{"id":4132,"date":"2025-07-16T18:57:40","date_gmt":"2025-07-16T15:57:40","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=4132"},"modified":"2025-07-16T18:57:41","modified_gmt":"2025-07-16T15:57:41","slug":"precision-biosciences-highlights-new-preclinical-data-pbgene-dmd","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/ar\/precision-biosciences-highlights-new-preclinical-data-pbgene-dmd\/","title":{"rendered":"Precision BioSciences \u064a\u0633\u0644\u0637 \u0627\u0644\u0636\u0648\u0621 \u0639\u0644\u0649 \u0628\u064a\u0627\u0646\u0627\u062a \u0645\u0627 \u0642\u0628\u0644 \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629 \u0627\u0644\u062c\u062f\u064a\u062f\u0629 \u0644\u0640 PBGENE-DMD \u0644\u0639\u0644\u0627\u062c \u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u062f\u0648\u0634\u064a\u0646"},"content":{"rendered":"<p class=\"wp-block-paragraph\">\u0623\u0639\u0644\u0646\u062a \u0627\u0644\u064a\u0648\u0645 \u0634\u0631\u0643\u0629 Precision BioSciences\u060c \u0648\u0647\u064a \u0634\u0631\u0643\u0629 \u062a\u062d\u0631\u064a\u0631 \u0627\u0644\u062c\u064a\u0646\u0627\u062a \u0641\u064a \u0627\u0644\u0645\u0631\u062d\u0644\u0629 \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629 \u0648\u0627\u0644\u062a\u064a \u062a\u0633\u062a\u062e\u062f\u0645 \u0645\u0646\u0635\u0629 ARCUS\u00ae \u0627\u0644\u062c\u062f\u064a\u062f\u0629 \u0627\u0644\u062e\u0627\u0635\u0629 \u0628\u0647\u0627 \u0644\u062a\u0637\u0648\u064a\u0631 \u0639\u0644\u0627\u062c\u0627\u062a \u062a\u062d\u0631\u064a\u0631 \u0627\u0644\u062c\u064a\u0646\u0627\u062a \u0641\u064a \u0627\u0644\u062c\u0633\u0645 \u0627\u0644\u062d\u064a \u0644\u0644\u0623\u0645\u0631\u0627\u0636 \u0630\u0627\u062a \u0627\u0644\u0627\u062d\u062a\u064a\u0627\u062c\u0627\u062a \u063a\u064a\u0631 \u0627\u0644\u0645\u0644\u0628\u0627\u0629 \u0627\u0644\u0639\u0627\u0644\u064a\u0629\u060c \u0639\u0646 \u0628\u064a\u0627\u0646\u0627\u062a \u0633\u0631\u064a\u0631\u064a\u0629 \u0625\u0636\u0627\u0641\u064a\u0629 \u0645\u062d\u062f\u062b\u0629 \u062a\u0624\u0643\u062f \u0628\u0634\u0643\u0644 \u0623\u0643\u0628\u0631 \u0627\u0644\u0623\u0633\u0627\u0633 \u0627\u0644\u0639\u0644\u0645\u064a \u0627\u0644\u062f\u0627\u0639\u0645 \u0644\u0644\u062a\u0637\u0648\u064a\u0631 \u0627\u0644\u0633\u0631\u064a\u0639 \u0644\u0640 PBGENE-DMD\u060c \u0648\u0647\u0648 \u0623\u0648\u0644 \u0646\u0647\u062c \u0644\u062a\u062d\u0631\u064a\u0631 \u0627\u0644\u062c\u064a\u0646\u0627\u062a \u0641\u064a \u0627\u0644\u062c\u0633\u0645 \u0627\u0644\u062d\u064a \u0645\u0646 \u0627\u0644\u0634\u0631\u0643\u0629 \u0644\u0645\u0631\u0636 \u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u062f\u0648\u0634\u064a\u0646 (DMD)\u060c \u0646\u062d\u0648 \u0623\u0648\u0644 \u062a\u062d\u0642\u064a\u0642 \u0633\u0631\u064a\u0631\u064a \u0628\u0634\u0631\u064a.