{"id":4151,"date":"2025-07-18T12:17:47","date_gmt":"2025-07-18T09:17:47","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=4151"},"modified":"2025-07-18T12:17:49","modified_gmt":"2025-07-18T09:17:49","slug":"uw-medicine-announces-new-gene-therapy-research-for-duchenne-muscular-dystrophy","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/ar\/uw-medicine-announces-new-gene-therapy-research-for-duchenne-muscular-dystrophy\/","title":{"rendered":"UW Medicine \u062a\u0639\u0644\u0646 \u0639\u0646 \u0628\u062d\u062b \u062c\u062f\u064a\u062f \u0641\u064a \u0645\u062c\u0627\u0644 \u0627\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u062c\u064a\u0646\u064a \u0644\u0645\u0631\u0636 \u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u062f\u0648\u0634\u064a\u0646"},"content":{"rendered":"<p class=\"wp-block-paragraph\">\u0628\u0627\u0644\u0646\u0633\u0628\u0629 \u0644\u0623\u0648\u0644\u0626\u0643 \u0627\u0644\u0630\u064a\u0646 \u064a\u0639\u0627\u0646\u0648\u0646 \u0645\u0646 \u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a (DMD)\u060c \u0641\u0625\u0646 \u0627\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u062c\u064a\u0646\u064a \u0627\u0644\u062c\u062f\u064a\u062f \u064a\u062d\u0645\u0644 \u0648\u0639\u062f\u064b\u0627 \u0628\u0648\u0642\u0641 \u0641\u0642\u062f\u0627\u0646 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0648\u0631\u0628\u0645\u0627 \u0627\u0633\u062a\u0639\u0627\u062f\u0629 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0627\u0644\u062a\u0627\u0644\u0641\u0629 \u0641\u064a \u0627\u0644\u0645\u0633\u062a\u0642\u0628\u0644. <strong>\u0648\u0642\u0627\u0644\u062a \u0634\u0631\u0643\u0629 UW Medicine \u0625\u0646 \u0627\u0644\u062e\u0637\u0648\u0629 \u0627\u0644\u062a\u0627\u0644\u064a\u0629 \u0644\u0644\u0639\u0644\u0627\u062c \u0633\u062a\u0643\u0648\u0646 \u0627\u0644\u062a\u062c\u0627\u0631\u0628 \u0627\u0644\u0628\u0634\u0631\u064a\u0629\u060c \u0648\u0627\u0644\u062a\u064a \u0645\u0646 \u0627\u0644\u0645\u062a\u0648\u0642\u0639 \u0623\u0646 \u062a\u0628\u062f\u0623 \u0641\u064a \u063a\u0636\u0648\u0646 \u0639\u0627\u0645\u064a\u0646 \u062a\u0642\u0631\u064a\u0628\u064b\u0627.<\/strong><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u062a\u0647\u062f\u0641 \u0627\u0644\u062f\u0631\u0627\u0633\u0629 \u0627\u0644\u062a\u064a \u0623\u062c\u0631\u0627\u0647\u0627 UW Medicine \u0625\u0644\u0649 \u0627\u0633\u062a\u0628\u062f\u0627\u0644 \u062c\u064a\u0646 \u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0627\u0644\u062a\u0627\u0644\u0641 \u0641\u064a \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0628\u0625\u062f\u062e\u0627\u0644 \u0633\u0644\u0633\u0644\u0629 \u0645\u0646 \u0627\u0644\u062d\u0632\u0645 \u0627\u0644\u0628\u0631\u0648\u062a\u064a\u0646\u064a\u0629 \u062f\u0627\u062e\u0644 \u0646\u0627\u0642\u0644 \u0645\u0643\u0648\u0643\u064a\u0651. \u0628\u0639\u062f \u0630\u0644\u0643\u060c \u0633\u064a\u062a\u0645 \u0625\u0646\u062a\u0627\u062c 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\u0627\u0644\u062f\u0643\u062a\u0648\u0631 \u062c\u064a\u0641\u0631\u064a \u062a\u0634\u0627\u0645\u0628\u0631\u0644\u064a\u0646\u061f<\/a><\/li><li><a href=\"#what-is-uw-medicines-new-gene-study\">\u0645\u0627 \u0647\u064a \u062f\u0631\u0627\u0633\u0629 \u0627\u0644\u062c\u064a\u0646 \u0627\u0644\u062c\u062f\u064a\u062f UW Medicine\u061f<\/a><\/li><li><a