{"id":2926,"date":"2026-04-16T21:18:18","date_gmt":"2026-04-16T18:18:18","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=2926"},"modified":"2026-04-16T21:21:56","modified_gmt":"2026-04-16T18:21:56","slug":"duchenne-muscular-dystrophy-treatment-access","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/ar\/duchenne-muscular-dystrophy-treatment-access\/","title":{"rendered":"\u0627\u0644\u0648\u0635\u0648\u0644 \u0625\u0644\u0649 \u0639\u0644\u0627\u062c \u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a: \u0641\u0634\u0644 \u0639\u0627\u0644\u0645\u064a \u0641\u064a \u0627\u0644\u0625\u0646\u0635\u0627\u0641 \u0648\u0627\u0644\u0633\u064a\u0627\u0633\u0627\u062a \u0648\u0627\u0644\u0645\u0633\u0627\u0621\u0644\u0629"},"content":{"rendered":"<p class=\"wp-block-paragraph\">\u0644\u0645 \u064a\u0639\u062f \u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a (DMD) \u062d\u0627\u0644\u0629 \u064a\u062a\u0645 \u062a\u0639\u0631\u064a\u0641\u0647\u0627 \u0641\u0642\u0637 \u0645\u0646 \u062e\u0644\u0627\u0644 \u0628\u064a\u0648\u0644\u0648\u062c\u064a\u062a\u0647\u0627. <strong>\u0627\u0644\u064a\u0648\u0645\u060c \u064a\u062a\u0645 \u062a\u062d\u062f\u064a\u062f\u0647\u0627 \u0628\u0646\u0641\u0633 \u0627\u0644\u0642\u062f\u0631 \u0645\u0646 \u062e\u0644\u0627\u0644 \u0645\u0646 \u064a\u0633\u062a\u0637\u064a\u0639 \u0627\u0644\u062d\u0635\u0648\u0644 \u0639\u0644\u0649 \u0627\u0644\u0639\u0644\u0627\u062c \u0648\u0645\u0646 \u0644\u0627 \u064a\u0633\u062a\u0637\u064a\u0639.<\/strong> \u0639\u0644\u0649 \u0627\u0644\u0631\u063a\u0645 \u0645\u0646 \u0627\u0644\u062a\u0642\u062f\u0645 \u0627\u0644\u0643\u0628\u064a\u0631 \u0641\u064a \u0627\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u062c\u064a\u0646\u064a\u060c \u0648\u0627\u0644\u0623\u062f\u0648\u064a\u0629 \u0627\u0644\u062a\u064a \u062a\u062a\u062e\u0637\u0649 \u0627\u0644\u0625\u0643\u0633\u0648\u0646\u060c \u0648\u0627\u0644\u0631\u0639\u0627\u064a\u0629 \u0645\u062a\u0639\u062f\u062f\u0629 \u0627\u0644\u062a\u062e\u0635\u0635\u0627\u062a\u060c \u0625\u0644\u0627 \u0623\u0646 \u0627\u0644\u0648\u0635\u0648\u0644 \u0625\u0644\u0649 \u0639\u0644\u0627\u062c \u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a \u0644\u0627 \u064a\u0632\u0627\u0644 \u063a\u064a\u0631 \u0645\u062a\u0643\u0627\u0641\u0626 \u0628\u0634\u0643\u0644 \u0643\u0628\u064a\u0631 \u0628\u064a\u0646 \u0627\u0644\u0628\u0644\u062f\u0627\u0646 \u0648\u0623\u0646\u0638\u0645\u0629 \u0627\u0644\u0631\u0639\u0627\u064a\u0629 \u0627\u0644\u0635\u062d\u064a\u0629 \u0648\u0627\u0644\u0641\u0626\u0627\u062a \u0627\u0644\u0627\u062c\u062a\u0645\u0627\u0639\u064a\u0629 \u0648\u0627\u0644\u0627\u0642\u062a\u0635\u0627\u062f\u064a\u0629.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0627\u0644\u062d\u0642\u064a\u0642\u0629 \u0645\u064f\u0631\u0651\u0629: \u0641\u0628\u064a\u0646\u0645\u0627 \u064a\u062a\u0644\u0642\u0649 \u0628\u0639\u0636 \u0627\u0644\u0623\u0637\u0641\u0627\u0644 \u0639\u0644\u0627\u062c\u0627\u062a \u0645\u062a\u0637\u0648\u0631\u0629 \u062a\u064f\u062d\u0633\u0651\u0646 \u0642\u062f\u0631\u062a\u0647\u0645 \u0639\u0644\u0649 \u0627\u0644\u062d\u0631\u0643\u0629 \u0648\u062a\u064f\u0637\u064a\u0644 \u0623\u0645\u062f \u0628\u0642\u0627\u0626\u0647\u0645 \u0639\u0644\u0649 \u0642\u064a\u062f \u0627\u0644\u062d\u064a\u0627\u0629\u060c \u064a\u064f\u062d\u0631\u0645 \u0622\u062e\u0631\u0648\u0646 \u062d\u062a\u0649 \u0645\u0646 \u0623\u0628\u0633\u0637 \u0645\u0639\u0627\u064a\u064a\u0631 \u0627\u0644\u0631\u0639\u0627\u064a\u0629. \u0648\u0647\u0630\u0627 \u0644\u064a\u0633 \u0642\u0635\u0648\u0631\u064b\u0627 \u0639\u0644\u0645\u064a\u064b\u0627. <strong>\u0625\u0646\u0647 \u0641\u0634\u0644 \u0646\u0638\u0627\u0645\u064a \u062a\u0634\u0643\u0644 \u0628\u0641\u0639\u0644 \u0646\u0645\u0627\u0630\u062c \u0627\u0644\u062a\u0633\u0639\u064a\u0631\u060c \u0648\u062c\u0645\u0648\u062f \u0627\u0644\u0633\u064a\u0627\u0633\u0627\u062a\u060c \u0648\u0639\u062f\u0645 \u0627\u0644\u0645\u0633\u0627\u0648\u0627\u0629 \u0641\u064a \u0627\u0644\u0635\u062d\u0629 \u0627\u0644\u0639\u0627\u0644\u0645\u064a\u0629.<\/strong><\/p>\n\n\n\n<div class=\"wp-block-rank-math-toc-block\" id=\"rank-math-toc\"><h2>\u062c\u062f\u0648\u0644 \u0627\u0644\u0645\u062d\u062a\u0648\u064a\u0627\u062a<\/h2><nav><ul><li><a href=\"#what-is-duchenne-muscular-dystrophy\">\u0645\u0627 \u0647\u0648 \u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a\u061f<\/a><\/li><li><a href=\"#the-current-landscape-of-duchenne-muscular-dystrophy-treatment-access\">\u0627\u0644\u0648\u0636\u0639 \u0627\u0644\u062d\u0627\u0644\u064a \u0644\u0625\u0645\u0643\u0627\u0646\u064a\u0629 \u0627\u0644\u0648\u0635\u0648\u0644 \u0625\u0644\u0649 \u0639\u0644\u0627\u062c \u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a<\/a><\/li><li><a href=\"#why-duchenne-muscular-dystrophy-treatment-access-is-so-unequal\">\u0644\u0645\u0627\u0630\u0627 \u064a\u062a\u0641\u0627\u0648\u062a \u0627\u0644\u0648\u0635\u0648\u0644 \u0625\u0644\u0649 \u0639\u0644\u0627\u062c \u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a \u0625\u0644\u0649 \u062d\u062f \u0643\u0628\u064a\u0631\u061f<\/a><\/li><li><a href=\"#pharmaceutical-companies-and-duchenne-muscular-dystrophy-treatment-access\">\u0634\u0631\u0643\u0627\u062a \u0627\u0644\u0623\u062f\u0648\u064a\u0629 \u0648\u0625\u0645\u0643\u0627\u0646\u064a\u0629 \u0627\u0644\u062d\u0635\u0648\u0644 \u0639\u0644\u0649 \u0639\u0644\u0627\u062c \u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a<\/a><\/li><li><a href=\"#government-responsibility-in-duchenne-muscular-dystrophy-treatment-access\">\u0645\u0633\u0624\u0648\u0644\u064a\u0629 \u0627\u0644\u062d\u0643\u0648\u0645\u0629 \u0641\u064a \u062a\u0648\u0641\u064a\u0631 \u0627\u0644\u0639\u0644\u0627\u062c \u0644\u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a<\/a><\/li><li><a href=\"#the-role-of-dmd-associations-in-treatment-access\">\u062f\u0648\u0631 \u062c\u0645\u0639\u064a\u0627\u062a \u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0627\u0644\u062f\u0648\u0634\u064a\u0646\u064a \u0641\u064a \u0627\u0644\u0648\u0635\u0648\u0644 \u0625\u0644\u0649 \u0627\u0644\u0639\u0644\u0627\u062c<\/a><\/li><li><a href=\"#families-and-the-burden-of-access\">\u0627\u0644\u0639\u0627\u0626\u0644\u0627\u062a \u0648\u0639\u0628\u0621 \u0627\u0644\u0648\u0635\u0648\u0644<\/a><\/li><li><a href=\"#clinical-evidence-supporting-early-and-equitable-access\">\u0627\u0644\u0623\u062f\u0644\u0629 \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629 \u0627\u0644\u062a\u064a \u062a\u062f\u0639\u0645 \u0627\u0644\u0648\u0635\u0648\u0644 \u0627\u0644\u0645\u0628\u0643\u0631 \u0648\u0627\u0644\u0639\u0627\u062f\u0644<\/a><\/li><li><a href=\"#ethical-imperative-access-as-a-human-right\">\u0627\u0644\u0636\u0631\u0648\u0631\u0629 \u0627\u0644\u0623\u062e\u0644\u0627\u0642\u064a\u0629: \u0627\u0644\u0648\u0635\u0648\u0644 \u0643\u062d\u0642 \u0645\u0646 \u062d\u0642\u0648\u0642 \u0627\u0644\u0625\u0646\u0633\u0627\u0646<\/a><\/li><li><a href=\"#solutions-to-improve-duchenne-muscular-dystrophy-treatment-access\">\u062d\u0644\u0648\u0644 \u0644\u062a\u062d\u0633\u064a\u0646 \u0627\u0644\u0648\u0635\u0648\u0644 \u0625\u0644\u0649 \u0639\u0644\u0627\u062c \u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a<\/a><\/li><li><a href=\"#final-thoughts\">\u0627\u0644\u0623\u0641\u0643\u0627\u0631 \u0627\u0644\u0646\u0647\u0627\u0626\u064a\u0629<\/a><\/li><\/ul><\/nav><\/div>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"what-is-duchenne-muscular-dystrophy\">\u0645\u0627 \u0647\u0648 \u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a\u061f<\/h2>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"genetic-basis-and-disease-mechanism\">\u0627\u0644\u0623\u0633\u0627\u0633 \u0627\u0644\u062c\u064a\u0646\u064a \u0648\u0622\u0644\u064a\u0629 \u0627\u0644\u0645\u0631\u0636<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u064a\u0646\u062a\u062c \u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a \u0639\u0646 \u0637\u0641\u0631\u0627\u062a \u0641\u064a \u062c\u064a\u0646 \u0627\u0644\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0627\u0644\u0645\u0648\u062c\u0648\u062f \u0639\u0644\u0649 \u0627\u0644\u0643\u0631\u0648\u0645\u0648\u0633\u0648\u0645 X. \u0648\u064a\u0624\u062f\u064a \u063a\u064a\u0627\u0628 \u0627\u0644\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0625\u0644\u0649 \u0636\u0645\u0648\u0631 \u0639\u0636\u0644\u064a \u062a\u062f\u0631\u064a\u062c\u064a\u060c \u0648\u0627\u0644\u062a\u0647\u0627\u0628 \u0645\u0632\u0645\u0646\u060c \u0648\u0627\u0633\u062a\u0628\u062f\u0627\u0644 \u0646\u0633\u064a\u062c \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0641\u064a \u0646\u0647\u0627\u064a\u0629 \u0627\u0644\u0645\u0637\u0627\u0641 \u0628\u0627\u0644\u062f\u0647\u0648\u0646 \u0648\u0627\u0644\u062a\u0644\u064a\u0641. \u0627\u0642\u0631\u0623 \u0627\u0644\u0645\u0632\u064a\u062f:\u00a0<a href=\"https:\/\/dmdwarrior.com\/ar\/what-is-duchenne\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u0645\u0627 \u0647\u0648 \u062f\u0648\u0634\u064a\u0646\u061f<\/a><\/p>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"clinical-progression-and-outcomes\">\u0627\u0644\u062a\u0637\u0648\u0631 \u0627\u0644\u0633\u0631\u064a\u0631\u064a \u0648\u0627\u0644\u0646\u062a\u0627\u0626\u062c<\/h3>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u0628\u062f\u0627\u064a\u0629 \u0638\u0647\u0648\u0631 \u0627\u0644\u0623\u0639\u0631\u0627\u0636: \u0645\u0646 \u0639\u0645\u0631 \u0633\u0646\u062a\u064a\u0646 \u0625\u0644\u0649 \u062e\u0645\u0633 \u0633\u0646\u0648\u0627\u062a<\/li>\n\n\n\n<li>\u0641\u0642\u062f\u0627\u0646 \u0627\u0644\u0642\u062f\u0631\u0629 \u0639\u0644\u0649 \u0627\u0644\u0645\u0634\u064a: \u062d\u0648\u0627\u0644\u064a 10-12 \u0633\u0646\u0629<\/li>\n\n\n\n<li>\u0627\u0639\u062a\u0644\u0627\u0644 \u0639\u0636\u0644\u0629 \u0627\u0644\u0642\u0644\u0628 \u0648\u0627\u0644\u0641\u0634\u0644 \u0627\u0644\u062a\u0646\u0641\u0633\u064a: \u0627\u0644\u0645\u0631\u0627\u0647\u0642\u0629<\/li>\n\n\n\n<li>\u0645\u062a\u0648\u0633\u0637 \u0627\u0644\u0639\u0645\u0631 \u0627\u0644\u0645\u062a\u0648\u0642\u0639: \u062a\u062d\u0633\u0646 \u0628\u0634\u0643\u0644 \u0645\u0644\u062d\u0648\u0638 \u0645\u0639 \u0627\u0644\u0631\u0639\u0627\u064a\u0629\u060c \u0648\u0644\u0643\u0646\u0647 \u0644\u0627 \u064a\u0632\u0627\u0644 \u0645\u062d\u062f\u0648\u062f\u064b\u0627<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\"><a href=\"https:\/\/pubmed.ncbi.nlm.nih.gov\/19945913\/\" target=\"_blank\" rel=\"noopener\">\u0648\u0641\u0642\u064b\u0627 \u0644\u0628\u0648\u0634\u0628\u064a \u0648\u0622\u062e\u0631\u0648\u0646.<\/a> (2010)\u060c \u064a\u0645\u0643\u0646 \u0644\u0644\u062a\u062f\u062e\u0644 \u0627\u0644\u0645\u0628\u0643\u0631 \u0648\u0627\u0644\u0625\u062f\u0627\u0631\u0629 \u0645\u062a\u0639\u062f\u062f\u0629 \u0627\u0644\u062a\u062e\u0635\u0635\u0627\u062a \u0623\u0646 \u064a\u062d\u0633\u0646\u0627 \u0628\u0634\u0643\u0644 \u0643\u0628\u064a\u0631 \u0645\u0646 \u0641\u0631\u0635 \u0627\u0644\u0628\u0642\u0627\u0621 \u0639\u0644\u0649 \u0642\u064a\u062f \u0627\u0644\u062d\u064a\u0627\u0629 \u0648\u0646\u0648\u0639\u064a\u0629 \u0627\u0644\u062d\u064a\u0627\u0629.<br><br>\u064a\u062a\u0639\u0644\u0645 \u0623\u0643\u062b\u0631: <a href=\"https:\/\/dmdwarrior.com\/ar\/life-expectancy-in-duchenne-muscular-dystrophy\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u0645\u062a\u0648\u0633\u0637 \u0627\u0644\u0639\u0645\u0631 \u0627\u0644\u0645\u062a\u0648\u0642\u0639 \u0641\u064a \u062f\u0648\u0634\u064a\u0646<\/a><\/p>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"the-current-landscape-of-duchenne-muscular-dystrophy-treatment-access\">\u0627\u0644\u0648\u0636\u0639 \u0627\u0644\u062d\u0627\u0644\u064a \u0644\u0625\u0645\u0643\u0627\u0646\u064a\u0629 \u0627\u0644\u0648\u0635\u0648\u0644 \u0625\u0644\u0649 \u0639\u0644\u0627\u062c \u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a<\/h2>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"available-therapies\">\u0627\u0644\u0639\u0644\u0627\u062c\u0627\u062a \u0627\u0644\u0645\u062a\u0627\u062d\u0629<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u064a\u0634\u0645\u0644 \u0627\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u062d\u062f\u064a\u062b \u0644\u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0627\u0644\u062f\u0648\u0634\u064a\u0646\u064a \u0645\u0627 \u064a\u0644\u064a:<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u0627\u0644\u0643\u0648\u0631\u062a\u064a\u0643\u0648\u0633\u062a\u064a\u0631\u0648\u064a\u062f\u0627\u062a (\u0627\u0644\u0645\u0639\u064a\u0627\u0631 \u0627\u0644\u0639\u0644\u0627\u062c\u064a)<\/li>\n\n\n\n<li>\u062f\u0639\u0645 \u0627\u0644\u0642\u0644\u0628 \u0648\u0627\u0644\u062c\u0647\u0627\u0632 \u0627\u0644\u062a\u0646\u0641\u0633\u064a<\/li>\n\n\n\n<li>\u0627\u0644\u0639\u0644\u0627\u062c\u0627\u062a \u0627\u0644\u062a\u064a \u062a\u062a\u062e\u0637\u0649 \u0627\u0644\u0625\u0643\u0633\u0648\u0646 (\u0627\u0644\u0645\u062e\u0635\u0635\u0629 \u0644\u0644\u0637\u0641\u0631\u0629)<\/li>\n\n\n\n<li>\u0627\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u062c\u064a\u0646\u064a (\u0646\u0627\u0634\u0626\u060c \u0639\u0627\u0644\u064a \u0627\u0644\u062a\u0643\u0644\u0641\u0629)<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\">\u064a\u062a\u0639\u0644\u0645 \u0623\u0643\u062b\u0631: <a href=\"https:\/\/dmdwarrior.com\/ar\/category\/care-guidelines\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u0625\u0631\u0634\u0627\u062f\u0627\u062a \u0631\u0639\u0627\u064a\u0629 \u0645\u0631\u0636\u0649 \u062f\u0648\u0634\u064a\u0646<\/a><\/p>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"the-access-gap\">\u0641\u062c\u0648\u0629 \u0627\u0644\u0648\u0635\u0648\u0644<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u0639\u0644\u0649 \u0627\u0644\u0631\u063a\u0645 \u0645\u0646 \u0648\u062c\u0648\u062f \u0627\u0644\u0639\u0644\u0627\u062c\u0627\u062a\u060c \u0625\u0644\u0627 \u0623\u0646 \u0627\u0644\u0648\u0635\u0648\u0644 \u0625\u0644\u064a\u0647\u0627 \u064a\u062a\u062d\u062f\u062f \u0628\u0645\u0627 \u064a\u0644\u064a:<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u0633\u064a\u0627\u0633\u0627\u062a \u0627\u0644\u062a\u0639\u0648\u064a\u0636 \u0627\u0644\u0648\u0637\u0646\u064a\u0629<\/li>\n\n\n\n<li>\u0627\u0644\u0628\u0646\u064a\u0629 \u0627\u0644\u062a\u062d\u062a\u064a\u0629 \u0644\u0644\u0631\u0639\u0627\u064a\u0629 \u0627\u0644\u0635\u062d\u064a\u0629<\/li>\n\n\n\n<li>\u0623\u0633\u0639\u0627\u0631 \u0627\u0644\u0623\u062f\u0648\u064a\u0629 \u0648\u062a\u0648\u0627\u0641\u0631\u0647\u0627<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\">\u062a\u0633\u0644\u0637 \u0645\u0646\u0638\u0645\u0629 \u0627\u0644\u0635\u062d\u0629 \u0627\u0644\u0639\u0627\u0644\u0645\u064a\u0629 \u0627\u0644\u0636\u0648\u0621 \u0639\u0644\u0649 \u0627\u0644\u0623\u0645\u0631\u0627\u0636 \u0627\u0644\u0646\u0627\u062f\u0631\u0629 \u0628\u0627\u0639\u062a\u0628\u0627\u0631\u0647\u0627 \u0648\u0627\u062d\u062f\u0629 \u0645\u0646 \u0623\u0643\u062b\u0631 \u0627\u0644\u0645\u062c\u0627\u0644\u0627\u062a \u0625\u0647\u0645\u0627\u0644\u0627\u064b \u0641\u064a \u0645\u062c\u0627\u0644 \u0627\u0644\u0639\u062f\u0627\u0644\u0629 \u0627\u0644\u0635\u062d\u064a\u0629 \u0627\u0644\u0639\u0627\u0644\u0645\u064a\u0629.<\/p>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"why-duchenne-muscular-dystrophy-treatment-access-is-so-unequal\">\u0644\u0645\u0627\u0630\u0627 \u064a\u062a\u0641\u0627\u0648\u062a \u0627\u0644\u0648\u0635\u0648\u0644 \u0625\u0644\u0649 \u0639\u0644\u0627\u062c \u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a \u0625\u0644\u0649 \u062d\u062f \u0643\u0628\u064a\u0631\u061f<\/h2>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"economic-barriers\">\u0627\u0644\u0639\u0648\u0627\u0626\u0642 \u0627\u0644\u0627\u0642\u062a\u0635\u0627\u062f\u064a\u0629<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u062a\u064f\u0639\u062f \u0639\u0644\u0627\u062c\u0627\u062a \u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0627\u0644\u062f\u0648\u0634\u064a\u0646\u064a \u0645\u0646 \u0628\u064a\u0646 \u0623\u063a\u0644\u0649 \u0627\u0644\u0639\u0644\u0627\u062c\u0627\u062a \u0641\u064a \u0645\u062c\u0627\u0644 \u0627\u0644\u0637\u0628:<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u0627\u0644\u0623\u062f\u0648\u064a\u0629 \u0627\u0644\u062a\u064a \u062a\u062a\u062e\u0637\u0649 \u0627\u0644\u0625\u0643\u0633\u0648\u0646: $300,000\u2013$1M \u0633\u0646\u0648\u064a\u0627\u064b<\/li>\n\n\n\n<li><a href=\"https:\/\/dmdwarrior.com\/ar\/elevidys-gene-therapy-efficacy-in-dmd\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u0627\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u062c\u064a\u0646\u064a: &gt;$2.9M \u0644\u0643\u0644 \u0639\u0644\u0627\u062c<\/a><\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u062a\u0624\u062f\u064a \u0647\u0630\u0647 \u0627\u0644\u062a\u0643\u0627\u0644\u064a\u0641 \u0625\u0644\u0649 \u0627\u0633\u062a\u0628\u0639\u0627\u062f \u0645\u0646\u0647\u062c\u064a\u060c \u0644\u0627 \u0633\u064a\u0645\u0627 \u0641\u064a \u0627\u0644\u0628\u0644\u062f\u0627\u0646 \u0630\u0627\u062a \u0627\u0644\u062f\u062e\u0644 \u0627\u0644\u0645\u0646\u062e\u0641\u0636 \u0648\u0627\u0644\u0645\u062a\u0648\u0633\u0637.<\/strong><\/p>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"regulatory-fragmentation\">\u0627\u0644\u062a\u062c\u0632\u0626\u0629 \u0627\u0644\u062a\u0646\u0638\u064a\u0645\u064a\u0629<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u062d\u062a\u0649 \u0628\u0639\u062f \u0645\u0648\u0627\u0641\u0642\u0629 \u0648\u0643\u0627\u0644\u0627\u062a \u0645\u062b\u0644 \u0625\u062f\u0627\u0631\u0629 \u0627\u0644\u063a\u0630\u0627\u0621 \u0648\u0627\u0644\u062f\u0648\u0627\u0621 \u0627\u0644\u0623\u0645\u0631\u064a\u0643\u064a\u0629:<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u0642\u062f \u062a\u062a\u0623\u062e\u0631 \u0627\u0644\u0645\u0648\u0627\u0641\u0642\u0627\u062a \u0627\u0644\u0648\u0637\u0646\u064a\u0629<\/li>\n\n\n\n<li>\u0642\u062f \u062a\u0633\u062a\u063a\u0631\u0642 \u0642\u0631\u0627\u0631\u0627\u062a \u0627\u0644\u062a\u0639\u0648\u064a\u0636 \u0633\u0646\u0648\u0627\u062a<\/li>\n\n\n\n<li>\u064a\u0628\u0642\u0649 \u0627\u0644\u0645\u0631\u0636\u0649 \u062f\u0648\u0646 \u0639\u0644\u0627\u062c \u062e\u0644\u0627\u0644 \u0641\u062a\u0631\u0627\u062a \u0627\u0644\u062a\u0623\u062e\u064a\u0631.