<\/p>\n\n\n\n<div class=\"wp-block-rank-math-toc-block\" id=\"rank-math-toc\"><h2>\u062c\u062f\u0648\u0644 \u0627\u0644\u0645\u062d\u062a\u0648\u064a\u0627\u062a<\/h2><nav><ul><li><a href=\"#new-preclinical-data-for-pbgene-dmd\">\u0628\u064a\u0627\u0646\u0627\u062a \u0645\u0627 \u0642\u0628\u0644 \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629 \u0627\u0644\u062c\u062f\u064a\u062f\u0629 \u0644\u0640 PBGENE-DMD<\/a><\/li><li><a href=\"#pbgene-dmd-is-the-first-in-vivo-gene-editing-program\">PBGENE-DMD \u0647\u0648 \u0623\u0648\u0644 \u0628\u0631\u0646\u0627\u0645\u062c \u0644\u062a\u062d\u0631\u064a\u0631 \u0627\u0644\u062c\u064a\u0646\u0627\u062a \u0641\u064a \u0627\u0644\u062c\u0633\u0645 \u0627\u0644\u062d\u064a<\/a><\/li><li><a href=\"#pbgene-dmd-between-exons-45-55\">PBGENE-DMD: \u0628\u064a\u0646 \u0627\u0644\u0625\u0643\u0633\u0648\u0646\u0627\u062a 45-55<\/a><\/li><li><a href=\"#what-is-pbgene-dmd\">\u0645\u0627 \u0647\u0648 PBGENE-DMD\u061f<\/a><\/li><\/ul><\/nav><\/div>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"new-preclinical-data-for-pbgene-dmd\">\u0628\u064a\u0627\u0646\u0627\u062a \u0645\u0627 \u0642\u0628\u0644 \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629 \u0627\u0644\u062c\u062f\u064a\u062f\u0629 \u0644\u0640 PBGENE-DMD<\/h2>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u062a\u064f\u0638\u0647\u0631 \u0627\u0644\u0628\u064a\u0627\u0646\u0627\u062a \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629 \u0627\u0644\u0623\u0648\u0644\u064a\u0629 \u0627\u0644\u062c\u062f\u064a\u062f\u0629 \u0644\u0644\u0645\u0631\u0634\u062d \u0627\u0644\u0633\u0631\u064a\u0631\u064a \u0627\u0644\u0646\u0647\u0627\u0626\u064a PBGENE-DMD \u0632\u064a\u0627\u062f\u0629 \u0641\u064a \u0627\u0644\u062e\u0644\u0627\u064a\u0627 \u0627\u0644\u0639\u0636\u0644\u064a\u0629 \u0627\u0644\u0625\u064a\u062c\u0627\u0628\u064a\u0629 \u0644\u0644\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0639\u0628\u0631 \u0623\u0646\u0648\u0627\u0639 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0627\u0644\u0631\u0626\u064a\u0633\u064a\u0629\u060c \u0648\u0627\u0644\u062a\u064a \u0642\u062f \u062a\u0643\u0648\u0646 \u0645\u062f\u0641\u0648\u0639\u0629 \u0628\u062a\u062d\u0631\u064a\u0631 \u0627\u0644\u062e\u0644\u0627\u064a\u0627 \u0627\u0644\u0642\u0645\u0631\u064a\u0629 \u0644\u0644\u0639\u0636\u0644\u0627\u062a -<\/li>\n<\/ul>\n\n\n\n<ul class=\"wp-block-list\">\n<li>PBGENE-DMD \u0647\u0648 \u0646\u0647\u062c \u062a\u062d\u0631\u064a\u0631 \u0627\u0644\u062c\u064a\u0646\u0627\u062a \u0627\u0644\u0623\u0648\u0644 \u0645\u0646 \u0646\u0648\u0639\u0647 \u0641\u064a \u0627\u0644\u062c\u0633\u0645 \u0627\u0644\u062d\u064a \u0644\u0645\u0627 \u064a\u0635\u0644 \u0625\u0644\u0649 60% \u0645\u0646 \u0645\u0631\u0636\u0649 \u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a\u060c \u0648\u062e\u0627\u0635\u0629 \u0623\u0648\u0644\u0626\u0643 \u0627\u0644\u0645\u062a\u0623\u062b\u0631\u064a\u0646 \u0628\u0637\u0641\u0631\u0627\u062a \u0627\u0644\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0641\u064a \u0645\u0646\u0637\u0642\u0629 &quot;\u0627\u0644\u0646\u0642\u0637\u0629 \u0627\u0644\u0633\u0627\u062e\u0646\u0629&quot; \u0628\u064a\u0646 \u0627\u0644\u0625\u0643\u0633\u0648\u0646\u0627\u062a 45-55 -<\/li>\n<\/ul>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u0627\u0633\u062a\u0647\u062f\u0627\u0641 \u062f\u0642\u064a\u0642 \u0644\u062a\u0642\u062f\u064a\u0645 \u062f\u0648\u0627\u0621 \u062c\u062f\u064a\u062f \u0642\u064a\u062f \u0627\u0644\u0628\u062d\u062b (IND) \u0648\/\u0623\u0648 \u0637\u0644\u0628 \u062a\u062c\u0631\u0628\u0629 \u0633\u0631\u064a\u0631\u064a\u0629 (CTA) \u0644\u0640 PBGENE-DMD \u0641\u064a \u0639\u0627\u0645 2025 \u0645\u0639 \u062a\u0648\u0642\u0639 \u0627\u0644\u0628\u064a\u0627\u0646\u0627\u062a \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629 \u0641\u064a \u0639\u0627\u0645 2026 -<\/li>\n<\/ul>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"pbgene-dmd-is-the-first-in-vivo-gene-editing-program\">PBGENE-DMD \u0647\u0648 \u0623\u0648\u0644 \u0628\u0631\u0646\u0627\u0645\u062c \u0644\u062a\u062d\u0631\u064a\u0631 \u0627\u0644\u062c\u064a\u0646\u0627\u062a \u0641\u064a \u0627\u0644\u062c\u0633\u0645 \u0627\u0644\u062d\u064a<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\"><br>&quot;\u0641\u064a \u062f\u0631\u0627\u0633\u0629 \u0637\u0648\u064a\u0644\u0629 \u0627\u0644\u0623\u0645\u062f \u062d\u0648\u0644 \u0627\u0644\u0645\u062a\u0627\u0646\u0629 \u0641\u064a \u0646\u0645\u0648\u0630\u062c \u0641\u0623\u0631 \u0645\u0635\u0627\u0628 \u0628\u0645\u0631\u0636 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a\u060c \u0644\u0627\u062d\u0638\u0646\u0627 \u0632\u064a\u0627\u062f\u0629 \u062a\u0635\u0644 \u0625\u0644\u0649 \u062b\u0644\u0627\u062b\u0629 \u0623\u0636\u0639\u0627\u0641 \u0641\u064a \u0627\u0644\u062e\u0644\u0627\u064a\u0627 \u0627\u0644\u0639\u0636\u0644\u064a\u0629 \u0627\u0644\u0625\u064a\u062c\u0627\u0628\u064a\u0629 \u0644\u0644\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0628\u064a\u0646 \u062b\u0644\u0627\u062b\u0629 \u0648\u062a\u0633\u0639\u0629 \u0623\u0634\u0647\u0631 \u0641\u064a \u0627\u0644\u0639\u0636\u0644\u0629 \u0627\u0644\u0631\u0628\u0627\u0639\u064a\u0629 \u0627\u0644\u0631\u0624\u0648\u0633\u060c \u0648\u0639\u0636\u0644\u0629 \u0627\u0644\u0633\u0627\u0642\u060c \u0648\u0627\u0644\u0642\u0644\u0628\u060c \u0648\u0627\u0644\u062d\u062c\u0627\u0628 \u0627\u0644\u062d\u0627\u062c\u0632. <strong>\u0642\u0627\u0644\u062a \u0627\u0644\u062f\u0643\u062a\u0648\u0631\u0629 \u0643\u0627\u0633\u064a \u062c\u0648\u0631\u0633\u0648\u062a\u0634\u060c \u0643\u0628\u064a\u0631\u0629 \u0627\u0644\u0645\u0633\u0624\u0648\u0644\u064a\u0646 \u0627\u0644\u0639\u0644\u0645\u064a\u064a\u0646 \u0641\u064a Precision BioSciences: &quot;\u0641\u064a \u0639\u0636\u0644\u0629 \u0627\u0644\u0633\u0627\u0642\u060c \u0643\u0627\u0646 \u0645\u0627 \u064a\u0635\u0644 \u0625\u0644\u0649 85% \u0645\u0646 \u0627\u0644\u062e\u0644\u0627\u064a\u0627 \u0625\u064a\u062c\u0627\u0628\u064a\u0629 \u0644\u0644\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646&quot;.