{"id":2261,"date":"2026-04-10T14:26:46","date_gmt":"2026-04-10T11:26:46","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=2261"},"modified":"2026-04-24T13:04:53","modified_gmt":"2026-04-24T10:04:53","slug":"new-gene-therapies-for-duchenne-muscular-dystrophy","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/ar\/new-gene-therapies-for-duchenne-muscular-dystrophy\/","title":{"rendered":"\u0639\u0644\u0627\u062c\u0627\u062a \u062c\u064a\u0646\u064a\u0629 \u062c\u062f\u064a\u062f\u0629 \u0645\u062d\u062a\u0645\u0644\u0629 \u0644\u0645\u0631\u0636 \u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u062f\u0648\u0634\u064a\u0646"},"content":{"rendered":"<p class=\"wp-block-paragraph\"><strong>\u064a\u062a\u0637\u0648\u0631 \u0645\u0634\u0647\u062f \u0627\u0644\u0639\u0644\u0627\u062c\u0627\u062a \u0627\u0644\u062c\u064a\u0646\u064a\u0629 \u0627\u0644\u062c\u062f\u064a\u062f\u0629 \u0627\u0644\u0645\u062d\u062a\u0645\u0644\u0629 \u0644\u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a (DMD) \u0628\u0633\u0631\u0639\u0629\u060c \u0645\u0645\u0627 \u064a\u0648\u0641\u0631 \u0623\u0645\u0644\u0627\u064b \u0645\u062a\u062c\u062f\u062f\u0627\u064b \u0644\u0644\u0645\u0631\u0636\u0649 \u0648\u0639\u0627\u0626\u0644\u0627\u062a\u0647\u0645 \u0627\u0644\u0645\u062a\u0623\u062b\u0631\u0629 \u0628\u0647\u0630\u0627 \u0627\u0644\u0627\u0636\u0637\u0631\u0627\u0628 \u0627\u0644\u0639\u0635\u0628\u064a \u0627\u0644\u0639\u0636\u0644\u064a \u0627\u0644\u0645\u062f\u0645\u0631.<\/strong> \u0648\u0645\u0646 \u0628\u064a\u0646 \u0623\u0643\u062b\u0631 \u0627\u0644\u0623\u0633\u0627\u0644\u064a\u0628 \u0627\u0644\u062a\u064a \u062a\u062d\u0638\u0649 \u0628\u0645\u062a\u0627\u0628\u0639\u0629 \u062f\u0642\u064a\u0642\u0629 Solid Biosciences SGT-003 \u0648 RegenxBio RGX-202 \u0648 Genethon GNT-0004\u060c \u0648\u0627\u0644\u062a\u064a \u062a\u0645\u062b\u0644 \u0627\u0644\u0645\u0648\u062c\u0629 \u0627\u0644\u062a\u0627\u0644\u064a\u0629 \u0645\u0646 \u0627\u0644\u0627\u0628\u062a\u0643\u0627\u0631 \u0641\u064a \u0627\u0644\u0637\u0628 \u0627\u0644\u062c\u064a\u0646\u064a. <strong>\u062a\u0647\u062f\u0641 \u0647\u0630\u0647 \u0627\u0644\u0639\u0644\u0627\u062c\u0627\u062a \u0627\u0644\u0646\u0627\u0634\u0626\u0629 - \u0648\u0627\u0644\u062a\u064a \u064a\u0634\u0627\u0631 \u0625\u0644\u064a\u0647\u0627 \u0623\u064a\u0636\u064b\u0627 \u0628\u0627\u0633\u0645 \u0639\u0644\u0627\u062c\u0627\u062a \u0627\u0644\u062c\u064a\u0646\u0627\u062a \u0645\u0646 \u0627\u0644\u062c\u064a\u0644 \u0627\u0644\u062a\u0627\u0644\u064a \u0644\u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a\u060c \u0648\u0646\u0647\u062c \u0646\u0642\u0644 \u062c\u064a\u0646 \u0627\u0644\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0627\u0644\u0635\u063a\u064a\u0631\u060c \u0648\u0627\u0644\u0639\u0644\u0627\u062c\u0627\u062a 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\u0644\u0627\u0633\u062a\u0639\u0627\u062f\u0629 \u0627\u0644\u062a\u0639\u0628\u064a\u0631 \u0627\u0644\u0648\u0638\u064a\u0641\u064a \u0644\u0644\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0648\u0631\u0628\u0645\u0627 \u062a\u063a\u064a\u064a\u0631 \u0645\u0633\u0627\u0631 \u0627\u0644\u0645\u0631\u0636 \u0639\u0644\u0649 \u0645\u0633\u062a\u0648\u0649 \u0623\u0633\u0627\u0633\u064a.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u064a\u0646\u062a\u062c \u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a \u0639\u0646 \u0637\u0641\u0631\u0627\u062a \u0641\u064a \u062c\u064a\u0646 DMD\u060c \u0645\u0645\u0627 \u064a\u0624\u062f\u064a \u0625\u0644\u0649 \u063a\u064a\u0627\u0628 \u0627\u0644\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646\u060c \u0648\u0647\u0648 \u0628\u0631\u0648\u062a\u064a\u0646 \u0623\u0633\u0627\u0633\u064a \u0644\u0644\u062d\u0641\u0627\u0638 \u0639\u0644\u0649 \u0633\u0644\u0627\u0645\u0629 \u0627\u0644\u0639\u0636\u0644\u0627\u062a. \u0645\u0639 \u0645\u0631\u0648\u0631 \u0627\u0644\u0648\u0642\u062a\u060c \u062a\u062a\u062f\u0647\u0648\u0631 \u0623\u0644\u064a\u0627\u0641 \u0627\u0644\u0639\u0636\u0644\u0627\u062a\u060c \u0645\u0645\u0627 \u064a\u0646\u062a\u062c \u0639\u0646\u0647 \u0636\u0639\u0641 \u062a\u062f\u0631\u064a\u062c\u064a\u060c \u0648\u0641\u0642\u062f\u0627\u0646 \u0627\u0644\u0642\u062f\u0631\u0629 \u0639\u0644\u0649 \u0627\u0644\u0645\u0634\u064a\u060c \u0648\u0645\u0636\u0627\u0639\u0641\u0627\u062a \u062a\u0646\u0641\u0633\u064a\u0629\u060c \u0648\u0627\u0639\u062a\u0644\u0627\u0644 \u0639\u0636\u0644\u0629 \u0627\u0644\u0642\u0644\u0628. <strong>\u064a\u0645\u062b\u0644 \u062a\u0637\u0648\u064a\u0631 \u0639\u0644\u0627\u062c\u0627\u062a \u062c\u064a\u0646\u064a\u0629 \u062c\u062f\u064a\u062f\u0629 \u0645\u062d\u062a\u0645\u0644\u0629 \u0644\u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a \u062a\u062d\u0648\u0644\u0627\u064b \u0646\u0645\u0648\u0630\u062c\u064a\u0627\u064b - \u0645\u0646 \u0627\u0644\u0631\u0639\u0627\u064a\u0629 \u0627\u0644\u062f\u0627\u0639\u0645\u0629 \u0625\u0644\u0649 \u0627\u0644\u062a\u062f\u062e\u0644\u0627\u062a \u0627\u0644\u0645\u0639\u062f\u0644\u0629 \u0644\u0644\u0645\u0631\u0636 \u0648\u0627\u0644\u062a\u064a \u0642\u062f \u062a\u0637\u064a\u0644 \u0628\u0634\u0643\u0644 \u0643\u0628\u064a\u0631 \u0643\u0644\u0627\u064b \u0645\u0646 \u0627\u0644\u0639\u0645\u0631 \u0648\u0646\u0648\u0639\u064a\u0629 \u0627\u0644\u062d\u064a\u0627\u0629.