062f \u0627\u0644\u0639\u0644\u0627\u062c. \u0638\u0644 \u0623\u062d\u062f \u0627\u0644\u0645\u0631\u0636\u0649 \u063a\u064a\u0631 \u0642\u0627\u062f\u0631 \u0639\u0644\u0649 \u0627\u0644\u0645\u0634\u064a\u060c \u0648\u0644\u0645 \u064a\u0643\u0646 \u0645\u0646 \u0627\u0644\u0645\u0645\u0643\u0646 \u0636\u0628\u0637 \u062a\u0648\u0642\u064a\u062a\u0647 \u0644\u0627\u062e\u062a\u0628\u0627\u0631 \u0627\u0644\u0645\u0634\u064a \u0644\u0645\u062f\u0629 \u0639\u0634\u0631 \u062f\u0642\u0627\u0626\u0642 \u0623\u0648 \u0627\u0644\u0642\u064a\u0627\u0645 \u0628\u0642\u0641\u0632\u0629 \u0623\u0631\u0636\u064a\u0629\u060c \u0628\u064a\u0646\u0645\u0627 \u0623\u0638\u0647\u0631 \u0645\u0631\u064a\u0636 \u0622\u062e\u0631 \u062a\u062d\u0633\u0646\u064b\u0627 \u062a\u062f\u0631\u064a\u062c\u064a\u064b\u0627 \u0641\u064a \u0633\u0631\u0639\u0629 \u0627\u062e\u062a\u0628\u0627\u0631 \u0627\u0644\u0645\u0634\u064a \u0644\u0645\u062f\u0629 \u0639\u0634\u0631 \u062f\u0642\u0627\u0626\u0642 \u0639\u0644\u0649 \u0645\u062f\u0627\u0631 \u0634\u0647\u0631\u064a\u0646\u060c \u0628\u064a\u0646\u0645\u0627 \u0623\u0638\u0647\u0631 \u0627\u062b\u0646\u0627\u0646 \u0627\u0646\u062e\u0641\u0627\u0636\u064b\u0627 \u0641\u064a \u0627\u0644\u0633\u0631\u0639\u0629\u060c \u0628\u064a\u0646\u0645\u0627 \u0638\u0644 \u0645\u0631\u064a\u0636 \u0648\u0627\u062d\u062f \u062f\u0648\u0646 \u062a\u063a\u064a\u064a\u0631. \u062a\u0634\u064a\u0631 \u0647\u0630\u0647 \u0627\u0644\u0646\u062a\u0627\u0626\u062c\u060c \u0625\u0644\u0649 \u062c\u0627\u0646\u0628 \u0645\u0644\u0627\u062d\u0638\u0627\u062a \u0627\u0644\u0622\u0628\u0627\u0621 \u0648\u0627\u0644\u0623\u0645\u0647\u0627\u062a\u060c \u0625\u0644\u0649 \u0623\u0646 \u0632\u064a\u0627\u062f\u0629 \u0627\u0644\u0648\u0632\u0646 \u0627\u0644\u0646\u0627\u062a\u062c\u0629 \u0639\u0646 \u0627\u0644\u0633\u062a\u064a\u0631\u0648\u064a\u062f \u0642\u062f \u062a\u0624\u062b\u0631 \u0639\u0644\u0649 \u0648\u0638\u064a\u0641\u0629 \u0627\u0644\u0645\u0631\u064a\u0636 \u0628\u0639\u062f \u0627\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u062c\u064a\u0646\u064a.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0647\u0646\u0627\u0643 \u062d\u0627\u062c\u0629 \u0625\u0644\u0649 \u0645\u0632\u064a\u062f \u0645\u0646 \u0627\u0644\u0628\u064a\u0627\u0646\u0627\u062a \u0627\u0644\u0623\u0643\u0628\u0631 \u0641\u064a \u0627\u0644\u0639\u0627\u0644\u0645 \u0627\u0644\u062d\u0642\u064a\u0642\u064a \u0644\u062a\u0623\u0643\u064a\u062f \u0633\u0644\u0627\u0645\u0629 \u0648\u0641\u0639\u0627\u0644\u064a\u0629 \u0639\u0642\u0627\u0631 \u062f\u064a\u0644\u0627\u0646\u062f\u0633\u062a\u0631\u0648\u062c\u064a\u0646 \u0645\u0648\u0643\u0633\u064a\u0628\u0627\u0631\u0641\u0648\u0641\u064a\u0643 \u0644\u0639\u0644\u0627\u062c \u0645\u0631\u0636\u0649 \u062f\u0648\u0634\u064a\u0646.