<\/strong> \u062a\u0639\u062a\u0645\u062f \u0647\u0630\u0647 \u0627\u0644\u0628\u064a\u0627\u0646\u0627\u062a \u0627\u0644\u062c\u062f\u064a\u062f\u0629 \u0639\u0644\u0649 \u0627\u0644\u0628\u064a\u0627\u0646\u0627\u062a \u0645\u0627 \u0642\u0628\u0644 \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629 \u0627\u0644\u062a\u064a \u0639\u064f\u0631\u0636\u062a \u0641\u064a \u0645\u0624\u062a\u0645\u0631 ASGCT \u0641\u064a \u0645\u0627\u064a\u0648 2025\u060c \u0648\u0627\u0644\u062a\u064a \u062a\u064f\u062b\u0628\u062a \u0623\u0646 \u0639\u0644\u0627\u062c PBGENE-DMD \u0642\u062f \u0623\u062f\u0649 \u0625\u0644\u0649 \u062a\u062d\u0633\u0646 \u0645\u0644\u062d\u0648\u0638 \u0648\u0645\u0633\u062a\u062f\u0627\u0645 \u0641\u064a \u0623\u0642\u0635\u0649 \u0642\u0648\u0629 \u0646\u0627\u062a\u062c\u0629 \u0641\u064a \u0646\u0641\u0633 \u0627\u0644\u0641\u062a\u0631\u062a\u064a\u0646 \u0627\u0644\u0632\u0645\u0646\u064a\u062a\u064a\u0646 (\u062b\u0644\u0627\u062b\u0629 \u0648\u062a\u0633\u0639\u0629 \u0623\u0634\u0647\u0631). \u0647\u0630\u0647 \u0627\u0644\u0632\u064a\u0627\u062f\u0629 \u0627\u0644\u0643\u0628\u064a\u0631\u0629 \u0641\u064a \u0627\u0644\u062e\u0644\u0627\u064a\u0627 \u0627\u0644\u0625\u064a\u062c\u0627\u0628\u064a\u0629 \u0644\u0644\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646\u060c \u0625\u0644\u0649 \u062c\u0627\u0646\u0628 \u0632\u064a\u0627\u062f\u0629 \u0628\u0631\u0648\u062a\u064a\u0646 \u0627\u0644\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0627\u0644\u0645\u064f\u0643\u062a\u0634\u0641 \u0641\u064a \u0627\u0644\u0623\u0646\u0633\u062c\u0629\u060c \u062a\u064f\u0624\u0643\u062f \u0635\u062d\u0629 \u062a\u062d\u0633\u0646 \u0648\u0638\u064a\u0641\u0629 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0627\u0644\u0630\u064a \u0644\u0648\u062d\u0638 \u0628\u0645\u0631\u0648\u0631 \u0627\u0644\u0648\u0642\u062a\u060c \u0648\u0627\u0644\u0630\u064a \u0642\u062f \u064a\u064f\u0639\u0632\u0649 \u0625\u0644\u0649 \u0627\u0644\u062e\u0644\u0627\u064a\u0627 \u0627\u0644\u0633\u0627\u062a\u0644\u064a\u0629 \u0627\u0644\u0645\u064f\u062d\u0631\u0631\u0629\u060c \u0648\u0627\u0644\u062a\u064a \u0644\u0648\u062d\u0638\u062a \u0623\u064a\u0636\u064b\u0627 \u0641\u064a \u0647\u0630\u0647 \u0627\u0644\u062f\u0631\u0627\u0633\u0629. \u0646\u0639\u062a\u0642\u062f \u0623\u0646 \u0647\u0630\u0647 \u0627\u0644\u0646\u062a\u0627\u0626\u062c \u062a\u064f\u0638\u0647\u0631 \u0627\u0644\u0625\u0645\u0643\u0627\u0646\u0627\u062a \u0627\u0644\u0641\u0631\u064a\u062f\u0629 \u0644\u0646\u0647\u062c \u062a\u062d\u0631\u064a\u0631 \u062c\u064a\u0646 PBGENE-DMD \u0641\u064a \u062a\u062d\u0642\u064a\u0642 \u0641\u0627\u0626\u062f\u0629 \u0648\u0638\u064a\u0641\u064a\u0629 \u0645\u0633\u062a\u062f\u0627\u0645\u0629 \u062f\u0648\u0646 \u0627\u0644\u062d\u0627\u062c\u0629 \u0625\u0644\u0649 \u0627\u0633\u062a\u0645\u0631\u0627\u0631\u064a\u0629 AAV\u060c \u0648\u0647\u0648 \u0627\u0644\u0634\u0631\u0637 \u0627\u0644\u0645\u0637\u0644\u0648\u0628 \u0644\u0646\u0647\u062c microdystrophin. \u0646\u062a\u0637\u0644\u0639 \u0625\u0644\u0649 \u0639\u0631\u0636 \u0645\u062c\u0645\u0648\u0639\u0629 \u0627\u0644\u0628\u064a\u0627\u0646\u0627\u062a \u0627\u0644\u0643\u0627\u0645\u0644\u0629 \u0641\u064a \u0645\u0624\u062a\u0645\u0631 \u0639\u0644\u0645\u064a \u0645\u0633\u062a\u0642\u0628\u0644\u064a. \u0648\u0646\u0638\u0631\u064b\u0627 \u0644\u062a\u0648\u0627\u0641\u0631 \u0627\u0644\u0623\u062f\u0644\u0629 \u0645\u0627 \u0642\u0628\u0644 \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629\u060c \u0641\u0625\u0646\u0646\u0627 \u0644\u0627 \u0646\u0632\u0627\u0644 \u0645\u062a\u062d\u0645\u0633\u064a\u0646 \u0648\u0639\u0627\u0632\u0645\u064a\u0646 \u0639\u0644\u0649 \u062a\u0637\u0648\u064a\u0631 \u0647\u0630\u0627 \u0627\u0644\u0628\u0631\u0646\u0627\u0645\u062c \u0646\u062d\u0648 \u0627\u0644\u062a\u0637\u0628\u064a\u0642 \u0627\u0644\u0633\u0631\u064a\u0631\u064a.<\/p>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"pbgene-dmd-between-exons-45-55\">PBGENE-DMD: \u0628\u064a\u0646 \u0627\u0644\u0625\u0643\u0633\u0648\u0646\u0627\u062a 45-55<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u0644\u0627 \u062a\u0648\u062c\u062f \u062d\u0627\u0644\u064a\u064b\u0627 \u0639\u0644\u0627\u062c\u0627\u062a \u0645\u0639\u062a\u0645\u062f\u0629 \u0623\u0648 \u0639\u0644\u0627\u062c\u0627\u062a \u0642\u064a\u062f \u0627\u0644\u062a\u0637\u0648\u064a\u0631 \u062a\u0639\u0645\u0644 \u0639\u0644\u0649 \u062a\u062d\u0633\u064a\u0646 \u0648\u0638\u064a\u0641\u0629 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0628\u0634\u0643\u0644 \u0643\u0628\u064a\u0631 \u0628\u0645\u0631\u0648\u0631 \u0627\u0644\u0648\u0642\u062a \u0644\u062a\u063a\u064a\u064a\u0631 \u0627\u0644\u062a\u0634\u062e\u064a\u0635 \u0637\u0648\u064a\u0644 \u0627\u0644\u0623\u0645\u062f \u0644\u0645\u0631\u0636 \u062f\u0648\u0634\u064a\u0646 \u0628\u0634\u0643\u0644 \u0645\u0641\u064a\u062f. <strong>PBGENE-DMD \u0647\u0648 \u0623\u0648\u0644 \u0628\u0631\u0646\u0627\u0645\u062c \u0644\u062a\u062d\u0631\u064a\u0631 \u0627\u0644\u062c\u064a\u0646\u0627\u062a \u0641\u064a \u0627\u0644\u062c\u0633\u0645 \u0627\u0644\u062d\u064a \u0644\u062f\u064a\u0647 \u0627\u0644\u0642\u062f\u0631\u0629 \u0639\u0644\u0649 \u062a\u062d\u0648\u064a\u0644 \u0646\u0645\u0648\u0630\u062c \u0627\u0644\u0639\u0644\u0627\u062c \u0648\u062a\u062d\u0642\u064a\u0642 \u062a\u062d\u0633\u0646 \u0648\u0638\u064a\u0641\u064a \u062f\u0627\u0626\u0645 \u0644\u0645\u0639\u0638\u0645 \u0627\u0644\u0645\u0631\u0636\u0649\u060c \u062d\u064a\u062b \u0623\u0646 \u0645\u0627 \u064a\u0635\u0644 \u0625\u0644\u0649 60% \u0645\u0646 \u0647\u0624\u0644\u0627\u0621 \u0627\u0644\u0645\u0635\u0627\u0628\u064a\u0646 \u064a\u062d\u0645\u0644\u0648\u0646 \u0637\u0641\u0631\u0627\u062a \u0641\u064a \u0645\u0646\u0637\u0642\u0629 &quot;\u0627\u0644\u0646\u0642\u0637\u0629 \u0627\u0644\u0633\u0627\u062e\u0646\u0629&quot; \u0628\u064a\u0646 \u0627\u0644\u0625\u0643\u0633\u0648\u0646\u0627\u062a 45-55.