<\/strong><\/p>\n\n\n\n<div class=\"wp-block-rank-math-toc-block\" id=\"rank-math-toc\"><h2>\u062c\u062f\u0648\u0644 \u0627\u0644\u0645\u062d\u062a\u0648\u064a\u0627\u062a<\/h2><nav><ul><li><a href=\"#the-scientific-foundation-behind-gene-therapy-in-dmd\">\u0627\u0644\u0623\u0633\u0627\u0633 \u0627\u0644\u0639\u0644\u0645\u064a \u0648\u0631\u0627\u0621 \u0627\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u062c\u064a\u0646\u064a \u0641\u064a \u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0627\u0644\u062f\u0648\u0634\u064a\u0646\u064a<\/a><\/li><li><a href=\"#solid-biosciences-sgt-003\">Solid Biosciences SGT-003<\/a><ul><\/ul><\/li><li><a href=\"#regenx-bio-rgx-202\">\u0631\u064a\u062c\u064a\u0646\u0643\u0633 \u0628\u064a\u0648 RGX-202<\/a><ul><\/ul><\/li><li><a href=\"#genethon-gnt-0004\">\u062c\u064a\u0646\u062b\u0648\u0646 GNT-0004<\/a><ul><\/ul><\/li><li><a href=\"#emerging-gene-therapy-research-in-china-and-russia\">\u0623\u0628\u062d\u0627\u062b \u0627\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u062c\u064a\u0646\u064a \u0627\u0644\u0646\u0627\u0634\u0626\u0629 \u0641\u064a \u0627\u0644\u0635\u064a\u0646 \u0648\u0631\u0648\u0633\u064a\u0627<\/a><ul><li><a href=\"#china\">\u0627\u0644\u0635\u064a\u0646<\/a><\/li><li><a href=\"#russia\">\u0631\u0648\u0633\u064a\u0627<\/a><\/li><li><a href=\"#a-hopeful-outlook\">\u0646\u0638\u0631\u0629 \u0645\u062a\u0641\u0627\u0626\u0644\u0629<\/a><\/li><\/ul><\/li><li><a href=\"#challenges-and-limitations-of-gene-therapy-in-dmd\">\u062a\u062d\u062f\u064a\u0627\u062a \u0648\u0642\u064a\u0648\u062f \u0627\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u062c\u064a\u0646\u064a \u0641\u064a \u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0627\u0644\u062f\u0648\u0634\u064a\u0646\u064a<\/a><ul><\/ul><\/li><li><a href=\"#future-directions-and-innovations\">\u0627\u0644\u062a\u0648\u062c\u0647\u0627\u062a \u0627\u0644\u0645\u0633\u062a\u0642\u0628\u0644\u064a\u0629 \u0648\u0627\u0644\u0627\u0628\u062a\u0643\u0627\u0631\u0627\u062a<\/a><\/li><li><a href=\"#conclusion\">\u062e\u0627\u062a\u0645\u0629<\/a><\/li><\/ul><\/nav><\/div>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"the-scientific-foundation-behind-gene-therapy-in-dmd\">\u0627\u0644\u0623\u0633\u0627\u0633 \u0627\u0644\u0639\u0644\u0645\u064a \u0648\u0631\u0627\u0621 \u0627\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u062c\u064a\u0646\u064a \u0641\u064a \u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0627\u0644\u062f\u0648\u0634\u064a\u0646\u064a<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u064a\u0639\u062a\u0645\u062f \u0627\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u062c\u064a\u0646\u064a \u0644\u0645\u0631\u0636 \u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0627\u0644\u062f\u0648\u0634\u064a\u0646\u064a \u0628\u0634\u0643\u0644 \u0623\u0633\u0627\u0633\u064a \u0639\u0644\u0649 \u0646\u0627\u0642\u0644\u0627\u062a \u0627\u0644\u0641\u064a\u0631\u0648\u0633 \u0627\u0644\u0645\u0631\u062a\u0628\u0637 \u0628\u0627\u0644\u063a\u062f\u0627\u0646\u064a (AAV) \u0644\u062a\u0648\u0635\u064a\u0644 \u0646\u0633\u062e\u0629 \u0645\u062e\u062a\u0635\u0631\u0629 \u0648\u0644\u0643\u0646\u0647\u0627 \u0648\u0638\u064a\u0641\u064a\u0629 \u0645\u0646 \u062c\u064a\u0646 \u0627\u0644\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646\u060c \u0648\u0627\u0644\u062a\u064a \u064a\u0634\u0627\u0631 \u0625\u0644\u064a\u0647\u0627 \u0639\u0627\u062f\u0629 \u0628\u0627\u0633\u0645 \u0627\u0644\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0627\u0644\u0635\u063a\u064a\u0631.<\/strong> \u0646\u0638\u0631\u0627\u064b \u0644\u0623\u0646 \u062c\u064a\u0646 \u0627\u0644\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0627\u0644\u0643\u0627\u0645\u0644 \u0643\u0628\u064a\u0631 \u062c\u062f\u0627\u064b \u0628\u062d\u064a\u062b \u0644\u0627 \u064a\u0645\u0643\u0646 \u0648\u0636\u0639\u0647 \u0641\u064a \u0627\u0644\u0646\u0648\u0627\u0642\u0644 \u0627\u0644\u0641\u064a\u0631\u0648\u0633\u064a\u0629\u060c \u0641\u0642\u062f \u0642\u0627\u0645 \u0627\u0644\u0628\u0627\u062d\u062b\u0648\u0646 \u0628\u062a\u0635\u0645\u064a\u0645 \u0646\u0633\u062e \u0645\u0636\u063a\u0648\u0637\u0629 \u062a\u062d\u062a\u0641\u0638 \u0628\u0627\u0644\u0645\u062c\u0627\u0644\u0627\u062a \u0627\u0644\u0648\u0638\u064a\u0641\u064a\u0629 \u0627\u0644\u0647\u0627\u0645\u0629.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u062a\u0634\u0645\u0644 \u0627\u0644\u0622\u0644\u064a\u0627\u062a \u0627\u0644\u0631\u0626\u064a\u0633\u064a\u0629 \u0645\u0627 \u064a\u0644\u064a:<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u0625\u064a\u0635\u0627\u0644 \u062c\u064a\u0646\u0627\u062a \u0627\u0644\u0645\u064a\u0643\u0631\u0648-\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0625\u0644\u0649 \u0627\u0644\u062e\u0644\u0627\u064a\u0627 \u0627\u0644\u0639\u0636\u0644\u064a\u0629<\/li>\n\n\n\n<li>\u0627\u0633\u062a\u0639\u0627\u062f\u0629 \u0627\u0633\u062a\u0642\u0631\u0627\u0631 \u0627\u0644\u063a\u0634\u0627\u0621 \u0627\u0644\u0639\u0636\u0644\u064a<\/li>\n\n\n\n<li>\u0627\u0644\u062d\u062f \u0645\u0646 \u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0648\u0627\u0644\u0627\u0644\u062a\u0647\u0627\u0628<\/li>\n\n\n\n<li>\u062a\u062d\u0633\u064a\u0646 \u0642\u0648\u0629 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0648\u0648\u0638\u064a\u0641\u062a\u0647\u0627<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\">\u064a\u062a\u0639\u0644\u0645 \u0623\u0643\u062b\u0631: <a href=\"https:\/\/dmdwarrior.com\/ar\/micro-dystrophin\/\" target=\"_blank\" data-type=\"post\" data-id=\"3807\" rel=\"noreferrer noopener\">\u0645\u0627 \u0647\u0648 \u0627\u0644\u0645\u064a\u0643\u0631\u0648-\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646\u061f<\/a><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0631\u063a\u0645 \u0648\u062c\u0648\u062f \u0628\u0639\u0636 \u0627\u0644\u062a\u062d\u062f\u064a\u0627\u062a - \u0645\u062b\u0644 \u0627\u0644\u0627\u0633\u062a\u062c\u0627\u0628\u0627\u062a \u0627\u0644\u0645\u0646\u0627\u0639\u064a\u0629\u060c \u0648\u0643\u0641\u0627\u0621\u0629 \u062a\u0648\u0635\u064a\u0644 \u0627\u0644\u0646\u0648\u0627\u0642\u0644\u060c \u0648\u0627\u0633\u062a\u062f\u0627\u0645\u0629 \u0627\u0644\u062a\u0639\u0628\u064a\u0631 \u0627\u0644\u062c\u064a\u0646\u064a - \u0641\u0625\u0646 \u0627\u0644\u062a\u0642\u062f\u0645 \u0641\u064a \u0627\u0644\u0639\u0644\u0627\u062c\u0627\u062a \u0627\u0644\u062c\u064a\u0646\u064a\u0629 \u0627\u0644\u062c\u062f\u064a\u062f\u0629 \u0627\u0644\u0645\u062d\u062a\u0645\u0644\u0629 \u0644\u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a \u064a\u062a\u0633\u0627\u0631\u0639. \u0627\u0642\u0631\u0623 \u0627\u0644\u0645\u0632\u064a\u062f: <a href=\"https:\/\/dmdwarrior.com\/ar\/biomarkers-in-duchenne-muscular-dystrophy\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u0627\u0644\u0645\u0624\u0634\u0631\u0627\u062a \u0627\u0644\u062d\u064a\u0648\u064a\u0629 \u0641\u064a \u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a<\/a><\/p>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"solid-biosciences-sgt-003\">Solid Biosciences SGT-003<\/h2>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"overview-of-sgt-003\">\u0646\u0638\u0631\u0629 \u0639\u0627\u0645\u0629 \u0639\u0644\u0649 SGT-003<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u064a\u064f\u0639\u062f\u0651 Solid Biosciences&#039; SGT-003 \u0623\u062d\u062f \u0623\u0643\u062b\u0631 \u0627\u0644\u0639\u0644\u0627\u062c\u0627\u062a \u0627\u0644\u062c\u064a\u0646\u064a\u0629 \u0627\u0644\u062c\u062f\u064a\u062f\u0629 \u062a\u0637\u0648\u0631\u0627\u064b \u0644\u0639\u0644\u0627\u062c \u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a\u060c \u0648\u0647\u0648 \u0645\u0635\u0645\u0645 \u0643\u062c\u064a\u0644 \u062c\u062f\u064a\u062f \u0645\u0646 \u0627\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u062c\u064a\u0646\u064a \u0627\u0644\u0642\u0627\u0626\u0645 \u0639\u0644\u0649 \u0627\u0644\u0641\u064a\u0631\u0648\u0633\u0627\u062a \u0627\u0644\u063a\u062f\u064a\u0629 \u0627\u0644\u0645\u0631\u062a\u0628\u0637\u0629 (AAV) \u0644\u0625\u0646\u062a\u0627\u062c \u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u062f\u0642\u064a\u0642. \u0648\u064a\u062a\u0636\u0645\u0646 \u0647\u0630\u0627 \u0627\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u0639\u062f\u064a\u062f \u0645\u0646 \u0627\u0644\u062a\u062d\u0633\u064a\u0646\u0627\u062a \u0645\u0642\u0627\u0631\u0646\u0629\u064b \u0628\u0627\u0644\u062a\u0631\u0643\u064a\u0628\u0627\u062a \u0627\u0644\u0633\u0627\u0628\u0642\u0629\u060c \u0628\u0645\u0627 \u0641\u064a \u0630\u0644\u0643 \u0627\u0633\u062a\u0647\u062f\u0627\u0641 \u0627\u0644\u0642\u0644\u0628 \u0628\u0634\u0643\u0644 \u0623\u0641\u0636\u0644 \u0648\u062a\u062d\u0633\u064a\u0646 \u0627\u0644\u062a\u0639\u0628\u064a\u0631 \u0627\u0644\u062c\u064a\u0646\u064a.<\/p>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"clinical-development-and-findings\">\u0627\u0644\u062a\u0637\u0648\u0631 \u0627\u0644\u0633\u0631\u064a\u0631\u064a \u0648\u0627\u0644\u0646\u062a\u0627\u0626\u062c<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u062a\u0634\u064a\u0631 \u0627\u0644\u0628\u064a\u0627\u0646\u0627\u062a \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629 \u0627\u0644\u0645\u0628\u0643\u0631\u0629 \u0645\u0646 \u062a\u062c\u0627\u0631\u0628 SGT-003 \u0625\u0644\u0649 \u0645\u0627 \u064a\u0644\u064a:<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u0627\u0644\u062a\u0639\u0628\u064a\u0631 \u0627\u0644\u0642\u0648\u064a \u0639\u0646 \u0628\u0631\u0648\u062a\u064a\u0646 \u0627\u0644\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0627\u0644\u0635\u063a\u064a\u0631 \u0641\u064a \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0627\u0644\u0647\u064a\u0643\u0644\u064a\u0629 \u0648\u0627\u0644\u0642\u0644\u0628\u064a\u0629<\/li>\n\n\n\n<li>\u062a\u062d\u0633\u064a\u0646 \u0627\u0644\u0645\u0624\u0634\u0631\u0627\u062a \u0627\u0644\u062d\u064a\u0648\u064a\u0629 \u0627\u0644\u0645\u0631\u062a\u0628\u0637\u0629 \u0628\u0633\u0644\u0627\u0645\u0629 \u0627\u0644\u0639\u0636\u0644\u0627\u062a<\/li>\n\n\n\n<li>\u0645\u0644\u0641 \u0623\u0645\u0627\u0646 \u062c\u064a\u062f \u0645\u0642\u0627\u0631\u0646\u0629 \u0628\u0627\u0644\u0645\u0631\u0634\u062d\u064a\u0646 \u0627\u0644\u0633\u0627\u0628\u0642\u064a\u0646<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\">\u0648\u0627\u0644\u062c\u062f\u064a\u0631 \u0628\u0627\u0644\u0630\u0643\u0631 \u0623\u0646 SGT-003 \u064a\u0633\u062a\u062e\u062f\u0645 \u063a\u0644\u0627\u0641\u064b\u0627 \u062c\u062f\u064a\u062f\u064b\u0627 \u0645\u0635\u0645\u0645\u064b\u0627 \u0644\u062a\u062d\u0633\u064a\u0646 \u0643\u0641\u0627\u0621\u0629 \u0627\u0644\u062a\u0648\u0635\u064a\u0644\u060c \u0648\u062e\u0627\u0635\u0629 \u0625\u0644\u0649 \u0623\u0646\u0633\u062c\u0629 \u0627\u0644\u0642\u0644\u0628 - \u0648\u0647\u0648 \u0639\u0627\u0645\u0644 \u062d\u0627\u0633\u0645 \u0646\u0638\u0631\u064b\u0627 \u0644\u0623\u0646 \u0627\u0639\u062a\u0644\u0627\u0644 \u0639\u0636\u0644\u0629 \u0627\u0644\u0642\u0644\u0628 \u0647\u0648 \u0633\u0628\u0628 \u0631\u0626\u064a\u0633\u064a \u0644\u0644\u0648\u0641\u064a\u0627\u062a \u0644\u062f\u0649 \u0645\u0631\u0636\u0649 \u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0627\u0644\u062f\u0648\u0634\u064a\u0646\u064a.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u064a\u062a\u0639\u0644\u0645 \u0623\u0643\u062b\u0631: <a href=\"https:\/\/clinicaltrials.gov\/study\/NCT06138639\" target=\"_blank\" rel=\"noopener\">\u062d\u0648\u0644 SGT-003<\/a><\/p>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"strategic-importance\">\u0627\u0644\u0623\u0647\u0645\u064a\u0629 \u0627\u0644\u0627\u0633\u062a\u0631\u0627\u062a\u064a\u062c\u064a\u0629<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u062a\u0643\u0645\u0646 \u0623\u0647\u0645\u064a\u0629 SGT-003 \u0641\u064a \u0627\u0644\u0645\u062c\u0627\u0644 \u0627\u0644\u0623\u0648\u0633\u0639 \u0644\u0644\u0639\u0644\u0627\u062c\u0627\u062a \u0627\u0644\u062c\u064a\u0646\u064a\u0629 \u0627\u0644\u062c\u062f\u064a\u062f\u0629 \u0627\u0644\u0645\u062d\u062a\u0645\u0644\u0629 \u0644\u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a \u0641\u064a \u0645\u062d\u0627\u0648\u0644\u062a\u0647\u0627 \u0645\u0639\u0627\u0644\u062c\u0629 \u0627\u0644\u0642\u064a\u0648\u062f \u0627\u0644\u0633\u0627\u0628\u0642\u0629 \u0641\u064a \u0627\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u062c\u064a\u0646\u064a\u060c \u0648\u062e\u0627\u0635\u0629:<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u062a\u0648\u0635\u064a\u0644 \u063a\u064a\u0631 \u0645\u062b\u0627\u0644\u064a \u0644\u0644\u0642\u0644\u0628<\/li>\n\n\n\n<li>\u0627\u0644\u0623\u062d\u062f\u0627\u062b \u0627\u0644\u0636\u0627\u0626\u0631\u0629 \u0627\u0644\u0645\u062a\u0639\u0644\u0642\u0629 \u0628\u0627\u0644\u0645\u0646\u0627\u0639\u0629<\/li>\n\n\n\n<li>\u0627\u0644\u062a\u0628\u0627\u064a\u0646 \u0641\u064a \u0645\u0633\u062a\u0648\u064a\u0627\u062a \u0627\u0644\u062a\u0639\u0628\u064a\u0631<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\">\u0625\u0630\u0627 \u0646\u062c\u062d \u0627\u0644\u0623\u0645\u0631\u060c \u0641\u0642\u062f \u064a\u0645\u062b\u0644 SGT-003 \u062e\u0637\u0648\u0629 \u0643\u0628\u064a\u0631\u0629 \u0625\u0644\u0649 \u0627\u0644\u0623\u0645\u0627\u0645 \u0641\u064a \u062a\u062d\u0642\u064a\u0642 \u0646\u062a\u0627\u0626\u062c \u0639\u0644\u0627\u062c\u064a\u0629 \u0645\u062a\u0633\u0642\u0629 \u0648\u062f\u0627\u0626\u0645\u0629.