<\/li>\n<\/ul>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"geographic-inequality\">\u0639\u062f\u0645 \u0627\u0644\u0645\u0633\u0627\u0648\u0627\u0629 \u0627\u0644\u062c\u063a\u0631\u0627\u0641\u064a\u0629<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u0627\u0644\u0645\u0631\u0636\u0649 \u0641\u064a \u0623\u0645\u0631\u064a\u0643\u0627 \u0627\u0644\u0634\u0645\u0627\u0644\u064a\u0629 \u0648\u0623\u0648\u0631\u0648\u0628\u0627 \u0627\u0644\u063a\u0631\u0628\u064a\u0629:<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u0627\u0644\u0648\u0635\u0648\u0644 \u0625\u0644\u0649 \u0627\u0644\u062a\u062c\u0627\u0631\u0628 \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629<\/li>\n\n\n\n<li>\u0627\u0644\u062d\u0635\u0648\u0644 \u0639\u0644\u0649 \u0627\u0644\u0645\u0648\u0627\u0641\u0642\u0627\u062a \u0627\u0644\u0645\u0628\u0643\u0631\u0629<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\">\u0627\u0644\u0645\u0631\u0636\u0649 \u0641\u064a \u0623\u0645\u0627\u0643\u0646 \u0623\u062e\u0631\u0649:<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u0645\u0648\u0627\u062c\u0647\u0629 \u062a\u0623\u062e\u0631 \u0627\u0644\u062a\u0634\u062e\u064a\u0635<\/li>\n\n\n\n<li>\u0627\u0646\u0639\u062f\u0627\u0645 \u0627\u0644\u0648\u0635\u0648\u0644 \u0628\u0634\u0643\u0644 \u0643\u0627\u0645\u0644<\/li>\n<\/ul>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"pharmaceutical-companies-and-duchenne-muscular-dystrophy-treatment-access\">\u0634\u0631\u0643\u0627\u062a \u0627\u0644\u0623\u062f\u0648\u064a\u0629 \u0648\u0625\u0645\u0643\u0627\u0646\u064a\u0629 \u0627\u0644\u062d\u0635\u0648\u0644 \u0639\u0644\u0649 \u0639\u0644\u0627\u062c \u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a<\/h2>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"pricing-strategies-and-market-exclusivity\">\u0627\u0633\u062a\u0631\u0627\u062a\u064a\u062c\u064a\u0627\u062a \u0627\u0644\u062a\u0633\u0639\u064a\u0631 \u0648\u062d\u0635\u0631\u064a\u0629 \u0627\u0644\u0633\u0648\u0642<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u062a\u0628\u0631\u0631 \u0634\u0631\u0643\u0627\u062a \u0627\u0644\u0623\u062f\u0648\u064a\u0629 \u0627\u0631\u062a\u0641\u0627\u0639 \u0623\u0633\u0639\u0627\u0631\u0647\u0627 \u0645\u0646 \u062e\u0644\u0627\u0644:<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u062a\u0643\u0627\u0644\u064a\u0641 \u0627\u0644\u0628\u062d\u062b \u0648\u0627\u0644\u062a\u0637\u0648\u064a\u0631<\/li>\n\n\n\n<li>\u0623\u0639\u062f\u0627\u062f \u0627\u0644\u0645\u0631\u0636\u0649 \u0627\u0644\u0635\u063a\u064a\u0631\u0629<\/li>\n\n\n\n<li>\u0645\u062e\u0627\u0637\u0631 \u0627\u0644\u0627\u0628\u062a\u0643\u0627\u0631<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\">\u0648\u0645\u0639 \u0630\u0644\u0643\u060c \u062a\u0634\u064a\u0631 \u0627\u0644\u0623\u062f\u0644\u0629 \u0625\u0644\u0649 \u0645\u0627 \u064a\u0644\u064a:<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u063a\u0627\u0644\u0628\u0627\u064b \u0645\u0627 \u064a\u062f\u0639\u0645 \u0627\u0644\u062a\u0645\u0648\u064a\u0644 \u0627\u0644\u0639\u0627\u0645 \u0627\u0644\u0623\u0628\u062d\u0627\u062b \u0627\u0644\u0645\u0628\u0643\u0631\u0629<\/li>\n\n\n\n<li>\u064a\u0645\u0643\u0646 \u0623\u0646 \u062a\u0643\u0648\u0646 \u0647\u0648\u0627\u0645\u0634 \u0627\u0644\u0631\u0628\u062d \u0643\u0628\u064a\u0631\u0629<\/li>\n\n\n\n<li><strong>\u064a\u062a\u0645 \u062a\u062d\u0633\u064a\u0646 \u0627\u0633\u062a\u0631\u0627\u062a\u064a\u062c\u064a\u0627\u062a \u0627\u0644\u062a\u0633\u0639\u064a\u0631 \u0644\u062a\u062d\u0642\u064a\u0642 \u0623\u0642\u0635\u0649 \u0642\u062f\u0631 \u0645\u0646 \u0627\u0644\u0625\u064a\u0631\u0627\u062f\u0627\u062a\u060c \u0648\u0644\u064a\u0633 \u0623\u0642\u0635\u0649 \u0642\u062f\u0631 \u0645\u0646 \u0627\u0644\u0648\u0635\u0648\u0644.<\/strong><\/li>\n<\/ul>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"ethical-concerns\">\u0627\u0644\u0645\u062e\u0627\u0648\u0641 \u0627\u0644\u0623\u062e\u0644\u0627\u0642\u064a\u0629<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u0639\u0646\u062f\u0645\u0627 \u062a\u0643\u0648\u0646 \u0623\u0633\u0639\u0627\u0631 \u0627\u0644\u0639\u0644\u0627\u062c\u0627\u062a \u0627\u0644\u0645\u0646\u0642\u0630\u0629 \u0644\u0644\u062d\u064a\u0627\u0629 \u0628\u0627\u0647\u0638\u0629 \u0644\u0644\u063a\u0627\u064a\u0629\u060c \u0641\u0625\u0646 \u0627\u0644\u0642\u0636\u064a\u0629 \u062a\u062a\u062d\u0648\u0644 \u0645\u0646 \u0627\u0644\u0627\u0642\u062a\u0635\u0627\u062f \u0625\u0644\u0649 \u0627\u0644\u0623\u062e\u0644\u0627\u0642.<\/p>\n\n\n\n<blockquote class=\"wp-block-quote is-layout-flow wp-block-quote-is-layout-flow\">\n<p class=\"wp-block-paragraph\">\u0625\u0646 \u0627\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u0645\u0648\u062c\u0648\u062f \u0648\u0644\u0643\u0646\u0647 \u063a\u064a\u0631 \u0645\u062a\u0627\u062d \u0644\u064a\u0633 \u0627\u0628\u062a\u0643\u0627\u0631\u0627\u064b\u060c \u0628\u0644 \u0647\u0648 \u0625\u0642\u0635\u0627\u0621.<\/p>\n<\/blockquote>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"what-pharmaceutical-companies-should-do\">\u0645\u0627 \u0627\u0644\u0630\u064a \u064a\u0646\u0628\u063a\u064a \u0639\u0644\u0649 \u0634\u0631\u0643\u0627\u062a \u0627\u0644\u0623\u062f\u0648\u064a\u0629 \u0641\u0639\u0644\u0647\u061f<\/h3>\n\n\n\n<h4 class=\"wp-block-heading\" id=\"implement-tiered-pricing\">\u062a\u0637\u0628\u064a\u0642 \u0646\u0638\u0627\u0645 \u0627\u0644\u062a\u0633\u0639\u064a\u0631 \u0627\u0644\u0645\u062a\u062f\u0631\u062c<\/h4>\n\n\n\n<p class=\"wp-block-paragraph\">\u0642\u0645 \u0628\u062a\u0639\u062f\u064a\u0644 \u0627\u0644\u0623\u0633\u0639\u0627\u0631 \u0628\u0646\u0627\u0621\u064b \u0639\u0644\u0649 \u0645\u0633\u062a\u0648\u064a\u0627\u062a \u0627\u0644\u062f\u062e\u0644 \u0627\u0644\u0642\u0648\u0645\u064a.<\/p>\n\n\n\n<h4 class=\"wp-block-heading\" id=\"expand-global-access-programs\">\u062a\u0648\u0633\u064a\u0639 \u0628\u0631\u0627\u0645\u062c \u0627\u0644\u0648\u0635\u0648\u0644 \u0627\u0644\u0639\u0627\u0644\u0645\u064a<\/h4>\n\n\n\n<p class=\"wp-block-paragraph\">\u0636\u0645\u0627\u0646 \u0639\u062f\u0645 \u0627\u0642\u062a\u0635\u0627\u0631 \u0627\u0644\u0627\u0633\u062a\u062e\u062f\u0627\u0645 \u0627\u0644\u0631\u062d\u064a\u0645 \u0639\u0644\u0649 \u0645\u0646\u0627\u0637\u0642 \u0645\u062d\u062f\u062f\u0629.