<\/strong> \u0635\u064f\u0645\u0645 \u0646\u0647\u062c \u0628\u0631\u064a\u0633\u064a\u062c\u0646 \u0644\u062a\u0639\u062f\u064a\u0644 \u062a\u0633\u0644\u0633\u0644 \u0627\u0644\u062d\u0645\u0636 \u0627\u0644\u0646\u0648\u0648\u064a \u0644\u0644\u0645\u0631\u064a\u0636 \u0628\u0634\u0643\u0644 \u062f\u0627\u0626\u0645\u060c \u0645\u0645\u0627 \u064a\u0646\u062a\u062c \u0639\u0646\u0647 \u0628\u0631\u0648\u062a\u064a\u0646 \u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0637\u0628\u064a\u0639\u064a\u060c \u0634\u0628\u0647 \u0643\u0627\u0645\u0644 \u0627\u0644\u0637\u0648\u0644\u060c \u0645\u0639\u0631\u0648\u0641 \u0628\u0641\u0639\u0627\u0644\u064a\u062a\u0647 \u0644\u062f\u0649 \u0627\u0644\u0628\u0634\u0631. \u0648\u062a\u062c\u0631\u064a \u062d\u0627\u0644\u064a\u064b\u0627 \u062f\u0631\u0627\u0633\u0627\u062a \u0627\u0644\u0633\u0645\u0648\u0645 \u0627\u0644\u0646\u0647\u0627\u0626\u064a\u0629 \u0627\u0644\u062a\u064a \u062a\u064f\u0645\u0643\u0651\u0646 \u0645\u0646 IND\u060c \u0648\u0645\u0646 \u0627\u0644\u0645\u0642\u0631\u0631 \u062a\u0642\u062f\u064a\u0645 \u0637\u0644\u0628 IND \u0648\/\u0623\u0648 CTA \u0641\u064a \u0639\u0627\u0645 2025\u060c \u0648\u0645\u0646 \u0627\u0644\u0645\u062a\u0648\u0642\u0639 \u0635\u062f\u0648\u0631 \u0627\u0644\u0628\u064a\u0627\u0646\u0627\u062a \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629 \u0627\u0644\u0623\u0648\u0644\u064a\u0629 \u0641\u064a \u0639\u0627\u0645 2026. \u0648\u062a\u0639\u062a\u0642\u062f \u0627\u0644\u0634\u0631\u0643\u0629 \u0623\u0646 \u0627\u0644\u0633\u064a\u0648\u0644\u0629 \u0627\u0644\u0646\u0642\u062f\u064a\u0629 \u0627\u0644\u062d\u0627\u0644\u064a\u0629 \u0633\u062a\u0643\u0648\u0646 \u0643\u0627\u0641\u064a\u0629 \u0644\u0625\u062a\u0645\u0627\u0645 \u0643\u0644 \u0645\u0646 PBGENE-HBV\u060c \u0648\u0647\u0648 \u0623\u0635\u0644\u0647\u0627 \u0627\u0644\u062d\u0627\u0644\u064a \u0641\u064a \u0627\u0644\u0645\u0631\u062d\u0644\u0629 \u0627\u0644\u0623\u0648\u0644\u0649\u060c \u0648PBGENE-DMD \u0645\u0646 \u062e\u0644\u0627\u0644 \u0627\u0644\u0642\u0631\u0627\u0621\u0627\u062a \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629 \u0644\u0644\u0645\u0631\u062d\u0644\u0629 \u0627\u0644\u0623\u0648\u0644\u0649.