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u064a\u062a\u0639\u0644\u0645 \u0623\u0643\u062b\u0631:<\/strong>&nbsp;<a href=\"https:\/\/dmdwarrior.com\/ar\/inspire-duchenne-sgt-003-clinical-trial-update\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u0627\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u062c\u064a\u0646\u064a SGT-003: \u062f\u0631\u0627\u0633\u0629 \u0627\u0644\u0645\u0631\u062d\u0644\u0629 \u0627\u0644\u062b\u0627\u0644\u062b\u0629 INSPIRE DUCHENNE<\/a><\/p>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"regenx-bio-rgx-202\">\u0631\u064a\u062c\u064a\u0646\u0643\u0633 \u0628\u064a\u0648 RGX-202<\/h2>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"overview-of-rgx-202\">\u0646\u0638\u0631\u0629 \u0639\u0627\u0645\u0629 \u0639\u0644\u0649 RGX-202<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u064a\u064f\u0639\u062f RGX-202\u060c \u0627\u0644\u0630\u064a \u0637\u0648\u0631\u062a\u0647 \u0634\u0631\u0643\u0629 RegenxBio\u060c \u0645\u0631\u0634\u062d\u064b\u0627 \u0648\u0627\u0639\u062f\u064b\u0627 \u0622\u062e\u0631 \u0645\u0646 \u0628\u064a\u0646 \u0627\u0644\u0639\u0644\u0627\u062c\u0627\u062a \u0627\u0644\u062c\u064a\u0646\u064a\u0629 \u0627\u0644\u062c\u062f\u064a\u062f\u0629 \u0627\u0644\u0645\u062d\u062a\u0645\u0644\u0629 \u0644\u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a.<\/strong> \u062a\u0633\u062a\u0641\u064a\u062f \u0647\u0630\u0647 \u0627\u0644\u062a\u0642\u0646\u064a\u0629 \u0645\u0646 \u0645\u0646\u0635\u0629 \u0646\u0627\u0642\u0644 \u0627\u0644\u0641\u064a\u0631\u0648\u0633\u0627\u062a \u0627\u0644\u063a\u062f\u064a\u0629 \u0627\u0644\u0645\u0631\u062a\u0628\u0637\u0629 (NAV\u00ae AAV) \u0627\u0644\u062e\u0627\u0635\u0629 \u0628\u0627\u0644\u0634\u0631\u0643\u0629 \u0644\u062a\u0642\u062f\u064a\u0645 \u0628\u0646\u064a\u0629 \u062c\u062f\u064a\u062f\u0629 \u0645\u0646 \u0627\u0644\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0627\u0644\u0645\u064a\u0643\u0631\u0648\u064a.<\/p>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"unique-features\">\u0645\u064a\u0632\u0627\u062a \u0641\u0631\u064a\u062f\u0629<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u064a\u062a\u0645\u064a\u0632 \u062c\u0647\u0627\u0632 RGX-202 \u0628\u0645\u0627 \u064a\u0644\u064a:<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u0642\u062f \u064a\u0624\u062f\u064a \u062a\u0636\u0645\u064a\u0646 \u0627\u0644\u0646\u0637\u0627\u0642 \u0627\u0644\u0637\u0631\u0641\u064a \u0627\u0644\u0643\u0631\u0628\u0648\u0643\u0633\u064a\u0644\u064a \u0644\u0644\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0625\u0644\u0649 \u062a\u062d\u0633\u064a\u0646 \u0648\u0638\u064a\u0641\u0629 \u0627\u0644\u0639\u0636\u0644\u0627\u062a<\/li>\n\n\n\n<li>\u0628\u0646\u064a\u0629 \u062c\u064a\u0646\u064a\u0629 \u0645\u062d\u0633\u0651\u0646\u0629 \u0644\u062a\u062d\u0633\u064a\u0646 \u062a\u0648\u0637\u064a\u0646 \u0627\u0644\u0628\u0631\u0648\u062a\u064a\u0646<\/li>\n\n\n\n<li>\u0643\u0641\u0627\u0621\u0629 \u0639\u0627\u0644\u064a\u0629 \u0641\u064a \u0646\u0642\u0644 \u0627\u0644\u0625\u0634\u0627\u0631\u0629 \u0641\u064a \u0627\u0644\u0623\u0646\u0633\u062c\u0629 \u0627\u0644\u0639\u0636\u0644\u064a\u0629<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\">\u062a\u0645 \u062a\u0635\u0645\u064a\u0645 \u0647\u0630\u0647 \u0627\u0644\u0645\u064a\u0632\u0627\u062a \u0644\u0625\u0646\u062a\u0627\u062c \u0646\u0633\u062e\u0629 \u0623\u0643\u062b\u0631 \u0627\u0643\u062a\u0645\u0627\u0644\u0627\u064b \u0645\u0646 \u0627\u0644\u0646\u0627\u062d\u064a\u0629 \u0627\u0644\u0648\u0638\u064a\u0641\u064a\u0629 \u0645\u0646 \u0627\u0644\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0645\u0642\u0627\u0631\u0646\u0629 \u0628\u0639\u0644\u0627\u062c\u0627\u062a \u0627\u0644\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0627\u0644\u062f\u0642\u064a\u0642\u0629 \u0627\u0644\u0633\u0627\u0628\u0642\u0629.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u064a\u062a\u0639\u0644\u0645 \u0623\u0643\u062b\u0631: <a href=\"https:\/\/clinicaltrials.gov\/study\/NCT05693142\" target=\"_blank\" rel=\"noreferrer noopener\">\u062d\u0648\u0644 RGX-202<\/a><\/p>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"clinical-insights\">\u0631\u0624\u0649 \u0633\u0631\u064a\u0631\u064a\u0629<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u062a\u0634\u064a\u0631 \u0627\u0644\u0628\u064a\u0627\u0646\u0627\u062a \u0627\u0644\u0623\u0648\u0644\u064a\u0629 \u0645\u0646 \u0627\u0644\u062a\u062c\u0627\u0631\u0628 \u0627\u0644\u062c\u0627\u0631\u064a\u0629 \u0625\u0644\u0649 \u0645\u0627 \u064a\u0644\u064a:<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u0645\u0633\u062a\u0648\u064a\u0627\u062a \u0639\u0627\u0644\u064a\u0629 \u0645\u0646 \u0627\u0644\u062a\u0639\u0628\u064a\u0631 \u0627\u0644\u062c\u064a\u0646\u064a \u0639\u0628\u0631 \u0645\u062c\u0645\u0648\u0639\u0627\u062a \u0627\u0644\u0639\u0636\u0644\u0627\u062a<\/li>\n\n\n\n<li>\u0646\u062a\u0627\u0626\u062c \u0648\u0638\u064a\u0641\u064a\u0629 \u0645\u0634\u062c\u0639\u0629 \u0644\u062f\u0649 \u0627\u0644\u0645\u0631\u0636\u0649 \u0641\u064a \u0627\u0644\u0645\u0631\u0627\u062d\u0644 \u0627\u0644\u0645\u0628\u0643\u0631\u0629<\/li>\n\n\n\n<li>\u0645\u0644\u0641 \u0623\u0645\u0627\u0646 \u064a\u0645\u0643\u0646 \u0627\u0644\u062a\u062d\u0643\u0645 \u0641\u064a\u0647 \u0645\u0639 \u0628\u0631\u0648\u062a\u0648\u0643\u0648\u0644\u0627\u062a \u0643\u0628\u062a \u0627\u0644\u0645\u0646\u0627\u0639\u0629 \u0627\u0644\u0642\u064a\u0627\u0633\u064a\u0629<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u064a\u0639\u062a\u0628\u0631 RGX-202 \u0623\u062d\u062f \u0623\u0643\u062b\u0631 \u0627\u0644\u0639\u0644\u0627\u062c\u0627\u062a \u0627\u0644\u062c\u064a\u0646\u064a\u0629 \u0627\u0644\u062c\u062f\u064a\u062f\u0629 \u0627\u0644\u0645\u062d\u062a\u0645\u0644\u0629 \u062a\u0637\u0648\u0631\u0627\u064b \u0645\u0646 \u0627\u0644\u0646\u0627\u062d\u064a\u0629 \u0627\u0644\u062a\u0642\u0646\u064a\u0629 \u0644\u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a\u060c \u0645\u0639 \u0648\u062c\u0648\u062f \u0623\u0633\u0627\u0633 \u0639\u0644\u0645\u064a \u0642\u0648\u064a \u064a\u062f\u0639\u0645 \u062a\u0635\u0645\u064a\u0645\u0647.