{"id":3953,"date":"2025-06-20T18:39:58","date_gmt":"2025-06-20T15:39:58","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=3953"},"modified":"2025-06-20T18:43:44","modified_gmt":"2025-06-20T15:43:44","slug":"capricor-therapeutics-announces-positive-4-year-data-of-deramiocel-cap-1002-in-duchenne-muscular-dystrophy","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/ar\/capricor-therapeutics-announces-positive-4-year-data-of-deramiocel-cap-1002-in-duchenne-muscular-dystrophy\/","title":{"rendered":"Capricor Therapeutics \u062a\u0639\u0644\u0646 \u0639\u0646 \u0628\u064a\u0627\u0646\u0627\u062a \u0625\u064a\u062c\u0627\u0628\u064a\u0629 \u0639\u0644\u0649 \u0645\u062f\u0649 \u0623\u0631\u0628\u0639 \u0633\u0646\u0648\u0627\u062a \u0644\u0640 Deramiocel (CAP-1002) \u0641\u064a \u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u062f\u0648\u0634\u064a\u0646"},"content":{"rendered":"<p class=\"wp-block-paragraph\">\u0623\u0639\u0644\u0646\u062a \u0634\u0631\u0643\u0629 Capricor Therapeutics\u060c \u0648\u0647\u064a \u0634\u0631\u0643\u0629 \u062a\u0643\u0646\u0648\u0644\u0648\u062c\u064a\u0627 \u062d\u064a\u0648\u064a\u0629 \u062a\u064f\u0637\u0648\u0651\u0631 \u0639\u0644\u0627\u062c\u0627\u062a \u062a\u062d\u0648\u064a\u0644\u064a\u0629 \u0642\u0627\u0626\u0645\u0629 \u0639\u0644\u0649 \u0627\u0644\u062e\u0644\u0627\u064a\u0627 \u0648\u0627\u0644\u062c\u0633\u064a\u0645\u0627\u062a \u0627\u0644\u062e\u0627\u0631\u062c\u064a\u0629 \u0644\u0644\u0623\u0645\u0631\u0627\u0636 \u0627\u0644\u0646\u0627\u062f\u0631\u0629\u060c \u0627\u0644\u064a\u0648\u0645 \u0639\u0646 \u0646\u062a\u0627\u0626\u062c \u0625\u064a\u062c\u0627\u0628\u064a\u0629 \u0644\u0633\u0644\u0627\u0645\u0629 \u0648\u0641\u0639\u0627\u0644\u064a\u0629 \u062f\u0631\u0627\u0633\u0629 HOPE-2 \u0627\u0644\u0645\u0641\u062a\u0648\u062d\u0629 (OLE) \u0627\u0644\u0645\u0633\u062a\u0645\u0631\u0629 \u0644\u0639\u0642\u0627\u0631 Deramiocel\u060c \u0648\u0647\u0648 \u0627\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u062e\u0644\u0648\u064a \u0627\u0644\u0631\u0627\u0626\u062f \u0627\u0644\u0630\u064a \u062a\u064f\u0642\u062f\u0651\u0645\u0647 \u0627\u0644\u0634\u0631\u0643\u0629 \u0644\u0639\u0644\u0627\u062c \u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u062f\u0648\u0634\u064a\u0646 (DMD). - \u0627\u0642\u0631\u0623 \u0627\u0644\u0645\u0632\u064a\u062f: <a href=\"https:\/\/dmdwarrior.com\/ar\/what-is-deramiocel\/\">\u0645\u0627 \u0647\u0648 Deramiocel\u061f \u0645\u0627 \u0647\u064a \u0648\u0638\u064a\u0641\u0629 CAP-1002\u061f<\/a> \u2013<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0628\u0639\u062f \u0623\u0631\u0628\u0639 \u0633\u0646\u0648\u0627\u062a \u0645\u0646 \u0627\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u0645\u062a\u0648\u0627\u0635\u0644\u060c \u0623\u0638\u0647\u0631 \u0627\u0644\u0645\u0631\u0636\u0649 \u0627\u0644\u0630\u064a\u0646 \u0639\u0648\u0644\u062c\u0648\u0627 \u0628\u0640 Deramiocel \u062a\u063a\u064a\u0631\u064b\u0627 \u0645\u062a\u0648\u0633\u0637\u064b\u0627 \u0642\u062f\u0631\u0647 -0.5 \u0646\u0642\u0637\u0629 \u0645\u0642\u0627\u0631\u0646\u0629\u064b \u0628\u0627\u0644\u0642\u064a\u0645\u0629 \u0627\u0644\u0623\u0633\u0627\u0633\u064a\u0629. \u0639\u0644\u0627\u0648\u0629\u064b \u0639\u0644\u0649 \u0630\u0644\u0643\u060c \u0623\u0638\u0647\u0631 \u062a\u062d\u0644\u064a\u0644 \u0645\u062c\u0645\u0648\u0639\u0629 \u0641\u0631\u0639\u064a\u0629 \u0645\u0646 \u0627\u0644\u0645\u0631\u0636\u0649 \u0627\u0644\u0630\u064a\u0646 \u0643\u0627\u0646\u062a \u0642\u064a\u0645\u0629 \u0642\u0630\u0641 \u0627\u0644\u0628\u0637\u064a\u0646 \u0627\u0644\u0623\u064a\u0633\u0631 \u0644\u062f\u064a\u0647\u0645 &gt;45% \u0642\u064a\u0645\u0629 \u0623\u0633\u0627\u0633\u064a\u0629 \u0641\u0627\u0626\u062f\u0629 \u0633\u0631\u064a\u0631\u064a\u0629 \u0623\u0643\u0628\u0631\u060c \u0645\u0645\u0627 \u064a\u062f\u0639\u0645 \u0627\u0644\u062a\u062f\u062e\u0644 \u0627\u0644\u0645\u0628\u0643\u0631 \u0628\u0627\u0633\u062a\u062e\u062f\u0627\u0645 Deramiocel \u0644\u0644\u062d\u0641\u0627\u0638 \u0639\u0644\u0649 \u0648\u0638\u064a\u0641\u0629 \u0627\u0644\u0642\u0644\u0628.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0628\u0627\u0644\u0625\u0636\u0627\u0641\u0629 \u0625\u0644\u0649 \u0630\u0644\u0643\u060c \u0627\u0633\u062a\u0645\u0631 \u0627\u0644\u0639\u0644\u0627\u062c \u0641\u064a \u0625\u0628\u0637\u0627\u0621 \u062a\u0642\u062f\u0645 \u0645\u0631\u0636 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0627\u0644\u0647\u064a\u0643\u0644\u064a\u0629\u060c \u0643\u0645\u0627 \u062a\u0645 \u0642\u064a\u0627\u0633\u0647 \u0645\u0646 \u062e\u0644\u0627\u0644 \u0623\u062f\u0627\u0621 \u0627\u0644\u0637\u0631\u0641 \u0627\u0644\u0639\u0644\u0648\u064a (PUL v2.0)\u060c \u062d\u064a\u062b \u0634\u0647\u062f \u0627\u0644\u0645\u0631\u0636\u0649 \u0627\u0646\u062e\u0641\u0627\u0636\u064b\u0627 \u0645\u062a\u0648\u0633\u0637\u064b\u0627 \u0623\u0635\u063a\u0631 \u0641\u064a \u0627\u0644\u0633\u0646\u0629 \u0627\u0644\u0631\u0627\u0628\u0639\u0629 (0.6 \u0646\u0642\u0637\u0629) \u0645\u0642\u0627\u0631\u0646\u0629 \u0628\u0627\u0644\u0633\u0646\u0629 \u0627\u0644\u0623\u0648\u0644\u0649 (1.8 \u0646\u0642\u0637\u0629). <strong>\u062a\u0634\u064a\u0631 \u0647\u0630\u0647 \u0627\u0644\u0646\u062a\u0627\u0626\u062c \u0645\u062c\u062a\u0645\u0639\u0629 \u0625\u0644\u0649 \u0623\u0646 \u0627\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u0645\u0637\u0648\u0644 \u0628\u0627\u0633\u062a\u062e\u062f\u0627\u0645 Deramiocel \u0642\u062f \u064a\u0633\u0627\u0639\u062f \u0641\u064a \u0627\u0644\u062a\u062e\u0641\u064a\u0641 \u0645\u0646 \u062a\u0637\u0648\u0631 \u0645\u0631\u0636 \u062f\u0648\u0634\u064a\u0646 \u0628\u0645\u0631\u0648\u0631 \u0627\u0644\u0648\u0642\u062a.