{"id":3230,"date":"2025-03-17T14:28:46","date_gmt":"2025-03-17T11:28:46","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=3230"},"modified":"2025-03-17T14:28:48","modified_gmt":"2025-03-17T11:28:48","slug":"avidity-biosciences-announces-positive-topline-del-zota-data-showing-consistent-statistically-significant-improvements-in-dystrophin","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/ar\/avidity-biosciences-announces-positive-topline-del-zota-data-showing-consistent-statistically-significant-improvements-in-dystrophin\/","title":{"rendered":"\u0623\u0639\u0644\u0646\u062a \u0634\u0631\u0643\u0629 Avidity Biosciences \u0639\u0646 \u0628\u064a\u0627\u0646\u0627\u062a Del-zota \u0627\u0644\u0625\u064a\u062c\u0627\u0628\u064a\u0629 \u0627\u0644\u062a\u064a \u062a\u064f\u0638\u0647\u0631 \u062a\u062d\u0633\u0646\u0627\u062a \u062b\u0627\u0628\u062a\u0629 \u0648\u0647\u0627\u0645\u0629 \u0625\u062d\u0635\u0627\u0626\u064a\u064b\u0627 \u0641\u064a \u0627\u0644\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646"},"content":{"rendered":"<p class=\"wp-block-paragraph\">\u0623\u0639\u0644\u0646\u062a \u0634\u0631\u0643\u0629 Avidity Biosciences \u0639\u0646 \u0628\u064a\u0627\u0646\u0627\u062a Del-zota \u0627\u0644\u0625\u064a\u062c\u0627\u0628\u064a\u0629 \u0627\u0644\u062a\u064a \u062a\u0638\u0647\u0631 \u062a\u062d\u0633\u0646\u0627\u062a \u062b\u0627\u0628\u062a\u0629 \u0648\u0647\u0627\u0645\u0629 \u0625\u062d\u0635\u0627\u0626\u064a\u064b\u0627 \u0641\u064a \u0627\u0644\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0648\u062a\u062e\u0637\u064a \u0627\u0644\u0625\u0643\u0633\u0648\u0646 \u0648\u0643\u064a\u0646\u0627\u0632 \u0627\u0644\u0643\u0631\u064a\u0627\u062a\u064a\u0646 \u0644\u062f\u0649 \u0627\u0644\u0645\u0634\u0627\u0631\u0643\u064a\u0646 \u0641\u064a \u062a\u062c\u0631\u0628\u0629 EXPLORE44\u00ae \u0641\u064a \u0627\u0644\u0645\u0631\u062d\u0644\u0629 1\/2 \u0627\u0644\u0645\u0635\u0627\u0628\u064a\u0646 \u0628\u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0642\u0627\u0628\u0644\u064a\u0646 \u0644\u062a\u062e\u0637\u064a \u0627\u0644\u0625\u0643\u0633\u0648\u0646 44.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0633\u064a\u062a\u0645 \u062a\u0633\u0644\u064a\u0637 \u0627\u0644\u0636\u0648\u0621 \u0639\u0644\u0649 \u0627\u0644\u0628\u064a\u0627\u0646\u0627\u062a \u0641\u064a \u0639\u0631\u0636 \u0634\u0641\u0648\u064a \u0648\u0645\u0644\u0635\u0642 \u0641\u064a \u0627\u0644\u0645\u0624\u062a\u0645\u0631 \u0627\u0644\u0639\u0644\u0645\u064a \u0648\u0627\u0644\u0633\u0631\u064a\u0631\u064a \u0644\u062c\u0645\u0639\u064a\u0629 \u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a (MDA) \u0644\u0639\u0627\u0645 2025\u060c \u0648\u0627\u0644\u0630\u064a \u0633\u064a\u0639\u0642\u062f \u0641\u064a \u0627\u0644\u0641\u062a\u0631\u0629 \u0645\u0646 16 \u0625\u0644\u0649 19 \u0645\u0627\u0631\u0633 2025 \u0641\u064a \u062f\u0627\u0644\u0627\u0633\u060c \u062a\u0643\u0633\u0627\u0633.