<\/strong><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u064a\u062a\u0639\u0644\u0645 \u0623\u0643\u062b\u0631: <a href=\"https:\/\/dmdwarrior.com\/ar\/regenxbio-phase-1-2-affinity-duchenne-trial-of-rgx-202\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u0623\u0639\u0644\u0646\u062a \u0634\u0631\u0643\u0629 Regenxbio \u0639\u0646 \u0628\u064a\u0627\u0646\u0627\u062a \u0623\u0648\u0644\u064a\u0629 \u0625\u064a\u062c\u0627\u0628\u064a\u0629 \u062c\u062f\u064a\u062f\u0629 \u0645\u0646 \u0627\u0644\u0645\u0631\u062d\u0644\u0629 \u0627\u0644\u0623\u0648\u0644\u0649\/\u0627\u0644\u062b\u0627\u0646\u064a\u0629 \u0645\u0646 \u062a\u062c\u0631\u0628\u0629 Affinity Duchenne \u0644\u0639\u0642\u0627\u0631 Rgx-202<\/a><\/p>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"genethon-gnt-0004\">\u062c\u064a\u0646\u062b\u0648\u0646 GNT-0004<\/h2>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"overview-of-gnt-0004\">\u0646\u0638\u0631\u0629 \u0639\u0627\u0645\u0629 \u0639\u0644\u0649 GNT-0004<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u064a\u0645\u062b\u0644 GNT-0004 \u0627\u0644\u062a\u0627\u0628\u0639 \u0644\u0634\u0631\u0643\u0629 Genethon \u062c\u0647\u062f\u064b\u0627 \u0623\u0648\u0631\u0648\u0628\u064a\u064b\u0627 \u064a\u0642\u0648\u062f\u0647 \u0627\u0644\u0623\u0648\u0631\u0648\u0628\u064a\u0648\u0646 \u0641\u064a \u062a\u0637\u0648\u064a\u0631 \u0639\u0644\u0627\u062c\u0627\u062a \u062c\u064a\u0646\u064a\u0629 \u062c\u062f\u064a\u062f\u0629 \u0645\u062d\u062a\u0645\u0644\u0629 \u0644\u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a.<\/strong> \u062a\u0645 \u062a\u0637\u0648\u064a\u0631 \u0647\u0630\u0627 \u0627\u0644\u0639\u0644\u0627\u062c \u0628\u0627\u0633\u062a\u062e\u062f\u0627\u0645 \u0623\u0628\u062d\u0627\u062b \u0645\u0627 \u0642\u0628\u0644 \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629 \u0627\u0644\u0645\u0643\u062b\u0641\u0629\u060c \u0648\u064a\u0647\u062f\u0641 \u0625\u0644\u0649 \u062a\u062d\u0642\u064a\u0642 \u062a\u0639\u0628\u064a\u0631 \u0645\u0633\u062a\u062f\u0627\u0645 \u0639\u0646 \u0628\u0631\u0648\u062a\u064a\u0646 \u0627\u0644\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0627\u0644\u0635\u063a\u064a\u0631 \u0645\u0639 \u062a\u062d\u0633\u064a\u0646 \u0627\u0644\u0633\u0644\u0627\u0645\u0629.<\/p>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"clinical-development\">\u0627\u0644\u062a\u0637\u0648\u064a\u0631 \u0627\u0644\u0633\u0631\u064a\u0631\u064a<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u062f\u062e\u0644 \u0627\u0644\u0645\u0631\u0643\u0628 GNT-0004 \u0645\u0631\u062d\u0644\u0629 \u0627\u0644\u062a\u0642\u064a\u064a\u0645 \u0627\u0644\u0633\u0631\u064a\u0631\u064a \u0628\u0645\u0624\u0634\u0631\u0627\u062a \u0645\u0628\u0643\u0631\u0629 \u0648\u0627\u0639\u062f\u0629:<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u0627\u0644\u062a\u0639\u0628\u064a\u0631 \u0627\u0644\u0645\u0633\u062a\u0642\u0631 \u0639\u0646 \u0627\u0644\u0645\u064a\u0643\u0631\u0648-\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0644\u062f\u0649 \u0627\u0644\u0645\u0631\u0636\u0649 \u0627\u0644\u0645\u0639\u0627\u0644\u062c\u064a\u0646<\/li>\n\n\n\n<li>\u0633\u062c\u0644 \u0623\u0645\u0627\u0646 \u0625\u064a\u062c\u0627\u0628\u064a \u0645\u0639 \u0639\u062f\u0645 \u0627\u0644\u0625\u0628\u0644\u0627\u063a \u0639\u0646 \u0623\u064a \u0623\u062d\u062f\u0627\u062b \u0636\u0627\u0626\u0631\u0629 \u062e\u0637\u064a\u0631\u0629 \u0641\u064a \u0627\u0644\u0645\u062c\u0645\u0648\u0639\u0627\u062a \u0627\u0644\u0623\u0648\u0644\u064a\u0629.<\/li>\n\n\n\n<li>\u0623\u062f\u0644\u0629 \u0639\u0644\u0649 \u0627\u062a\u062c\u0627\u0647\u0627\u062a \u0627\u0644\u062a\u062d\u0633\u0646 \u0627\u0644\u0648\u0638\u064a\u0641\u064a<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\">\u064a\u062a\u0639\u0644\u0645 \u0623\u0643\u062b\u0631: <a href=\"https:\/\/dmdwarrior.com\/ar\/genethon-gnt0004-gene-therapy-duchenne-muscular-dystrophy\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u062d\u0648\u0644 GNT-0004<\/a><\/p>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"scientific-contribution\">\u0627\u0644\u0645\u0633\u0627\u0647\u0645\u0629 \u0627\u0644\u0639\u0644\u0645\u064a\u0629<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u064a\u0631\u0643\u0632 \u0646\u0647\u062c Genethon \u0639\u0644\u0649 \u0645\u0627 \u064a\u0644\u064a:<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u0647\u0646\u062f\u0633\u0629 \u0627\u0644\u0645\u062a\u062c\u0647\u0627\u062a \u0627\u0644\u062f\u0642\u064a\u0642\u0629<\/li>\n\n\n\n<li>\u0627\u0646\u062e\u0641\u0627\u0636 \u0627\u0644\u0642\u062f\u0631\u0629 \u0639\u0644\u0649 \u0625\u062b\u0627\u0631\u0629 \u0627\u0644\u0627\u0633\u062a\u062c\u0627\u0628\u0629 \u0627\u0644\u0645\u0646\u0627\u0639\u064a\u0629<\/li>\n\n\n\n<li>\u0627\u0633\u062a\u062f\u0627\u0645\u0629 \u0627\u0644\u062a\u0639\u0628\u064a\u0631 \u0627\u0644\u062c\u064a\u0646\u064a \u0639\u0644\u0649 \u0627\u0644\u0645\u062f\u0649 \u0627\u0644\u0637\u0648\u064a\u0644<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\">\u0648\u0647\u0630\u0627 \u064a\u062c\u0639\u0644 GNT-0004 \u0645\u0646\u0627\u0641\u0633\u064b\u0627 \u0642\u0648\u064a\u064b\u0627 \u0641\u064a \u0627\u0644\u0645\u062c\u0627\u0644 \u0627\u0644\u062a\u0646\u0627\u0641\u0633\u064a \u0644\u0644\u0639\u0644\u0627\u062c\u0627\u062a \u0627\u0644\u062c\u064a\u0646\u064a\u0629 \u0627\u0644\u062c\u062f\u064a\u062f\u0629 \u0627\u0644\u0645\u062d\u062a\u0645\u0644\u0629 \u0644\u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a.