{"id":4428,"date":"2025-09-07T13:07:26","date_gmt":"2025-09-07T10:07:26","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=4428"},"modified":"2025-11-03T20:20:56","modified_gmt":"2025-11-03T17:20:56","slug":"gnr-097-duchenne-gene-therapy-phase-1-2-study-started-by-generium","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/ar\/gnr-097-duchenne-gene-therapy-phase-1-2-study-started-by-generium\/","title":{"rendered":"GNR-097: \u062f\u0631\u0627\u0633\u0629 \u0627\u0644\u0645\u0631\u062d\u0644\u0629 \u0627\u0644\u0623\u0648\u0644\u0649\/\u0627\u0644\u062b\u0627\u0646\u064a\u0629 \u0644\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u062c\u064a\u0646\u064a \u0644\u0645\u0631\u0636 \u062f\u0648\u0634\u064a\u0646\u060c \u0628\u062f\u0623\u0647\u0627 Generium"},"content":{"rendered":"<p class=\"wp-block-paragraph\"><strong>\u062d\u0635\u0644\u062a \u0634\u0631\u0643\u0629 Generium \u0627\u0644\u0631\u0648\u0633\u064a\u0629 \u0644\u0644\u062a\u0643\u0646\u0648\u0644\u0648\u062c\u064a\u0627 \u0627\u0644\u062d\u064a\u0648\u064a\u0629 \u0627\u0644\u0645\u0628\u062a\u0643\u0631\u0629 \u0639\u0644\u0649 \u0627\u0644\u0645\u0648\u0627\u0641\u0642\u0629 \u0644\u0625\u062c\u0631\u0627\u0621 \u062a\u062c\u0631\u0628\u0629 \u0633\u0631\u064a\u0631\u064a\u0629 \u0639\u0644\u0649 \u0639\u0642\u0627\u0631 \u0627\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u062c\u064a\u0646\u064a GNR-097 \u0644\u0639\u0644\u0627\u062c \u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u062a\u062f\u0631\u064a\u062c\u064a (DMD).<\/strong><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u062a\u062a\u0636\u0645\u0646 \u0647\u0630\u0647 \u0627\u0644\u062a\u062c\u0631\u0628\u0629 \u0645\u062a\u0639\u062f\u062f\u0629 \u0627\u0644\u0645\u0631\u0627\u0643\u0632\u060c \u0623\u062d\u0627\u062f\u064a\u0629 \u0627\u0644\u062a\u0639\u0645\u064a\u0629\u060c \u0639\u0634\u0648\u0627\u0626\u064a\u0629\u060c \u0645\u064f\u062d\u0643\u0645\u0629 \u0628\u0627\u0633\u062a\u062e\u062f\u0627\u0645 \u062f\u0648\u0627\u0621 \u0648\u0647\u0645\u064a\u060c \u0625\u0639\u0637\u0627\u0621\u064b \u0648\u0631\u064a\u062f\u064a\u064b\u0627 \u0648\u0627\u062d\u062f\u064b\u0627 \u0644\u062f\u0648\u0627\u0621 \u0627\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u062c\u064a\u0646\u064a \u0644\u0645\u0631\u0636\u0649 \u0623\u0637\u0641\u0627\u0644 \u0645\u0635\u0627\u0628\u064a\u0646 \u0628\u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a \u0627\u0644\u062a\u062f\u0631\u064a\u062c\u064a. \u062a\u0647\u062f\u0641 \u0647\u0630\u0647 \u0627\u0644\u062f\u0631\u0627\u0633\u0629\u060c \u0648\u0647\u064a \u062f\u0631\u0627\u0633\u0629 \u0645\u0646 \u0627\u0644\u0645\u0631\u062d\u0644\u0629 \u0627\u0644\u0623\u0648\u0644\u0649 \u0648\u0627\u0644\u062b\u0627\u0646\u064a\u0629\u060c \u0625\u0644\u0649 \u062a\u0642\u064a\u064a\u0645 \u0645\u062f\u0649 \u062a\u062d\u0645\u0651\u0644 \u062f\u0648\u0627\u0621 GNR-097 \u0648\u0633\u0644\u0627\u0645\u062a\u0647 \u0648\u0641\u0639\u0627\u0644\u064a\u062a\u0647.<\/p>\n\n\n\n<h2 class=\"wp-block-heading\">\u0627\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u062c\u064a\u0646\u064a \u0644\u062f\u0648\u0634\u064a\u0646 GNR-097<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>GNR-097 \u0647\u0648 \u0646\u0627\u0642\u0644 \u0641\u064a\u0631\u0648\u0633\u064a \u0645\u0631\u062a\u0628\u0637 \u0628\u0627\u0644\u063a\u062f\u0629 \u0627\u0644\u062f\u0631\u0642\u064a\u0629 \u0645\u0646 \u0627\u0644\u0646\u0645\u0637 \u0627\u0644\u0645\u0635\u0644\u064a 9\u060c \u0648\u0647\u0648 \u064a\u0634\u0641\u0631 \u062c\u064a\u0646 \u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0645\u0642\u0637\u0648\u0639.