<\/p>\n\n\n\n<h2 class=\"wp-block-heading\">\u0627\u0644\u062a\u062c\u0627\u0631\u0628 \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629 \u0644\u0640 Avidity Biosciences EXPLORE44 (Del-zota)<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u0623\u0638\u0647\u0631 \u062f\u0648\u0627\u0621 \u062f\u064a\u0644-\u0632\u0648\u062a\u0627 \u062a\u062d\u0633\u0646\u064b\u0627 \u0645\u0644\u062d\u0648\u0638\u064b\u0627 \u0641\u064a \u0639\u062f\u0629 \u0645\u0642\u0627\u064a\u064a\u0633\u060c \u0628\u0645\u0627 \u0641\u064a \u0630\u0644\u0643 \u0632\u064a\u0627\u062f\u0629 \u0643\u0628\u064a\u0631\u0629 \u0641\u064a \u0625\u0646\u062a\u0627\u062c \u0627\u0644\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0648\u0627\u0646\u062e\u0641\u0627\u0636 \u0645\u0644\u062d\u0648\u0638 \u0641\u064a \u0645\u0633\u062a\u0648\u064a\u0627\u062a \u0643\u064a\u0646\u0627\u0632 \u0627\u0644\u0643\u0631\u064a\u0627\u062a\u064a\u0646 \u0641\u064a \u0627\u0644\u0645\u0635\u0644 \u0625\u0644\u0649 \u0645\u0633\u062a\u0648\u064a\u0627\u062a \u0634\u0628\u0647 \u0637\u0628\u064a\u0639\u064a\u0629 \u0628\u0639\u062f \u062b\u0644\u0627\u062b \u062c\u0631\u0639\u0627\u062a \u0641\u0642\u0637. \u064a\u0624\u0643\u062f \u062b\u0628\u0627\u062a \u0647\u0630\u0647 \u0627\u0644\u0646\u062a\u0627\u0626\u062c \u0641\u064a \u0647\u0630\u0647 \u0627\u0644\u0641\u062a\u0631\u0629 \u0627\u0644\u0632\u0645\u0646\u064a\u0629 \u0627\u0644\u0642\u0635\u064a\u0631\u0629\u060c \u0625\u0644\u0649 \u062c\u0627\u0646\u0628 \u0627\u0644\u0633\u0644\u0627\u0645\u0629 \u0648\u0627\u0644\u062a\u062d\u0645\u0644 \u0627\u0644\u0625\u064a\u062c\u0627\u0628\u064a\u060c \u0639\u0644\u0649 \u0625\u0645\u0643\u0627\u0646\u064a\u0629 \u0623\u0646 \u064a\u0635\u0628\u062d del-zota \u0639\u0644\u0627\u062c\u064b\u0627 \u0631\u0627\u0626\u062f\u064b\u0627 \u0644\u0644\u0623\u0641\u0631\u0627\u062f \u0627\u0644\u0645\u0635\u0627\u0628\u064a\u0646 \u0628\u0645\u0631\u0636 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a \u0630\u0648\u064a \u0627\u0644\u0645\u062a\u063a\u064a\u0631\u0627\u062a \u0627\u0644\u062c\u064a\u0646\u064a\u0629 \u0627\u0644\u0642\u0627\u0628\u0644\u0629 \u0644\u062a\u062e\u0637\u064a \u0627\u0644\u0625\u0643\u0633\u0648\u0646 44\u060c \u0643\u0645\u0627 \u0635\u0631\u0651\u062d \u0627\u0644\u062f\u0643\u062a\u0648\u0631 \u0623\u0631\u0627\u0641\u064a\u0646\u062f\u0627\u0646 \u0641\u064a\u0631\u0627\u0628\u0627\u0646\u062f\u064a\u0627\u0646\u060c \u0623\u0633\u062a\u0627\u0630 \u0645\u0634\u0627\u0631\u0643 \u0641\u064a \u0637\u0628 \u0627\u0644\u0623\u0637\u0641\u0627\u0644 \u0628\u062c\u0627\u0645\u0639\u0629 \u0623\u0631\u0643\u0646\u0633\u0627\u0633 \u0644\u0644\u0639\u0644\u0648\u0645 \u0627\u0644\u0637\u0628\u064a\u0629 \u0648\u0645\u0633\u062a\u0634\u0641\u0649 \u0623\u0631\u0643\u0646\u0633\u0627\u0633 \u0644\u0644\u0623\u0637\u0641\u0627\u0644.