{"id":4065,"date":"2025-07-10T11:42:12","date_gmt":"2025-07-10T08:42:12","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=4065"},"modified":"2025-07-10T11:43:34","modified_gmt":"2025-07-10T08:43:34","slug":"jcr-pharmaceuticals-proprietary-just-aav-capsids-may-be-used-in-the-development-of-duchenne-cures","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/ar\/jcr-pharmaceuticals-proprietary-just-aav-capsids-may-be-used-in-the-development-of-duchenne-cures\/","title":{"rendered":"\u064a\u0645\u0643\u0646 \u0627\u0633\u062a\u062e\u062f\u0627\u0645 \u0643\u0628\u0633\u0648\u0644\u0627\u062a JCR Pharmaceuticals \u0627\u0644\u0645\u0645\u0644\u0648\u0643\u0629 \u0644\u0640 JUST-AAV \u0641\u064a \u062a\u0637\u0648\u064a\u0631 \u0639\u0644\u0627\u062c\u0627\u062a \u062f\u0648\u0634\u064a\u0646"},"content":{"rendered":"<p class=\"wp-block-paragraph\">Alexion\u060c \u0627\u0644\u0634\u0631\u0643\u0629 \u0627\u0644\u062a\u0627\u0628\u0639\u0629 \u0644\u0634\u0631\u0643\u0629 AstraZeneca \u0627\u0644\u0645\u062a\u062e\u0635\u0635\u0629 \u0641\u064a \u0639\u0644\u0627\u062c \u0627\u0644\u0623\u0645\u0631\u0627\u0636 \u0627\u0644\u0646\u0627\u062f\u0631\u0629\u060c \u062a\u062d\u0635\u0644 \u0639\u0644\u0649 \u062a\u0631\u062e\u064a\u0635 \u0644\u0645\u0631\u0643\u0628\u0627\u062a \u0627\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u062c\u064a\u0646\u064a \u0627\u0644\u0645\u062a\u062e\u0635\u0635\u0629 \u0645\u0646 \u0627\u0644\u0634\u0631\u0643\u0629 \u0627\u0644\u064a\u0627\u0628\u0627\u0646\u064a\u0629 JCR Pharmaceuticals.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u0648\u062a\u0645\u0646\u062d \u0627\u0644\u0635\u0641\u0642\u0629\u060c \u0627\u0644\u062a\u064a \u062a\u0645 \u0627\u0644\u0625\u0639\u0644\u0627\u0646 \u0639\u0646\u0647\u0627 \u0641\u064a 8 \u064a\u0648\u0646\u064a\u0648 2025\u060c \u0634\u0631\u0643\u0629 Alexion \u0625\u0645\u0643\u0627\u0646\u064a\u0629 \u0627\u0644\u0648\u0635\u0648\u0644 \u0625\u0644\u0649 \u0643\u0628\u0633\u0648\u0644\u0627\u062a JUST-AAV \u0645\u0646 JCR \u0644\u0627\u0633\u062a\u062e\u062f\u0627\u0645\u0647\u0627 \u0641\u064a \u0645\u0627 \u064a\u0635\u0644 \u0625\u0644\u0649 \u062e\u0645\u0633\u0629 \u0645\u0646 \u0628\u0631\u0627\u0645\u062c \u0627\u0644\u0623\u062f\u0648\u064a\u0629 \u0627\u0644\u062c\u064a\u0646\u0648\u0645\u064a\u0629 \u0627\u0644\u062e\u0627\u0635\u0629 \u0628\u0634\u0631\u0643\u0629 Alexion.