<\/p>\n\n\n\n<h4 class=\"wp-block-heading\" id=\"increase-transparency\">\u0632\u064a\u0627\u062f\u0629 \u0627\u0644\u0634\u0641\u0627\u0641\u064a\u0629<\/h4>\n\n\n\n<p class=\"wp-block-paragraph\">\u0623\u0641\u0635\u062d \u0639\u0646 \u0627\u0644\u062a\u0643\u0627\u0644\u064a\u0641 \u0627\u0644\u062d\u0642\u064a\u0642\u064a\u0629 \u0644\u0644\u0628\u062d\u062b \u0648\u0627\u0644\u062a\u0637\u0648\u064a\u0631 \u0648\u0627\u0644\u0625\u0646\u062a\u0627\u062c.<\/p>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"government-responsibility-in-duchenne-muscular-dystrophy-treatment-access\">\u0645\u0633\u0624\u0648\u0644\u064a\u0629 \u0627\u0644\u062d\u0643\u0648\u0645\u0629 \u0641\u064a \u062a\u0648\u0641\u064a\u0631 \u0627\u0644\u0639\u0644\u0627\u062c \u0644\u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a<\/h2>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"budget-priorities\">\u0623\u0648\u0644\u0648\u064a\u0627\u062a \u0627\u0644\u0645\u064a\u0632\u0627\u0646\u064a\u0629<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u062a\u062e\u0635\u0635 \u0627\u0644\u062d\u0643\u0648\u0645\u0627\u062a \u0645\u0644\u064a\u0627\u0631\u0627\u062a \u0627\u0644\u062f\u0648\u0644\u0627\u0631\u0627\u062a \u0644\u0644\u062f\u0641\u0627\u0639 \u0628\u064a\u0646\u0645\u0627:<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u0644\u0627 \u064a\u0632\u0627\u0644 \u062a\u0645\u0648\u064a\u0644 \u0627\u0644\u0623\u0645\u0631\u0627\u0636 \u0627\u0644\u0646\u0627\u062f\u0631\u0629 \u0636\u0626\u064a\u0644\u0627\u064b<\/li>\n\n\n\n<li>\u062a\u0633\u062a\u062b\u0646\u064a \u0623\u0646\u0638\u0645\u0629 \u0627\u0644\u0633\u062f\u0627\u062f \u0627\u0644\u0639\u0644\u0627\u062c\u0627\u062a \u0639\u0627\u0644\u064a\u0629 \u0627\u0644\u062a\u0643\u0644\u0641\u0629.<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u0647\u0630\u0627 \u064a\u0639\u0643\u0633 \u062e\u064a\u0627\u0631\u0627\u062a \u0627\u0644\u0633\u064a\u0627\u0633\u0629 \u0627\u0644\u0639\u0627\u0645\u0629\u060c \u0648\u0644\u064a\u0633 \u0646\u062f\u0631\u0629 \u0627\u0644\u0645\u0648\u0627\u0631\u062f.<\/strong><\/p>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"policy-failures\">\u0625\u062e\u0641\u0627\u0642\u0627\u062a \u0627\u0644\u0633\u064a\u0627\u0633\u0629<\/h3>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u062a\u0623\u062e\u0631 \u0642\u0631\u0627\u0631\u0627\u062a \u0627\u0644\u0633\u062f\u0627\u062f<\/li>\n\n\n\n<li>\u063a\u064a\u0627\u0628 \u0627\u0633\u062a\u0631\u0627\u062a\u064a\u062c\u064a\u0627\u062a \u0648\u0637\u0646\u064a\u0629 \u0644\u0644\u0623\u0645\u0631\u0627\u0636 \u0627\u0644\u0646\u0627\u062f\u0631\u0629<\/li>\n\n\n\n<li>\u0628\u0631\u0627\u0645\u062c \u0641\u062d\u0635 \u063a\u064a\u0631 \u0643\u0627\u0641\u064a\u0629<\/li>\n<\/ul>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"what-governments-should-do\">\u0645\u0627 \u064a\u0646\u0628\u063a\u064a \u0639\u0644\u0649 \u0627\u0644\u062d\u0643\u0648\u0645\u0627\u062a \u0641\u0639\u0644\u0647<\/h3>\n\n\n\n<h4 class=\"wp-block-heading\" id=\"establish-rare-disease-funds\">\u0625\u0646\u0634\u0627\u0621 \u0635\u0646\u0627\u062f\u064a\u0642 \u0644\u0644\u0623\u0645\u0631\u0627\u0636 \u0627\u0644\u0646\u0627\u062f\u0631\u0629<\/h4>\n\n\n\n<p class=\"wp-block-paragraph\">\u0645\u064a\u0632\u0627\u0646\u064a\u0627\u062a \u0645\u062e\u0635\u0635\u0629 \u0644\u0644\u0639\u0644\u0627\u062c\u0627\u062a \u0639\u0627\u0644\u064a\u0629 \u0627\u0644\u062a\u0643\u0644\u0641\u0629.<\/p>\n\n\n\n<h4 class=\"wp-block-heading\" id=\"accelerate-reimbursement-pathways\">\u062a\u0633\u0631\u064a\u0639 \u0645\u0633\u0627\u0631\u0627\u062a \u0627\u0644\u0633\u062f\u0627\u062f<\/h4>\n\n\n\n<p class=\"wp-block-paragraph\">\u062a\u0642\u0644\u064a\u0644 \u0627\u0644\u062a\u0623\u062e\u064a\u0631\u0627\u062a \u0628\u064a\u0646 \u0627\u0644\u0645\u0648\u0627\u0641\u0642\u0629 \u0648\u0627\u0644\u0648\u0635\u0648\u0644.<\/p>\n\n\n\n<h4 class=\"wp-block-heading\" id=\"implement-newborn-screening\">\u062a\u0637\u0628\u064a\u0642 \u0641\u062d\u0635 \u062d\u062f\u064a\u062b\u064a \u0627\u0644\u0648\u0644\u0627\u062f\u0629<\/h4>\n\n\n\n<p class=\"wp-block-paragraph\">\u0627\u0644\u062a\u0634\u062e\u064a\u0635 \u0627\u0644\u0645\u0628\u0643\u0631 \u064a\u064f\u0645\u0643\u0651\u0646 \u0645\u0646 \u0627\u0644\u062a\u062f\u062e\u0644 \u0627\u0644\u0645\u0628\u0643\u0631.<\/p>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"the-role-of-dmd-associations-in-treatment-access\">\u062f\u0648\u0631 \u062c\u0645\u0639\u064a\u0627\u062a \u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0627\u0644\u062f\u0648\u0634\u064a\u0646\u064a \u0641\u064a \u0627\u0644\u0648\u0635\u0648\u0644 \u0625\u0644\u0649 \u0627\u0644\u0639\u0644\u0627\u062c<\/h2>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"advocacy-achievements\">\u0625\u0646\u062c\u0627\u0632\u0627\u062a \u0641\u064a \u0645\u062c\u0627\u0644 \u0627\u0644\u0645\u0646\u0627\u0635\u0631\u0629<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u0644\u062f\u0649 \u0645\u0646\u0638\u0645\u0627\u062a \u0627\u0644\u0645\u0631\u0636\u0649 \u0645\u0627 \u064a\u0644\u064a:<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u0632\u064a\u0627\u062f\u0629 \u0627\u0644\u0648\u0639\u064a<\/li>\n\n\n\n<li>\u062a\u0645\u0648\u064a\u0644 \u0627\u0644\u0628\u062d\u062b \u0627\u0644\u0645\u062f\u0639\u0648\u0645<\/li>\n\n\n\n<li>\u0627\u0644\u0645\u0633\u0627\u0631\u0627\u062a \u0627\u0644\u062a\u0646\u0638\u064a\u0645\u064a\u0629 \u0627\u0644\u0645\u062a\u0623\u062b\u0631\u0629<\/li>\n<\/ul>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"limitations-and-challenges\">\u0627\u0644\u0642\u064a\u0648\u062f \u0648\u0627\u0644\u062a\u062d\u062f\u064a\u0627\u062a<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u062a\u0648\u0627\u062c\u0647 \u0628\u0639\u0636 \u0627\u0644\u0645\u0646\u0638\u0645\u0627\u062a \u0645\u0627 \u064a\u0644\u064a:<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u0627\u0644\u0639\u0644\u0627\u0642\u0627\u062a \u0627\u0644\u0645\u0627\u0644\u064a\u0629 \u0645\u0639 \u0627\u0644\u0635\u0646\u0627\u0639\u0629<\/li>\n\n\n\n<li>\u062a\u0623\u062b\u064a\u0631 \u0645\u062d\u062f\u0648\u062f \u0639\u0644\u0649 \u0627\u0644\u0633\u064a\u0627\u0633\u0627\u062a<\/li>\n\n\n\n<li>\u0627\u0644\u062a\u0631\u0643\u064a\u0632 \u0627\u0644\u0645\u0641\u0631\u0637 \u0639\u0644\u0649 \u0627\u0644\u0648\u0639\u064a \u0639\u0644\u0649 \u062d\u0633\u0627\u0628 \u0627\u0644\u0648\u0635\u0648\u0644<\/li>\n<\/ul>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"what-associations-should-do\">\u0645\u0627 \u064a\u0646\u0628\u063a\u064a \u0639\u0644\u0649 \u0627\u0644\u062c\u0645\u0639\u064a\u0627\u062a \u0641\u0639\u0644\u0647<\/h3>\n\n\n\n<h4 class=\"wp-block-heading\" id=\"strengthen-policy-advocacy\">\u062a\u0639\u0632\u064a\u0632 \u062c\u0647\u0648\u062f \u0627\u0644\u0645\u0646\u0627\u0635\u0631\u0629 \u0627\u0644\u0633\u064a\u0627\u0633\u064a\u0629<\/h4>\n\n\n\n<p class=\"wp-block-paragraph\">\u062d\u0648\u0651\u0644 \u0627\u0644\u062a\u0631\u0643\u064a\u0632 \u0646\u062d\u0648 \u0627\u0644\u062a\u063a\u064a\u064a\u0631 \u0627\u0644\u0645\u0646\u0647\u062c\u064a.<\/p>\n\n\n\n<h4 class=\"wp-block-heading\" id=\"maintain-independence\">\u0627\u0644\u062d\u0641\u0627\u0638 \u0639\u0644\u0649 \u0627\u0644\u0627\u0633\u062a\u0642\u0644\u0627\u0644\u064a\u0629<\/h4>\n\n\n\n<p class=\"wp-block-paragraph\">\u062a\u062c\u0646\u0628 \u062a\u0636\u0627\u0631\u0628 \u0627\u0644\u0645\u0635\u0627\u0644\u062d.<\/p>\n\n\n\n<h4 class=\"wp-block-heading\" id=\"build-global-coalitions\">\u0628\u0646\u0627\u0621 \u062a\u062d\u0627\u0644\u0641\u0627\u062a \u0639\u0627\u0644\u0645\u064a\u0629<\/h4>\n\n\n\n<p class=\"wp-block-paragraph\">\u062a\u0646\u0633\u064a\u0642 \u062c\u0647\u0648\u062f \u0627\u0644\u0645\u0646\u0627\u0635\u0631\u0629 \u0627\u0644\u062f\u0648\u0644\u064a\u0629.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u064a\u062a\u0639\u0644\u0645 \u0623\u0643\u062b\u0631: <a href=\"https:\/\/dmdwarrior.com\/ar\/dmd-donations-how-associations-use-donations\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u0623\u0632\u0645\u0629 \u0627\u0644\u0645\u0633\u0627\u0621\u0644\u0629 \u0641\u064a \u062c\u0645\u0639\u064a\u0627\u062a \u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a (DMD)<\/a><\/p>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"families-and-the-burden-of-access\">\u0627\u0644\u0639\u0627\u0626\u0644\u0627\u062a \u0648\u0639\u0628\u0621 \u0627\u0644\u0648\u0635\u0648\u0644<\/h2>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"navigating-complex-systems\">\u0627\u0644\u062a\u0646\u0642\u0644 \u0641\u064a \u0627\u0644\u0623\u0646\u0638\u0645\u0629 \u0627\u0644\u0645\u0639\u0642\u062f\u0629<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u064a\u062c\u0628 \u0639\u0644\u0649 \u0627\u0644\u0639\u0627\u0626\u0644\u0627\u062a:<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u062a\u0641\u0633\u064a\u0631 \u0627\u0644\u062a\u0642\u0627\u0631\u064a\u0631 \u0627\u0644\u062c\u064a\u0646\u064a\u0629<\/li>\n\n\n\n<li>\u0645\u0646\u0627\u0635\u0631\u0629 \u0627\u0644\u0639\u0644\u0627\u062c<\/li>\n\n\n\n<li>\u062a\u0623\u0645\u064a\u0646 \u0627\u0644\u062a\u0645\u0648\u064a\u0644<\/li>\n<\/ul>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"the-rise-of-crowdfunding\">\u0635\u0639\u0648\u062f \u0627\u0644\u062a\u0645\u0648\u064a\u0644 \u0627\u0644\u062c\u0645\u0627\u0639\u064a<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u062a\u0639\u062a\u0645\u062f \u0627\u0644\u0639\u062f\u064a\u062f \u0645\u0646 \u0627\u0644\u0639\u0627\u0626\u0644\u0627\u062a \u0639\u0644\u0649:<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u0627\u0644\u062a\u0628\u0631\u0639\u0627\u062a \u0627\u0644\u0639\u0627\u0645\u0629<\/li>\n\n\n\n<li>\u062d\u0645\u0644\u0627\u062a \u0648\u0633\u0627\u0626\u0644 \u0627\u0644\u062a\u0648\u0627\u0635\u0644 \u0627\u0644\u0627\u062c\u062a\u0645\u0627\u0639\u064a<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\">\u0648\u0647\u0630\u0627 \u064a\u062e\u0644\u0642 \u0639\u062f\u0645 \u0645\u0633\u0627\u0648\u0627\u0629 \u0642\u0627\u0626\u0645\u0629 \u0639\u0644\u0649 \u0623\u0633\u0627\u0633 \u0627\u0644\u0638\u0647\u0648\u0631 \u0628\u062f\u0644\u0627\u064b \u0645\u0646 \u0627\u0644\u062d\u0627\u062c\u0629.<\/p>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"what-families-can-do\">\u0645\u0627 \u0627\u0644\u0630\u064a \u064a\u0645\u0643\u0646 \u0644\u0644\u0639\u0627\u0626\u0644\u0627\u062a \u0641\u0639\u0644\u0647\u061f<\/h3>\n\n\n\n<h4 class=\"wp-block-heading\" id=\"collective-advocacy\">\u0627\u0644\u0645\u0646\u0627\u0635\u0631\u0629 \u0627\u0644\u062c\u0645\u0627\u0639\u064a\u0629<\/h4>\n\n\n\n<p class=\"wp-block-paragraph\">\u0627\u0646\u0636\u0645 \u0625\u0644\u0649 \u0627\u0644\u0634\u0628\u0643\u0627\u062a \u0644\u062a\u0636\u062e\u064a\u0645 \u0627\u0644\u0623\u0635\u0648\u0627\u062a.<\/p>\n\n\n\n<h4 class=\"wp-block-heading\" id=\"demand-policy-change\">\u062a\u063a\u064a\u064a\u0631 \u0633\u064a\u0627\u0633\u0629 \u0627\u0644\u0637\u0644\u0628<\/h4>\n\n\n\n<p class=\"wp-block-paragraph\">\u062d\u0648\u0651\u0644 \u0627\u0644\u062a\u0631\u0643\u064a\u0632 \u0645\u0646 \u0627\u0644\u0623\u0639\u0645\u0627\u0644 \u0627\u0644\u062e\u064a\u0631\u064a\u0629 \u0625\u0644\u0649 \u0627\u0644\u062d\u0642\u0648\u0642.