<\/strong> \u064a\u0648\u0627\u0635\u0644 Deramiocel \u0627\u0644\u062d\u0641\u0627\u0638 \u0639\u0644\u0649 \u0645\u0633\u062a\u0648\u0649 \u0623\u0645\u0627\u0646 \u0625\u064a\u062c\u0627\u0628\u064a \u0637\u0648\u0627\u0644 \u0627\u0644\u062f\u0631\u0627\u0633\u0629. - \u062a\u0639\u0631\u0641 \u0639\u0644\u0649 \u0627\u0644\u0645\u0632\u064a\u062f: <a href=\"https:\/\/dmdwarrior.com\/ar\/capricor-therapeutics-deramiocel-mid-cycle-review-meeting-with-fda\/\">\u0623\u0639\u0644\u0646\u062a Capricor Therapeutics \u0639\u0646 \u0627\u0643\u062a\u0645\u0627\u0644 \u0627\u062c\u062a\u0645\u0627\u0639 \u0645\u0631\u0627\u062c\u0639\u0629 \u0645\u0646\u062a\u0635\u0641 \u0627\u0644\u062f\u0648\u0631\u0629 \u0645\u0639 FDA \u0639\u0644\u0649 Deramiocel<\/a> \u2013<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0642\u0627\u0644 \u0628\u0627\u062a \u0641\u0648\u0631\u0644\u0648\u0646\u062c\u060c \u0627\u0644\u0631\u0626\u064a\u0633 \u0627\u0644\u0645\u0624\u0633\u0633 \u0648\u0627\u0644\u0631\u0626\u064a\u0633 \u0627\u0644\u062a\u0646\u0641\u064a\u0630\u064a \u0644\u0634\u0631\u0643\u0629 PPMD: &quot;\u0644\u0627 \u064a\u0632\u0627\u0644 \u0627\u0639\u062a\u0644\u0627\u0644 \u0639\u0636\u0644\u0629 \u0627\u0644\u0642\u0644\u0628 \u0623\u062d\u062f \u0627\u0644\u0623\u0633\u0628\u0627\u0628 \u0627\u0644\u0631\u0626\u064a\u0633\u064a\u0629 \u0644\u0644\u0648\u0641\u0627\u0629 \u0641\u064a \u062f\u0648\u0634\u064a\u0646\u060c \u0648\u0645\u0639\u0627\u0644\u062c\u0629 \u0647\u0630\u0627 \u0627\u0644\u062c\u0627\u0646\u0628 \u0645\u0646 \u0627\u0644\u0645\u0631\u0636 \u0623\u0645\u0631 \u0628\u0627\u0644\u063a \u0627\u0644\u0623\u0647\u0645\u064a\u0629 \u0644\u062a\u062d\u0633\u064a\u0646 \u0627\u0644\u0646\u062a\u0627\u0626\u062c&quot;. \u0648\u0623\u0636\u0627\u0641: &quot;\u0627\u0644\u0628\u064a\u0627\u0646\u0627\u062a \u0637\u0648\u064a\u0644\u0629 \u0627\u0644\u0645\u062f\u0649 \u0645\u0646 \u062f\u0631\u0627\u0633\u0629 HOPE-2 OLE \u0645\u0634\u062c\u0639\u0629\u060c \u0644\u0627 \u0633\u064a\u0645\u0627 \u0641\u064a \u0625\u0638\u0647\u0627\u0631 \u0627\u0633\u062a\u0642\u0631\u0627\u0631 \u0627\u0644\u0642\u0644\u0628 \u0639\u0644\u0649 \u0645\u062f\u0649 \u0623\u0631\u0628\u0639 \u0633\u0646\u0648\u0627\u062a. \u064a\u0645\u062b\u0644 Deramiocel \u0646\u0647\u062c\u064b\u0627 \u0639\u0644\u0627\u062c\u064a\u064b\u0627 \u0645\u0647\u0645\u064b\u0627\u060c \u0648\u0646\u062d\u0646 \u0646\u062f\u0639\u0645 \u0627\u0644\u062a\u0642\u062f\u0645 \u0627\u0644\u0645\u0633\u062a\u0645\u0631 \u0639\u0628\u0631 \u0627\u0644\u0645\u0633\u0627\u0631 \u0627\u0644\u062a\u0646\u0638\u064a\u0645\u064a \u0644\u0636\u0645\u0627\u0646 \u062a\u0648\u0641\u0631 \u0627\u0644\u0639\u0644\u0627\u062c\u0627\u062a \u0627\u0644\u062a\u064a \u062a\u0633\u062a\u0647\u062f\u0641 \u0648\u0638\u0627\u0626\u0641 \u0627\u0644\u0642\u0644\u0628 \u0648\u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0644\u0645\u062c\u062a\u0645\u0639\u0646\u0627 \u0641\u064a \u0623\u0633\u0631\u0639 \u0648\u0642\u062a \u0645\u0645\u0643\u0646&quot;.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0635\u0631\u062d\u062a \u0627\u0644\u062f\u0643\u062a\u0648\u0631\u0629 \u0644\u064a\u0646\u062f\u0627 \u0645\u0627\u0631\u0628\u0627\u0646\u060c \u0627\u0644\u0631\u0626\u064a\u0633\u0629 \u0627\u0644\u062a\u0646\u0641\u064a\u0630\u064a\u0629 \u0644\u0634\u0631\u0643\u0629 Capricor Therapeutics: &quot;\u062a\u0639\u0632\u0632 \u0647\u0630\u0647 \u0627\u0644\u0628\u064a\u0627\u0646\u0627\u062a \u0627\u0644\u062a\u064a \u062a\u0645\u062a\u062f \u0644\u0623\u0631\u0628\u0639 \u0633\u0646\u0648\u0627\u062a \u0642\u0648\u0629 \u0648\u0645\u062a\u0627\u0646\u0629 \u0627\u0644\u0641\u0648\u0627\u0626\u062f \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629 \u0644\u0640 Deramiocel \u0648\u0645\u0633\u062a\u0648\u0649 \u0627\u0644\u0633\u0644\u0627\u0645\u0629 \u0627\u0644\u0625\u064a\u062c\u0627\u0628\u064a \u0641\u064a \u0648\u0638\u0627\u0626\u0641 \u0627\u0644\u0642\u0644\u0628 \u0648\u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0627\u0644\u0647\u064a\u0643\u0644\u064a\u0629&quot;. \u0648\u0623\u0636\u0627\u0641\u062a: &quot;\u0645\u0639 \u0645\u0631\u0627\u062c\u0639\u0629 \u0637\u0644\u0628 \u062a\u0631\u062e\u064a\u0635 \u0627\u0644\u0628\u064a\u0648\u0644\u0648\u062c\u064a\u0627 \u0627\u0644\u0628\u064a\u0648\u0644\u0648\u062c\u064a\u0629 (BLA) \u0627\u0644\u062e\u0627\u0635 \u0628\u0646\u0627 \u0639\u0644\u0649 \u0648\u062c\u0647 \u0627\u0644\u0623\u0648\u0644\u0648\u064a\u0629\u060c \u0648\u0627\u0633\u062a\u0643\u0645\u0627\u0644 \u0627\u0644\u0639\u062f\u064a\u062f \u0645\u0646 \u0627\u0644\u062e\u0637\u0648\u0627\u062a \u0627\u0644\u062a\u0646\u0638\u064a\u0645\u064a\u0629 \u0627\u0644\u0631\u0626\u064a\u0633\u064a\u0629\u060c \u0646\u0648\u0627\u0635\u0644 \u0627\u0644\u0639\u0645\u0644 \u0628\u062a\u0631\u0643\u064a\u0632 \u0648\u0633\u0631\u0639\u0629 \u0641\u064a \u0633\u0628\u064a\u0644 \u0627\u0644\u062d\u0635\u0648\u0644 \u0639\u0644\u0649 \u0627\u0644\u0645\u0648\u0627\u0641\u0642\u0629 \u0627\u0644\u0645\u062d\u062a\u0645\u0644\u0629. \u0648\u064a\u0633\u062a\u0645\u0631 \u062d\u0648\u0627\u0631\u0646\u0627 \u0627\u0644\u0645\u0633\u062a\u0645\u0631 \u0645\u0639 FDA \u0639\u0644\u0649 \u0627\u0644\u0645\u0633\u0627\u0631 \u0627\u0644\u0635\u062d\u064a\u062d \u062f\u0648\u0646 \u0623\u064a \u062f\u0644\u064a\u0644 \u0639\u0644\u0649 \u0623\u064a \u062a\u0623\u062e\u064a\u0631. \u0646\u0634\u0643\u0631 \u0627\u0644\u0645\u0631\u0636\u0649 \u0648\u0639\u0627\u0626\u0644\u0627\u062a\u0647\u0645 \u0648\u0627\u0644\u0623\u0637\u0628\u0627\u0621 \u0627\u0644\u0630\u064a\u0646 \u0633\u0627\u0647\u0645\u0648\u0627 \u0628\u062f\u0648\u0631 \u0641\u0639\u0627\u0644 \u0641\u064a \u062a\u0637\u0648\u064a\u0631 \u0647\u0630\u0627 \u0627\u0644\u0628\u0631\u0646\u0627\u0645\u062c&quot;.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0627\u0642\u0631\u0623 \u0627\u0644\u0645\u0632\u064a\u062f: <a href=\"https:\/\/dmdwarrior.com\/ar\/capricor-therapeutics-announces-bmd-orphan-drug-designation-and-dmd-program-regulatory-development-for-deramiocel-cap-1002\/\">Capricor Therapeutics \u062a\u0639\u0644\u0646 \u0639\u0646 \u062a\u0635\u0646\u064a\u0641 \u062f\u0648\u0627\u0621 \u064a\u062a\u064a\u0645 BMD \u0648\u062a\u0637\u0648\u064a\u0631 \u0628\u0631\u0646\u0627\u0645\u062c DMD \u0627\u0644\u062a\u0646\u0638\u064a\u0645\u064a \u0644\u0640 Deramiocel (CAP-1002)<\/a><\/p>","protected":false},"excerpt":{"rendered":"<p>Capricor Therapeutics, a biotechnology company developing transformative cell and exosome-based therapeutics for rare diseases, today announced positive four-year safety and efficacy results from its ongoing HOPE-2 Open-Label Extension (OLE) study of Deramiocel, the Company\u2019s lead cell therapy candidate for Duchenne Muscular Dystrophy (DMD). &#8211; Read More: What is Deramiocel? What Does CAP-1002 Do? &#8211; After [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":3954,"comment_status":"open","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[281],"tags":[90,86,87,89,85,362,301],"class_list":["post-3953","post","type-post","status-publish","format-standard","has-post-thumbnail","category-press-releases","tag-cap-1002","tag-capricor","tag-capricor-therapeutics","tag-cardiomyopathy","tag-deramiocel","tag-dmd-cardiomyopathy","tag-hope-2"],"_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/posts\/3953","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/comments?post=3953"}],"version-history":[{"count":0,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/posts\/3953\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/media\/3954"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/media?parent=3953"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/categories?post=3953"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/tags?post=3953"}],"curies":[{"name":"\u0648\u0648\u0631\u062f\u0628\u0631\u064a\u0633","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}