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u064a\u062a\u0639\u0644\u0645 \u0623\u0643\u062b\u0631<\/strong>: <a href=\"https:\/\/dmdwarrior.com\/ar\/biomarkers-in-duchenne-muscular-dystrophy\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u0644\u0627 \u064a\u0643\u0641\u064a \u0627\u0633\u062a\u062e\u062f\u0627\u0645 \u0645\u0636\u0627\u062f\u0627\u062a \u0627\u0644\u0627\u0644\u062a\u0647\u0627\u0628 \u063a\u064a\u0631 \u0627\u0644\u0633\u062a\u064a\u0631\u0648\u064a\u062f\u064a\u0629 \u0648\u062d\u062f\u0647\u0627: \u0644\u0645\u0627\u0630\u0627 \u064a\u062c\u0628 \u0623\u0646 \u062a\u0643\u0648\u0646 \u0645\u0633\u062a\u0648\u064a\u0627\u062a \u0627\u0644\u0643\u0631\u064a\u0627\u062a\u064a\u0646 \u0643\u064a\u0646\u0627\u0632 (CK) \u0648AST \u0648ALT \u0648\u0627\u0644\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0645\u062a\u0627\u062d\u0629 \u0644\u0644\u0639\u0627\u0645\u0629\u061f<\/a><\/p>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"conclusion\">\u062e\u0627\u062a\u0645\u0629<\/h2>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u0646\u0639\u0645\u060c \u064a\u0624\u062f\u064a \u0627\u0644\u0639\u0644\u0627\u062c \u0628\u0627\u0633\u062a\u062e\u062f\u0627\u0645 ELEVIDYS \u0625\u0644\u0649 \u0632\u064a\u0627\u062f\u0629 \u0627\u0644\u062a\u0639\u0628\u064a\u0631 \u0639\u0646 \u0627\u0644\u0645\u064a\u0643\u0631\u0648\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0641\u064a \u0627\u0644\u0639\u0636\u0644\u0627\u062a (\u0645\u0639 \u0623\u0631\u0642\u0627\u0645 \u0645\u062b\u0644 ~28% \u0641\u064a \u0625\u062d\u062f\u0649 \u0627\u0644\u062f\u0631\u0627\u0633\u0627\u062a).<\/li>\n\n\n\n<li>\u0644\u0645 \u064a\u062a\u0645 \u0627\u0644\u0625\u0639\u0644\u0627\u0646 \u0639\u0646 \u062f\u0631\u062c\u0629 \u0627\u0646\u062e\u0641\u0627\u0636 CK \u0628\u0634\u0643\u0644 \u062c\u064a\u062f \u0623\u0648 \u0648\u0635\u0641\u0647\u0627 \u0628\u0634\u0643\u0644 \u0642\u0648\u064a \u0641\u064a \u0627\u0644\u062f\u0631\u0627\u0633\u0627\u062a \u0648\u0627\u0633\u0639\u0629 \u0627\u0644\u0646\u0637\u0627\u0642 \u0627\u0644\u062a\u064a \u062a\u0645\u062a \u0645\u0631\u0627\u062c\u0639\u062a\u0647\u0627 \u0645\u0646 \u0642\u0628\u0644 \u0627\u0644\u0646\u0638\u0631\u0627\u0621 - \u0644\u0630\u0644\u0643 \u062a\u0638\u0644 &quot;\u0645\u0633\u0623\u0644\u0629 \u0641\u0636\u0648\u0644&quot;.<\/li>\n\n\n\n<li>\u0648\u062a\u0638\u0644 \u0627\u0644\u0641\u0627\u0626\u062f\u0629 \u0627\u0644\u0648\u0638\u064a\u0641\u064a\u0629 \u0637\u0648\u064a\u0644\u0629 \u0627\u0644\u0623\u0645\u062f \u0642\u064a\u062f \u0627\u0644\u062a\u062d\u0642\u0642\u060c \u0645\u0645\u0627 \u064a\u0639\u0646\u064a \u0623\u0646 \u062a\u062d\u0633\u064a\u0646\u0627\u062a \u0627\u0644\u0645\u0624\u0634\u0631\u0627\u062a \u0627\u0644\u062d\u064a\u0648\u064a\u0629 (\u0627\u0631\u062a\u0641\u0627\u0639 \u0627\u0644\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646\u060c \u0648\u0627\u0646\u062e\u0641\u0627\u0636 CK \u0631\u0628\u0645\u0627) \u0645\u0634\u062c\u0639\u0629 \u0648\u0644\u0643\u0646\u0647\u0627 \u0644\u0627 \u062a\u0636\u0645\u0646 \u0628\u0634\u0643\u0644 \u0642\u0627\u0637\u0639 \u062d\u062a\u0649 \u0627\u0644\u0622\u0646 \u062a\u062d\u0633\u064a\u0646 \u0627\u0644\u0646\u062a\u0627\u0626\u062c \u0627\u0644\u062d\u0631\u0643\u064a\u0629.