href=\"#human-trials-should-begin-in-approximately-two-years\">\u0645\u0646 \u0627\u0644\u0645\u0642\u0631\u0631 \u0623\u0646 \u062a\u0628\u062f\u0623 \u0627\u0644\u062a\u062c\u0627\u0631\u0628 \u0639\u0644\u0649 \u0627\u0644\u0628\u0634\u0631 \u062e\u0644\u0627\u0644 \u0639\u0627\u0645\u064a\u0646 \u062a\u0642\u0631\u064a\u0628\u064b\u0627<\/a><\/li><\/ul><\/nav><\/div>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"currently-no-cure-for-dmd\">\u0644\u0627 \u064a\u0648\u062c\u062f \u0639\u0644\u0627\u062c \u0644\u0645\u0631\u0636 \u062f\u0648\u0634\u064a\u0646 \u062d\u0627\u0644\u064a\u064b\u0627<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u0644\u0627 \u064a\u0648\u062c\u062f \u0639\u0644\u0627\u062c \u0645\u0639\u0631\u0648\u0641 \u0644\u0647\u0630\u0627 \u0627\u0644\u0645\u0631\u0636 \u062d\u0627\u0644\u064a\u064b\u0627\u060c \u0648\u0627\u0644\u0623\u062f\u0648\u064a\u0629 \u0648\u0627\u0644\u0639\u0644\u0627\u062c\u0627\u062a \u0627\u0644\u0645\u062a\u0627\u062d\u0629 \u062a\u064f\u0628\u0637\u0626\u0647 \u0628\u0628\u0633\u0627\u0637\u0629. \u0648\u0644\u0623\u0646 \u0627\u0644\u062c\u064a\u0646 \u0627\u0644\u0645\u0639\u064a\u0628 \u064a\u0642\u0639 \u0639\u0644\u0649 \u0627\u0644\u0643\u0631\u0648\u0645\u0648\u0633\u0648\u0645 X\u060c \u0641\u0625\u0646 \u0627\u0644\u0645\u0635\u0627\u0628\u064a\u0646 \u0628\u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a\u060c \u0645\u0648\u0636\u0648\u0639 \u0647\u0630\u0647 \u0627\u0644\u062f\u0631\u0627\u0633\u0629\u060c \u0647\u0645 \u0630\u0643\u0648\u0631 \u062a\u0645\u0627\u0645\u064b\u0627. \u062a\u0628\u062f\u0623 \u0623\u0639\u0631\u0627\u0636 \u0627\u0644\u0645\u0631\u0636 \u0628\u0627\u0644\u0638\u0647\u0648\u0631 \u0639\u0644\u064a\u0647\u0645 \u0641\u064a \u0633\u0646 \u0627\u0644\u0631\u0627\u0628\u0639\u0629\u060c \u0648\u0639\u0627\u062f\u0629\u064b \u0645\u0627 \u064a\u062a\u0648\u0641\u0648\u0646 \u0641\u064a \u0627\u0644\u0639\u0634\u0631\u064a\u0646\u0627\u062a \u0623\u0648 \u0627\u0644\u062b\u0644\u0627\u062b\u064a\u0646\u0627\u062a \u0645\u0646 \u0639\u0645\u0631\u0647\u0645.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0646\u064f\u0634\u0631\u062a \u0646\u062a\u0627\u0626\u062c \u0627\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u062c\u064a\u0646\u064a \u0627\u0644\u062c\u062f\u064a\u062f \u0644\u0645\u0631\u0636 \u062f\u0648\u0634\u064a\u0646 \u0641\u064a \u0645\u062c\u0644\u0629 Nature. <a href=\"https:\/\/www.nature.com\/articles\/s41586-024-07710-8\" target=\"_blank\" rel=\"noreferrer noopener\">\u0627\u0642\u0631\u0623 \u0627\u0644\u0645\u0632\u064a\u062f<\/a> \u2013<\/p>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"who-is-dr-jeffrey-chamberlain\">\u0645\u0646 \u0647\u0648 \u0627\u0644\u062f\u0643\u062a\u0648\u0631 \u062c\u064a\u0641\u0631\u064a \u062a\u0634\u0627\u0645\u0628\u0631\u0644\u064a\u0646\u061f<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u0643\u0631\u0651\u0633 \u0627\u0644\u062f\u0643\u062a\u0648\u0631 \u062c\u064a\u0641\u0631\u064a \u062a\u0634\u0627\u0645\u0628\u0631\u0644\u064a\u0646\u060c \u0627\u0644\u0628\u0627\u062d\u062b \u0627\u0644\u0631\u0626\u064a\u0633\u064a \u0641\u064a \u0627\u0644\u062f\u0631\u0627\u0633\u0629\u060c \u0648\u0647\u0648 \u0639\u0627\u0644\u0645 \u0648\u0631\u0627\u062b\u0629 \u0648\u0623\u062e\u0635\u0627\u0626\u064a \u0623\u0639\u0635\u0627\u0628 \u0641\u064a UW Medicine\u060c \u062d\u064a\u0627\u062a\u0647 \u0627\u0644\u0645\u0647\u0646\u064a\u0629 \u0644\u0644\u0628\u062d\u062b \u0639\u0646 \u0639\u0644\u0627\u062c \u0623\u0648 \u062f\u0648\u0627\u0621 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id=\"what-is-uw-medicines-new-gene-study\">\u0645\u0627 \u0647\u064a \u062f\u0631\u0627\u0633\u0629 \u0627\u0644\u062c\u064a\u0646 \u0627\u0644\u062c\u062f\u064a\u062f UW Medicine\u061f<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u0648\u0628\u0627\u0633\u062a\u062e\u062f\u0627\u0645 \u0645\u062c\u0645\u0648\u0639\u0629 \u0645\u062a\u0646\u0648\u0639\u0629 \u0645\u0646 \u0627\u0644\u0646\u0648\u0627\u0642\u0644 \u0627\u0644\u0641\u064a\u0631\u0648\u0633\u064a\u0629 \u0627\u0644\u0645\u0631\u062a\u0628\u0637\u0629 \u0628\u0627\u0644\u063a\u062f\u0629\u060c \u0623\u0648 AAVs - \u0648\u0647\u064a \u0639\u0628\u0627\u0631\u0629 \u0639\u0646 \u0645\u0643\u0648\u0643\u0627\u062a \u0635\u063a\u064a\u0631\u0629 \u064a\u062a\u0645 \u0625\u0646\u062a\u0627\u062c\u0647\u0627 \u0645\u0646 \u0641\u064a\u0631\u0648\u0633 \u064a\u062a\u0645 \u0627\u0633\u062a\u062e\u062f\u0627\u0645\u0647\u0627 \u0644\u0646\u0642\u0644 \u0627\u0644\u0639\u0644\u0627\u062c\u0627\u062a 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\u0648\u0627\u062d\u062f\u060c \u0648\u0627\u0644\u0630\u064a \u064a\u0623\u062e\u0630 \u0623\u062c\u0632\u0627\u0621 \u0645\u0646 \u0627\u0644\u0628\u0631\u0648\u062a\u064a\u0646 \u0627\u0644\u0639\u0644\u0627\u062c\u064a \u0645\u0646 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0648\u064a\u0636\u0645\u0646 \u0627\u0644\u062a\u0639\u0644\u064a\u0645\u0627\u062a \u0644\u0628\u062f\u0621 \u0648\u0636\u0639 \u0627\u0644\u0625\u0635\u0644\u0627\u062d \u0627\u0644\u062c\u064a\u0646\u064a \u0627\u0644\u0645\u0637\u0644\u0648\u0628 \u0645\u0639\u064b\u0627 \u062f\u0627\u062e\u0644 \u0627\u0644\u062c\u0633\u0645.<\/strong><\/p>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"human-trials-should-begin-in-approximately-two-years\">\u0645\u0646 \u0627\u0644\u0645\u0642\u0631\u0631 \u0623\u0646 \u062a\u0628\u062f\u0623 \u0627\u0644\u062a\u062c\u0627\u0631\u0628 \u0639\u0644\u0649 \u0627\u0644\u0628\u0634\u0631 \u062e\u0644\u0627\u0644 \u0639\u0627\u0645\u064a\u0646 \u062a\u0642\u0631\u064a\u0628\u064b\u0627<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u0648\u062a\u064f\u0639\u062f \u0627\u0644\u062a\u062c\u0627\u0631\u0628 \u0627\u0644\u0628\u0634\u0631\u064a\u0629 \u0647\u064a \u0627\u0644\u0645\u0631\u062d\u0644\u0629 \u0627\u0644\u062a\u0627\u0644\u064a\u0629 \u0645\u0646 \u0627\u0644\u0639\u0644\u0627\u062c\u060c \u0648\u0645\u0646 \u0627\u0644\u0645\u0642\u0631\u0631 \u0623\u0646 \u062a\u0628\u062f\u0623 \u062e\u0644\u0627\u0644 \u062d\u0648\u0627\u0644\u064a \u0639\u0627\u0645\u064a\u0646\u060c \u0648\u0641\u0642\u064b\u0627 \u0644\u062a\u0634\u0627\u0645\u0628\u0631\u0644\u064a\u0646.