<\/p>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"clinical-evidence-supporting-early-and-equitable-access\">\u0627\u0644\u0623\u062f\u0644\u0629 \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629 \u0627\u0644\u062a\u064a \u062a\u062f\u0639\u0645 \u0627\u0644\u0648\u0635\u0648\u0644 \u0627\u0644\u0645\u0628\u0643\u0631 \u0648\u0627\u0644\u0639\u0627\u062f\u0644<\/h2>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"key-studies\">\u062f\u0631\u0627\u0633\u0627\u062a \u0631\u0626\u064a\u0633\u064a\u0629<\/h3>\n\n\n\n<ul class=\"wp-block-list\">\n<li><strong><a href=\"https:\/\/www.cell.com\/molecular-therapy-family\/molecular-therapy\/fulltext\/S1525-0016(20)30664-X\" target=\"_blank\" rel=\"noreferrer noopener\">\u0645\u064a\u0646\u062f\u0644 \u062c\u064a\u0647 \u0622\u0631 \u0648\u0622\u062e\u0631\u0648\u0646 (2020)<\/a><\/strong> \u2013 \u0627\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u062c\u064a\u0646\u064a \u064a\u064f\u0638\u0647\u0631 \u062a\u062d\u0633\u0646\u0627\u064b \u0648\u0638\u064a\u0641\u064a\u0627\u064b<\/li>\n\n\n\n<li><strong><a href=\"https:\/\/www.thelancet.com\/journals\/laneur\/article\/PIIS1474-4422(18)30024-3\/abstract\" target=\"_blank\" rel=\"noreferrer noopener\">\u0628\u064a\u0631\u0646\u0643\u0631\u0627\u0646\u062a \u062f\u064a \u062c\u064a\u0647 \u0648\u0622\u062e\u0631\u0648\u0646 (2018)<\/a><\/strong> - \u0627\u0644\u0631\u0639\u0627\u064a\u0629 \u0645\u062a\u0639\u062f\u062f\u0629 \u0627\u0644\u062a\u062e\u0635\u0635\u0627\u062a \u062a\u062d\u0633\u0646 \u0641\u0631\u0635 \u0627\u0644\u0628\u0642\u0627\u0621 \u0639\u0644\u0649 \u0642\u064a\u062f \u0627\u0644\u062d\u064a\u0627\u0629<\/li>\n\n\n\n<li><strong>\u0628\u0648\u0634\u0628\u064a \u0643 \u0648\u0622\u062e\u0631\u0648\u0646 (2014)<\/strong> - \u0627\u0644\u062a\u0634\u062e\u064a\u0635 \u0648\u0627\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u0645\u0628\u0643\u0631\u0627\u0646 \u0623\u0645\u0631\u0627\u0646 \u0628\u0627\u0644\u063a\u0627 \u0627\u0644\u0623\u0647\u0645\u064a\u0629<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\">\u062a\u0624\u0643\u062f \u0647\u0630\u0647 \u0627\u0644\u062f\u0631\u0627\u0633\u0627\u062a \u0645\u0627 \u064a\u0644\u064a:<\/p>\n\n\n\n<blockquote class=\"wp-block-quote is-layout-flow wp-block-quote-is-layout-flow\">\n<p class=\"wp-block-paragraph\">\u064a\u0624\u062b\u0631 \u0627\u0644\u062d\u0635\u0648\u0644 \u0639\u0644\u0649 \u0627\u0644\u0639\u0644\u0627\u062c \u0628\u0634\u0643\u0644 \u0645\u0628\u0627\u0634\u0631 \u0639\u0644\u0649 \u0627\u0644\u0646\u062a\u0627\u0626\u062c.<\/p>\n<\/blockquote>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"ethical-imperative-access-as-a-human-right\">\u0627\u0644\u0636\u0631\u0648\u0631\u0629 \u0627\u0644\u0623\u062e\u0644\u0627\u0642\u064a\u0629: \u0627\u0644\u0648\u0635\u0648\u0644 \u0643\u062d\u0642 \u0645\u0646 \u062d\u0642\u0648\u0642 \u0627\u0644\u0625\u0646\u0633\u0627\u0646<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u062a\u064f\u0642\u0631\u0651 \u0627\u0644\u0623\u0645\u0645 \u0627\u0644\u0645\u062a\u062d\u062f\u0629 \u0628\u0623\u0646 \u0627\u0644\u0635\u062d\u0629 \u062d\u0642 \u0623\u0633\u0627\u0633\u064a \u0645\u0646 \u062d\u0642\u0648\u0642 \u0627\u0644\u0625\u0646\u0633\u0627\u0646. \u0648\u0645\u0639 \u0630\u0644\u0643\u060c \u0641\u064a \u062d\u0627\u0644\u0629 \u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0627\u0644\u062f\u0648\u0634\u064a\u0646\u064a:<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u064a\u0639\u062a\u0645\u062f \u0627\u0644\u0648\u0635\u0648\u0644 \u0639\u0644\u0649 \u0627\u0644\u0645\u0648\u0642\u0639 \u0627\u0644\u062c\u063a\u0631\u0627\u0641\u064a<\/li>\n\n\n\n<li>\u064a\u0639\u062a\u0645\u062f \u0627\u0644\u0639\u0644\u0627\u062c \u0639\u0644\u0649 \u0627\u0644\u062b\u0631\u0648\u0629<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\">\u0647\u0630\u0627 \u0627\u0644\u062a\u0646\u0627\u0642\u0636 \u064a\u0642\u0648\u0636 \u0627\u0644\u0639\u062f\u0627\u0644\u0629 \u0627\u0644\u0635\u062d\u064a\u0629 \u0627\u0644\u0639\u0627\u0644\u0645\u064a\u0629.<\/p>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"solutions-to-improve-duchenne-muscular-dystrophy-treatment-access\">\u062d\u0644\u0648\u0644 \u0644\u062a\u062d\u0633\u064a\u0646 \u0627\u0644\u0648\u0635\u0648\u0644 \u0625\u0644\u0649 \u0639\u0644\u0627\u062c \u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a<\/h2>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"global-pricing-reform\">\u0625\u0635\u0644\u0627\u062d \u0627\u0644\u062a\u0633\u0639\u064a\u0631 \u0627\u0644\u0639\u0627\u0644\u0645\u064a<\/h3>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u0646\u0645\u0627\u0630\u062c \u0627\u0644\u062a\u0633\u0639\u064a\u0631 \u0627\u0644\u0645\u062a\u062f\u0631\u062c\u0629<\/li>\n\n\n\n<li>\u0623\u0637\u0631 \u0627\u0644\u062a\u0641\u0627\u0648\u0636 \u0627\u0644\u062f\u0648\u0644\u064a\u0629<\/li>\n<\/ul>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"public-private-partnerships\">\u0627\u0644\u0634\u0631\u0627\u0643\u0627\u062a \u0628\u064a\u0646 \u0627\u0644\u0642\u0637\u0627\u0639\u064a\u0646 \u0627\u0644\u0639\u0627\u0645 \u0648\u0627\u0644\u062e\u0627\u0635<\/h3>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u0627\u0644\u062a\u0645\u0648\u064a\u0644 \u0627\u0644\u0645\u0634\u062a\u0631\u0643 \u0644\u0644\u0628\u062d\u0648\u062b \u0648\u0627\u0644\u0648\u0635\u0648\u0644<\/li>\n\n\n\n<li>\u0627\u062a\u0641\u0627\u0642\u064a\u0629 \u062a\u0642\u0627\u0633\u0645 \u0627\u0644\u0645\u062e\u0627\u0637\u0631<\/li>\n<\/ul>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"expanded-clinical-trials\">\u0627\u0644\u062a\u062c\u0627\u0631\u0628 \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629 \u0627\u0644\u0645\u0648\u0633\u0639\u0629<\/h3>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u0625\u062f\u0631\u0627\u062c \u0627\u0644\u0645\u0646\u0627\u0637\u0642 \u0627\u0644\u0645\u0645\u062b\u0644\u0629 \u062a\u0645\u062b\u064a\u0644\u0627\u064b \u0646\u0627\u0642\u0635\u0627\u064b<\/li>\n\n\n\n<li>\u0627\u0644\u0627\u0633\u062a\u062b\u0645\u0627\u0631 \u0641\u064a \u0627\u0644\u0628\u0646\u064a\u0629 \u0627\u0644\u062a\u062d\u062a\u064a\u0629<\/li>\n<\/ul>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"data-sharing-and-collaboration\">\u0645\u0634\u0627\u0631\u0643\u0629 \u0627\u0644\u0628\u064a\u0627\u0646\u0627\u062a \u0648\u0627\u0644\u062a\u0639\u0627\u0648\u0646<\/h3>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u0627\u0644\u0633\u062c\u0644\u0627\u062a \u0627\u0644\u0639\u0627\u0644\u0645\u064a\u0629<\/li>\n\n\n\n<li>\u062c\u0645\u0639 \u0627\u0644\u0623\u062f\u0644\u0629 \u0645\u0646 \u0627\u0644\u0639\u0627\u0644\u0645 \u0627\u0644\u062d\u0642\u064a\u0642\u064a<\/li>\n<\/ul>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"final-thoughts\">\u0627\u0644\u0623\u0641\u0643\u0627\u0631 \u0627\u0644\u0646\u0647\u0627\u0626\u064a\u0629<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u0625\u0630\u0627 \u0627\u062f\u0639\u062a \u0627\u0644\u062d\u0643\u0648\u0645\u0627\u062a \u0645\u0631\u0627\u0631\u0627\u064b \u0648\u062a\u0643\u0631\u0627\u0631\u0627\u064b \u0623\u0646 \u0627\u0642\u062a\u0635\u0627\u062f\u0627\u062a\u0647\u0627 &quot;\u0642\u0648\u064a\u0629&quot;\u060c \u0648\u0645\u0639 \u0630\u0644\u0643 \u0641\u0634\u0644\u062a \u0641\u064a \u062a\u0623\u0645\u064a\u0646 \u0627\u0644\u062d\u0635\u0648\u0644 \u0639\u0644\u0649 \u0639\u0644\u0627\u062c \u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a\u060c \u0641\u0625\u0646 \u0647\u0630\u0627 \u0627\u0644\u062a\u0646\u0627\u0642\u0636 \u0644\u0627 \u064a\u0645\u0643\u0646 \u062a\u062c\u0627\u0647\u0644\u0647.