<\/p>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"emerging-gene-therapy-research-in-china-and-russia\">\u0623\u0628\u062d\u0627\u062b \u0627\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u062c\u064a\u0646\u064a \u0627\u0644\u0646\u0627\u0634\u0626\u0629 \u0641\u064a \u0627\u0644\u0635\u064a\u0646 \u0648\u0631\u0648\u0633\u064a\u0627<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u0625\u0644\u0649 \u062c\u0627\u0646\u0628 \u0634\u0631\u0643\u0627\u062a \u0627\u0644\u062a\u0643\u0646\u0648\u0644\u0648\u062c\u064a\u0627 \u0627\u0644\u062d\u064a\u0648\u064a\u0629 \u0627\u0644\u063a\u0631\u0628\u064a\u0629\u060c \u064a\u062c\u0631\u064a \u0627\u0644\u0628\u062d\u062b \u0628\u0646\u0634\u0627\u0637 \u0641\u064a \u0627\u0644\u0635\u064a\u0646 \u0648\u0631\u0648\u0633\u064a\u0627 \u0639\u0646 \u0639\u0644\u0627\u062c\u0627\u062a \u062c\u064a\u0646\u064a\u0629 \u062c\u062f\u064a\u062f\u0629 \u0645\u062d\u062a\u0645\u0644\u0629 \u0644\u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a. \u0648\u062a\u0633\u0627\u0647\u0645 \u0647\u0627\u062a\u0627\u0646 \u0627\u0644\u0645\u0646\u0637\u0642\u062a\u0627\u0646 \u0628\u0634\u0643\u0644 \u0645\u062a\u0632\u0627\u064a\u062f \u0641\u064a \u0627\u0644\u062c\u0647\u0648\u062f \u0627\u0644\u0639\u0627\u0644\u0645\u064a\u0629 \u0644\u0644\u0628\u062d\u0648\u062b \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629.<\/p>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"china\">\u0627\u0644\u0635\u064a\u0646<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u0627\u0644\u0645\u0624\u0633\u0633\u0627\u062a \u0627\u0644\u0628\u062d\u062b\u064a\u0629 \u0648\u0634\u0631\u0643\u0627\u062a \u0627\u0644\u062a\u0643\u0646\u0648\u0644\u0648\u062c\u064a\u0627 \u0627\u0644\u062d\u064a\u0648\u064a\u0629 \u0627\u0644\u0635\u064a\u0646\u064a\u0629 \u0647\u064a:<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u062a\u0637\u0648\u064a\u0631 \u0627\u0644\u0639\u0644\u0627\u062c\u0627\u062a \u0627\u0644\u062c\u064a\u0646\u064a\u0629 \u0627\u0644\u0642\u0627\u0626\u0645\u0629 \u0639\u0644\u0649 \u0627\u0644\u0641\u064a\u0631\u0648\u0633\u0627\u062a \u0627\u0644\u063a\u062f\u064a\u0629 \u0627\u0644\u0645\u0631\u062a\u0628\u0637\u0629 (AAV) \u0628\u0627\u0633\u062a\u062e\u062f\u0627\u0645 \u0623\u063a\u0644\u0641\u0629 \u062c\u062f\u064a\u062f\u0629<\/li>\n\n\n\n<li>\u0625\u062c\u0631\u0627\u0621 \u0627\u0644\u062a\u062c\u0627\u0631\u0628 \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629 \u0641\u064a \u0627\u0644\u0645\u0631\u0627\u062d\u0644 \u0627\u0644\u0645\u0628\u0643\u0631\u0629<\/li>\n\n\n\n<li>\u0627\u0633\u062a\u0643\u0634\u0627\u0641 \u0627\u0633\u062a\u0631\u0627\u062a\u064a\u062c\u064a\u0627\u062a \u0627\u0644\u062a\u0635\u0646\u064a\u0639 \u0627\u0644\u0641\u0639\u0627\u0644\u0629 \u0645\u0646 \u062d\u064a\u062b \u0627\u0644\u062a\u0643\u0644\u0641\u0629<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\">\u062a\u0634\u064a\u0631 \u0627\u0644\u062a\u0642\u0627\u0631\u064a\u0631 \u0627\u0644\u0623\u0648\u0644\u064a\u0629 \u0625\u0644\u0649 \u0645\u0633\u062a\u0648\u064a\u0627\u062a \u0648\u0627\u0639\u062f\u0629 \u0645\u0646 \u0627\u0644\u062a\u0639\u0628\u064a\u0631 \u0639\u0646 \u0627\u0644\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0648\u0627\u0644\u062a\u062d\u0633\u0646 \u0627\u0644\u0648\u0638\u064a\u0641\u064a\u060c \u0639\u0644\u0649 \u0627\u0644\u0631\u063a\u0645 \u0645\u0646 \u0627\u0644\u062d\u0627\u062c\u0629 \u0625\u0644\u0649 \u0628\u064a\u0627\u0646\u0627\u062a \u0637\u0648\u064a\u0644\u0629 \u0627\u0644\u0623\u062c\u0644.<\/p>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"russia\">\u0631\u0648\u0633\u064a\u0627<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u0641\u064a \u0631\u0648\u0633\u064a\u0627\u060c \u0645\u0631\u0627\u0643\u0632 \u0627\u0644\u0628\u062d\u0648\u062b \u0627\u0644\u0623\u0643\u0627\u062f\u064a\u0645\u064a\u0629 \u0648\u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629 \u0647\u064a:<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u0627\u0644\u0628\u062d\u062b \u0641\u064a \u0627\u0644\u0646\u0648\u0627\u0642\u0644 \u0627\u0644\u0641\u064a\u0631\u0648\u0633\u064a\u0629 \u0627\u0644\u0628\u062f\u064a\u0644\u0629 \u0648\u0637\u0631\u0642 \u062a\u0648\u0635\u064a\u0644\u0647\u0627<\/li>\n\n\n\n<li>\u062a\u0637\u0648\u064a\u0631 \u0645\u0646\u0635\u0627\u062a \u0627\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u062c\u064a\u0646\u064a \u0627\u0644\u0645\u0646\u062a\u062c\u0629 \u0645\u062d\u0644\u064a\u0627\u064b<\/li>\n\n\n\n<li>\u062a\u0648\u0633\u064a\u0639 \u0646\u0637\u0627\u0642 \u0627\u0644\u0648\u0635\u0648\u0644 \u0625\u0644\u0649 \u0627\u0644\u0639\u0644\u0627\u062c\u0627\u062a \u0627\u0644\u062a\u062c\u0631\u064a\u0628\u064a\u0629<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\">\u0639\u0644\u0649 \u0627\u0644\u0631\u063a\u0645 \u0645\u0646 \u0623\u0646 \u0634\u0641\u0627\u0641\u064a\u0629 \u0627\u0644\u0628\u064a\u0627\u0646\u0627\u062a \u0644\u0627 \u062a\u0632\u0627\u0644 \u0645\u062d\u062f\u0648\u062f\u0629\u060c \u0625\u0644\u0627 \u0623\u0646 \u0627\u0644\u0645\u0624\u0634\u0631\u0627\u062a \u0627\u0644\u0645\u0628\u0643\u0631\u0629 \u062a\u0634\u064a\u0631 \u0625\u0644\u0649 \u0623\u0646 \u0647\u0630\u0647 \u0627\u0644\u062f\u0631\u0627\u0633\u0627\u062a \u0642\u062f \u062a\u0633\u0627\u0647\u0645 \u0641\u064a \u062a\u0642\u062f\u064a\u0645 \u0631\u0624\u0649 \u0642\u064a\u0645\u0629 \u062d\u0648\u0644 \u0627\u0644\u062a\u0637\u0648\u0631 \u0627\u0644\u0639\u0627\u0644\u0645\u064a \u0644\u0644\u0639\u0644\u0627\u062c\u0627\u062a \u0627\u0644\u062c\u064a\u0646\u064a\u0629 \u0627\u0644\u062c\u062f\u064a\u062f\u0629 \u0627\u0644\u0645\u062d\u062a\u0645\u0644\u0629 \u0644\u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a.