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0644\u0642\u062f \u0639\u0627\u0644\u062c \u0647\u0630\u0627 \u0627\u0644\u0646\u0647\u062c \u062c\u0632\u0621\u064b\u0627 \u0643\u0628\u064a\u0631\u064b\u0627 \u0645\u0646 \u0627\u0644\u0623\u0645\u0631\u0627\u0636 \u0627\u0644\u0645\u0631\u062a\u0628\u0637\u0629 \u0628\u0627\u0644\u0636\u0645\u0648\u0631 \u0641\u064a \u0627\u0644\u0645\u062e\u062a\u0628\u0631\u060c \u0628\u0627\u0644\u0625\u0636\u0627\u0641\u0629 \u0625\u0644\u0649 \u0625\u064a\u0642\u0627\u0641 \u062a\u0641\u0627\u0642\u0645 \u0627\u0644\u0645\u0631\u0636. \u0648\u064a\u0623\u0645\u0644 \u062a\u0634\u0627\u0645\u0628\u0631\u0644\u064a\u0646 \u0648\u062a\u0627\u0633\u0641\u0627\u0648\u062a \u0623\u0646 \u064a\u064f\u0633\u0647\u0645 \u0647\u0630\u0627 \u0627\u0644\u0646\u0647\u062c \u0641\u064a \u0646\u0647\u0627\u064a\u0629 \u0627\u0644\u0645\u0637\u0627\u0641 \u0641\u064a \u0639\u0643\u0633 \u0645\u0633\u0627\u0631 \u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0648\u0627\u0633\u062a\u0639\u0627\u062f\u0629 \u0635\u062d\u0629 \u0627\u0644\u0623\u0646\u0633\u062c\u0629 \u0627\u0644\u0639\u0636\u0644\u064a\u0629 \u0627\u0644\u0637\u0628\u064a\u0639\u064a\u0629.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0648\u0628\u062d\u0633\u0628 \u062a\u0634\u0627\u0645\u0628\u0631\u0644\u064a\u0646\u060c \u0641\u0625\u0646 \u0627\u0644\u0637\u0631\u064a\u0642\u0629 \u0627\u0644\u0623\u062d\u062f\u062b \u062a\u0633\u062a\u062e\u062f\u0645 \u0623\u064a\u0636\u064b\u0627 \u0646\u0648\u0639\u064b\u0627 \u062c\u062f\u064a\u062f\u064b\u0627 \u0645\u0646 \u0646\u0627\u0642\u0644\u0627\u062a AAV \u064a\u0633\u0645\u062d \u0628\u0627\u0633\u062a\u062e\u062f\u0627\u0645 \u062c\u0631\u0639\u0627\u062a \u0623\u0642\u0644\u060c \u0645\u0645\u0627 \u064a\u0642\u0644\u0644 \u0623\u0648 \u064a\u0632\u064a\u0644 \u0639\u062f\u062f\u064b\u0627 \u0645\u0646 \u0627\u0644\u0639\u0648\u0627\u0642\u0628 \u0627\u0644\u0633\u0644\u0628\u064a\u0629 \u0644\u0644\u0637\u0631\u0642 \u0627\u0644\u0633\u0627\u0628\u0642\u0629.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u064a\u062a\u0639\u0644\u0645 \u0623\u0643\u062b\u0631: <a href=\"https:\/\/dmdwarrior.com\/ar\/new-gene-therapies-for-duchenne-muscular-dystrophy\/\">\u0639\u0644\u0627\u062c\u0627\u062a \u062c\u064a\u0646\u064a\u0629 \u062c\u062f\u064a\u062f\u0629 \u0645\u062d\u062a\u0645\u0644\u0629 \u0644\u0645\u0631\u0636 \u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u062f\u0648\u0634\u064a\u0646<\/a><\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><\/p>","protected":false},"excerpt":{"rendered":"<p>For those who suffer from Duchenne muscular dystrophy (DMD), a novel gene therapy holds promise for both stopping muscle loss and maybe restoring the damaged muscle in the future. The next step for the treatment will be human trials, which are expected to begin in about two years, UW Medicine said. The goal of the [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":4158,"comment_status":"open","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[27],"tags":[61,396],"class_list":["post-4151","post","type-post","status-publish","format-standard","has-post-thumbnail","category-research","tag-gene-therapy","tag-uw-medicine"],"_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/posts\/4151","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/comments?post=4151"}],"version-history":[{"count":0,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/posts\/4151\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/media\/4158"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/media?parent=4151"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/categories?post=4151"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/tags?post=4151"}],"curies":[{"name":"\u0648\u0648\u0631\u062f\u0628\u0631\u064a\u0633","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}