<\/strong><\/p>\n\n\n\n<h2 class=\"wp-block-heading\">\u062f\u0627\u0646\u064a\u064a\u0644 \u062a\u0627\u0644\u064a\u0627\u0646\u0633\u0643\u064a\u060c \u0627\u0644\u0631\u0626\u064a\u0633 \u0627\u0644\u062a\u0646\u0641\u064a\u0630\u064a \u0644\u0634\u0631\u0643\u0629 GENERIUM:<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u064a\u064f\u0639\u062f \u0627\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u062c\u064a\u0646\u064a \u0623\u062d\u062f\u062b\u064e \u0648\u0623\u062d\u062f\u062b\u064e \u0645\u062c\u0627\u0644\u064d \u0641\u064a \u0645\u062c\u0627\u0644 \u0627\u0644\u0623\u062f\u0648\u064a\u0629 \u0648\u0627\u0644\u0639\u0644\u0648\u0645 \u0627\u0644\u0637\u0628\u064a\u0629 \u0627\u0644\u0639\u0627\u0644\u0645\u064a\u0629. \u0648\u0642\u062f \u0623\u062a\u0627\u062d\u062a \u0627\u0644\u062e\u0628\u0631\u0629\u064f \u0627\u0644\u0641\u0631\u064a\u062f\u0629\u064f \u0644\u0644\u0639\u0644\u0645\u0627\u0621\u0650 \u0627\u0644\u0631\u0648\u0633 \u062a\u0637\u0648\u064a\u0631\u064e \u0646\u0627\u0642\u0644\u064d \u0641\u064a\u0631\u0648\u0633\u064a\u064d\u0651 \u0645\u064f\u0639\u0627\u062f\u0650 \u0627\u0644\u062a\u0631\u0643\u064a\u0628\u0650 \u0645\u0631\u062a\u0628\u0637\u064d \u0628\u0627\u0644\u063a\u062f\u0629\u0650 \u0627\u0644\u063a\u062f\u064a\u0629\u0650\u060c \u064a\u064f\u0634\u0641\u0650\u0651\u0631\u064f \u062c\u064a\u0646\u064e \u0627\u0644\u0645\u064a\u0643\u0631\u0648\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646. \u0648\u0646\u062d\u0646\u064f \u0627\u0644\u0622\u0646 \u0628\u0635\u062f\u062f\u0650 \u0628\u062f\u0621\u0650 \u0627\u0644\u062a\u062c\u0627\u0631\u0628\u0650 \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629\u0650 \u0644\u0647\u0630\u0627 \u0627\u0644\u062f\u0648\u0627\u0621\u0650 \u0627\u0644\u0623\u0635\u0644\u064a\u0650\u0651\u060c \u0627\u0644\u0630\u064a \u064a\u062d\u0645\u0644\u064f \u0622\u0645\u0627\u0644\u064b\u0627 \u0643\u0628\u064a\u0631\u0629\u064b.<\/p>\n\n\n\n<h2 class=\"wp-block-heading\">\u0627\u0644\u062a\u062c\u0631\u0628\u0629 \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629 \u0644\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u062c\u064a\u0646\u064a GNR-097<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u062a\u062c\u0631\u0628\u0629 \u0647\u0630\u0627 \u0627\u0644\u062f\u0648\u0627\u0621 \u0627\u0644\u0645\u0628\u062a\u0643\u0631 \u062f\u0648\u0644\u064a\u0629\u060c \u0648\u0633\u062a\u064f\u062c\u0631\u0649 \u0641\u064a \u0627\u0644\u0627\u062a\u062d\u0627\u062f \u0627\u0644\u0631\u0648\u0633\u064a \u0648\u062c\u0645\u0647\u0648\u0631\u064a\u0629 \u0628\u064a\u0644\u0627\u0631\u0648\u0633\u064a\u0627. \u0641\u064a \u0631\u0648\u0633\u064a\u0627\u060c \u0633\u062a\u064f\u062c\u0631\u0649 \u0627\u0644\u062f\u0631\u0627\u0633\u0629 \u0641\u064a \u062e\u0645\u0633\u0629 \u0645\u0631\u0627\u0643\u0632 \u0637\u0628\u064a\u0629: \u0627\u0644\u0645\u0639\u0647\u062f \u0627\u0644\u0628\u062d\u062b\u064a \u0627\u0644\u0633\u0631\u064a\u0631\u064a \u0644\u0637\u0628 \u0627\u0644\u0623\u0637\u0641\u0627\u0644 \u0648\u062c\u0631\u0627\u062d\u0629 \u0627\u0644\u0623\u0637\u0641\u0627\u0644\u060c \u0627\u0644\u0630\u064a \u064a\u062d\u0645\u0644 \u0627\u0633\u0645 \u0627\u0644\u0623\u0643\u0627\u062f\u064a\u0645\u064a \u064a\u0648. \u0625\u064a. \u0641\u064a\u0644\u062a\u064a\u0634\u064a\u0641\u060c \u0648\u062c\u0627\u0645\u0639\u0629 \u0628\u064a\u0631\u0648\u063a\u0648\u0641 \u0627\u0644\u0631\u0648\u0633\u064a\u0629 \u0627\u0644\u0648\u0637\u0646\u064a\u0629 \u0644\u0644\u0623\u0628\u062d\u0627\u062b \u0627\u0644\u0637\u0628\u064a\u0629\u060c \u0648\u062c\u0627\u0645\u0639\u0629 \u0633\u0627\u0646\u062a \u0628\u0637\u0631\u0633\u0628\u0631\u063a \u0627\u0644\u062d\u0643\u0648\u0645\u064a\u0629 \u0644\u0637\u0628 \u0627\u0644\u0623\u0637\u0641\u0627\u0644\u060c \u0648\u0627\u0644\u0645\u0633\u062a\u0634\u0641\u0649 \u0627\u0644\u0625\u0642\u0644\u064a\u0645\u064a \u0644\u0644\u0623\u0637\u0641\u0627\u0644 \u0627\u0644\u0633\u0631\u064a\u0631\u064a \u0641\u064a \u064a\u0643\u0627\u062a\u0631\u064a\u0646\u0628\u0648\u0631\u063a\u060c \u0648\u0627\u0644\u0645\u0631\u0643\u0632 \u0627\u0644\u0648\u0637\u0646\u064a \u0644\u0644\u0623\u0628\u062d\u0627\u062b \u0627\u0644\u0637\u0628\u064a\u0629 \u0644\u0635\u062d\u0629 \u0627\u0644\u0623\u0637\u0641\u0627\u0644. \u0623\u0645\u0627 \u0641\u064a \u0628\u064a\u0644\u0627\u0631\u0648\u0633\u064a\u0627\u060c \u0641\u0633\u062a\u064f\u062c\u0631\u0649 \u0627\u0644\u062a\u062c\u0631\u0628\u0629 \u0641\u064a \u0627\u0644\u0645\u0631\u0643\u0632 \u0627\u0644\u062c\u0645\u0647\u0648\u0631\u064a \u0627\u0644\u0639\u0644\u0645\u064a \u0648\u0627\u0644\u0639\u0645\u0644\u064a &quot;\u0627\u0644\u0623\u0645 \u0648\u0627\u0644\u0637\u0641\u0644&quot;.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u0627\u0642\u0631\u0623 \u0627\u0644\u0645\u0632\u064a\u062f<\/strong>:\u00a0<a href=\"https:\/\/dmdwarrior.com\/ar\/dmd-therapies\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u0627\u0644\u062a\u062c\u0627\u0631\u0628 \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629 \u0644\u0645\u0631\u0636 \u062f\u0648\u0634\u064a\u0646 (\u0642\u0627\u0626\u0645\u0629 \u0628\u062c\u0645\u064a\u0639 \u0627\u0644\u0623\u0628\u062d\u0627\u062b)<\/a><\/p>","protected":false},"excerpt":{"rendered":"<p>Generium is a Russian innovative biotechnology company has received approval to conduct a clinical trial of GNR-097 gene therapy drug for the treatment of progressive Duchenne muscular dystrophy (DMD). The multicenter, single-blind, randomized placebo-controlled trial involves a single intravenous administration of the gene therapy drug to pediatric patients with progressive Duchenne muscular dystrophy. This Phase [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":4430,"comment_status":"open","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[27],"tags":[137,415,61,241,414,135],"class_list":["post-4428","post","type-post","status-publish","format-standard","has-post-thumbnail","category-research","tag-clinical-trial","tag-daniil-talyansky","tag-gene-therapy","tag-generium","tag-gnr-097","tag-russia"],"_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/posts\/4428","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/comments?post=4428"}],"version-history":[{"count":0,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/posts\/4428\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/media\/4430"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/media?parent=4428"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/categories?post=4428"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/tags?post=4428"}],"curies":[{"name":"\u0648\u0648\u0631\u062f\u0628\u0631\u064a\u0633","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}