<\/strong> \u0641\u064a \u0627\u0644\u0645\u0642\u0627\u0628\u0644\u060c \u0633\u062a\u062f\u0641\u0639 \u0634\u0631\u0643\u0629 Alexion \u0644\u0634\u0631\u0643\u0629 JCR \u0631\u0633\u0648\u0645\u064b\u0627 \u0645\u0642\u062f\u0645\u0629 \u0644\u0645 \u064a\u064f\u0643\u0634\u0641 \u0639\u0646\u0647\u0627\u060c \u0628\u0627\u0644\u0625\u0636\u0627\u0641\u0629 \u0625\u0644\u0649 \u0645\u0627 \u064a\u0635\u0644 \u0625\u0644\u0649 225 \u0645\u0644\u064a\u0648\u0646 \u062f\u0648\u0644\u0627\u0631 \u0623\u0645\u0631\u064a\u0643\u064a \u0643\u0645\u062f\u0641\u0648\u0639\u0627\u062a \u0645\u0631\u062d\u0644\u064a\u0629 \u062a\u062a\u0639\u0644\u0642 \u0628\u0627\u0644\u0628\u062d\u062b \u0648\u0627\u0644\u062a\u0637\u0648\u064a\u0631\u060c \u0628\u0627\u0644\u0625\u0636\u0627\u0641\u0629 \u0625\u0644\u0649 600 \u0645\u0644\u064a\u0648\u0646 \u062f\u0648\u0644\u0627\u0631 \u0623\u0645\u0631\u064a\u0643\u064a \u0625\u0636\u0627\u0641\u064a\u0629 \u0643\u0645\u062f\u0641\u0648\u0639\u0627\u062a \u0645\u0631\u062d\u0644\u064a\u0629 \u062a\u062a\u0639\u0644\u0642 \u0628\u0627\u0644\u0645\u0628\u064a\u0639\u0627\u062a. \u0643\u0645\u0627 \u0633\u062a\u062d\u0635\u0644 JCR \u0639\u0644\u0649 \u0625\u062a\u0627\u0648\u0627\u062a \u0645\u062a\u062f\u0631\u062c\u0629 \u062a\u062a\u0639\u0644\u0642 \u0628\u0627\u0644\u0645\u0628\u064a\u0639\u0627\u062a\u060c \u062f\u0648\u0646 \u0627\u0644\u0643\u0634\u0641 \u0639\u0646 \u062a\u0641\u0627\u0635\u064a\u0644\u0647\u0627.<\/p>\n\n\n\n<div class=\"wp-block-rank-math-toc-block\" id=\"rank-math-toc\"><h2>\u062c\u062f\u0648\u0644 \u0627\u0644\u0645\u062d\u062a\u0648\u064a\u0627\u062a<\/h2><nav><ul><li><a href=\"#whar-is-just-aav-capsids\">\u0645\u0627 \u0647\u064a \u0643\u0628\u0633\u0648\u0644\u0627\u062a JUST-AAV\u061f<\/a><\/li><li><a href=\"#just-aav-capsids-may-be-used-for-duchenne-cures\">\u064a\u0645\u0643\u0646 \u0627\u0633\u062a\u062e\u062f\u0627\u0645 \u0643\u0628\u0633\u0648\u0644\u0627\u062a JUST-AAV \u0644\u0639\u0644\u0627\u062c \u0645\u0631\u0636 \u062f\u0648\u0634\u064a\u0646<\/a><\/li><li><a href=\"#pre-clinical-trials-of-just-aav-capsids\">\u0627\u0644\u062a\u062c\u0627\u0631\u0628 \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629 \u0627\u0644\u0623\u0648\u0644\u064a\u0629 \u0644\u0643\u0628\u0633\u0648\u0644\u0627\u062a JUST-AAV<\/a><\/li><\/ul><\/nav><\/div>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"whar-is-just-aav-capsids\">\u0645\u0627 \u0647\u064a \u0643\u0628\u0633\u0648\u0644\u0627\u062a JUST-AAV\u061f<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>JUST-AAV \u0647\u064a \u062a\u0642\u0646\u064a\u0629 \u0645\u0646\u0635\u0629 \u062e\u0627\u0635\u0629 \u062a\u0633\u062a\u062e\u062f\u0645 \u0646\u0627\u0642\u0644\u0627\u062a \u0641\u064a\u0631\u0648\u0633 \u0627\u0644\u063a\u062f\u0629 \u0627\u0644\u062f\u0631\u0642\u064a\u0629 \u0627\u0644\u0645\u0639\u062f\u0644\u0629 (AAV).