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u0627\u0642\u0631\u0623 \u0627\u0644\u0645\u0632\u064a\u062f<\/strong>: <a href=\"https:\/\/dmdwarrior.com\/ar\/precision-biosciences-pbgene-dmd-restores-production-of-nearly-full-length-dystrophin-protein\/\">Precision BioSciences PBGENE-DMD \u064a\u0633\u062a\u0639\u064a\u062f \u0625\u0646\u062a\u0627\u062c \u0628\u0631\u0648\u062a\u064a\u0646 \u0627\u0644\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0643\u0627\u0645\u0644 \u0627\u0644\u0637\u0648\u0644 \u062a\u0642\u0631\u064a\u0628\u064b\u0627<\/a><\/p>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"what-is-pbgene-dmd\">\u0645\u0627 \u0647\u0648 PBGENE-DMD\u061f<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">PBGENE-DMD \u0647\u0648 \u0628\u0631\u0646\u0627\u0645\u062c \u062a\u0637\u0648\u064a\u0631 Precision \u0644\u0639\u0644\u0627\u062c DMD. <strong>\u064a\u0639\u062a\u0645\u062f \u0627\u0644\u0646\u0647\u062c \u0639\u0644\u0649 \u0646\u0648\u0643\u0644\u064a\u0627\u0632\u064a\u0646 \u0645\u062a\u0643\u0627\u0645\u0644\u064a\u0646 \u0645\u0646 \u0646\u0648\u0639 ARCUS \u064a\u062a\u0645 \u062a\u0648\u0635\u064a\u0644\u0647\u0645\u0627 \u0639\u0628\u0631 \u0625\u062f\u0627\u0631\u0629 \u0644\u0645\u0631\u0629 \u0648\u0627\u062d\u062f\u0629 \u0641\u064a AAV \u0648\u0627\u062d\u062f \u0644\u0627\u0633\u062a\u0626\u0635\u0627\u0644 \u0627\u0644\u0625\u0643\u0633\u0648\u0646\u0627\u062a 45-55 \u0645\u0646 \u062c\u064a\u0646 \u0627\u0644\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0628\u0647\u062f\u0641 \u0627\u0633\u062a\u0639\u0627\u062f\u0629 \u0637\u0648\u0644 \u0628\u0631\u0648\u062a\u064a\u0646 \u0627\u0644\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0628\u0627\u0644\u0643\u0627\u0645\u0644 \u062a\u0642\u0631\u064a\u0628\u064b\u0627 \u062f\u0627\u062e\u0644 \u0627\u0644\u062c\u0633\u0645 \u0644\u062a\u062d\u0633\u064a\u0646 \u0627\u0644\u0646\u062a\u0627\u0626\u062c \u0627\u0644\u0648\u0638\u064a\u0641\u064a\u0629.<\/strong> \u064a\u0647\u062f\u0641 PBGENE-DMD \u0625\u0644\u0649 \u0645\u0639\u0627\u0644\u062c\u0629 \u0623\u0643\u062b\u0631 \u0645\u0646 60% \u0645\u0646 \u0645\u0631\u0636\u0649 \u062f\u0648\u0634\u064a\u0646.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0641\u064a \u0627\u0644\u062f\u0631\u0627\u0633\u0627\u062a \u0645\u0627 \u0642\u0628\u0644 \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629\u060c \u0623\u0638\u0647\u0631 \u0628\u0631\u0648\u062a\u064a\u0646 PBGENE-DMD \u0642\u062f\u0631\u062a\u0647 \u0639\u0644\u0649 \u0627\u0633\u062a\u0647\u062f\u0627\u0641 \u0623\u0646\u0648\u0627\u0639 \u0639\u0636\u0644\u064a\u0629 \u0631\u0626\u064a\u0633\u064a\u0629 \u0645\u0631\u062a\u0628\u0637\u0629 \u0628\u062a\u0637\u0648\u0631 \u0645\u0631\u0636 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a\u060c \u0648\u0623\u062d\u062f\u062b \u062a\u062d\u0633\u064a\u0646\u0627\u062a \u0648\u0638\u064a\u0641\u064a\u0629 \u0645\u0644\u062d\u0648\u0638\u0629 \u0648\u062f\u0627\u0626\u0645\u0629 \u0641\u064a \u0646\u0645\u0648\u0630\u062c \u0641\u0623\u0631 \u0645\u0635\u0627\u0628 \u0628\u0645\u0631\u0636 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a. \u0627\u0633\u062a\u0639\u0627\u062f \u0628\u0631\u0648\u062a\u064a\u0646 PBGENE-DMD \u0642\u062f\u0631\u0629 \u0627\u0644\u062c\u0633\u0645 \u0639\u0644\u0649 \u0625\u0646\u062a\u0627\u062c \u0628\u0631\u0648\u062a\u064a\u0646 \u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0648\u0638\u064a\u0641\u064a \u0643\u0627\u0645\u0644 \u062a\u0642\u0631\u064a\u0628\u064b\u0627 \u0641\u064a \u0639\u0636\u0644\u0627\u062a \u0645\u062a\u0639\u062f\u062f\u0629\u060c \u0628\u0645\u0627 \u0641\u064a \u0630\u0644\u0643 \u0623\u0646\u0633\u062c\u0629 \u0627\u0644\u0642\u0644\u0628 \u0648\u0645\u062c\u0645\u0648\u0639\u0627\u062a \u0639\u0636\u0644\u064a\u0629 \u0647\u064a\u0643\u0644\u064a\u0629 \u0631\u0626\u064a\u0633\u064a\u0629 \u0645\u062e\u062a\u0644\u0641\u0629. \u0628\u0627\u0644\u0625\u0636\u0627\u0641\u0629 \u0625\u0644\u0649 \u0630\u0644\u0643\u060c \u0639\u062f\u0651\u0644 \u0628\u0631\u0648\u062a\u064a\u0646 PBGENE-DMD \u0627\u0644\u062e\u0644\u0627\u064a\u0627 \u0627\u0644\u062c\u0630\u0639\u064a\u0629 \u0627\u0644\u0639\u0636\u0644\u064a\u0629 \u0627\u0644\u0633\u0627\u062a\u0644\u064a\u0629\u060c \u0648\u0627\u0644\u062a\u064a \u064a\u064f\u0639\u062a\u0642\u062f \u0623\u0646\u0647\u0627 \u0636\u0631\u0648\u0631\u064a\u0629 \u0644\u062a\u062d\u0642\u064a\u0642 \u0627\u0644\u0645\u062a\u0627\u0646\u0629 \u0639\u0644\u0649 \u0627\u0644\u0645\u062f\u0649 \u0627\u0644\u0637\u0648\u064a\u0644 \u0648\u0627\u0644\u062a\u062d\u0633\u064a\u0646 \u0627\u0644\u0648\u0638\u064a\u0641\u064a \u0627\u0644\u0645\u0633\u062a\u062f\u0627\u0645.<\/p>","protected":false},"excerpt":{"rendered":"<p>Precision BioSciences a clinical stage gene editing company utilizing its novel proprietary ARCUS\u00ae platform to develop in vivo gene editing therapies for diseases with high unmet need, today announced updated additional preclinical data further validating the scientific rationale supporting the rapid development of PBGENE-DMD, the Company\u2019s first-in-class in vivo gene editing approach for Duchenne muscular [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":4134,"comment_status":"open","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[281],"tags":[359,72,314,313],"class_list":["post-4132","post","type-post","status-publish","format-standard","has-post-thumbnail","category-press-releases","tag-full-length-dystrophin","tag-gene-editing","tag-pbgene-dmd","tag-precision-biosciences"],"_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/posts\/4132","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/comments?post=4132"}],"version-history":[{"count":0,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/posts\/4132\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/media\/4134"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/media?parent=4132"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/categories?post=4132"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/tags?post=4132"}],"curies":[{"name":"\u0648\u0648\u0631\u062f\u0628\u0631\u064a\u0633","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}