<\/p>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"a-hopeful-outlook\">\u0646\u0638\u0631\u0629 \u0645\u062a\u0641\u0627\u0626\u0644\u0629<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u0645\u0646 \u0627\u0644\u0645\u0634\u062c\u0639 \u0623\u0646 \u062a\u062a\u0648\u0633\u0639 \u0623\u0628\u062d\u0627\u062b \u0627\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u062c\u064a\u0646\u064a \u0639\u0627\u0644\u0645\u064a\u064b\u0627. \u0646\u062a\u0627\u0628\u0639 \u0647\u0630\u0647 \u0627\u0644\u062a\u0637\u0648\u0631\u0627\u062a \u0639\u0646 \u0643\u062b\u0628\u060c \u0648\u062a\u0634\u064a\u0631 \u0627\u0644\u0645\u0624\u0634\u0631\u0627\u062a \u0627\u0644\u0623\u0648\u0644\u064a\u0629 \u0625\u0644\u0649 \u0623\u0646 \u0627\u0644\u062f\u0631\u0627\u0633\u0627\u062a \u0627\u0644\u062c\u0627\u0631\u064a\u0629 \u0641\u064a \u0643\u0644 \u0645\u0646 \u0627\u0644\u0635\u064a\u0646 \u0648\u0631\u0648\u0633\u064a\u0627 \u0648\u0627\u0639\u062f\u0629. <strong>\u0645\u0639 \u062a\u0648\u0641\u0631 \u0627\u0644\u0645\u0632\u064a\u062f \u0645\u0646 \u0627\u0644\u0628\u064a\u0627\u0646\u0627\u062a\u060c \u0642\u062f \u062a\u0624\u062f\u064a \u0647\u0630\u0647 \u0627\u0644\u062c\u0647\u0648\u062f \u0625\u0644\u0649 \u062a\u0633\u0631\u064a\u0639 \u0643\u0628\u064a\u0631 \u0641\u064a \u062a\u0648\u0641\u064a\u0631 \u0627\u0644\u0639\u0644\u0627\u062c\u0627\u062a \u0627\u0644\u062c\u064a\u0646\u064a\u0629 \u0627\u0644\u062c\u062f\u064a\u062f\u0629 \u0627\u0644\u0645\u062d\u062a\u0645\u0644\u0629 \u0644\u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a \u0641\u064a \u062c\u0645\u064a\u0639 \u0623\u0646\u062d\u0627\u0621 \u0627\u0644\u0639\u0627\u0644\u0645 \u0648\u0628\u0623\u0633\u0639\u0627\u0631 \u0645\u0639\u0642\u0648\u0644\u0629.<\/strong><\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u062a\u0627\u0628\u0639 \u0647\u0630\u0647 \u0627\u0644\u0635\u0641\u062d\u0629<\/strong>&nbsp;&gt;&gt;&gt;&nbsp;<a href=\"https:\/\/dmdwarrior.com\/ar\/dmd-therapies\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u062c\u0645\u064a\u0639 \u0627\u0644\u062a\u062c\u0627\u0631\u0628 \u0627\u0644\u0633\u0631\u064a\u0631\u064a\u0629 \u0644\u0645\u0631\u0636 \u062f\u0648\u0634\u064a\u0646<\/a><\/p>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"challenges-and-limitations-of-gene-therapy-in-dmd\">\u062a\u062d\u062f\u064a\u0627\u062a \u0648\u0642\u064a\u0648\u062f \u0627\u0644\u0639\u0644\u0627\u062c \u0627\u0644\u062c\u064a\u0646\u064a \u0641\u064a \u0636\u0645\u0648\u0631 \u0627\u0644\u0639\u0636\u0644\u0627\u062a \u0627\u0644\u062f\u0648\u0634\u064a\u0646\u064a<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u0639\u0644\u0649 \u0627\u0644\u0631\u063a\u0645 \u0645\u0646 \u0627\u0644\u062a\u0642\u062f\u0645 \u0627\u0644\u0643\u0628\u064a\u0631\u060c \u0644\u0627 \u062a\u0632\u0627\u0644 \u0647\u0646\u0627\u0643 \u0639\u062f\u0629 \u062a\u062d\u062f\u064a\u0627\u062a \u0642\u0627\u0626\u0645\u0629:<\/p>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"immunogenicity\">\u0627\u0644\u0642\u062f\u0631\u0629 \u0639\u0644\u0649 \u0625\u062d\u062f\u0627\u062b \u0627\u0633\u062a\u062c\u0627\u0628\u0629 \u0645\u0646\u0627\u0639\u064a\u0629<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u064a\u0645\u0643\u0646 \u0623\u0646 \u062a\u062d\u062f \u0627\u0644\u0623\u062c\u0633\u0627\u0645 \u0627\u0644\u0645\u0636\u0627\u062f\u0629 \u0627\u0644\u0645\u0648\u062c\u0648\u062f\u0629 \u0645\u0633\u0628\u0642\u064b\u0627 \u0636\u062f \u0646\u0627\u0642\u0644\u0627\u062a \u0627\u0644\u0641\u064a\u0631\u0648\u0633\u0627\u062a \u0627\u0644\u063a\u062f\u064a\u0629 \u0627\u0644\u0645\u0631\u062a\u0628\u0637\u0629 (AAV) \u0645\u0646 \u0623\u0647\u0644\u064a\u0629 \u0627\u0644\u0645\u0631\u064a\u0636.<\/p>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"durability\">\u0645\u062a\u0627\u0646\u0629<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u0644\u0627 \u064a\u0632\u0627\u0644 \u0627\u0644\u062a\u0639\u0628\u064a\u0631 \u0637\u0648\u064a\u0644 \u0627\u0644\u0623\u0645\u062f \u0639\u0646 \u0628\u0631\u0648\u062a\u064a\u0646 \u0627\u0644\u062f\u064a\u0633\u062a\u0631\u0648\u0641\u064a\u0646 \u0627\u0644\u0635\u063a\u064a\u0631 \u063a\u064a\u0631 \u0645\u0624\u0643\u062f.<\/p>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"manufacturing-constraints\">\u0642\u064a\u0648\u062f \u0627\u0644\u062a\u0635\u0646\u064a\u0639<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u0625\u0646 \u062a\u0648\u0633\u064a\u0639 \u0646\u0637\u0627\u0642 \u0627\u0644\u0625\u0646\u062a\u0627\u062c \u0645\u0639 \u0627\u0644\u062d\u0641\u0627\u0638 \u0639\u0644\u0649 \u0627\u0644\u062c\u0648\u062f\u0629 \u0623\u0645\u0631 \u0645\u0639\u0642\u062f \u0648\u0645\u0643\u0644\u0641.<\/p>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"cost-and-accessibility\">\u0627\u0644\u062a\u0643\u0644\u0641\u0629 \u0648\u0625\u0645\u0643\u0627\u0646\u064a\u0629 \u0627\u0644\u0648\u0635\u0648\u0644<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u0645\u0646 \u0627\u0644\u0645\u062a\u0648\u0642\u0639 \u0623\u0646 \u062a\u0643\u0648\u0646 \u0627\u0644\u0639\u0644\u0627\u062c\u0627\u062a \u0627\u0644\u062c\u064a\u0646\u064a\u0629 \u0628\u0627\u0647\u0638\u0629 \u0627\u0644\u062b\u0645\u0646 \u0644\u0644\u063a\u0627\u064a\u0629\u060c \u0645\u0645\u0627 \u064a\u062b\u064a\u0631 \u0645\u062e\u0627\u0648\u0641 \u0628\u0634\u0623\u0646 \u0625\u0645\u0643\u0627\u0646\u064a\u0629 \u0627\u0644\u0648\u0635\u0648\u0644 \u0625\u0644\u064a\u0647\u0627 \u0639\u0644\u0649 \u0645\u0633\u062a\u0648\u0649 \u0627\u0644\u0639\u0627\u0644\u0645.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u064a\u062a\u0639\u0644\u0645 \u0623\u0643\u062b\u0631: <a href=\"https:\/\/dmdwarrior.com\/ar\/duchenne-muscular-dystrophy-treatment-cost\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u0644\u0645\u0627\u0630\u0627 \u0623\u0635\u0628\u062d\u062a \u062a\u0643\u0627\u0644\u064a\u0641 \u0639\u0644\u0627\u062c \u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a \u062e\u0627\u0631\u062c\u0629 \u0639\u0646 \u0627\u0644\u0633\u064a\u0637\u0631\u0629\u061f<\/a><\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u0625\u0646 \u0645\u0639\u0627\u0644\u062c\u0629 \u0647\u0630\u0647 \u0627\u0644\u062a\u062d\u062f\u064a\u0627\u062a \u0623\u0645\u0631 \u0636\u0631\u0648\u0631\u064a \u0644\u0627\u0639\u062a\u0645\u0627\u062f \u0648\u0627\u0633\u0639 \u0627\u0644\u0646\u0637\u0627\u0642 \u0644\u0644\u0639\u0644\u0627\u062c\u0627\u062a \u0627\u0644\u062c\u064a\u0646\u064a\u0629 \u0627\u0644\u062c\u062f\u064a\u062f\u0629 \u0627\u0644\u0645\u062d\u062a\u0645\u0644\u0629 \u0644\u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a.