<\/strong><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0648\u062a\u062a\u0636\u0645\u0646 \u0647\u0630\u0647 \u0627\u0644\u062a\u0642\u0646\u064a\u0629 \u0625\u062f\u062e\u0627\u0644 \u0623\u062c\u0633\u0627\u0645 \u0645\u0636\u0627\u062f\u0629 \u0645\u0635\u063a\u0631\u0629 \u0636\u062f \u0645\u0633\u062a\u0642\u0628\u0644\u0627\u062a \u0639\u0644\u0649 \u0623\u0646\u0633\u062c\u0629 \u0623\u0648 \u0623\u0639\u0636\u0627\u0621 \u0645\u062e\u062a\u0627\u0631\u0629 \u0623\u0648 \u062d\u0627\u062c\u0632 \u0627\u0644\u062f\u0645 \u0641\u064a \u0627\u0644\u062f\u0645\u0627\u063a \u0639\u0644\u0649 \u0633\u0637\u062d \u0627\u0644\u063a\u0644\u0627\u0641\u060c \u0645\u0645\u0627 \u064a\u0639\u0632\u0632 \u0627\u0633\u062a\u0647\u062f\u0627\u0641 \u0647\u0630\u0647 \u0627\u0644\u0623\u0646\u0633\u062c\u0629 \u0648\u0627\u0644\u0623\u0639\u0636\u0627\u0621.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u062a\u064f\u0642\u0644\u0644 \u062a\u0639\u062f\u064a\u0644\u0627\u062a \u0627\u0644\u0642\u0641\u064a\u0635\u0629 \u0627\u0644\u0625\u0636\u0627\u0641\u064a\u0629 \u0645\u0646 \u0627\u0644\u062a\u0623\u062b\u064a\u0631\u0627\u062a \u063a\u064a\u0631 \u0627\u0644\u0645\u0642\u0635\u0648\u062f\u0629 \u0648\u062a\u064f\u062d\u0633\u0651\u0646 \u0627\u0644\u0633\u0644\u0627\u0645\u0629. \u0627\u0644\u0627\u0633\u0645 \u0645\u064f\u0634\u062a\u0642 \u0645\u0646 &quot;JCR&quot; (\u0627\u0644\u0647\u062f\u0641 \u0627\u0644\u0646\u0647\u0627\u0626\u064a \u0644\u0644\u0639\u0636\u0648)\u060c \u0648&quot;\u0627\u0644\u062d\u0645\u0627\u064a\u0629 \u0645\u0646 \u0627\u0644\u062a\u0648\u0635\u064a\u0644 \u063a\u064a\u0631 \u0627\u0644\u0645\u0642\u0635\u0648\u062f&quot;\u060c \u0648&quot;\u0627\u0644\u062a\u0643\u0646\u0648\u0644\u0648\u062c\u064a\u0627 \u0627\u0644\u062a\u062d\u0648\u064a\u0644\u064a\u0629&quot;\u060c \u0645\u0645\u0627 \u064a\u0639\u0643\u0633 \u0625\u0645\u0643\u0627\u0646\u0627\u062a\u0647\u0627 \u0641\u064a \u062a\u0637\u0628\u064a\u0642 \u0648\u0627\u0633\u0639 \u0627\u0644\u0646\u0637\u0627\u0642 \u0639\u0644\u0649 \u0623\u0645\u0631\u0627\u0636 \u0645\u064f\u062e\u062a\u0644\u0641\u0629.<\/p>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"just-aav-capsids-may-be-used-for-duchenne-cures\">\u064a\u0645\u0643\u0646 \u0627\u0633\u062a\u062e\u062f\u0627\u0645 \u0643\u0628\u0633\u0648\u0644\u0627\u062a JUST-AAV \u0644\u0639\u0644\u0627\u062c \u0645\u0631\u0636 \u062f\u0648\u0634\u064a\u0646<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u0648\u0644\u0645 \u064a\u062a\u0645 \u062a\u062d\u062f\u064a\u062f \u0623\u064a\u0636\u064b\u0627 \u0627\u0644\u0645\u0624\u0634\u0631\u0627\u062a \u0627\u0644\u062a\u064a \u0642\u062f \u064a\u0633\u062a\u062e\u062f\u0645\u0647\u0627 Alexion \u0644\u0647\u0630\u0647 \u0627\u0644\u0643\u0628\u0633\u0648\u0644\u0627\u062a. \u0625\u0646 \u062e\u0637 \u0623\u0646\u0627\u0628\u064a\u0628 \u0627\u0644\u0623\u0645\u0631\u0627\u0636 \u0627\u0644\u0646\u0627\u062f\u0631\u0629 AstraZeneca \u0645\u0644\u064a\u0621 \u0628\u0627\u0644\u0623\u0635\u0648\u0644 \u0641\u064a \u0627\u0644\u0645\u0631\u062d\u0644\u0629 \u0627\u0644\u0645\u062a\u0648\u0633\u0637\u0629 \u0625\u0644\u0649 \u0627\u0644\u0645\u062a\u0623\u062e\u0631\u0629 \u0641\u064a \u0623\u0645\u0631\u0627\u0636 \u0645\u062b\u0644 \u0627\u0644\u0648\u0647\u0646 \u0627\u0644\u0639\u0636\u0644\u064a \u0627\u0644\u0648\u0628\u064a\u0644 \u0648\u0627\u0644\u062a\u0647\u0627\u0628 \u0627\u0644\u0643\u0644\u064a\u0629 \u0627\u0644\u0630\u0626\u0628\u064a.