<\/li>\n\n\n\n<li>\u0648\u0645\u0639 \u0638\u0647\u0648\u0631 \u0628\u064a\u0627\u0646\u0627\u062a \u0625\u0636\u0627\u0641\u064a\u0629 \u0645\u0646 \u0627\u0644\u062a\u062c\u0627\u0631\u0628 \u0627\u0644\u062a\u0623\u0643\u064a\u062f\u064a\u0629 \u0648\u0627\u0644\u0633\u062c\u0644\u0627\u062a \u0641\u064a \u0627\u0644\u0639\u0627\u0644\u0645 \u0627\u0644\u062d\u0642\u064a\u0642\u064a\u060c \u0646\u062a\u0648\u0642\u0639 \u0623\u0646 \u0646\u0631\u0649 \u0623\u0631\u0642\u0627\u0645\u064b\u0627 \u0623\u0643\u062b\u0631 \u062a\u0641\u0635\u064a\u0644\u0627\u064b \u0644\u0627\u0646\u062e\u0641\u0627\u0636 CK\u060c \u0648\u0627\u0633\u062a\u062f\u0627\u0645\u0629 \u0627\u0644\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646\/\u0627\u0644\u0645\u064a\u0643\u0631\u0648\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646\u060c \u0648\u0627\u0644\u0627\u0631\u062a\u0628\u0627\u0637 \u0628\u0627\u0644\u0648\u0638\u064a\u0641\u0629 \u0627\u0644\u062d\u0631\u0643\u064a\u0629 - \u0648\u0647\u0630\u0627 \u0645\u0646 \u0634\u0623\u0646\u0647 \u0623\u0646 \u064a\u0633\u0627\u0639\u062f \u0627\u0644\u0623\u0633\u0631 \u0648\u0627\u0644\u0623\u0637\u0628\u0627\u0621 \u0639\u0644\u0649 \u0627\u062a\u062e\u0627\u0630 \u0642\u0631\u0627\u0631\u0627\u062a \u0623\u0643\u062b\u0631 \u0627\u0633\u062a\u0646\u0627\u0631\u0629.<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u064a\u062a\u0639\u0644\u0645 \u0623\u0643\u062b\u0631<\/strong>:&nbsp;<a href=\"https:\/\/dmdwarrior.com\/ar\/frequently-asked-questions-about-elevidys-used-for-duchenne-muscular-dystrophy\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u0627\u0644\u0623\u0633\u0626\u0644\u0629 \u0627\u0644\u0634\u0627\u0626\u0639\u0629 \u062d\u0648\u0644 Elevidys<\/a><\/p>","protected":false},"excerpt":{"rendered":"<p>It remains a matter of curiosity how much Creatine Kinase (CK) levels decrease, NSAA score and normal dystrophin levels increase in children with DMD who receive ELEVIDYS (delandistrogene moxeparvovec-rokl), one of the world&#8217;s most expensive therapies developed by Sarepta Therapeutics for Duchenne muscular dystrophy. ELEVIDYS (delandistrogene moxeparvovec-rokl), developed by Sarepta Therapeutics, is a one-time AAV [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":5211,"comment_status":"open","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[282],"tags":[121,33,179,203,65],"class_list":["post-4942","post","type-post","status-publish","format-standard","has-post-thumbnail","category-editorials","tag-delandistrogene-moxeparvovec","tag-elevidys","tag-elevidys-gene-therapy","tag-roche","tag-sarepta"],"_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/posts\/4942","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/comments?post=4942"}],"version-history":[{"count":0,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/posts\/4942\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/media\/5211"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/media?parent=4942"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/categories?post=4942"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/tags?post=4942"}],"curies":[{"name":"\u0648\u0648\u0631\u062f\u0628\u0631\u064a\u0633","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}