<\/strong><\/p>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"future-directions-and-innovations\">\u0627\u0644\u062a\u0648\u062c\u0647\u0627\u062a \u0627\u0644\u0645\u0633\u062a\u0642\u0628\u0644\u064a\u0629 \u0648\u0627\u0644\u0627\u0628\u062a\u0643\u0627\u0631\u0627\u062a<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u0642\u062f \u062a\u0634\u0645\u0644 \u0645\u0633\u062a\u0642\u0628\u0644 \u0627\u0644\u0639\u0644\u0627\u062c\u0627\u062a \u0627\u0644\u062c\u064a\u0646\u064a\u0629 \u0627\u0644\u062c\u062f\u064a\u062f\u0629 \u0627\u0644\u0645\u062d\u062a\u0645\u0644\u0629 \u0644\u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a \u0645\u0627 \u064a\u0644\u064a:<\/strong><\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li><strong>\u062a\u0642\u0646\u064a\u0627\u062a \u062a\u0639\u062f\u064a\u0644 \u0627\u0644\u062c\u064a\u0646\u0627\u062a (CRISPR\/Cas9) \u0644\u062a\u0635\u062d\u064a\u062d \u0627\u0644\u0637\u0641\u0631\u0627\u062a \u0645\u0628\u0627\u0634\u0631\u0629<\/strong><\/li>\n\n\n\n<li>\u0646\u0648\u0627\u0642\u0644 \u0645\u0646 \u0627\u0644\u062c\u064a\u0644 \u0627\u0644\u062a\u0627\u0644\u064a \u0630\u0627\u062a \u0642\u062f\u0631\u0629 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\u0646\u0637\u0627\u0642 \u0627\u0644\u0645\u0631\u0636\u0649 \u0627\u0644\u0645\u0624\u0647\u0644\u064a\u0646 \u0644\u0644\u0639\u0644\u0627\u062c.<\/p>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"conclusion\">\u062e\u0627\u062a\u0645\u0629<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u064a\u0645\u062b\u0644 \u062a\u0637\u0648\u064a\u0631 \u0639\u0644\u0627\u062c\u0627\u062a \u062c\u064a\u0646\u064a\u0629 \u062c\u062f\u064a\u062f\u0629 \u0645\u062d\u062a\u0645\u0644\u0629 \u0644\u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a \u0623\u062d\u062f \u0623\u0647\u0645 \u0627\u0644\u062a\u0637\u0648\u0631\u0627\u062a \u0641\u064a \u0637\u0628 \u0627\u0644\u0623\u0639\u0635\u0627\u0628 \u0648\u0627\u0644\u0639\u0636\u0644\u0627\u062a.<\/strong> \u062a\u064f\u0638\u0647\u0631 \u0639\u0644\u0627\u062c\u0627\u062a \u0645\u062b\u0644 SGT-003 \u0648RGX-202 \u0648GNT-0004 \u0627\u0644\u0648\u062a\u064a\u0631\u0629 \u0627\u0644\u0633\u0631\u064a\u0639\u0629 \u0644\u0644\u0627\u0628\u062a\u0643\u0627\u0631 \u0648\u0627\u0644\u062a\u0637\u0648\u0631 \u0627\u0644\u0645\u062a\u0632\u0627\u064a\u062f \u0644\u062a\u0642\u0646\u064a\u0627\u062a \u062a\u0648\u0635\u064a\u0644 \u0627\u0644\u062c\u064a\u0646\u0627\u062a.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u0648\u0641\u064a \u0627\u0644\u0648\u0642\u062a \u0646\u0641\u0633\u0647\u060c \u0641\u0625\u0646 \u062a\u0648\u0633\u064a\u0639 \u062c\u0647\u0648\u062f \u0627\u0644\u0628\u062d\u062b \u0641\u064a \u0627\u0644\u0635\u064a\u0646 \u0648\u0631\u0648\u0633\u064a\u0627 \u064a\u0648\u0641\u0631 \u0623\u0645\u0644\u0627\u064b \u0625\u0636\u0627\u0641\u064a\u0627\u064b \u0641\u064a \u0623\u0646 \u0627\u0644\u062a\u0639\u0627\u0648\u0646 \u0627\u0644\u0639\u0627\u0644\u0645\u064a \u0633\u064a\u0633\u0631\u0639 \u0627\u0644\u062a\u0642\u062f\u0645 \u0648\u064a\u062d\u0633\u0646 \u0625\u0645\u0643\u0627\u0646\u064a\u0629 \u0627\u0644\u0648\u0635\u0648\u0644.<\/strong> \u0639\u0644\u0649 \u0627\u0644\u0631\u063a\u0645 \u0645\u0646 \u0627\u0633\u062a\u0645\u0631\u0627\u0631 \u0648\u062c\u0648\u062f \u0627\u0644\u062a\u062d\u062f\u064a\u0627\u062a\u060c \u0625\u0644\u0627 \u0623\u0646 \u0645\u0633\u0627\u0631 \u0647\u0630\u0647 \u0627\u0644\u0639\u0644\u0627\u062c\u0627\u062a \u0648\u0627\u0639\u062f \u0628\u0644\u0627 \u0634\u0643\u060c \u0645\u0645\u0627 \u064a\u0642\u0631\u0628\u0646\u0627 \u0645\u0646 \u0645\u0633\u062a\u0642\u0628\u0644 \u064a\u0645\u0643\u0646 \u0641\u064a\u0647 \u0625\u062f\u0627\u0631\u0629 \u0636\u0645\u0648\u0631 \u062f\u0648\u0634\u064a\u0646 \u0627\u0644\u0639\u0636\u0644\u064a \u0628\u0634\u0643\u0644 \u0641\u0639\u0627\u0644 - \u0623\u0648 \u062d\u062a\u0649 \u062a\u063a\u064a\u064a\u0631\u0647 \u0628\u0634\u0643\u0644 \u062c\u0630\u0631\u064a - \u0645\u0646 \u062e\u0644\u0627\u0644 \u0627\u0644\u0637\u0628 \u0627\u0644\u062c\u064a\u0646\u064a.<\/p>","protected":false},"excerpt":{"rendered":"<p>The landscape of potential new gene therapies for Duchenne muscular dystrophy (DMD) is rapidly evolving, offering renewed hope for patients and families affected by this devastating neuromuscular disorder. Among the most closely watched approaches are Solid Biosciences SGT-003, RegenxBio RGX-202, and Genethon GNT-0004, which represent the next wave of innovation in genetic medicine. These emerging [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":7484,"comment_status":"open","ping_status":"open","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[282],"tags":[33,72,61,105,106,107,108,65,110,109],"class_list":["post-2261","post","type-post","status-publish","format-standard","has-post-thumbnail","category-editorials","tag-elevidys","tag-gene-editing","tag-gene-therapy","tag-genethon","tag-gnt-0004","tag-regenxbio","tag-rgx-202","tag-sarepta","tag-sgt-003","tag-solid-biosciences"],"_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/posts\/2261","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/comments?post=2261"}],"version-history":[{"count":0,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/posts\/2261\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/media\/7484"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/media?parent=2261"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/categories?post=2261"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/ar\/wp-json\/wp\/v2\/tags?post=2261"}],"curies":[{"name":"\u0648\u0648\u0631\u062f\u0628\u0631\u064a\u0633","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}