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u062a\u0641\u062a\u062e\u0631 \u0634\u0631\u0643\u0629 JCR \u0628\u0623\u0646 \u0643\u0628\u0633\u0648\u0644\u0627\u062a\u0647\u0627 \u0627\u0644\u062e\u0627\u0635\u0629 JUST-AAV \u062a\u0623\u062a\u064a \u0641\u064a \u0639\u062f\u0629 \u0623\u0646\u0648\u0627\u0639\u060c \u0648\u062a\u0633\u0644\u0637 \u0627\u0644\u0636\u0648\u0621 \u0628\u0634\u0643\u0644 \u062e\u0627\u0635 \u0639\u0644\u0649 \u0627\u0644\u0645\u062a\u063a\u064a\u0631\u0627\u062a &quot;\u0627\u0644\u0645\u062d\u0627\u0641\u0638\u0629 \u0639\u0644\u0649 \u0627\u0644\u0643\u0628\u062f&quot; \u0648\u0627\u0633\u062a\u0647\u062f\u0627\u0641 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0648\u0627\u0633\u062a\u0647\u062f\u0627\u0641 \u0627\u0644\u062f\u0645\u0627\u063a.<\/strong> \u062e\u0636\u0639\u062a \u0625\u0635\u0627\u0628\u0627\u062a \u0627\u0644\u0643\u0628\u062f \u0627\u0644\u0646\u0627\u062c\u0645\u0629 \u0639\u0646 \u0627\u0644\u0639\u0644\u0627\u062c\u0627\u062a \u0627\u0644\u062c\u064a\u0646\u064a\u0629 \u0644\u062a\u062f\u0642\u064a\u0642 \u0645\u0643\u062b\u0641 \u0641\u064a \u0627\u0644\u0622\u0648\u0646\u0629 \u0627\u0644\u0623\u062e\u064a\u0631\u0629\u060c \u0648\u0630\u0644\u0643 \u0628\u0639\u062f \u0648\u0641\u0627\u0629 \u0645\u0631\u064a\u0636\u064a\u0646 \u0646\u062a\u064a\u062c\u0629 \u0625\u0635\u0627\u0628\u0629 \u0627\u0644\u0643\u0628\u062f \u0628\u0639\u062f \u062a\u0644\u0642\u064a\u0647\u0645\u0627 \u0627\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u062c\u064a\u0646\u064a Elevidys \u0645\u0646 \u0634\u0631\u0643\u0629 Sarepta \u0644\u0645\u0631\u0636 \u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u062f\u0648\u0634\u064a\u0646\u060c \u0641\u064a \u0648\u0642\u062a \u0633\u0627\u0628\u0642 \u0645\u0646 \u0647\u0630\u0627 \u0627\u0644\u0639\u0627\u0645. - \u0627\u0642\u0631\u0623 \u0627\u0644\u0645\u0632\u064a\u062f: <a href=\"https:\/\/dmdwarrior.com\/ar\/sarepta-reported-elevidys-gene-therapy-for-duchenne-muscular-dystrophy-will-not-be-used-in-non-ambulatory-patients\/\">\u0644\u0646 \u064a\u062a\u0645 \u0627\u0633\u062a\u062e\u062f\u0627\u0645 \u0627\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u062c\u064a\u0646\u064a Elevidys \u0641\u064a \u0627\u0644\u0645\u0631\u0636\u0649 \u063a\u064a\u0631 \u0627\u0644\u0642\u0627\u062f\u0631\u064a\u0646 \u0639\u0644\u0649 \u0627\u0644\u0645\u0634\u064a<\/a> \u2013<\/p>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"pre-clinical-trials-of-just-aav-capsids\">\u0627\u0644\u062a\u062c\u0627\u0631\u0628 \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629 \u0627\u0644\u0623\u0648\u0644\u064a\u0629 \u0644\u0643\u0628\u0633\u0648\u0644\u0627\u062a JUST-AAV<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u0646\u062c\u062d \u0627\u0644\u0628\u0627\u062d\u062b\u0648\u0646 \u0641\u064a \u0625\u0646\u0634\u0627\u0621 \u0646\u0627\u0642\u0644 \u0641\u064a\u0631\u0648\u0633 \u0627\u0644\u063a\u062f\u0629 \u0627\u0644\u062f\u0631\u0642\u064a\u0629 \u0627\u0644\u0645\u0631\u062a\u0628\u0637 \u0628\u0627\u0644\u062f\u0645\u0627\u063a (JUST-AAV) \u0639\u0646 \u0637\u0631\u064a\u0642 \u062f\u0645\u062c \u062c\u0633\u0645 \u0645\u0636\u0627\u062f \u0645\u0635\u063a\u0631 \u064a\u0631\u062a\u0628\u0637 \u0628\u0645\u0633\u062a\u0642\u0628\u0644 \u0627\u0644\u062a\u0631\u0627\u0646\u0633\u0641\u064a\u0631\u064a\u0646 \u0641\u064a \u063a\u0644\u0627\u0641 \u0641\u064a\u0631\u0648\u0633 \u0627\u0644\u063a\u062f\u0629 \u0627\u0644\u062f\u0631\u0642\u064a\u0629 \u0627\u0644\u0645\u0631\u062a\u0628\u0637 \u0628\u0627\u0644\u062f\u0645\u0627\u063a. \u0639\u0644\u0627\u0648\u0629 \u0639\u0644\u0649 \u0630\u0644\u0643\u060c \u0623\u062f\u062a \u0627\u0644\u062a\u0639\u062f\u064a\u0644\u0627\u062a \u0627\u0644\u0641\u0631\u064a\u062f\u0629 \u0639\u0644\u0649 \u062a\u0633\u0644\u0633\u0644 \u063a\u0644\u0627\u0641 \u0641\u064a\u0631\u0648\u0633 \u0627\u0644\u063a\u062f\u0629 \u0627\u0644\u062f\u0631\u0642\u064a\u0629 \u0627\u0644\u0645\u0631\u062a\u0628\u0637 \u0628\u0627\u0644\u062f\u0645\u0627\u063a \u0625\u0644\u0649 \u062a\u0642\u0644\u064a\u0644 \u062a\u0631\u0627\u0643\u0645 \u0646\u0627\u0642\u0644 \u0641\u064a\u0631\u0648\u0633 \u0627\u0644\u063a\u062f\u0629 \u0627\u0644\u062f\u0631\u0642\u064a\u0629 \u0627\u0644\u0645\u0631\u062a\u0628\u0637 \u0628\u0627\u0644\u062f\u0645\u0627\u063a \u0628\u0634\u0643\u0644 \u0645\u0644\u062d\u0648\u0638 \u0641\u064a \u0627\u0644\u0643\u0628\u062f\u060c \u0648\u0647\u0648 \u0645\u0635\u062f\u0631 \u0645\u0639\u0631\u0648\u0641 \u0644\u0644\u0622\u062b\u0627\u0631 \u0627\u0644\u062c\u0627\u0646\u0628\u064a\u0629.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0641\u064a \u062f\u0631\u0627\u0633\u0627\u062a \u0623\u062c\u0631\u064a\u062a \u0639\u0644\u0649 \u0627\u0644\u0641\u0626\u0631\u0627\u0646\u060c \u062d\u0642\u0642 \u0646\u0627\u0642\u0644 JUST-AAV \u062a\u0639\u0628\u064a\u0631\u064b\u0627 \u0623\u0639\u0644\u0649 \u0628\u0645\u0642\u062f\u0627\u0631 77 \u0636\u0639\u0641\u064b\u0627 \u0639\u0646 \u0627\u0644\u0628\u0631\u0648\u062a\u064a\u0646 \u0627\u0644\u0641\u0644\u0648\u0631\u064a \u0627\u0644\u0623\u062e\u0636\u0631 (GFP) \u0641\u064a \u0627\u0644\u062f\u0645\u0627\u063a \u0645\u0642\u0627\u0631\u0646\u0629\u064b \u0628\u0646\u0627\u0642\u0644 