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">&quot;\u062a\u062c\u0644\u0628 \u0647\u0630\u0647 \u0627\u0644\u0646\u062a\u0627\u0626\u062c \u0623\u0645\u0644\u0627\u064b \u062c\u062f\u064a\u062f\u064b\u0627 \u0644\u0644\u0645\u0631\u0636\u0649 \u0648\u0627\u0644\u0623\u0633\u0631 \u0627\u0644\u0645\u062a\u0636\u0631\u0631\u0629 \u0645\u0646 \u0645\u0631\u0636 \u062f\u0648\u0634\u064a\u0646 \u0648\u0627\u0644\u0630\u064a\u0646 \u0647\u0645 \u0641\u064a \u062d\u0627\u062c\u0629 \u0645\u0627\u0633\u0629 \u0625\u0644\u0649 \u0639\u0644\u0627\u062c\u0627\u062a \u0645\u0633\u062a\u0647\u062f\u0641\u0629 \u064a\u0645\u0643\u0646\u0647\u0627 \u0627\u0644\u062d\u0641\u0627\u0638 \u0639\u0644\u0649 \u0633\u0644\u0627\u0645\u0629 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0648\u0631\u0628\u0645\u0627 \u0645\u0646\u0639 \u0623\u0648 \u062a\u0623\u062e\u064a\u0631 \u062a\u0637\u0648\u0631 \u0636\u0639\u0641 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0648\u0641\u0642\u062f\u0627\u0646 \u0627\u0644\u0648\u0638\u064a\u0641\u0629 \u0627\u0644\u0645\u0631\u062a\u0628\u0637\u0629 \u0628\u0647\u0630\u0627 \u0627\u0644\u0645\u0631\u0636.&quot;<\/p>\n\n\n\n<h2 class=\"wp-block-heading\">\u0645\u0627 \u0647\u0648 \u062f\u064a\u0644 \u0632\u0648\u062a\u0627\u061f<\/h2>\n\n\n\n<figure class=\"wp-block-image size-large\"><img loading=\"lazy\" decoding=\"async\" width=\"1024\" height=\"576\" src=\"https:\/\/dmdwarrior.com\/wp-content\/uploads\/2025\/03\/Avidity-Biosciences-Del-Zota-1024x576.jpg\" alt=\"Avidity Biosciences Del-zota EXPLORE44 \u062a\u062e\u0637\u064a \u0627\u0644\u0625\u0643\u0633\u0648\u0646 44\" class=\"wp-image-3234\" title=\"\" srcset=\"https:\/\/dmdwarrior.com\/wp-content\/uploads\/2025\/03\/Avidity-Biosciences-Del-Zota-1024x576.jpg 1024w, https:\/\/dmdwarrior.com\/wp-content\/uploads\/2025\/03\/Avidity-Biosciences-Del-Zota-300x169.jpg 300w, https:\/\/dmdwarrior.com\/wp-content\/uploads\/2025\/03\/Avidity-Biosciences-Del-Zota-768x432.jpg 768w, https:\/\/dmdwarrior.com\/wp-content\/uploads\/2025\/03\/Avidity-Biosciences-Del-Zota-1536x864.jpg 1536w, https:\/\/dmdwarrior.com\/wp-content\/uploads\/2025\/03\/Avidity-Biosciences-Del-Zota-18x10.jpg 18w, https:\/\/dmdwarrior.com\/wp-content\/uploads\/2025\/03\/Avidity-Biosciences-Del-Zota-747x420.jpg 747w, https:\/\/dmdwarrior.com\/wp-content\/uploads\/2025\/03\/Avidity-Biosciences-Del-Zota-150x84.jpg 150w, https:\/\/dmdwarrior.com\/wp-content\/uploads\/2025\/03\/Avidity-Biosciences-Del-Zota-696x392.jpg 696w, https:\/\/dmdwarrior.com\/wp-content\/uploads\/2025\/03\/Avidity-Biosciences-Del-Zota-1068x601.jpg 1068w, https:\/\/dmdwarrior.com\/wp-content\/uploads\/2025\/03\/Avidity-Biosciences-Del-Zota.jpg 1920w\" sizes=\"auto, (max-width: 1024px) 100vw, 1024px\" \/><\/figure>\n\n\n\n<p class=\"wp-block-paragraph\">\u0635\u064f\u0645\u0645 \u062f\u064a\u0644-\u0632\u0648\u062a\u0627 \u0644\u062a\u0648\u0635\u064a\u0644 \u0623\u0648\u0644\u064a\u063a\u0648\u0645\u0631\u0627\u062a \u0641\u0648\u0633\u0641\u0648\u0631\u0648\u062f\u064a\u0627\u0645\u064a\u062f\u0627\u062a \u0645\u0648\u0631\u0641\u0648\u0644\u064a\u0646\u0648 (PMOs) \u0625\u0644\u0649 \u0623\u0646\u0633\u062c\u0629 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0627\u0644\u0647\u064a\u0643\u0644\u064a\u0629 \u0648\u0627\u0644\u0642\u0644\u0628\u064a\u0629\u060c \u0648\u0630\u0644\u0643 \u0644\u062a\u062e\u0637\u064a \u0627\u0644\u0625\u0643\u0633\u0648\u0646 44 \u0645\u0646 \u062c\u064a\u0646 \u0627\u0644\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u062a\u062d\u062f\u064a\u062f\u064b\u0627\u060c \u0648\u062a\u0645\u0643\u064a\u0646 \u0625\u0646\u062a\u0627\u062c \u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0634\u0628\u0647 \u0643\u0627\u0645\u0644 \u0627\u0644\u0637\u0648\u0644. \u0648\u0642\u062f \u0645\u064f\u0646\u062d \u062f\u064a\u0644-\u0632\u0648\u062a\u0627 \u062a\u0635\u0646\u064a\u0641 &quot;\u064a\u062a\u064a\u0645&quot; \u0645\u0646 \u0642\u0650\u0628\u0644 \u0625\u062f\u0627\u0631\u0629 \u0627\u0644\u063a\u0630\u0627\u0621 \u0648\u0627\u0644\u062f\u0648\u0627\u0621 \u0627\u0644\u0623\u0645\u0631\u064a\u0643\u064a\u0629 (FDA) \u0648\u0627\u0644\u0648\u0643\u0627\u0644\u0629 \u0627\u0644\u0623\u0648\u0631\u0648\u0628\u064a\u0629 \u0644\u0644\u0623\u062f\u0648\u064a\u0629 (EMA). \u0643\u0645\u0627 \u0645\u064f\u0646\u062d FDA \u062a\u0635\u0646\u064a\u0641 &quot;\u0645\u0631\u0636 \u0627\u0644\u0623\u0637\u0641\u0627\u0644 \u0627\u0644\u0646\u0627\u062f\u0631&quot; \u0648\u062a\u0635\u0646\u064a\u0641 &quot;\u0627\u0644\u0645\u0633\u0627\u0631 \u0627\u0644\u0633\u0631\u064a\u0639&quot;. \u062f\u064a\u0644-\u0632\u0648\u062a\u0627 \u0647\u0648 \u0627\u0644\u0623\u0648\u0644 \u0645\u0646 \u0628\u064a\u0646 \u0627\u0644\u0639\u062f\u064a\u062f \u0645\u0646 \u0645\u064f\u062b\u0628\u0637\u0627\u062a \u0627\u0644\u0646\u0648\u0643\u0644\u064a\u0648\u062a\u064a\u062f\u0627\u062a \u0627\u0644\u062a\u064a \u064a\u062c\u0631\u064a \u062a\u0637\u0648\u064a\u0631\u0647\u0627 \u062d\u0627\u0644\u064a\u064b\u0627 \u0641\u064a \u0634\u0631\u0643\u0629 \u0623\u0641\u064a\u062f\u064a\u062a\u064a \u0644\u0639\u0644\u0627\u062c \u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0627\u0644\u062f\u0648\u0634\u064a\u0646\u064a.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u062a\u0633\u0644\u0637 \u0627\u0644\u0628\u064a\u0627\u0646\u0627\u062a \u0627\u0644\u0645\u0642\u062f\u0645\u0629 \u0641\u064a MDA \u0627\u0644\u0636\u0648\u0621 \u0639\u0644\u0649 \u0627\u0644\u0628\u064a\u0627\u0646\u0627\u062a \u0627\u0644\u0645\u062a\u0633\u0642\u0629 \u0639\u0628\u0631 \u062c\u0645\u064a\u0639 \u0627\u0644\u0645\u0639\u0644\u0645\u0627\u062a \u0641\u064a \u0643\u0644 \u0645\u0646 \u0645\u062c\u0645\u0648\u0639\u062a\u064a 5 \u0645\u062c\u0645 \/ \u0643\u062c\u0645 \u0648 10 \u0645\u062c\u0645 \/ \u0643\u062c\u0645 \u0645\u0646 del-zota\u060c \u0628\u0645\u0627 \u0641\u064a \u0630\u0644\u0643:<\/strong><\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u062a\u0648\u0635\u064a\u0644 \u0645\u0633\u062a\u0647\u062f\u0641 \u0644\u0640 PMOs \u0645\u0645\u0627 \u064a\u0624\u062f\u064a \u0625\u0644\u0649 \u062a\u0631\u0643\u064a\u0632\u0627\u062a \u0623\u0646\u0633\u062c\u0629 \u062a\u0628\u0644\u063a \u062d\u0648\u0627\u0644\u064a 200 \u0646\u0627\u0646\u0648\u0645\u0648\u0644 \u0641\u064a \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0627\u0644\u0647\u064a\u0643\u0644\u064a\u0629\u061b<\/li>\n\n\n\n<li>\u0632\u064a\u0627\u062f\u0629 \u0643\u0628\u064a\u0631\u0629 \u0625\u062d\u0635\u0627\u0626\u064a\u064b\u0627 \u0628\u062d\u0648\u0627\u0644\u064a 40% \u0641\u064a \u062a\u062e\u0637\u064a \u0627\u0644\u0625\u0643\u0633\u0648\u0646 44\u061b<\/li>\n\n\n\n<li>\u0632\u064a\u0627\u062f\u0629 \u0643\u0628\u064a\u0631\u0629 \u0625\u062d\u0635\u0627\u0626\u064a\u064b\u0627 \u0628\u0646\u062d\u0648 25% \u0645\u0646 \u0627\u0644\u0645\u0639\u062f\u0644 \u0627\u0644\u0637\u0628\u064a\u0639\u064a \u0641\u064a \u0625\u0646\u062a\u0627\u062c \u0627\u0644\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0648\u0627\u0633\u062a\u0639\u0627\u062f\u0629 \u0627\u0644\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0627\u0644\u0643\u0644\u064a \u062d\u062a\u0649 58% \u0645\u0646 \u0627\u0644\u0645\u0639\u062f\u0644 \u0627\u0644\u0637\u0628\u064a\u0639\u064a\u061b<\/li>\n\n\n\n<li>\u0627\u0646\u062e\u0641\u0627\u0636 \u0645\u0633\u062a\u0648\u064a\u0627\u062a \u0643\u064a\u0646\u0627\u0632 \u0627\u0644\u0643\u0631\u064a\u0627\u062a\u064a\u0646 \u0625\u0644\u0649 \u0645\u0627 \u064a\u0642\u0631\u0628 \u0645\u0646 \u0627\u0644\u0645\u0639\u062f\u0644 \u0627\u0644\u0637\u0628\u064a\u0639\u064a \u0645\u0639 \u0627\u0646\u062e\u0641\u0627\u0636\u0627\u062a \u0623\u0643\u0628\u0631 \u0645\u0646 80% \u0645\u0642\u0627\u0631\u0646\u0629 \u0628\u0627\u0644\u0623\u0633\u0627\u0633:\n<ul class=\"wp-block-list\">\n<li>\u0648\u0639\u0644\u0649 \u0646\u062d\u0648 \u0645\u0645\u0627\u062b\u0644\u060c \u0623\u0638\u0647\u0631 \u0627\u0644\u0645\u0634\u0627\u0631\u0643\u0648\u0646 \u0641\u064a \u0627\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u0648\u0647\u0645\u064a \u0627\u0646\u062e\u0641\u0627\u0636\u064b\u0627 \u0641\u064a \u0645\u0633\u062a\u0648\u064a\u0627\u062a \u0643\u064a\u0646\u0627\u0632 \u0627\u0644\u0643\u0631\u064a\u0627\u062a\u064a\u0646 \u0625\u0644\u0649 \u0645\u0627 \u064a\u0642\u0631\u0628 \u0645\u0646 \u0627\u0644\u0645\u0639\u062f\u0644 \u0627\u0644\u0637\u0628\u064a\u0639\u064a \u0639\u0646\u062f \u0627\u0644\u0639\u0644\u0627\u062c \u0628\u0640 del-zota\u061b<\/li>\n\n\n\n<li>\u062a\u0645 \u0627\u0644\u062d\u0641\u0627\u0638 \u0639\u0644\u0649 \u0627\u0646\u062e\u0641\u0627\u0636\u0627\u062a \u0643\u0628\u064a\u0631\u0629 \u0641\u064a \u0645\u0633\u062a\u0648\u064a\u0627\u062a \u0643\u064a\u0646\u0627\u0632 \u0627\u0644\u0643\u0631\u064a\u0627\u062a\u064a\u0646 \u0641\u064a \u062a\u062c\u0631\u0628\u0629 EXPLORE44-OLE \u0645\u0639 \u0627\u0633\u062a\u0645\u0631\u0627\u0631 \u0627\u0644\u0639\u0644\u0627\u062c \u0644\u0645\u062f\u0629 \u062a\u0635\u0644 \u0625\u0644\u0649 \u0639\u0627\u0645 \u0648\u0627\u062d\u062f\u061b \u0648\u060c<\/li>\n<\/ul>\n<\/li>\n\n\n\n<li>\u0623\u0638\u0647\u0631 \u062f\u0648\u0627\u0621 \u062f\u064a\u0644-\u0632\u0648\u062a\u0627 \u0633\u0644\u0627\u0645\u0629 \u0648\u062a\u062d\u0645\u0644\u064b\u0627 \u0625\u064a\u062c\u0627\u0628\u064a\u064b\u0627 \u0641\u064a \u0643\u0644\u062a\u0627 \u0627\u0644\u062c\u0631\u0639\u062a\u064a\u0646\u060c \u062d\u064a\u062b \u0643\u0627\u0646\u062a \u0645\u0639\u0638\u0645 \u0627\u0644\u0623\u062d\u062f\u0627\u062b \u0627\u0644\u0633\u0644\u0628\u064a\u0629 \u0627\u0644\u0646\u0627\u0634\u0626\u0629 \u0639\u0646 \u0627\u0644\u0639\u0644\u0627\u062c (TEAEs) \u062e\u0641\u064a\u0641\u0629 \u0623\u0648 \u0645\u0639\u062a\u062f\u0644\u0629.<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u064a\u062a\u0639\u0644\u0645 \u0623\u0643\u062b\u0631:<\/strong> <a href=\"https:\/\/dmdwarrior.com\/ar\/next-generation-exon-skipping-therapies-for-duchenne-muscular-dystrophy\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u062a\u0645 \u062a\u0637\u0648\u064a\u0631 \u0627\u0644\u062c\u064a\u0644 \u0627\u0644\u0642\u0627\u062f\u0645 \u0645\u0646 \u0639\u0644\u0627\u062c\u0627\u062a \u062a\u062e\u0637\u064a \u0627\u0644\u0625\u0643\u0633\u0648\u0646 \u0644\u0639\u0644\u0627\u062c \u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u062f\u0648\u0634\u064a\u0646<\/a><\/p>","protected":false},"excerpt":{"rendered":"<p>Avidity Biosciences Announces Positive Topline Del-zota Data Showing Consistent, Statistically Significant Improvements in Dystrophin, Exon Skipping, and Creatine Kinase in Phase 1\/2 EXPLORE44\u00ae Trial Participants with Duchenne Muscular Dystrophy Amenable to Exon 44 Skipping. The data will be highlighted in an oral and poster presentation at the 2025 Muscular Dystrophy Association (MDA) Clinical &amp; Scientific [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":3232,"comment_status":"open","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[281],"tags":[126,298,141,127,246,299],"class_list":["post-3230","post","type-post","status-publish","format-standard","has-post-thumbnail","category-press-releases","tag-avidity-biosciences","tag-del-zota","tag-exon-44","tag-exon-44-skipping","tag-exon-44-skipping-therapies","tag-explore44"],"_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/posts\/3230","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/comments?post=3230"}],"version-history":[{"count":0,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/posts\/3230\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/media\/3232"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/media?parent=3230"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/categories?post=3230"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/tags?post=3230"}],"curies":[{"name":"\u0648\u0648\u0631\u062f\u0628\u0631\u064a\u0633","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}