<\/strong> \u0644\u0627 \u062a\u064f\u0642\u0627\u0633 \u0627\u0644\u0642\u0648\u0629 \u0627\u0644\u0627\u0642\u062a\u0635\u0627\u062f\u064a\u0629 \u0628\u0623\u0631\u0642\u0627\u0645 \u0627\u0644\u0646\u0627\u062a\u062c \u0627\u0644\u0645\u062d\u0644\u064a \u0627\u0644\u0625\u062c\u0645\u0627\u0644\u064a \u0623\u0648 \u0645\u0634\u0627\u0631\u064a\u0639 \u0627\u0644\u0628\u0646\u064a\u0629 \u0627\u0644\u062a\u062d\u062a\u064a\u0629 \u0623\u0648 \u0627\u0644\u0625\u0646\u0641\u0627\u0642 \u0627\u0644\u062f\u0641\u0627\u0639\u064a \u0641\u0642\u0637\u060c \u0628\u0644 \u062a\u064f\u0642\u0627\u0633 \u0628\u0642\u062f\u0631\u0629 \u0627\u0644\u0646\u0638\u0627\u0645 \u0639\u0644\u0649 \u062d\u0645\u0627\u064a\u0629 \u0645\u0648\u0627\u0637\u0646\u064a\u0647 \u0627\u0644\u0623\u0643\u062b\u0631 \u0636\u0639\u0641\u0627\u064b \u0639\u0646\u062f\u0645\u0627 \u064a\u0643\u0648\u0646 \u0627\u0644\u0623\u0645\u0631 \u0641\u064a \u063a\u0627\u064a\u0629 \u0627\u0644\u0623\u0647\u0645\u064a\u0629.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u0639\u0646\u062f\u0645\u0627 \u0644\u0627 \u062a\u0633\u062a\u0637\u064a\u0639 \u062f\u0648\u0644\u0629 \u0645\u0627 \u0627\u0644\u062a\u0641\u0627\u0648\u0636 \u0639\u0644\u0649 \u0623\u0633\u0639\u0627\u0631 \u0645\u0633\u062a\u062f\u0627\u0645\u0629 \u0645\u0639 \u0634\u0631\u0643\u0627\u062a \u0627\u0644\u0623\u062f\u0648\u064a\u0629\u060c \u0648\u0644\u0627 \u062a\u0633\u062a\u0637\u064a\u0639 \u0627\u0644\u0627\u0633\u062a\u062b\u0645\u0627\u0631 \u0641\u064a \u0627\u0644\u0628\u062d\u062b \u0648\u0627\u0644\u0625\u0646\u062a\u0627\u062c \u0627\u0644\u0645\u062d\u0644\u064a\u064a\u0646\u060c \u0648\u0644\u0627 \u062a\u0633\u062a\u0637\u064a\u0639 \u0625\u0646\u0634\u0627\u0621 \u0645\u0633\u0627\u0631\u0627\u062a \u0641\u0639\u0627\u0644\u0629 \u0644\u0633\u062f\u0627\u062f \u062a\u0643\u0627\u0644\u064a\u0641 \u0627\u0644\u0639\u0644\u0627\u062c\u0627\u062a \u0627\u0644\u0645\u0646\u0642\u0630\u0629 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\u0645\u0644\u0645\u0648\u0633\u0629.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u0627\u0644\u062d\u0642\u064a\u0642\u0629 \u063a\u064a\u0631 \u0645\u0631\u064a\u062d\u0629: \u0625\u0630\u0627 \u0644\u0645 \u064a\u062a\u0645\u0643\u0646 \u0646\u0638\u0627\u0645 \u0645\u0627 \u0645\u0646 \u062a\u0648\u0641\u064a\u0631 \u0627\u0644\u0648\u0635\u0648\u0644 \u0625\u0644\u0649 \u0627\u0644\u0639\u0644\u0627\u062c\u0627\u062a \u0627\u0644\u0623\u0633\u0627\u0633\u064a\u0629 \u0641\u064a \u0638\u0644 \u0627\u0644\u062d\u0627\u062c\u0629 \u0627\u0644\u0645\u0639\u0631\u0648\u0641\u0629 \u0648\u0627\u0644\u0639\u0644\u0648\u0645 \u0627\u0644\u0645\u062a\u0627\u062d\u0629\u060c \u0641\u0625\u0646 \u0645\u0632\u0627\u0639\u0645\u0647 \u0628\u0627\u0644\u0642\u0648\u0629 \u062a\u0635\u0628\u062d \u0645\u062c\u0631\u062f \u0643\u0644\u0627\u0645.<\/strong> \u0627\u0644\u0642\u0648\u0629 \u0628\u062f\u0648\u0646 \u0645\u0633\u0627\u0621\u0644\u0629 \u0645\u062c\u0631\u062f 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\u0648\u0627\u0644\u062f\u0648\u0644 \u0648\u062c\u0645\u0639\u064a\u0627\u062a \u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0627\u0644\u062f\u0648\u0634\u064a\u0646\u064a \u0627\u0644\u062a\u064a \u0646\u0634\u064a\u0631 \u0625\u0644\u064a\u0647\u0627.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0627\u0642\u0631\u0623 \u0627\u0644\u0645\u0632\u064a\u062f: <a href=\"https:\/\/dmdwarrior.com\/ar\/duchenne-muscular-dystrophy-treatment-cost\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u0644\u0645\u0627\u0630\u0627 \u0623\u0635\u0628\u062d\u062a \u062a\u0643\u0627\u0644\u064a\u0641 \u0639\u0644\u0627\u062c \u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a \u062e\u0627\u0631\u062c\u0629 \u0639\u0646 \u0627\u0644\u0633\u064a\u0637\u0631\u0629\u061f<\/a><\/p>","protected":false},"excerpt":{"rendered":"<p>Duchenne muscular dystrophy (DMD) is no longer a condition defined solely by its biology. Today, it is equally defined by who can access treatment\u2014and who cannot. Despite major advances in gene therapy, exon-skipping drugs, and multidisciplinary care, Duchenne muscular dystrophy treatment access remains profoundly unequal across countries, healthcare systems, and socioeconomic groups. The reality is [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":7622,"comment_status":"open","ping_status":"open","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[282],"tags":[229,261,232,685,262],"class_list":["post-2926","post","type-post","status-publish","format-standard","has-post-thumbnail","category-editorials","tag-dmd-associations","tag-dmd-families","tag-dmd-treatments","tag-drug-access","tag-ministry-of-health"],"_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/posts\/2926","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/comments?post=2926"}],"version-history":[{"count":0,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/posts\/2926\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/media\/7622"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/media?parent=2926"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/categories?post=2926"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/tags?post=2926"}],"curies":[{"name":"\u0648\u0648\u0631\u062f\u0628\u0631\u064a\u0633","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}