AAV9\u060c \u0645\u0639 \u062a\u0642\u0644\u064a\u0644 \u0627\u0644\u062a\u0648\u062c\u0647 \u0646\u062d\u0648 \u0627\u0644\u0643\u0628\u062f \u0628\u0648\u0627\u0633\u0637\u0629 \u0646\u0627\u0642\u0644 99%. \u0648\u0644\u062a\u0639\u0632\u064a\u0632 \u0627\u0633\u062a\u0647\u062f\u0627\u0641 \u0627\u0644\u062f\u0645\u0627\u063a \u0648\u0646\u0641\u0627\u0630\u064a\u0629 \u0627\u0644\u062d\u0627\u062c\u0632 \u0627\u0644\u062f\u0645\u0648\u064a \u0627\u0644\u062f\u0645\u0627\u063a\u064a\u060c \u0623\u062f\u0631\u062c \u0627\u0644\u0628\u0627\u062d\u062b\u0648\u0646 \u062c\u0632\u064a\u0626\u0627\u062a \u0625\u0636\u0627\u0641\u064a\u0629 \u062a\u0631\u062a\u0628\u0637 \u0628\u0645\u0633\u062a\u0642\u0628\u0644\u0627\u062a \u0623\u062e\u0631\u0649 \u063a\u064a\u0631 \u0645\u0633\u062a\u0642\u0628\u0644 \u0627\u0644\u062a\u0631\u0627\u0646\u0633\u0641\u064a\u0631\u064a\u0646 \u0641\u064a \u063a\u0644\u0627\u0641 \u0646\u0627\u0642\u0644 AAV.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0648\u0641\u064a \u0627\u0644\u062f\u0631\u0627\u0633\u0627\u062a \u0627\u0644\u062a\u064a \u0623\u062c\u0631\u064a\u062a \u0639\u0644\u0649 \u0627\u0644\u0642\u0631\u0648\u062f\u060c \u0623\u0638\u0647\u0631 \u0647\u0630\u0627 \u0627\u0644\u0646\u0627\u0642\u0644 \u062b\u0646\u0627\u0626\u064a \u0627\u0644\u062a\u062e\u0635\u0635 \u0643\u0641\u0627\u0621\u0629 \u0645\u062d\u0633\u0646\u0629 \u0641\u064a \u062a\u0648\u0635\u064a\u0644 \u0627\u0644\u062c\u064a\u0646\u0627\u062a \u0625\u0644\u0649 \u0627\u0644\u062f\u0645\u0627\u063a \u0628\u0639\u062f\u0629 \u0623\u0648\u0627\u0645\u0631 \u0645\u0646 \u062d\u064a\u062b \u0627\u0644\u062d\u062c\u0645 \u0645\u0642\u0627\u0631\u0646\u0629 \u0628\u0640 AAV9\u060c \u0645\u0639 \u062a\u0642\u0644\u064a\u0644 \u0627\u0644\u0639\u062f\u0648\u0649 \u0641\u064a \u0627\u0644\u0623\u0646\u0633\u062c\u0629 \u0627\u0644\u062a\u064a \u064a\u062d\u062a\u0645\u0644 \u0623\u0646 \u062a\u0643\u0648\u0646 \u0645\u0634\u0643\u0644\u0629 \u0645\u062b\u0644 \u0627\u0644\u0643\u0628\u062f \u0648\u0627\u0644\u0639\u0642\u062f \u0627\u0644\u062c\u0630\u0631\u064a\u0629 \u0627\u0644\u0638\u0647\u0631\u064a\u0629 \u0628\u0623\u0643\u062b\u0631 \u0645\u0646 90%.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0623\u062f\u0649 \u062a\u0637\u0628\u064a\u0642 JUST-AAV \u0639\u0644\u0649 \u0646\u0645\u0648\u0630\u062c \u0641\u0623\u0631\u064a \u0644\u062f\u0627\u0621 \u0627\u0644\u0644\u064a\u0628\u0648\u0641\u0648\u0633\u064a\u0646\u0627\u062a \u0627\u0644\u0633\u064a\u0631\u0648\u064a\u062f\u064a\u0629 \u0627\u0644\u0639\u0635\u0628\u064a\u0629 \u0625\u0644\u0649 \u0627\u062e\u062a\u0641\u0627\u0621 \u0623\u0639\u0631\u0627\u0636 \u0645\u062b\u0644 \u0627\u0644\u0646\u0648\u0628\u0627\u062a \u0648\u0625\u0637\u0627\u0644\u0629 \u0627\u0644\u0639\u0645\u0631 \u0625\u0644\u0649 \u062d\u062f\u0651 \u0627\u0644\u0634\u0641\u0627\u0621 \u0627\u0644\u0648\u0638\u064a\u0641\u064a. \u062a\u0634\u064a\u0631 \u0647\u0630\u0647 \u0627\u0644\u0646\u062a\u0627\u0626\u062c \u0625\u0644\u0649 \u0623\u0646 \u062a\u0642\u0646\u064a\u0629 JUST-AAV \u0627\u0644\u0645\u064f\u0637\u0648\u0651\u0631\u0629 \u062d\u062f\u064a\u062b\u064b\u0627 \u062a\u064f\u062a\u064a\u062d \u0625\u0645\u0643\u0627\u0646\u064a\u0629 \u0627\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u062c\u064a\u0646\u064a \u0627\u0644\u0623\u0643\u062b\u0631 \u0623\u0645\u0627\u0646\u064b\u0627 \u0648\u0641\u0639\u0627\u0644\u064a\u0629\u064b \u0645\u0642\u0627\u0631\u0646\u0629\u064b \u0628\u0646\u0648\u0627\u0642\u0644 \u0646\u0642\u0644 \u0627\u0644\u062c\u064a\u0646\u0627\u062a \u0627\u0644\u062a\u0642\u0644\u064a\u062f\u064a\u0629. - \u0644\u0644\u0645\u0632\u064a\u062f \u0645\u0646 \u0627\u0644\u0645\u0639\u0644\u0648\u0645\u0627\u062a: <a href=\"https:\/\/jcrpharm.com\/updatedjcr-pharmaceuticals-presents-preclinical-gene-therapy-data-at-asgct-28th-annual-meeting\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u064a\u0642\u062f\u0645 JCR Pharmaceuticals \u0628\u064a\u0627\u0646\u0627\u062a \u0627\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u062c\u064a\u0646\u064a \u0642\u0628\u0644 \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629<\/a> \u2013<\/p>","protected":false},"excerpt":{"rendered":"<p>Alexion, AstraZeneca\u2019s rare disease subsidiary, is licensing specialized gene therapy vehicles from the Japanese firm JCR Pharmaceuticals. The deal, announced on 8th June 2025, gives Alexion access to JCR\u2019s JUST-AAV capsids to use in up to five of Alexion\u2019s genomic medicines programs. In exchange, Alexion will pay JCR an undisclosed upfront fee plus up to [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":4069,"comment_status":"open","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[281],"tags":[386,387,388,385],"class_list":["post-4065","post","type-post","status-publish","format-standard","has-post-thumbnail","category-press-releases","tag-alexion","tag-astrazeneca","tag-genomic-medicines","tag-jcr-pharmaceuticals"],"_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/posts\/4065","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/comments?post=4065"}],"version-history":[{"count":0,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/posts\/4065\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/media\/4069"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/media?parent=4065"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/categories?post=4065"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/tags?post=4065"}],"curies":[{"name":"\u0648\u0648\u0631\u062f\u0628\u0631\u064a\u0633","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}